Study to Assess Efficacy and Safety of Baloxavir Marboxil In Combination With Standard-of-Care Neuraminidase Inhibitor In Hospitalized Participants With Severe Influenza

NCT ID: NCT03684044

Last Updated: 2021-01-06

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

363 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-01-08

Study Completion Date

2020-03-16

Brief Summary

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This study will evaluate the efficacy, safety, and pharmacokinetics of baloxavir marboxil in combination with a standard-of-care (SOC) neuraminidase inhibitor (NAI) (i.e., oseltamivir, zanamivir, or peramivir) compared with a matching placebo in combination with a SOC NAI in hospitalized patients with influenza.

Detailed Description

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Conditions

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Influenza

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Baloxavir Marboxil

Participants will receive at least two doses of baloxavir marboxil on Days 1 and 4. A third dose of Baloxavir will be given on Day 7 for participants who have not improved according to protocol defined criteria on Day 5.

Study treatment will be given in combination with SOC NAI (i.e., oseltamivir, zanamivir, or peramivir) in accordance with local clinical practice.

Group Type EXPERIMENTAL

Baloxavir Marboxil

Intervention Type DRUG

Baloxavir marboxil will be administered as a weight-based dose on Days 1 and 4. A third dose will be given on Day 7 for participants who have not improved according to protocol defined criteria on Day 5.

Placebo

Participants will receive at least two doses of placebo on Day 1 and 4. A third dose of placebo will be given on Day 7 for participants who have not improved according to protocol defined criteria on Day 5.

Study treatment will be given in combination with SOC NAI (i.e., oseltamivir, zanamivir, or peramivir) in accordance with local clinical practice.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Participants will receive matching placebo on Days 1, 4 and 7.

Interventions

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Baloxavir Marboxil

Baloxavir marboxil will be administered as a weight-based dose on Days 1 and 4. A third dose will be given on Day 7 for participants who have not improved according to protocol defined criteria on Day 5.

Intervention Type DRUG

Placebo

Participants will receive matching placebo on Days 1, 4 and 7.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Adult participants: Signed informed consent by any participant capable of giving consent, or, where the participant is not capable of giving consent, by his or her legal/authorized representative
* Adolescent participants not able to legally consent: written informed consent for study participation is obtained from participant's parents or legal guardian, with assent as appropriate by the participant, depending on the participant's level of understanding and capability to provide assent
* Participants who require hospitalization for severe influenza or acquire influenza during hospitalization, the severity of which requires an extension of hospitalization
* Diagnosis of influenza A and/or B by a positive Rapid Influenza Diagnostic Test (RIDT) or reverse transcriptase-polymerase chain reaction (RT-PCR)
* The time interval between the onset of symptoms and randomization is within 96 hours
* A score of ≥4 based on the National Early Warning Score 2 (NEWS2)
* Participants will require objective criteria of seriousness defined by at least one of the following criteria:
* Requires ventilation or supplemental oxygen to support respiration
* Has a complication related to influenza that requires hospitalization (e.g., pneumonia, central nervous system involvement, myositis, rhabdomyolysis, acute exacerbation of chronic kidney disease, asthma or chronic obstructive pulmonary disease (COPD), severe dehydration, myocarditis, pericarditis, exacerbation of ischemic heart disease)
* For women of childbearing potential: Agreement to remain abstinent or use contraceptive methods with a failure rate of \< 1% per year during the treatment period and for 28 days after the last dose of study treatment. Hormonal contraceptive methods must be supplemented by a barrier method.

Exclusion Criteria

* Participants who have received more than 48 hours of antiviral treatment for the current influenza infection prior to screening
* Participants who have received baloxavir marboxil for the current influenza infection
* Known contraindication to neuraminidase inhibitors
* Participants hospitalized for exclusively social reasons (e.g., lack of caregivers at home)
* Participants expected to die or be discharged within 48 hours, according to the investigator's judgement
* Participants weighing \< 40 kg
* Participants with known severe renal impairment (estimated glomerular filtration rate \< 30 mL/min/1.73 m2) or receiving continuous renal replacement therapy, hemodialysis, peritoneal dialysis
* Participants with any of the following laboratory abnormalities detected within 24 hours prior to or during screening (according to local laboratory reference ranges:
* Alanine Transaminase (ALT) or Aspartate Transaminase (AST) level \> 5 times the upper limit of normal (ULN) OR
* ALT or AST \> 3 times the ULN and total bilirubin level \> 2 times the ULN
* Pregnant or breastfeeding, or positive pregnancy test in a predose examination, or intending to become pregnant during the study or within 28 days after the last dose of study treatment
* Exposure to an investigational drug within 5 half-lives or 30 days (whichever is longer) of randomization
* Any serious medical condition or abnormality in clinical laboratory tests that, in the investigator's judgment, precludes the participant's safe participation in and completion of the study
* Known hypersensitivity to baloxavir marboxil or the drug product excipients
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Torrance Memorial Medical Center

