Trial to Assess the Effect of Long Term Dosing of Inclisiran in Subjects With High CV Risk and Elevated LDL-C

NCT ID: NCT03814187

Last Updated: 2024-03-06

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

3275 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-04-16

Study Completion Date

2023-02-13

Brief Summary

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The purpose of this extension study was to evaluate the efficacy, safety, and tolerability of long-term dosing of Inclisiran. The study was a global multicenter study.

Detailed Description

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This study was an open label, long term extension study in subjects with atherosclerotic cardiovascular disease (ASCVD), ASCVD-risk equivalents (eg, diabetes and familial hypercholesterolemia), or heterozygous familial hypercholesterolemia (HeFH) and elevated low density lipoprotein cholesterol (LDL-C) despite maximum tolerated dose of LDL-C lowering therapies who have completed the inclisiran Phase II trial MDCO-PCS-16-01 (ORION-3; NCT03060577), or any of the following Phase III lipid lowering studies: MDCO-PCS-17-03 (ORION-9; NCT03397121), MDCO-PCS-17-04 (ORION-10; NCT03399370), or MDCO-PCS-17-08 (ORION-11; NCT03400800).

The End of Study (EOS) visit in the previous feeder studies was Day 1 in this extension study.The duration that each subject participated in this study was a maximum of 3 years. However, for subjects from the Study ORION-3, the Sponsor decided to end the study prior to completion of their full 3-year of participation. It is recorded in the database as discontinuation was due to Sponsor's decision.

In this Phase III extension study, the same study drug of inclisiran sodium 300 mg (equivalent to 284 mg inclisiran) was administered as a single subcutaneous (SC) dose every 180 days from the last dose in previous feeder study (except for subjects newly initiating inclisiran, who received the first two doses 90 days apart) until the end of the study.

On Day 1 (EOS visit in the feeder study), subjects from the previous feeder studies received blinded study medication except subjects from Study ORION-3. Subjects who received placebo in the previous Phase III feeder study received blinded inclisiran and subjects who received inclisiran in the previous feeder study received blinded placebo at this visit, so that subjects previously on placebo received the correct dosing regime, i.e. a dose at Day 1, Day 90 and every 180-days thereafter. Subjects previously treated with inclisiran did not need a dose of inclisiran to maintain every 180-dosing regime and therefore, were given placebo in order to maintain the blinding of the feeder study. Subjects that moved over from ORION-3 received the first study medication at Day 90, as this study was already open-label.

On Day 90, all subjects received inclisiran sodium 300 mg. This is 180 days after the last injection in the previous feeder study for subjects that received inclisiran and was the second dose of inclisiran for the subjects that received placebo in the feeder study. The EOS visit occurred at Day 1080.

This extension study allowed subjects continued access to inclisiran treatment and allowed the collection of additional efficacy and safety data for long-term use beyond the end of the feeder studies.

Conditions

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ASCVD Elevated Cholesterol Heterozygous Familial Hypercholesterolemia Homozygous Familial Hypercholesterolemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Inclisiran

Inclisiran sodium 300 milligrams (mg) was administered as a single SC injection on Day 1\*, 90, then every 180 days to Day 990.

\*Subjects who received blinded placebo in the feeder study received blinded inclisiran and subjects who received blinded inclisiran in the feeder study received blinded placebo on Day 1 in ORION-8. Subjects from the open label ORION-3 study did not receive any injection of study drug on Day 1. Their first dose of study medication was at day 90

Group Type EXPERIMENTAL

Inclisiran Sodium

Intervention Type DRUG

Inclisiran is a small interfering ribonucleic acid (RNA) that inhibits PCSK9 synthesis.

Interventions

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Inclisiran Sodium

Inclisiran is a small interfering ribonucleic acid (RNA) that inhibits PCSK9 synthesis.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Completion on a previously qualifying inclisiran Phase II trial MDCO-PCS-16-01 (ORION-3), or Phase III lipid lowering ORION feeder study \[MDCO-PCS-17-03 (ORION-9), MDCO-PCS-17-4 (ORION-10), or MDCO-PCS-17-08 (ORION-11)\] meaning the subject received the last dose of study drug and completed the final study visit per applicable protocol.
2. On current lipid-lowering therapies (such as a statin and/or ezetimibe) from previous study with no planned medication or dose change during study participation.
3. Willing and able to give informed consent before initiation of any study-related procedures and willing to comply with all required study procedures.

