A Study of the Efficacy and Safety of Relacorilant in Patients With Endogenous Cushing Syndrome

NCT ID: NCT03697109

Last Updated: 2025-07-16

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

152 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-11-15

Study Completion Date

2024-04-15

Brief Summary

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This is a Phase 3, double-blind, placebo-controlled, randomized-withdrawal study to assess the efficacy, safety and pharmacokinetics (PK) of relacorilant in patients with endogenous Cushing syndrome and concurrent type 2 diabetes mellitus/impaired glucose tolerance (DM/IGT) and/or uncontrolled hypertension (HTN).

Detailed Description

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The primary outcome is the assessment of efficacy of relacorilant treatment based on sustained blood pressure control during the Randomized-withdrawal (RW) Phase, wherein patients who had achieved the blood pressure response criteria during the Open-label (OL) Phase are randomized to receive either relacorilant or placebo for 12 weeks.

Patients in the OL Phase will dose-escalate in 100 mg increments to a maximum dose of 400 mg orally once daily. Patients will remain on OL treatment until Week 22 at which time they will be evaluated for the RW Phase based on predefined hyperglycemia and hypertension response criteria. Eligible patients will then be randomized to receive either relacorilant or placebo at a 1:1 ratio for 12 weeks. Patients who do not meet the criteria for the RW Phase will end treatment and may be eligible to roll over into an extension safety study. Patients who complete the RW Phase of the study may also be eligible to roll over into an extension study.

Conditions

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Cushing Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Relacorilant (OL Phase)

Patients will receive relacorilant increased sequentially from 100 mg once daily to a maximum dose of 400 mg once daily.

Group Type EXPERIMENTAL

Relacorilant

Intervention Type DRUG

Relacorilant is supplied as 100 mg capsules for oral dosing.

Relacorilant (RW Phase)

Patients who meet any of the response criteria will advance to the RW Phase of the study and receive the same dose of relacorilant as the last dose administered in the OL Phase.

Group Type EXPERIMENTAL

Relacorilant

Intervention Type DRUG

Relacorilant is supplied as 100 mg capsules for oral dosing.

Placebo (RW Phase)

Patients who meet any of the response criteria will advance to the RW Phase of the study and receive placebo matched to study drug.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo matched to study drug

Interventions

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Relacorilant

Relacorilant is supplied as 100 mg capsules for oral dosing.

Intervention Type DRUG

Placebo

Placebo matched to study drug

Intervention Type OTHER

Other Intervention Names

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CORT125134

Eligibility Criteria

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Inclusion Criteria

* Has a confirmed diagnosis of endogenous Cushing syndrome
* Meets at least 1 of the following criteria:

* Has Type 2 diabetes mellitus
* Has impaired glucose tolerance
* Has hypertension.

Exclusion Criteria

* Has non-endogenous source of hypercortisolism
* Has uncontrolled, clinically significant hypothyroidism or hyperthyroidism
* Has poorly controlled hypertension
* Has poorly controlled diabetes mellitus
* Has severe renal insufficiency.
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Corcept Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Andreas Moraitis, MD

Role: STUDY_DIRECTOR

Corcept Therapeutics

Locations

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Site 21

Phoenix, Arizona, United States

Site Status

Site 36

Los Angeles, California, United States

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Site 68

Torrance, California, United States

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Site 10

Miami, Florida, United States

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Site 14

Atlanta, Georgia, United States

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Site 41

Chicago, Illinois, United States

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Site 7

Indianapolis, Indiana, United States

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Site 2

Metairie, Louisiana, United States

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Site 45

Baltimore, Maryland, United States

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Site 46

Boston, Massachusetts, United States

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Site 20

Ann Arbor, Michigan, United States

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Site 4

Jackson, Mississippi, United States

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Site 13

St Louis, Missouri, United States

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Site 53

Omaha, Nebraska, United States

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Site 72

Reno, Nevada, United States

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Site 8

Albany, New York, United States

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Site 6

Jamaica, New York, United States

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Site 57

New York, New York, United States

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Site 35

New York, New York, United States

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Site 39

New York, New York, United States

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Site 1

Wilmington, North Carolina, United States

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Site 17

Columbus, Ohio, United States

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Site 11

Oklahoma City, Oklahoma, United States

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Site 62

Philadelphia, Pennsylvania, United States

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Site 19

Pittsburgh, Pennsylvania, United States

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Site 71

Pittsburgh, Pennsylvania, United States

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Site 5

Summerville, South Carolina, United States

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Site 51

Dallas, Texas, United States

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Site 3

El Paso, Texas, United States

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Site 65

Houston, Texas, United States

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Site 56

Shavano Park, Texas, United States

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Site 31

Everett, Washington, United States

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Site 47

Vienna, , Austria

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Site 27

Sofia, , Bulgaria

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Site 70

Halifax, Nova Scotia, Canada

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Site 58

Montreal, , Canada

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Site 54

München, , Germany

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Site 49

Würzburg, , Germany

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Site 30

Jerusalem, , Israel

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Site 29

Kfar Saba, , Israel

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Site 28

Petah Tikva, , Israel

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Site 69

Tel Aviv, , Israel

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Site 43

Ancona, , Italy

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Site 15

Messina, , Italy

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Site 26

Milan, , Italy

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Site 12

Napoli, , Italy

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Site 38

Orbassano, , Italy

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Site 67

Padua, , Italy

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Site 40

Roma, , Italy

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Site 16

Roma, , Italy

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Site 34

Rotterdam, , Netherlands

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Site 77

Bialystok, , Poland

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Site 37

Chrzanów, , Poland

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Site 59

Krakow, , Poland

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Site 33

Lublin, , Poland

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Site 66

Bucharest, , Romania

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Site 63

Bucharest, , Romania

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Site 64

Bucharest, , Romania

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Site 73

Iași, , Romania

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Site 75

Alicante, , Spain

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Site 25

Girona, , Spain

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Site 24

Madrid, , Spain

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Site 22

Málaga, , Spain

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Site 23

Seville, , Spain

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Countries

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United States Austria Bulgaria Canada Germany Israel Italy Netherlands Poland Romania Spain

References

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Pivonello R, Munster PN, Terzolo M, Ferrigno R, Simeoli C, Puglisi S, Bali U, Moraitis AG. Glucocorticoid Receptor Antagonism Upregulates Somatostatin Receptor Subtype 2 Expression in ACTH-Producing Neuroendocrine Tumors: New Insight Based on the Selective Glucocorticoid Receptor Modulator Relacorilant. Front Endocrinol (Lausanne). 2022 Jan 4;12:793262. doi: 10.3389/fendo.2021.793262. eCollection 2021.

Reference Type DERIVED
PMID: 35058882 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CORT125134-455

Identifier Type: -

Identifier Source: org_study_id

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