Study to Assess the Safety, Pharmacokinetics, and Efficacy of Baloxavir Marboxil in Healthy Pediatric Participants With Influenza-Like Symptoms

NCT ID: NCT03629184

Last Updated: 2020-04-29

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

173 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-11-20

Study Completion Date

2019-04-03

Brief Summary

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This study will evaluate the safety, pharmacokinetics, and efficacy of baloxavir marboxil compared with oseltamivir in a single influenza episode in otherwise healthy pediatric participants (i.e., 1 to \<12 years of age) with influenza-like symptoms.

Detailed Description

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Conditions

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Influenza

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Baloxavir Marboxil

Participants will receive a single oral dose of baloxavir marboxil on Day 1 (based on body weight). Oseltamivir matching placebo will also be administered orally twice daily (BID) for 5 days.

Group Type EXPERIMENTAL

Baloxavir Marboxil

Intervention Type DRUG

Baloxavir marboxil will be administered as oral suspension in a single dose on Day 1.

Oseltamivir matching placebo will also be administered as oral suspension twice daily (BID) for 5 days.

Oseltamivir

Participants will receive oseltamivir orally BID for 5 days (based on body weight). Baloxavir marboxil matching placebo will also be administered orally on Day 1

Group Type ACTIVE_COMPARATOR

Oseltamivir

Intervention Type DRUG

Oseltamivir will be administered as oral suspension BID for 5 days. Participants receiving oseltamivir will also receive baloxavir marboxil matching placebo as oral suspension, single dose on Day 1.

Interventions

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Baloxavir Marboxil

Baloxavir marboxil will be administered as oral suspension in a single dose on Day 1.

Oseltamivir matching placebo will also be administered as oral suspension twice daily (BID) for 5 days.

Intervention Type DRUG

Oseltamivir

Oseltamivir will be administered as oral suspension BID for 5 days. Participants receiving oseltamivir will also receive baloxavir marboxil matching placebo as oral suspension, single dose on Day 1.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Aged 1 to \< 12 years at randomization (Day 1).
* Written informed consent/assent for study participation obtained from participant's parents or legal guardian, with assent as appropriate by the participant, depending on the patient's level of understanding
* Participant able to comply with study requirements, depending on the patient's level of understanding
* Participant with a diagnosis of influenza virus infection confirmed by the presence of all of the following:
* Fever ≥ 38 degree celsius (tympanic temperature) at screening
* At least one respiratory symptom (either cough or nasal congestion)
* The time interval between the onset of symptoms and screening is ≤ 48 hours

Exclusion Criteria

* Severe symptoms of influenza virus infection requiring inpatient treatment
* Concurrent infections requiring systemic antiviral therapy at screening
* Require, in the opinion of the investigator, any of the prohibited medication during the study
* Previous treatment with peramivir, laninamivir, oseltamivir, zanamivir, or amantadine within 2 weeks prior to screening
* Immunization with a live/attenuated influenza vaccine in the 2 weeks prior to randomization
* Concomitant treatment with steroids or other immuno-suppressant therapy
* Known HIV infection or other immunosuppressive disorder
* Uncontrolled renal, vascular, neurologic, or metabolic disease (e.g., diabetes, thyroid disorders, adrenal disease), hepatitis, cirrhosis, or pulmonary disease or participants with known chronic renal failure.
* Active cancer at any site
* History of organ transplantation
* Known allergy to either study drug (i.e., baloxavir marboxil and oseltamivir) or to acetaminophen
* Females with child-bearing potential
* Participation in a clinical trial within 4 weeks or five half-lives of exposure to an investigational drug prior to screening, whichever is longer
Minimum Eligible Age

1 Year

Maximum Eligible Age

11 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Central Alabama Research; Pediatrics

Birmingham, Alabama, United States

Site Status

Harrisburg Family Medical Center

Harrisburg, Arkansas, United States

Site Status

The Children's Clinic of Jonesboro, P.A.