Exclusion Criteria

1. Any uncontrolled or serious disease, or any medical or surgical condition, that may either interfere with participation in the clinical study, and/or put the subject at significant risk \[according to investigator's (or delegate's) judgment\] if he/she participates in the clinical study.
2. An underlying known disease, or surgical, physical, or medical condition that, in the opinion of the investigator (or delegate) might interfere with interpretation of the clinical study results.
3. Severe concomitant noncardiovascular disease that carries the risk of reducing life expectancy to less than 3 years,
4. Active liver disease defined as any known current infectious, neoplastic, or metabolic pathology of the liver or unexplained alanine aminotransferase (ALT), aspartate aminotransferase (AST), elevation \>3x the upper limit of normal (ULN), or total bilirubin (TBIL) elevation \>2x ULN at the last recorded visit in the feeder study prior to study entry visit.
5. Females who are pregnant or nursing, or who are of childbearing potential and unwilling to use at least one method of acceptable effective contraception (eg, oral contraceptives, barrier methods, approved contraceptive implant, long-term injectable contraception, intrauterine device) for the entire duration of the study. Exemptions from this criterion:

1. Women \>2 years postmenopausal (defined as 1 year or longer since last menstrual period) and more than 55 years of age.
2. Postmenopausal women (as defined above) and less than 55 years of age with a negative pregnancy test within 24 hours of randomization.
3. Women who are surgically sterilized at least 3 months prior to enrollment.
6. Planned use of other investigational medicinal products other than inclisiran or devices during the course of the study.
7. Any condition that according to the investigator could interfere with the conduct of the study, such as but not limited to:

1. Subjects who are unable to communicate or to cooperate with the investigator
2. Unable to understand the protocol requirements, instructions and study-related restrictions, the nature, scope, and possible consequences of the study (including subjects whose cooperation is doubtful due to drug abuse or alcohol dependency)
3. Unlikely to comply with the protocol requirements, instructions, and study-related restrictions (eg, uncooperative attitude, inability to return for follow-up visits, and improbability of completing the study)
4. Have any medical or surgical condition, which in the opinion of the investigator would put the subject at increased risk from participating in the study
5. Persons directly involved in the conduct of the study.

The above information is not intended to contain all considerations relevant to a participant's potential participation in a clinical trial.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Scott Wright, MD

Role: PRINCIPAL_INVESTIGATOR

Mayo Clinic

Locations

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Research Site 10001-015

Birmingham, Alabama, United States

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Research Site 10001-138

Foley, Alabama, United States

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Research Site 10001-113

Huntsville, Alabama, United States

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Research Site 10001-058

Mobile, Alabama, United States

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Montgomery, Alabama, United States

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Research Site 10001-076

Saraland, Alabama, United States

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Chandler, Arizona, United States

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Mesa, Arizona, United States

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Phoenix, Arizona, United States

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Surprise, Arizona, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Beverly Hills, California, United States

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Canoga Park, California, United States

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Carlsbad, California, United States

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Research Site 10001-065

El Cajon, California, United States

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Los Angeles, California, United States

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Research Site 90001-005

Mission Viejo, California, United States

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Northridge, California, United States

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Northridge, California, United States

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Sacramento, California, United States

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San Ramon, California, United States

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Santa Rosa, California, United States

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Spring Valley, California, United States

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Stanford, California, United States

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Torrance, California, United States

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Boca Raton, Florida, United States

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Clearwater, Florida, United States

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Clearwater, Florida, United States

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Clearwater, Florida, United States

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Daytona Beach, Florida, United States

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Fleming Island, Florida, United States

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Fort Lauderdale, Florida, United States

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Hialeah, Florida, United States

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Jacksonville, Florida, United States

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Jacksonville, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami Springs, Florida, United States

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Pembroke Pines, Florida, United States

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Pembroke Pines, Florida, United States

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Pembroke Pines, Florida, United States

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Pembroke Pines, Florida, United States

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Pinellas Park, Florida, United States

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Ponte Vedra, Florida, United States

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Saint Augustine, Florida, United States

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Sarasota, Florida, United States

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St. Petersburg, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Dunwoody, Georgia, United States