Torrance, California, United States

Site Status

Denver Health Medical Center

Denver, Colorado, United States

Site Status

Atlanta Institute For Medical Research, Inc; DeKalb Medical Pharmacy

Decatur, Georgia, United States

Site Status

University of Chicago; Oncology Dept

Chicago, Illinois, United States

Site Status

NorthShore University HealthSystem

Evanston, Illinois, United States

Site Status

Barnum Medical Research, Inc.

Natchitoches, Louisiana, United States

Site Status

Detroit Receiving Hospital

Detroit, Michigan, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Mercury Street Medical Group

Butte, Montana, United States

Site Status

Creighton University Medical Center

Omaha, Nebraska, United States

Site Status

New York-Presbyterian Brooklyn Methodist Hospital; Department of Emergency Medicine

Brooklyn, New York, United States

Site Status

Temple University Hospital ; Lung Center

Philadelphia, Pennsylvania, United States

Site Status

Salem Veterans Affairs Medical Center - NAVREF; Pharmacy

Salem, Virginia, United States

Site Status

Froedtert and The Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Instituto Medico Platense

La Plata, , Argentina

Site Status

Royal Brisbane & Womens Hospital; Pharmacy Department

Herston, Queensland, Australia

Site Status

Royal Children's Hospital Melbourne - PIN

Parkville, Victoria, Australia

Site Status

Hopital Erasme; Chest Medicine, Cardiac & Thoracic Surgery

Brussels, , Belgium

Site Status

Cliniques Universitaires Saint-Luc; Hematology

Brussels, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

Santa Casa de Misericordia; de Belo Horizonte

Belo Horizonte, Minas Gerais, Brazil

Site Status

Hospital Sao Vicente de Paulo

Passo Fundo, Rio Grande do Sul, Brazil

Site Status

Centro de Estudos Clinicos do Interior Paulista

Jaú, São Paulo, Brazil

Site Status

Multiprofile Hospital For Active Treatment Sveta Ekaterina Dimitrovgrad EOOD; Internal Diseases

Dimitrovgrad, , Bulgaria

Site Status

Specialized Hospital for Active Treatment of Pneumophthisiatric Diseases - Haskovo EOOD

Haskovo, , Bulgaria

Site Status

MHAT Stamen Iliev AD; Pharmacy

Montana, , Bulgaria

Site Status

University Mulitiprofile Hospital for Active Treatment Sveti Georgi EAD; Pharmacy

Plovdiv, , Bulgaria

Site Status

Specialized Hospital for Active Treatment of Pneumophthisiatric Diseases Dr. D. Gramatikov - Ruse

Rousse, , Bulgaria

Site Status

Multiprofile Hospital for Active Treatment - Samokov EOOD

Samokov, , Bulgaria

Site Status

Multiprofile Hospital For Active Treatment Sliven То Military Hospital Sofia; Pharmacy

Sliven, , Bulgaria

Site Status

Multiprofile Hospital For Active Treatment - Dr. Bratan Shukerov AD; Pharmacy

Smolyan, , Bulgaria

Site Status

First Multiprofile Hospital for Active Treatment - Sofia EAD

Sofia, , Bulgaria

Site Status

Fifth Multiprofile Hospital for Active Treatment - Sofia EAD; Pharmacy

Sofia, , Bulgaria

Site Status

Military Medical Academy Multiprofile Hospital for Active Treatment - Sofia; Pharmacy

Sofia, , Bulgaria

Site Status

National Multiprofile Transport Hospital Tzar Boris Ill; Clinic of Internal Diseases

Sofia, , Bulgaria

Site Status

Multiprofile District Hospital for Active Treatment Dr. Stefan Cherkezov AD; Pharmacy

Veliko Tarnovo, , Bulgaria

Site Status

Specialized Hospital for Active Treatment of Pneumophthisiatric Diseases-Vratsa; Pharmacy

Vratsa, , Bulgaria

Site Status

Peter Lougheed Centre

Calgary, Alberta, Canada

Site Status

Foothills Medical Centre

Calgary, Alberta, Canada

Site Status

Carlson Urology

Calgary, Alberta, Canada

Site Status

South Health Campus

Calgary, Alberta, Canada

Site Status

University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

Toronto East General Hospital; Main Pharmacy G Wing Basement

East York, Ontario, Canada

Site Status

London Health Sciences Center; Pharmacy Dept.

