Study to Determine the Efficacy of Uproleselan (GMI-1271) in Combination With Chemotherapy to Treat Relapsed/Refractory Acute Myeloid Leukemia

NCT ID: NCT03616470

Last Updated: 2024-07-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

388 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-10-15

Study Completion Date

2024-03-31

Brief Summary

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This study will evaluate the efficacy of uproleselan (GMI-1271), a specific E-selectin antagonist, in combination with chemotherapy to treat relapsed/refractory AML, compared to chemotherapy alone. The safety of uproleselan when given with chemotherapy will also be investigated in patients with relapsed/refractory AML

Detailed Description

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Conditions

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Acute Myeloid Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Uproleselan (GMI-1271)

Uproleselan in combination with mitoxantrone, etoposide and cytarabine (MEC) or fludarabine, cytarabine and idarubicin (FAI)

Group Type EXPERIMENTAL

Uproleselan

Intervention Type DRUG

A rationally designed E-selectin antagonist used to inhibit binding of cells to E-selectin

Placebo (Saline, 0.9% Sodium Chloride)

Placebo in combination with mitoxantrone, etoposide and cytarabine (MEC) or fludarabine, cytarabine and idarubicin (FAI)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Saline, 0.9% Sodium Chloride

Interventions

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Uproleselan

A rationally designed E-selectin antagonist used to inhibit binding of cells to E-selectin

Intervention Type DRUG

Placebo

Saline, 0.9% Sodium Chloride

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* ≥18 years and ≤75 years in age
* Patients with relapsed or refractory AML
* No more than one prior stem cell transplant
* Has not received the chemotherapy regimen to be used for induction on this trial
* Is considered medically eligible to receive the chemotherapy regimen to be used for induction on this trial

Exclusion Criteria

* Patients with acute promyelocytic leukemia, acute leukemia of ambiguous lineage (biphenotypic leukemia), chronic myeloid leukemia with myeloid blast crisis, or secondary refractory AML.
* Active signs or symptoms of CNS involvement by malignancy.
* Stem cell transplantation ≤4 months prior to dosing.
* Any immunotherapy or radiotherapy therapy within 28 days of dosing; any other experimental therapy or chemotherapy within 14 days of dosing.
* Prior use of G-CSF, CM-CSF or plerixafor within 7 days of dosing.
* Inadequate organ function.
* Abnormal liver function.
* Known active infection with hepatitis A, B, or C, or human immunodeficiency virus.
* Moderate kidney dysfunction (glomerular filtration rate \<45 mL/min).
* Uncontrolled acute life-threatening bacterial, viral, or fungal infection.
* Clinically significant cardiovascular disease.
* Major surgery within 4 weeks of dosing.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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GlycoMimetics Incorporated

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Daniel J DeAngelo, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Dana-Farber Cancer Institute

Locations

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UC San Diego Moore Cancer Center

La Jolla, California, United States

Site Status

University of California, Los Angeles - UCLA

Los Angeles, California, United States

Site Status

University of California Irvine

Orange, California, United States

Site Status

Stanford Cancer Institute

Palo Alto, California, United States

Site Status

UC Davis Comprehensive Cancer Center

Sacramento, California, United States

Site Status

Emory Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Northside Hospital - Medical Tower

Atlanta, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

The University of Kansas Cancer Center

Westwood, Kansas, United States

Site Status

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

Hudson Valley Cancer Center

Hawthorne, New York, United States

Site Status

Columbia University Herbert Irving Comprehensive Cancer Center

New York, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

Duke University Health System (DUHS)

Durham, North Carolina, United States

Site Status

Wake Forest Baptist Hospital

Winston-Salem, North Carolina, United States

Site Status

University Hospital Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

The Ohio State University Wexner Medical Center and James Cancer Hospital

Columbus, Ohio, United States

Site Status

Stephenson Cancer Center

Oklahoma City, Oklahoma, United States

Site Status

Vanderbilt-Ingram Cancer Center Clinical Trials Office

Nashville, Tennessee, United States

Site Status

Charles A. Sammons Cancer Center at Dallas

Dallas, Texas, United States

Site Status

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Huntsman Cancer Institute, University of Utah

Salt Lake City, Utah, United States

Site Status

Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

Calvary Mater Newcastle

Waratah, New South Wales, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Perth, Australia

Site Status

Townsville Hospital

Douglas, Queensland, Australia

Site Status

Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status

Flinders Medical Centre

Bedford Park, South Australia, Australia

Site Status

Cancer Clinical Trials Centre (CCTC)

Heidelberg, Victoria, Australia

Site Status

Tom Baker Cancer Center

Calgary, Alberta, Canada

Site Status

University of Alberta Princess Margaret Hospital

Edmonton, Alberta, Canada

Site Status

The Leukemia/BMT Program of BC Vancouver General Hospital

Vancouver, British Columbia, Canada

Site Status

CancerCare Manitoba

Winnipeg, Manitoba, Canada

Site Status

Juravinski Cancer Centre

Hamilton, Ontario, Canada

Site Status

University Health Network (UHN) - Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status

Centre Hospitalier Universitaire d'Angers

Angers, , France

Site Status

Centre Hospitalier Universitaire de Bordeaux

Bordeaux, , France

Site Status

Centre Hospitalier Universitaire Grenoble Alpes

La Tronche, , France

Site Status

Unité d'Evaluation Thérapeutique en Onco-Hématologie (ETHO)

Marseille, , France

Site Status

Saint-Louis Hospital

Paris, , France

Site Status

Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status

Centre Hospitalier Universitaire de Poitiers

Poitiers, , France

Site Status

Galway University Hospital

Galway, , Ireland

Site Status

IRCCS Casa Sollievo della Sofferenza Hospital

San Giovanni Rotondo, FG, Italy

Site Status

Institute of Hematology and Medical Oncology "L. and A. Seràgnoli"

Bologna, , Italy

Site Status

Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori (IRST)

Meldola, , Italy

Site Status

Hospital of Ravenna

Ravenna, , Italy

Site Status

Fondazione Policlinico Tor Vergata, U.O.C. Ematologia

Roma, , Italy

Site Status

Università Cattolica del Sacro Cuore (UNICATT)

Rome, , Italy

Site Status

Ca' Foncello Hospital

Treviso, , Italy

Site Status

VU University Medical Center

Amsterdam, , Netherlands

Site Status

University Medical Center Groningen

Groningen, , Netherlands

Site Status

University Medical Centre Utrecht

Utrecht, , Netherlands

Site Status

Hospital San Pedro De Alcantra

Cáceres, , Spain

Site Status

Hospital MDACC

Madrid, , Spain

Site Status

Hospital Universitario Fundación Jiménez Diaz

Madrid, , Spain

Site Status

Hospital Virgen de la Victoria, Málaga

Málaga, , Spain

Site Status

Clínica Universidad de Navarra

Pamplona, , Spain

Site Status

Hospital Universitario de Salamanca

Salamanca, , Spain

Site Status

University Hospital of Hospital Marqués de Valdecilla

Santander, , Spain

Site Status

Hospital Universitari i Politècnic La Fe

Valencia, , Spain

Site Status

Radcliffe Hospitals and University of Oxford

Oxford, England, United Kingdom

Site Status

Cardiff University School of Medicine

Cardiff, , United Kingdom

Site Status

Countries

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United States Australia Canada France Ireland Italy Netherlands Spain United Kingdom

Other Identifiers

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GMI-1271-301

Identifier Type: -

Identifier Source: org_study_id

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