Eganelisib as Monotherapy and in Combination With Cytarabine in Relapsed/Refractory AML

NCT ID: NCT06533761

Last Updated: 2025-10-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

125 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-04-28

Study Completion Date

2028-03-15

Brief Summary

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This is a Phase 1b open-label, multicenter, dose-escalation and dose-optimization study designed to evaluate the safety, tolerability, pharmacokinetics (PK), pharmacodynamics (PD), and anti-tumor efficacy of eganelisib as monotherapy and in combination with cytarabine in patients with relapsed/refractory (r/r) acute myeloid leukemia (AML) or r/r higher-risk myelodysplastic syndromes (HR-MDS).

The study consists of 2 parts:

* Part 1: Dose Escalation (DE) in both monotherapy and in combination.
* Part 2: Dose Optimization

Detailed Description

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Conditions

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AML, Adult MDS

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Eganelisib

Group Type EXPERIMENTAL

Eganelisib

Intervention Type DRUG

eganelisib will be administered as monotherapy

Eganelisib in combination with cytarabine

Group Type EXPERIMENTAL

Eganelisib in combination with cytarabine

Intervention Type DRUG

eganelisib will be administered in combination with cytarabine

Interventions

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Eganelisib

eganelisib will be administered as monotherapy

Intervention Type DRUG

Eganelisib in combination with cytarabine

eganelisib will be administered in combination with cytarabine

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Pathological diagnosis of either: AML according to World Health Organization (WHO) 2022 revised criteria per the local pathology report and with ≥10% bone marrow blasts (acute promyelocytic leukemia is excluded but secondary AML and treatment-related AML can be included); Higher-risk (IPSS-R Intermediate, High or Very High Risk at time of study entry) myelodysplastic syndromes (HR-MDS) according to WHO 2022 revised criteria per the local pathology report and with ≥10% bone marrow blasts.
* Eastern Cooperative Oncology Group (ECOG) performance status ≤2.
* Adequate hepatic and renal function measured within 7 days prior to the first dose of eganelisib.

Exclusion Criteria

* Autologous or allogeneic stem cell transplant within 6 months prior to Cycle 1 Day 1.
* Receiving immunosuppressants (eg, cyclosporin) or systemic steroids (except for steroid use as cortisol replacement therapy in documented adrenal insufficiency).
* Active fungal disease or uncontrolled infection of any kind; patients receiving antibiotic, antifungal or antiviral treatment must be afebrile and hemodynamically stable for \>72 hours prior to treatment
* WBC count \>25 × 10\^9/L measured within 7 days prior to the first dose of eganelisib (hydroxyurea is permitted to decrease the WBC count).
* Presence of a clinically significant non-hematologic toxicity of prior therapy that has not resolved to Grade ≤1 or Baseline, whichever is worst, as determined by NCI CTCAE v 5.0, except alopecia or skin pigmentation. Fatigue and neuropathy must have resolved to Grade ≤2.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Stelexis BioSciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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City of Hope

Duarte, California, United States

Site Status RECRUITING

Anshutz Cancer Pavilion

Aurora, Colorado, United States

Site Status RECRUITING

Moffitt Cancer Center

Tampa, Florida, United States

Site Status RECRUITING

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

Washington University in St Louis

St Louis, Missouri, United States

Site Status RECRUITING

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status NOT_YET_RECRUITING

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

Montefiore Medical Center

New York, New York, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Ohio State University

Columbus, Ohio, United States

Site Status RECRUITING

MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Hospital San Pedro de Alcántara

Cáceres, , Spain

Site Status RECRUITING

Hospital Universitari i Politècnic La Fe

Valencia, , Spain

Site Status RECRUITING

Countries

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United States Spain

Central Contacts

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Clinical Trials Office Stelexis

Role: CONTACT

508-543-6979

Facility Contacts

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Shukaib Arslan

Role: primary

626-218-1133

Kara Grau

Role: primary

Wes Mungal

Role: primary

813-745-0851

Megan Forsyth

Role: primary

857-215-1405

Na'kie Coleman-Elhasan

Role: primary

314-454-8708

Anmol Shah

Role: primary

646-608-2813

Anmol Shah

Role: primary

646-608-2813

Davina Hoban

Role: primary

201-618-4725

Ibraheem Al-Aref

Role: primary

216-442-0461

Sarah Mayne

Role: primary

614-685-9573

Meagan Sachs

Role: primary

713-503-1589

Juan Miguel Bergua Burgues

Role: primary

+34 675 699735

Rebeca Rodriguez Veiga

Role: primary

+34 961 245876

Other Identifiers

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STLX-EGA-001

Identifier Type: -

Identifier Source: org_study_id

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