Safety and Efficacy of Different Dose Levels of Pasireotide in Patients With de Novo, Persistent or Recurrent Cushing's Disease

NCT ID: NCT00434148

Last Updated: 2016-03-08

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

162 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-12-31

Study Completion Date

2014-05-31

Brief Summary

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This study will evaluate the safety and efficacy of two different doses of Pasireotide in patients with de novo or recurrent/persistent Cushing's Disease.

Detailed Description

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Conditions

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Cushing's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Pasireotide 600 ug

At randomization, participants received 600 ug subcutaneously (sc) twice daily (bid). Participants continued at this dose until month 6 if their month 3 mean urinary free cortisol (mUFC) was \<= 2 x the upper limit of normal (ULN) and the mUFC was below or equal to their baseline mUFC. Participants not meeting the mUFC criteria at month 3 were unblinded and required to increase their dose to 900ug bid on an open label basis. Participants had the option to continue in the extension phase as long as they did not meet any discontinuation criteria or until pasireotide was available commercially in their country.

Group Type EXPERIMENTAL

Pasireotide

Intervention Type DRUG

Pasireotide 900 ug

At randomization, participants received 900 ug subcutaneously (sc) twice daily (bid). Participants continued at this dose until month 6 if their month 3 mean urinary free cortisol (mUFC) was \<= 2 x the upper limit of normal (ULN) and the mUFC was below or equal to their baseline mUFC. Participants not meeting the mUFC criteria at month 3 were unblinded and required to increase their dose to 1200 ug bid on an open label basis. Participants had the option to continue in the extension phase as long as they did not meet any discontinuation criteria or until pasireotide was available commercially in their country.

Group Type EXPERIMENTAL

Pasireotide

Intervention Type DRUG

Interventions

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Pasireotide

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* 18 years or greater
* Confirmed diagnosis of ACTH-dependent Cushing's disease
* Not considered candidate for pituitary surgery

Exclusion Criteria

* History of pituitary irradiation in the last 10 years
* Cushing's syndrome not caused by pituitary tumor
* Patients with active malignant disease (cancer) in the last 5 years
* Women who are pregnant or lactating
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Stanford University Medical Center Stanford Cancer Center (3)

Stanford, California, United States

Site Status

University Chicago Hospital Dept. of Univ of Chicago

Chicago, Illinois, United States

Site Status

Dana Farber Cancer Institute The Melanoma Program

Boston, Massachusetts, United States

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Columbia University Medical Center- New York Presbyterian Columbia University DeptofMed

New York, New York, United States

Site Status

Cleveland Clinic Foundation Dept. of Cleveland Clinic (6)

Cleveland, Ohio, United States

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Oregon Health & Sciences University Dept.ofOregonHealth&SciencesU.

Portland, Oregon, United States

Site Status

University of Texas Southwestern Medical Center Clinical-TranslationalRes.Ctr.

Dallas, Texas, United States

Site Status

University of Texas/MD Anderson Cancer Center Dept.ofMDAndersonCancerCtr(8)

Houston, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

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Swedish Medical Center Dept.ofSeattle Neuroscience(2)

