Study to Assess the Safety, Pharmacokinetics, and Efficacy of Baloxavir Marboxil in Healthy Pediatric Participants From Birth to < 1 Year With Influenza-Like Symptoms

NCT ID: NCT03653364

Last Updated: 2024-05-17

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

49 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-01-23

Study Completion Date

2023-04-03

Brief Summary

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This study will evaluate the safety, pharmacokinetics and efficacy of baloxavir marboxil in healthy pediatric participants from birth to \<1 year with influenza like symptoms

Detailed Description

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Conditions

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Influenza

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Baloxavir Marboxil

Participants will receive single oral dose of baloxavir marboxil on Day 1 (based on body weight and age).

Group Type EXPERIMENTAL

Baloxavir Marboxil

Intervention Type DRUG

Participants will receive single oral dose of baloxavir marboxil on Day 1 based on body weight and age. Participants aged ≥ 3 months to \<12 months old received baloxavir marboxil, 2 milligrams per kilograms (mg/kg). Participants from birth to \< 4 weeks old and ≥ 4 weeks to \< 3 months old received baloxavir marboxil, 1 mg/kg.

Interventions

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Baloxavir Marboxil

Participants will receive single oral dose of baloxavir marboxil on Day 1 based on body weight and age. Participants aged ≥ 3 months to \<12 months old received baloxavir marboxil, 2 milligrams per kilograms (mg/kg). Participants from birth to \< 4 weeks old and ≥ 4 weeks to \< 3 months old received baloxavir marboxil, 1 mg/kg.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age from birth to \< 1 year at screening
* Written informed consent for study participation obtained from participant's parents or legal guardian
* Parent/guardian willing and able to comply with study requirements, in the investigator's judgment
* Participants with a diagnosis of influenza virus infection confirmed by the presence of all of the following:

1. In the investigator's judgement there is a clinical suspicion of influenza
2. At least one respiratory symptom (either cough or coryza)

(b) Positive prescreening influenza test (RIDT or PCR) performed within 48 hours of screening
* Participants with a negative prescreening COVID-19 test (RAT or PCR) within 48 hours of screening
* The time interval between the onset of symptoms and screening is ≤ 96 hours (the onset of symptoms is defined as the time when body temperature first exceeded 37.5°C if known, or the time when the first symptom was noticed by the parent or caregiver)

Exclusion Criteria

* Hospitalized for complications of influenza or significant comorbidities
* Concurrent infections requiring systemic antiviral therapy at screening
* Require, in the opinion of the investigator, any of the prohibited medication during the study
* Preterm neonates (born at \< 37 weeks gestation) and/or weighing \< 2.5 kg at screening
* Previous treatment with peramivir, laninamivir, oseltamivir, zanamivir, or amantadine within 2 weeks prior to screening
* Immunization with a live/attenuated influenza vaccine during the 2 weeks prior to screening
* Concomitant treatment with steroids or other immuno-suppressant therapy
* Known HIV infection or other immunosuppressive disorder
* Uncontrolled renal, vascular, neurologic or metabolic disease (e.g., diabetes, thyroid disorders, adrenal disease), hepatitis, cirrhosis, or pulmonary disease or participants with known chronic renal failure
* Active cancer at any site
* History of organ transplant
* Known hypersensitivity to study drug (i.e., baloxavir marboxil) or to acetaminophen
* Participation in a clinical trial within 4 weeks or five half-lives of exposure to an investigational drug prior to screening, whichever is longer
Maximum Eligible Age

1 Year

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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The Children's Clinic of Jonesboro, P.A.

Jonesboro, Arkansas, United States

Site Status

Usf Health

Tampa, Florida, United States

Site Status

Clinical Research Prime

Idaho Falls, Idaho, United States

Site Status

Ann & Robert H. Lurie Children's Hospital of Chicago;Division of Infectious Disease

Chicago, Illinois, United States

Site Status

Kentucky Pediatric Research Center

Bardstown, Kentucky, United States

Site Status

Oak Cliff Research Company, LLC

Dallas, Texas, United States

Site Status

Mercury Clinical Research

Houston, Texas, United States

Site Status

Tekton Research

San Antonio, Texas, United States

Site Status

MHAT Stamen Iliev AD

Montana, , Bulgaria

Site Status

SHAT for Pneumo-Phtysiatric Diseases ?Dr. Dimitar Gramatikov?; Dept. of Pulmonology and Phtisiatrics

Rousse, , Bulgaria

Site Status

ICIMED Instituto de Investigación en Ciencias Médicas

San José, , Costa Rica

Site Status

TAYS Lastenklinikka; Lasten lääketutkimuskeskus Peetu

Tampere, , Finland

Site Status

Clalit Health Services- Pediatric Ambulatory Clinic; Pediatric Ambulatory Clinic

Petah Tikva, , Israel

Site Status

NZOZ Salmed

??czna, , Poland

Site Status

Samodzielny Zespol Publicznych Zakladow Opieki Zdrowotnej im. Dzieci Warszawy w Dziekanowie Lesnym

?omianki, , Poland

Site Status

Wojewodzki Szpital Obserwacyjno-Zakazny; Oddzia? Pediatrii, Chorób Infekcyjnych i Hepatologii

Bydgoszcz, , Poland

Site Status

IN VIVO Sp. z o.o.

Bydgoszcz, , Poland

Site Status

NZOZ Vitamed

Bydgoszcz, , Poland

Site Status

The scientific-research institute of epidemiology; Infectious clinical hospital ?2 of Moscow H.D.

Moskva, Moscow Oblast, Russia

Site Status

Global Clinical Trials; Clinical Trials

Gauteng, , South Africa

Site Status

GAMA; Clinical Research

Germiston, , South Africa

Site Status

Peermed Clinical Trial Centre

Kempton Park, , South Africa

Site Status

Metropolitan Clinical Research Institute

Polokwane, , South Africa

Site Status

Pholosho Netcare; Netcare Hospital

Polokwane, , South Africa

Site Status

Setshaba Research Centre; Clinical Research

Pretoria, , South Africa

Site Status

Complejo Hospitalario Universitario de Santiago (CHUS); Area Asistencial Integrada de Pediatría

Santiago de Compostela, LA Coruña, Spain

Site Status

Hospital Universitario 12 de Octubre; Servicio de Pediatria

Madrid, , Spain

Site Status

Countries

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United States Bulgaria Costa Rica Finland Israel Poland Russia South Africa Spain

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-002154-70

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CP40559

Identifier Type: -

Identifier Source: org_study_id

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