London, Ontario, Canada

Site Status

Institut Universitaire de Cardiologie et de Pneumologie

Québec, , Canada

Site Status

Beijing Ditan Hospital Capital Medical University

Beijing, , China

Site Status

Beijing Youan Hospital, Capital Medical University; Center for Infectious Diseases

Beijing, , China

Site Status

China-Japan Friendship Hospital

Beijing, , China

Site Status

West China Hospital, Sichuan University

Chengdu, , China

Site Status

The First Affiliated Hospital of Guangzhou Medical University

Guangzhou, , China

Site Status

The First Affiliated Hospital of College of Medicine, Zhejiang University

Hangzhou, , China

Site Status

The 1st Affiliated Hospital of Nanchang Unversity

Nanchang, , China

Site Status

Shanghai Jiao Tong University School of Medicine (SJTUSM) - Ruijin Hospital (GuangCi Hospital)

Shanghai, , China

Site Status

Zhongshan Hospital Fudan University

Shanghai, , China

Site Status

Shanghai Public Health Clinical Center

Shanghai, , China

Site Status

Fakultni nemocnice Brno; Interni hematologicka a onkologicka klinika

Brno, , Czechia

Site Status

Nemocnice Kyjov, prispevkova organizace

Kyjov, , Czechia

Site Status

East Tallinn Central Hospital

Tallinn, , Estonia

Site Status

Kuopion Yliopistollinen Sairaala; Silmätaudit

Kuopio, , Finland

Site Status

Oulun Yliopistollinen Sairaala; Teho-osasto

Oulu, , Finland

Site Status

Turku University Hospital

Turku, , Finland

Site Status

Centre Hospitalier Victor Dupouy

Argenteuil, , France

Site Status

CHRU Dijon Complexe Du Bocage

Dijon, , France

Site Status

Centre Hospitalier Departemental de Vendee

La Roche-sur-Yon, , France

Site Status

Hôpital Universitaire Dupuytren

Limoges, , France

Site Status

CHRU Nantes

Nantes, , France

Site Status

CHU de Nîmes - Hôpital Carémeau

Nîmes, , France

Site Status

Hopital de La Source

Orléans, , France

Site Status

Groupe Hospitalier Pitie Salpetriere; Service De Pneumologie

Paris, , France

Site Status

Nouvel Hopital Civil - CHU Strasbourg

Strasbourg, , France

Site Status

CHRU Bretonneau

Tours, , France

Site Status

Uniklinik Koln; Klinik I fur Innere Medizin

Cologne, , Germany

Site Status

Krankenhaus Donaustauf der LVA Niederbayern Oberpfalz

Donaustauf, , Germany

Site Status

Universitätsklinikum Carl Gustav Carus an der TU Dresden

Dresden, , Germany

Site Status

St. Josefskrankenhaus - Freiburg; Klinik fur Pneumologieund Beatmungsmedizin

Freiburg im Breisgau, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Universitatsklinikum Schleswig-Holstein; Klinik fuer Innere Medizin I

Lübeck, , Germany

Site Status

Klinikum Mannheim GmbH Universitätsklinikum

Mannheim, , Germany

Site Status

Klinikum der Universität Regensburg

Regensburg, , Germany

Site Status

Universitatsklinikum Tubingen

Tübingen, , Germany

Site Status

Princess Margaret Hospital

Hong Kong, , Hong Kong

Site Status

Queen Mary Hospital

Hong Kong, , Hong Kong

Site Status

Prince of Wales Hospital

Shatin, New Territories, , Hong Kong

Site Status

Soroka University Medical Centre

Beersheba, , Israel

Site Status

Edith Wolfson Medical Center

Holon, , Israel

Site Status

Galilee Medical Center

Nahariya, , Israel

Site Status

Chaim Sheba Medical Center; Allergy and Clinical Immunology Unit

Ramat Gan, , Israel

Site Status

Rambam Health Corporation; Oncology Institute

Rambam, , Israel

Site Status

ZIV Medical Center; Department Of Internal Medicine A

Safed, , Israel

Site Status

Tel Aviv Sourasky Medical Center; Pharmacy

Tel Aviv, , Israel

Site Status

Baruch Padeh Poria Medical Center; Pharmacy

Tiberias, , Israel

Site Status

Fujita General Hospital

Dategun Kunimimachi, , Japan

Site Status

Shin Komonji Hospital

Fukuoka, , Japan

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Fukuoka Shin Mizumaki Hospital

Fukuoka, , Japan

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Fukuoka Wajiro Hospital

Fukuoka, , Japan

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Rinku General Medical Center