Seattle, Washington, United States

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Novartis Investigative Site

Buenos Aires, Buenos Aires, Argentina

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Novartis Investigative Site

Buenos Aires, Buenos Aires, Argentina

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Novartis Investigative Site

Capital Federal, Buenos Aires, Argentina

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Novartis Investigative Site

Edegem, , Belgium

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Novartis Investigative Site

Ghent, , Belgium

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Novartis Investigative Site

Curitiba, Paraná, Brazil

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Novartis Investigative Site

Rio de Janeiro, Rio de Janeiro, Brazil

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Novartis Investigative Site

Porto Alegre, Rio Grande do Sul, Brazil

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Novartis Investigative Site

Ribeirão Preto, São Paulo, Brazil

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Novartis Investigative Site

São Paulo, São Paulo, Brazil

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Novartis Investigative Site

São Paulo, São Paulo, Brazil

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Novartis Investigative Site

Edmonton, Alberta, Canada

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Novartis Investigative Site

Halifax, Nova Scotia, Canada

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Montreal, Quebec, Canada

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Novartis Investigative Site

Beijing, Beijing Municipality, China

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Novartis Investigative Site

Beijing, , China

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Novartis Investigative Site

Shanghai, , China

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Novartis Investigative Site

Aarhus, , Denmark

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Novartis Investigative Site

Copenhagen, , Denmark

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Herlev, , Denmark

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Helsinki, , Finland

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Novartis Investigative Site

Angers, , France

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Novartis Investigative Site

Grenoble Cédex 9, , France

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Novartis Investigative Site

Lille, , France

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Limoges, , France

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Marseille, , France

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Paris, , France

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Pessac, , France

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Novartis Investigative Site

Saint-Priest-en-Jarez, , France

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Novartis Investigative Site

Toulouse, , France

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Novartis Investigative Site

München, Germany, Germany

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Novartis Investigative Site

Berlin, , Germany

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Essen, , Germany

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Würzburg, , Germany

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Novartis Investigative Site

Athens, GR, Greece

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Novartis Investigative Site

Athens, GR, Greece

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Novartis Investigative Site

Haifa, , Israel

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Novartis Investigative Site

Haifa, , Israel

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Jerusalem, , Israel

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Novartis Investigative Site

Petah Tikva, , Israel

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Novartis Investigative Site

Ancona, AN, Italy

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Novartis Investigative Site

Cona, FE, Italy

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Novartis Investigative Site

Milan, MI, Italy

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Novartis Investigative Site

Milan, MI, Italy

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Novartis Investigative Site

Padua, PD, Italy

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Novartis Investigative Site

Pisa, PI, Italy

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Novartis Investigative Site

Orbassano, TO, Italy

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Novartis Investigative Site

Torino, TO, Italy

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Novartis Investigative Site

Napoli, , Italy

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Novartis Investigative Site

Mexico City, Mexico City, Mexico

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Novartis Investigative Site

Mexico City, Mexico City, Mexico

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Novartis Investigative Site

Warsaw, , Poland

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Novartis Investigative Site

Porto, Portugal, Portugal

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Novartis Investigative Site

Seville, Andalusia, Spain

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Novartis Investigative Site

Barcelona, Barcelona, Spain

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Novartis Investigative Site

Ankara, , Turkey (Türkiye)

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Novartis Investigative Site

Balcova / Izmir, , Turkey (Türkiye)

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Novartis Investigative Site

Fatih / Istanbul, , Turkey (Türkiye)

Site Status

Countries

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United States Argentina Belgium Brazil Canada China Denmark Finland France Germany Greece Israel Italy Mexico Poland Portugal Spain Turkey (Türkiye)

References

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Lacroix A, Gu F, Schopohl J, Kandra A, Pedroncelli AM, Jin L, Pivonello R. Pasireotide treatment significantly reduces tumor volume in patients with Cushing's disease: results from a Phase 3 study. Pituitary. 2020 Jun;23(3):203-211. doi: 10.1007/s11102-019-01021-2.

Reference Type DERIVED
PMID: 31875276 (View on PubMed)

Yedinak CG, Hopkins S, Williams J, Ibrahim A, Cetas JS, Fleseriu M. Medical Therapy with Pasireotide in Recurrent Cushing's Disease: Experience of Patients Treated for At Least 1 Year at a Single Center. Front Endocrinol (Lausanne). 2017 Feb 27;8:35. doi: 10.3389/fendo.2017.00035. eCollection 2017.

Reference Type DERIVED
PMID: 28289402 (View on PubMed)

Schopohl J, Gu F, Rubens R, Van Gaal L, Bertherat J, Ligueros-Saylan M, Trovato A, Hughes G, Salgado LR, Boscaro M, Pivonello R; Pasireotide B2305 Study Group. Pasireotide can induce sustained decreases in urinary cortisol and provide clinical benefit in patients with Cushing's disease: results from an open-ended, open-label extension trial. Pituitary. 2015 Oct;18(5):604-12. doi: 10.1007/s11102-014-0618-1.

Reference Type DERIVED
PMID: 25537481 (View on PubMed)

MacKenzie Feder J, Bourdeau I, Vallette S, Beauregard H, Ste-Marie LG, Lacroix A. Pasireotide monotherapy in Cushing's disease: a single-centre experience with 5-year extension of phase III Trial. Pituitary. 2014 Dec;17(6):519-29. doi: 10.1007/s11102-013-0539-4.

Reference Type DERIVED
PMID: 24287689 (View on PubMed)

Petersenn S, Newell-Price J, Findling JW, Gu F, Maldonado M, Sen K, Salgado LR, Colao A, Biller BM; Pasireotide B2305 Study Group. High variability in baseline urinary free cortisol values in patients with Cushing's disease. Clin Endocrinol (Oxf). 2014 Feb;80(2):261-9. doi: 10.1111/cen.12259. Epub 2013 Jul 15.

Reference Type DERIVED
PMID: 23746264 (View on PubMed)

Colao A, Petersenn S, Newell-Price J, Findling JW, Gu F, Maldonado M, Schoenherr U, Mills D, Salgado LR, Biller BM; Pasireotide B2305 Study Group. A 12-month phase 3 study of pasireotide in Cushing's disease. N Engl J Med. 2012 Mar 8;366(10):914-24. doi: 10.1056/NEJMoa1105743.

Reference Type DERIVED
PMID: 22397653 (View on PubMed)

Related Links

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http://www.novartisclinicaltrials.com//webapp/etrials/searchTrial.do

Visit NovartisClinicalTrials.com: Pre-qualify for a trial, and view a list of trials and participating study centers.

Other Identifiers

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2006-004111-22

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CSOM230B2305

Identifier Type: -

Identifier Source: org_study_id

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