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Macon, Georgia, United States

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Arlington Heights, Illinois, United States

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Chicago, Illinois, United States

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Evanston, Illinois, United States

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Indianapolis, Indiana, United States

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Valparaiso, Indiana, United States

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West Des Moines, Iowa, United States

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Hutchinson, Kansas, United States

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Lexington, Kentucky, United States

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Lexington, Kentucky, United States

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Owensboro, Kentucky, United States

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Crowley, Louisiana, United States

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Lake Charles, Louisiana, United States

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Monroe, Louisiana, United States

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Boston, Massachusetts, United States

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Flint, Michigan, United States

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Grandville, Michigan, United States

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Sterling Heights, Michigan, United States

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Troy, Michigan, United States

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Edina, Minnesota, United States

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Saint Paul, Minnesota, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Butte, Montana, United States

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Omaha, Nebraska, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Las Vegas, Nevada, United States

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Bridgewater, New Jersey, United States

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Summit, New Jersey, United States

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Warren Township, New Jersey, United States

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Albany, New York, United States

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Binghamton, New York, United States

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Endwell, New York, United States

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New Windsor, New York, United States

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Poughkeepsie, New York, United States

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Williamsville, New York, United States

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Cary, North Carolina, United States

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Greensboro, North Carolina, United States

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Mooresville, North Carolina, United States

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Shelby, North Carolina, United States

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Akron, Ohio, United States

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Cincinnati, Ohio, United States

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Dayton, Ohio, United States

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Marion, Ohio, United States

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Wyomissing, Pennsylvania, United States

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Anderson, South Carolina, United States

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Greer, South Carolina, United States

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Greer, South Carolina, United States

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Myrtle Beach, South Carolina, United States

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Pelzer, South Carolina, United States

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Rapid City, South Dakota, United States

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Athens, Tennessee, United States

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Kingsport, Tennessee, United States

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Knoxville, Tennessee, United States

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Knoxville, Tennessee, United States

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Amarillo, Texas, United States

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Austin, Texas, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Edinburg, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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New Braunfels, Texas, United States

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Round Rock, Texas, United States

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San Antonio, Texas, United States

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Schertz, Texas, United States

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Shavano Park, Texas, United States

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Tomball, Texas, United States

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Layton, Utah, United States

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Salt Lake City, Utah, United States

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Salt Lake City, Utah, United States

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Falls Church, Virginia, United States

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Manassas, Virginia, United States

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Midlothian, Virginia, United States

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Richmond, Virginia, United States

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Research Site 10001-029

Suffolk, Virginia, United States

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Tacoma, Washington, United States

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Research Site 90011-005

Chicoutimi, Quebec, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Research Site 11420-002

Chomutov, , Czechia

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Research Site 90420-001

Prague, , Czechia

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Research Site 90420-006

Prague, , Czechia

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Uherské Hradiště, , Czechia

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Research Site 90045-001

Aalborg, North Denmark, Denmark

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Esbjerg, , Denmark

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Herning, , Denmark

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Hvidovre, , Denmark

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Roskilde, , Denmark

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Viborg, , Denmark

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Berlin, , Germany

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Bochum, , Germany

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Frankfurt, , Germany

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Heidelberg, , Germany

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Heidelberg, , Germany

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Research Site 11036-001

Budapest, , Hungary

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Debrecen, , Hungary

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Hatvan, , Hungary

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Research Site 11036-003

Zalaegerszeg, , Hungary

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Research Site 90031-001

Amersfoort, , Netherlands

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Research Site 90031-003

Amsterdam, , Netherlands

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Research Site 90031-006

Goes, , Netherlands

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Hoorn, , Netherlands

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Research Site 90031-005

Utrecht, , Netherlands

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Research SIte 11048-016

Brzozowie, , Poland

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Research Site 11048-018

Bydgoszcz, , Poland

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Research Site 11048-011

Bydgoszcz, , Poland

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Research Site 11048-004

Gdansk, , Poland

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Gdynia, , Poland

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Research Site 11048-007

Katowice, , Poland

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Research SIte 11048-012

Katowice, , Poland

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Research Site 11048-003

Krakow, , Poland

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Research SIte 11048-014

Krakow, , Poland

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Research Site 11048-008

Lublin, , Poland

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Research Site 11048-001

Poznan, , Poland

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Research Site 11048-019

Ruda Śląska, , Poland

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Research SIte 11048-013

Rzeszów, , Poland

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Research SIte 11048-015

Tarnów, , Poland

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Research Site 11048-006

Warsaw, , Poland

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Research Site 11048-009

Warsaw, , Poland

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Wroclaw, , Poland

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Research Site 11048-010

Wroclaw, , Poland

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Research Site 90027-008

Bellville, Cape Town, South Africa

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Lyttelton, Cape Town, South Africa