Izumisano, , Japan

Site Status

National Hospital Organization Minami Kyoto Hospital

Jōyō, , Japan

Site Status

National Hospital Organization Kanazawa Medical Center

Kanazawa, , Japan

Site Status

Japanese Red Cross Kumamoto Hospital

Kumamoto, , Japan

Site Status

Naha City Hospital

Naha, , Japan

Site Status

National Hospital Organization Ibarakihigashi National Hospital; Center for Clinical Research

Naka-gun, , Japan

Site Status

Japan Community Health care Organization Nihonmatsu hospital

Nihonmatsu, , Japan

Site Status

Social Corporation Keigakukai Minamiosaka Hosupital

Osaka, , Japan

Site Status

National Hospital Organaization Shibukawa Medical Center

Shibukawa, , Japan

Site Status

Tokyo Shinagawa Hospital Medical Corporation Association Tokyokyojuno-kai

Shinagawa City, , Japan

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Saka General Hospital

Shiogama, , Japan

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Local incorporated administrative agency Shizuoka City Shizuoka Hospital

Shizuoka, , Japan

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Iwase General Hospital

Sukagawa, , Japan

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Center Hospital of the National Center for Global Health and Medicine

Tokyo, , Japan

Site Status

Nagata Hospital; Department of pulmonary medicine

Yanagawa-shi, , Japan

Site Status

Instituto Nacional de Ciencias Médicas y Nutricion Dr. Salvador Zubiran; Hamatologia y Oncologia

México, Mexico CITY (federal District), Mexico

Site Status

Hospital Civil Fray Antonio Alcalde; Instituto de Patologia Infecciosa

Guadalajara, , Mexico

Site Status

Hospital Universitario Dr. Jose Eleuterio González; Enfermedades Pulmonares Crónicas

Monterrey, , Mexico

Site Status

Hospital General de Tijuana

Tijuana, , Mexico

Site Status

Leids Universitair Medisch Centrum; C5-P Stafcentrum Hartziekten

Leiden, , Netherlands

Site Status

Canisius Wilhelmina Ziekenhuis; Department Hematology

Nijmegen, , Netherlands

Site Status

Ikazia Ziekenhuis

Rotterdam, , Netherlands

Site Status

Zuyderland Medisch Centrum - Sittard Geleen

Sittard-Geleen, , Netherlands

Site Status

Universitair Medisch Centrum Utrecht

Utrecht, , Netherlands

Site Status

Wellington Hospital

Wellington, , New Zealand

Site Status

Hospital Alberto Sabogal Sologuren

Callao, , Peru

Site Status

Hospital Nacional Adolfo Guevara Velasco - ESSALUD; Servicio de Cardiología

Cusco, , Peru

Site Status

Prof. Dr. Matei Bals Institute of Infectious Diseases

Bucharest, , Romania

Site Status

Dr. Victor Babes Clinical Hospital For Tropical and Infectious Diseases

Bucharest, , Romania

Site Status

Spitalul Clinic de Boli Infectioase

Cluj-Napoca, , Romania

Site Status

Sf.Cuv. Parascheva Infectious Diseases Clinical Hospital

Galati, , Romania

Site Status

Spitalul Clinic de Boli Infectioase "Sfanta Parascheva" Iasi

Iași, , Romania

Site Status

Sibiu Emergency Clinical County Hospital

Sibiu, , Romania

Site Status

Sf. Ioan cel Nou Emergency County Hospital

Suceava, , Romania

Site Status

Clinical Center of Serbia

Belgrade, , Serbia

Site Status

Clinical Hospital Center Zvezdara

Belgrade, , Serbia

Site Status

Institute of Lung Diseases Vojvodina

Kamenitz, , Serbia

Site Status

Clinical Center Kragujevac

Kragujevac, , Serbia

Site Status

Clinical Center Nis; Clinic for Pulmonary Diseases and Tuberculosis Knez Selo

Niš, , Serbia

Site Status

Clinical Centre of Vojvodina

Nova Sad, , Serbia

Site Status

General Hospital Dr Radivoj Simonovic Sombor

Sombor, , Serbia

Site Status

Tan Tock Seng Hospital

Singapore, , Singapore

Site Status

The Catholic University of Korea Incheon St. Mary's Hospital

Incheon, , South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam-si, , South Korea

