Trial to Evaluate Efficacy and Safety of Lenabasum in Dermatomyositis

NCT ID: NCT03813160

Last Updated: 2022-08-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

176 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-12-17

Study Completion Date

2021-10-05

Brief Summary

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This is a Phase 3 multicenter, double-blind, randomized, placebo-controlled study assessing the efficacy and safety of lenabasum for the treatment of dermatomyositis. Approximately 150 subjects will be enrolled in this study at about 60 sites in North America, Europe, and Asia. The planned duration of double-blind treatment with study drug is up to 52 weeks.

Detailed Description

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Subjects will be randomized to receive lenabasum 20 mg twice per day, lenabasum 5 mg twice per day, or placebo twice per day in a 2:1:2 ratio. The primary efficacy outcome at Week 28 will compare lenabasum 20 mg BID to placebo the Total Improvement Score (TIS), which is a weighted composite measure of improvement from baseline in six endpoints: Physician Global Assessment of Disease Activity, Physician Assessment of Extramuscular Disease Activity, Patient Global Assessment of Disease Activity, Health Assessment Questionnaire (patient-reported disability), Manual Muscle Testing (MMT), and muscle enzymes.

Conditions

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Dermatomyositis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Lenabasum 20 mg

Subjects will receive lenabasum 20 mg twice daily

Group Type EXPERIMENTAL

Lenabasum 20 mg

Intervention Type DRUG

oral capsule

Lenabasum 5 mg

Subjects will receive lenabasum 5 mg twice daily

Group Type EXPERIMENTAL

Lenabasum 5 mg

Intervention Type DRUG

oral capsule

Placebo

Subjects will receive placebo twice daily

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

oral capsule

Interventions

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Lenabasum 20 mg

oral capsule

Intervention Type DRUG

Lenabasum 5 mg

oral capsule

Intervention Type DRUG

Placebo

oral capsule

Intervention Type DRUG

Other Intervention Names

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JBT-101 anabasum JBT-101 anabasum

Eligibility Criteria

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Inclusion Criteria

* Fulfill at least one of the following criteria for dermatomyositis:

1. Bohan and Peter criteria (Bohan and Peter, 1975a; Bohan and Peter 1975b)
2. ACR/EULAR criteria (Lundberg et al, 2017)
* Disease activity/severity fulfills at least one of the following three criteria:

1. MDGA ≥ 3 cm (0 - 10 cm Visual Analog Scale \[VAS\]) and MMT-8 score ≤ 142 (out of 150 total possible)
2. Sum of MDGA, PtGA and EMGA VAS scores is ≥ 10 cm (0-10 cm VAS for each)
3. MDGA ≥ 3 cm (0-10 cm VAS) and CDASI activity score of \> 14
* Stable doses of immunosuppressive medications for DM as defined by:

1. Unchanged dose of oral corticosteroids ≤ 20 mg per day prednisone or equivalent for ≥ 4 weeks before Visit 1
2. Unchanged dose of immunosuppressive medications other than oral corticosteroids for ≥ 8 weeks before Screening

Exclusion Criteria

* Unstable DM or DM with end-stage organ involvement at Screening or Visit 1
* Significant diseases or conditions other than DM that may influence response to the study drug or safety
* Any of the following values for laboratory tests at Screening:

1. A positive pregnancy test (or at Visit 1)
2. Hemoglobin \< 9 g/dL in males and \< 8 g/dL in females
3. Neutrophils \< 1.0 × 10\^9/L
4. Platelets \< 75 × 10\^9/L
5. Creatinine clearance \< 50 mL/min on screening blood test, per the Modification of Diet in Renal Disease Study or in 24 hour urine creatine clearance measurement
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Corbus Pharmaceuticals Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Victoria P Werth, MD