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Research Site 90027-003

Bloemfontein, Free State, South Africa

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Research Site 90027-010

Johannesburg, Gauteng, South Africa

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Research Site 11027-005

Kempton Park, Gauteng, South Africa

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Research Site 90027-006

Pretoria, Gauteng, South Africa

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Witbank, Gauteng, South Africa

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Research Site 90027-001

Cape Town, Western Cape, South Africa

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Research Site 11027-007

Kuils River, Western Cape, South Africa

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Paarl, Western Cape, South Africa

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Research Site 90027-004

Somerset West, Western Cape, South Africa

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Research Site 90027-005

Somerset West, Western Cape, South Africa

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Research Site 90034-004

Córdoba, Andalusia, Spain

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Research Site 90034-002

Zaragoza, Aragon, Spain

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Research Site 90034-005

Barcelona, Catalonia, Spain

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Research Site 90034-006

Barcelona, Catalonia, Spain

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Research Site 90034-001

Reus, Catalonia, Spain

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Research Site 90034-003

A Coruña, Galicia, Spain

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Research Site 90046-002

Gothenburg, , Sweden

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Stockholm, , Sweden

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Stockholm, , Sweden

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Cherkasy, , Ukraine

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Research Site 11380-008

Kharkiv, , Ukraine

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Research Site 11380-001

Kyiv, , Ukraine

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Research Site 11380-002

Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Uzhhorod, , Ukraine

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Zaporizhzhya, , Ukraine

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Research Site 11044-028

Bollington, Cheshire, United Kingdom

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Bury, , United Kingdom

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Cheadle Hulme, , United Kingdom

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Chorley, , United Kingdom

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Cornwell, , United Kingdom

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Derby, , United Kingdom

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Edgbaston, , United Kingdom

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Exeter, , United Kingdom

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Glasgow, , United Kingdom

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Hexham, , United Kingdom

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Research SIte 11044-020

Macclesfield, , United Kingdom

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Manchester, , United Kingdom

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Manchester, , United Kingdom

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Manchester, , United Kingdom

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Manchester, , United Kingdom

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Plymouth, , United Kingdom

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Research Site 11044-003

Reading, , United Kingdom

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Sale, , United Kingdom

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Research Site 11044-023

Sale, , United Kingdom

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Research Site 11044-002

Stockton-on-Tees, , United Kingdom

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Research Site 11044-021

Timperley, , United Kingdom

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Research Site 11044-007

Wales, , United Kingdom

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Research Site 11044-004

Waterloo, , United Kingdom

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Countries

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United States Canada Czechia Denmark Germany Hungary Netherlands Poland South Africa Spain Sweden Ukraine United Kingdom

References

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Wright RS, Raal FJ, Koenig W, Landmesser U, Leiter LA, Vikarunnessa S, Lesogor A, Maheux P, Talloczy Z, Zang X, Schwartz GG, Ray KK. Inclisiran administration potently and durably lowers LDL-C over an extended-term follow-up: the ORION-8 trial. Cardiovasc Res. 2024 Oct 14;120(12):1400-1410. doi: 10.1093/cvr/cvae109.

Reference Type DERIVED
PMID: 38753448 (View on PubMed)

Warden BA, Duell PB. Inclisiran: A Novel Agent for Lowering Apolipoprotein B-containing Lipoproteins. J Cardiovasc Pharmacol. 2021 Aug 1;78(2):e157-e174. doi: 10.1097/FJC.0000000000001053.

Reference Type DERIVED
PMID: 33990512 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CKJX839A12306B

Identifier Type: OTHER

Identifier Source: secondary_id

2017-003092-55

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MDCO-PCS-17-05

Identifier Type: -

Identifier Source: org_study_id

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