To Evaluate the Safety and Efficacy of GC1111 (Recombinant Human Iduronate-2-sulfatase) in Hunter Syndrome Patients

NCT ID: NCT01301898

Last Updated: 2012-02-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

31 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-05-31

Study Completion Date

2011-03-31

Brief Summary

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The purpose of this study is to evaluate the safety and efficacy of GC1111 (recombinant human iduronate-w-sulfatase) in Hunter Syndrome (Mucopolysaccharidosis II) patients

Detailed Description

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Conditions

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Mucopolysaccharidosis II

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Participants

Study Groups

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GC1111_0.5mg/kg

Group Type EXPERIMENTAL

GC1111_0.5mg/kg

Intervention Type DRUG

GC1111_1.0mg/kg

Group Type EXPERIMENTAL

GC1111_1.0mg/kg

Intervention Type DRUG

Elaprase_0.5mg/kg

Group Type ACTIVE_COMPARATOR

Elaprase_0.5mg/kg

Intervention Type DRUG

Interventions

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GC1111_0.5mg/kg

Intervention Type DRUG

GC1111_1.0mg/kg

Intervention Type DRUG

Elaprase_0.5mg/kg

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Patients with diagnosis of MPS II based on both clinical and biochemical criteria
2. Male, ages 6 to 35 years old
3. Patients who are able to comply with the study requirements
4. Patients who have given voluntary written consent to participate in the study
5. Patients who is acceptable for using an appropriate method of contraception

Exclusion Criteria

1. History of a tracheostomy or a bone marrow transplant
2. Known hypersensitivity to idursulfase
3. Known shock to idursulfase
4. History of receiving treatment with another investigational therapy within the past 30 days
5. History of a stem cell transplant
6. Known hypersensitivity to any of the components of idursulfase
7. Female
Minimum Eligible Age

6 Years

Maximum Eligible Age

35 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Green Cross Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Samsung Medical Center

Seoul, Irwon-dong, Gangnam-Gu, South Korea

Site Status

Countries

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South Korea

References

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Sohn YB, Cho SY, Park SW, Kim SJ, Ko AR, Kwon EK, Han SJ, Jin DK. Phase I/II clinical trial of enzyme replacement therapy with idursulfase beta in patients with mucopolysaccharidosis II (Hunter syndrome). Orphanet J Rare Dis. 2013 Mar 18;8:42. doi: 10.1186/1750-1172-8-42.

Reference Type DERIVED
PMID: 23497636 (View on PubMed)

Other Identifiers

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GC1111_P1/2

Identifier Type: -

Identifier Source: org_study_id

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