Role: PRINCIPAL_INVESTIGATOR

University of Pennsylvania

Chester V Oddis, MD

Role: PRINCIPAL_INVESTIGATOR

University of Pittsburgh Department of Medicine/Division of Rheumatology

Locations

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HonorHealth Neurology

Phoenix, Arizona, United States

Site Status

Mayo Clinic

Scottsdale, Arizona, United States

Site Status

Attune Health Center

Beverly Hills, California, United States

Site Status

UCLA Division of Rheumatology

Los Angeles, California, United States

Site Status

Denver Arthritis Clinic

Denver, Colorado, United States

Site Status

Georgetown University

Washington D.C., District of Columbia, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

DelRicht Research

New Orleans, Louisiana, United States

Site Status

Johns Hopkins Bayview Medical Center

Baltimore, Maryland, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

University of Minnesota, Division of Rheumatic and Autoimmune Diseases

Minneapolis, Minnesota, United States

Site Status

Washington University in St. Louis

St Louis, Missouri, United States

Site Status

Hospital for Special Surgery

New York, New York, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh, Division of Rheumatology

Pittsburgh, Pennsylvania, United States

Site Status

MUSC: Department of Neurology

Charleston, South Carolina, United States

Site Status

Austin Neuromuscular Center

Austin, Texas, United States

Site Status

Rheumatic Disease Center

Glendale, Wisconsin, United States

Site Status

University Hospital "Kaspela" Rheumatology Clinic

Plovdiv, , Bulgaria

Site Status

UMHAT "St. Ivan Rilski"

Sofia, , Bulgaria

Site Status

UMHAT

Stara Zagora, , Bulgaria

Site Status

University of British Columbia, Dept. of Dermatology and Skin Science

Vancouver, British Columbia, Canada

Site Status

Revmatologicky ustav

Prague, , Czechia

Site Status

Charite-Universitatsmedizin

Berlin, , Germany

Site Status

University Hospital Erlangen Nuremberg

Erlangen, , Germany

Site Status

University Medical Center Goettingen

Göttingen, , Germany

Site Status

University of Debrecen

Debrecen, , Hungary

Site Status

University Hospital Policlinico-Vittorio Emanuele

Catania, , Italy

Site Status

Fondazione Policlinico Universitario A.Gemelli-IRCCS

Roma, , Italy

Site Status

Gunma University Hospital

Gunma, , Japan

Site Status

Hokkaido University Hospital

Hokkaido, , Japan

Site Status

Yokohama City University Hospital

Kanagawa, , Japan

Site Status

Kyoto University Hospital

Kyoto, , Japan

Site Status

Tohoku University Hospital

Miyagi, , Japan

Site Status

Osaka University Hospital

Osaka, , Japan

Site Status

Keio University Hospital

Tokyo, , Japan

Site Status

Nippon Medical School Hospital

Tokyo, , Japan

Site Status

Wakayama Medical Hospital

Wakayama, , Japan

Site Status

KLIMED

Bialystok, , Poland

Site Status

Kliniczny Szpital Wojewodzki Nr 1. im Fryderyka Chopina Klinika Dermatologii

Rzeszów, , Poland

Site Status

KLIMED

Łomża, , Poland

Site Status

Inha University Hospital

Incheon, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Hanyang University Hospital

Seoul, , South Korea

Site Status

Seoul St. Mary's Hospital

Seoul, , South Korea

Site Status

Vall d'Hebron General Hospital

Barcelona, , Spain

Site Status

Hospital 12 Octubre

Madrid, , Spain

Site Status

Karolinska University Hospital, Rheumatology Clinic

Stockholm, , Sweden

Site Status

King's College Hospital NHS Foundation Trust

London, , United Kingdom

Site Status

Countries

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United States Bulgaria Canada Czechia Germany Hungary Italy Japan Poland South Korea Spain Sweden United Kingdom

References

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Kodali N, Diaz D, Dhiman R, Vazquez T, Feng R, Patel J, Dan J, Sprow G, Kleitsch J, Sharma M, Bashir M, Werth VP. Diverse Lenabasum pathway activation in dermatomyositis patients' blood. Sci Rep. 2025 May 18;15(1):17232. doi: 10.1038/s41598-025-92001-z.

Reference Type DERIVED
PMID: 40383862 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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JBT101-DM-002

Identifier Type: -

Identifier Source: org_study_id

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