Site Status

Korea University Anam Hospital

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

ChungAng University Hospital

Seoul, , South Korea

Site Status

Hallym University Kangnam Sacred Heart Hospital

Seoul, , South Korea

Site Status

Hospital Universitario Germans Trias i Pujol

Badalona, Barcelona, Spain

Site Status

Hospital Sant Joan de Deu - PIN; Unitat de Recerca - Farmacia

Esplugues de Llobregat, Barcelona, Spain

Site Status

Hospital Mutua de Terrassa

Terrassa, Barcelona, Spain

Site Status

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, Spain

Site Status

Hospital Universitario de Torrejon

Torrejón de Ardoz, Madrid, Spain

Site Status

Hospital General Universitario de Alicante

Alicante, , Spain

Site Status

Hospital del Mar

Barcelona, , Spain

Site Status

Hospital Universitario Vall d'Hebron - PPDS

Barcelona, , Spain

Site Status

Hospital Universitario Fundacion Jimenez Diaz.

Madrid, , Spain

Site Status

Hospital General Universitario Reina Sofia; Servicio de Nefrologia

Murcia, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

Hospital de La Ribera

Valencia, , Spain

Site Status

Sahlgrenska Universitetssjukhuset

Gothenburg, , Sweden

Site Status

Skånes Universitetssjukhus Malmö; Infektionskliniken

Malmo, , Sweden

Site Status

Hacettepe University Medical Faculty

Ankara, , Turkey (Türkiye)

Site Status

Akdeniz University Medical Faculty

Antalya, , Turkey (Türkiye)

Site Status

Selcuk University Medical Faculty; Internal Medicine

Konya, , Turkey (Türkiye)

Site Status

Karadeniz Technical University Faculty of Medicine

Trabzon, , Turkey (Türkiye)

Site Status

Regional Municipal Institution Chernivtsi Regional Clinical Hospital

Chernivtsi, Chernihiv Governorate, Ukraine

Site Status

Kyiv Oleksandrivska Clinical Hospital; Infectious Box Department #2

Kyiv, Katerynoslav Governorate, Ukraine

Site Status

Regional Municipal Institution Sumy Regional Infectious Clinical Hospital n.a. Z.Y. Krasovytskyi

Sumy, Katerynoslav Governorate, Ukraine

Site Status

Ternopil City Municipal Emergency Hospital; Infectious Department

Ternopil, KIEV Governorate, Ukraine

Site Status

Communal Non-Commercial Enterprise "Vinnytsia City Clinical Hospital №1"; Infectious Department

Vinnytsia, KIEV Governorate, Ukraine

Site Status

MI Vinnytsia Regional Clinical Children's Infectious Hospital; Infectiuos Box department

Vinnytsia, KIEV Governorate, Ukraine

Site Status

MI Dnipropetrovsk City Clinical Hospital #21 n.a. Prof. Popkova of DRC; The First Department

Dnipro, Podolia Governorate, Ukraine

Site Status

Municipal Institution City Clinical Infectious Diseases Hospital

Odesa, , Ukraine

Site Status

Countries

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United States Argentina Australia Belgium Brazil Bulgaria Canada China Czechia Estonia Finland France Germany Hong Kong Israel Japan Mexico Netherlands New Zealand Peru Romania Serbia Singapore South Korea Spain Sweden Turkey (Türkiye) Ukraine

References

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Stannard HL, Mifsud EJ, Wildum S, Brown SK, Koszalka P, Shishido T, Kojima S, Omoto S, Baba K, Kuhlbusch K, Hurt AC, Barr IG. Assessing the fitness of a dual-antiviral drug resistant human influenza virus in the ferret model. Commun Biol. 2022 Sep 28;5(1):1026. doi: 10.1038/s42003-022-04005-4.

Reference Type DERIVED
PMID: 36171475 (View on PubMed)

Kumar D, Ison MG, Mira JP, Welte T, Hwan Ha J, Hui DS, Zhong N, Saito T, Katugampola L, Collinson N, Williams S, Wildum S, Ackrill A, Clinch B, Lee N. Combining baloxavir marboxil with standard-of-care neuraminidase inhibitor in patients hospitalised with severe influenza (FLAGSTONE): a randomised, parallel-group, double-blind, placebo-controlled, superiority trial. Lancet Infect Dis. 2022 May;22(5):718-730. doi: 10.1016/S1473-3099(21)00469-2. Epub 2022 Jan 24.

Reference Type DERIVED
PMID: 35085510 (View on PubMed)

Young B, Tan TT, Leo YS. The place for remdesivir in COVID-19 treatment. Lancet Infect Dis. 2021 Jan;21(1):20-21. doi: 10.1016/S1473-3099(20)30911-7. Epub 2020 Nov 26. No abstract available.

Reference Type DERIVED
PMID: 33248473 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-001416-30

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CP40617

Identifier Type: -

Identifier Source: org_study_id

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