Jonesboro, Arkansas, United States

Site Status

The Probe Medical Research

Los Angeles, California, United States

Site Status

Orange County Research Institute

Ontario, California, United States

Site Status

Khruz Biotechnology Research Institute

San Diego, California, United States

Site Status

Avanza Medical Research Center

Pensacola, Florida, United States

Site Status

Clinical Research Prime

Idaho Falls, Idaho, United States

Site Status

Cotton O'Neil Clinic; Stormont-Vail Hlth Care

Topeka, Kansas, United States

Site Status

Kentucky Pediatric Research Center

Bardstown, Kentucky, United States

Site Status

Spiegel, Craig

Bridgeton, Missouri, United States

Site Status

Meridian Clinical Research, Llc

Omaha, Nebraska, United States

Site Status

Machuca Family Medicine

Las Vegas, Nevada, United States

Site Status

OnSite Clinical Solutions LLC

Charlotte, North Carolina, United States

Site Status

Montgomery Medical Research /Frontier Clinical Research

Smithfield, North Carolina, United States

Site Status

Ohio Pediatric Research Association

Dayton, Ohio, United States

Site Status

Coastal Pediatric Research

Charleston, South Carolina, United States

Site Status

AFC Urgent Care- Cleveland

Cleveland, Tennessee, United States

Site Status

Holston Medical Group

Kingsport, Tennessee, United States

Site Status

Oak Cliff Research Company, LLC

Dallas, Texas, United States

Site Status

HD Research Corp

Houston, Texas, United States

Site Status

Mercury Clinical Research

Houston, Texas, United States

Site Status

Tekton Research

San Antonio, Texas, United States

Site Status

DM Clinical Research

Tomball, Texas, United States

Site Status

ClinPoint Trials

Waxahachie, Texas, United States

Site Status

FirstMed East (J Lewis Research)

Salt Lake City, Utah, United States

Site Status

Advanced Clinical Research - Jordan Ridge Family Medicine

Salt Lake City, Utah, United States

Site Status

ICIMED Instituto de Investigación en Ciencias Médicas

San José, , Costa Rica

Site Status

Clalit Health Services- Pediatric Ambulatory Clinic; Pediatric Ambulatory Clinic

Petah Tikva, , Israel

Site Status

Hospital San Jose; Centro de investigacion y transferencia en salud del Tec de Monterrey

Monterrey, N.L, , Mexico

Site Status

Wojewodzki Szpital Obserwacyjno-Zakazny; Oddział Pediatrii, Chorób Infekcyjnych i Hepatologii

Bydgoszcz, , Poland

Site Status

NZOZ Vitamed

Bydgoszcz, , Poland

Site Status

Prywatny Gabinet Lekarski

Dębica, , Poland

Site Status

NZLA Michalkowice Jarosz i partnerzy Spolka Lekarska

Siemianowice Śląskie, , Poland

Site Status

MC Gepatolog

Samara, , Russia

Site Status

Complejo Hospitalario Universitario de Santiago (CHUS); Area Asistencial Integrada de Pediatría

Santiago de Compostela, LA Coruña, Spain

Site Status

Hospital Universitario 12 de Octubre; Servicio de Pediatria

Madrid, , Spain

Site Status

Countries

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United States Costa Rica Israel Mexico Poland Russia Spain

References

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Baker J, Block SL, Matharu B, Burleigh Macutkiewicz L, Wildum S, Dimonaco S, Collinson N, Clinch B, Piedra PA. Baloxavir Marboxil Single-dose Treatment in Influenza-infected Children: A Randomized, Double-blind, Active Controlled Phase 3 Safety and Efficacy Trial (miniSTONE-2). Pediatr Infect Dis J. 2020 Aug;39(8):700-705. doi: 10.1097/INF.0000000000002747.

Reference Type DERIVED
PMID: 32516282 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-002169-21

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CP40563

Identifier Type: -

Identifier Source: org_study_id

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