A Study of INCMGA00012 in Metastatic Merkel Cell Carcinoma (POD1UM-201)

NCT ID: NCT03599713

Last Updated: 2025-08-05

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

107 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-02-25

Study Completion Date

2024-06-28

Brief Summary

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The purpose of this study is to assess the clinical activity and safety of INCMGA00012 in participants with advanced/metastatic Merkel cell carcinoma (MCC).

Detailed Description

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Conditions

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Metastatic Merkel Cell Carcinoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Retifanlimab: Chemotherapy: Naïve

Group Type EXPERIMENTAL

Retifanlimab

Intervention Type DRUG

INCMGA00012 administered at 500 milligrams (mg) by intravenous infusion once every 4 weeks

Retifanlimab: Chemotherapy: Refractory

Group Type EXPERIMENTAL

Retifanlimab

Intervention Type DRUG

INCMGA00012 administered at 500 milligrams (mg) by intravenous infusion once every 4 weeks

Interventions

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Retifanlimab

INCMGA00012 administered at 500 milligrams (mg) by intravenous infusion once every 4 weeks

Intervention Type DRUG

Other Intervention Names

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MGA012 INCMGA00012

Eligibility Criteria

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Inclusion Criteria

* Signed informed consent.
* Diagnosis of MCC with distant metastatic disease or recurrent, advanced locoregional disease not amenable to surgery or radiation
* Eastern Cooperative Oncology Group performance status of 0 to 1.
* Measurable disease according to RECIST v1.1.
* Availability of tumor tissue (fresh or archival) for central pathology review.
* Willingness to avoid pregnancy or fathering children based on protocol-defined criteria.

Exclusion Criteria

* Prior systemic therapy for MCC, including chemotherapy and prior PD-1 or PD-L1-directed therapy.
* Treatment with anticancer drugs or participation in another interventional clinical study within 21 days before the first administration of study drug.
* Has not recovered to ≤ Grade 1 or baseline from toxic effects of prior therapy (with the exceptions for anemia not requiring transfusion support and any grade of alopecia) and/or complications from prior surgical intervention within 7 days before starting study treatment.
* Radiation therapy administered within 2 weeks of first dose of study treatment or radiation therapy to the thoracic region that is \> 30 Gy within 6 months of the first dose of study treatment.
* Known central nervous system (CNS) metastases and/or carcinomatous meningitis.
* History of second malignancy within 3 years (with exceptions).
* Laboratory values outside the protocol-defined range at screening.
* Clinically significant pulmonary, cardiac, gastrointestinal or autoimmune disorders.
* Active bacterial, fungal, or viral infections, including hepatitis A, B, and C.
* Receipt of a live vaccine within 28 days of planned start of study therapy.
* Current use of protocol-defined prohibited medication.
* Known hypersensitivity to another monoclonal antibody that cannot be controlled with standard measures (eg, antihistamines and corticosteroids).
* Inability or unlikely, in the opinion of the investigator, to comply with the Protocol requirements.
* Participant who is pregnant or breastfeeding.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Incyte Medical Monitor

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Stanford Cancer Institute

Palo Alto, California, United States

Site Status

University of California San Francisco Comprehensive Cancer Center

San Francisco, California, United States

Site Status

University of Colorado Cancer Center

Aurora, Colorado, United States

Site Status

Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

Rush University

Chicago, Illinois, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status

John Theurer Cancer Center, Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Rutgers Cancer Institute of Nj

New Brunswick, New Jersey, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

The Christ Hospital

Cincinnati, Ohio, United States

Site Status

Upmc Cancercenter

Pittsburgh, Pennsylvania, United States

Site Status

Inova Fairfax Hospital

Fairfax, Virginia, United States

Site Status

University of Washington - Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

West Virginia University Hospitals Inc

Morgantown, West Virginia, United States

Site Status

St Vincent'S Hospital Sydney

Darlinghurst, New South Wales, Australia

Site Status

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status

Tom Baker Cancer Centre

Calgary AB, CA, Canada

Site Status

London Health Sciences Centre Lhsc - South Street Hospital

London, Ontario, Canada

Site Status

Sir Mortimer B. Davis Jewish General Hospital Segal Cancer Ctr

Montreal, Quebec, Canada

Site Status

McGill University Health Centre/Glen Site/Cedars Cancer Centre

Montreal, Quebec, Canada

Site Status

Fakultni Nemocnice Olomouc

Olomouc, , Czechia

Site Status

Prof Mudr Petr Arenberger Drsc Mba

Prague, , Czechia

Site Status

Nemocnice Na Bulovce

Prague, , Czechia

Site Status

Thomayerova Nemocnice

Praha 4-krc, , Czechia

Site Status

H�PITAL AMBROISE PAR

Boulogne-Billancourt, , France

Site Status

Chu Hopital de La Timone

Marseille, , France

Site Status

Centre Hospitalier Universitaire de Nantes (Chu de Nantes) - Hotel-Dieu

Nantes, , France

Site Status

CHU DE NICE - H�PITAL L'ARCHET 1

Nice, , France

Site Status

Hospital Saint Louis

Paris, , France

Site Status

HOPITAL CHARLES NICOLLE CHU ROUEN - H�PITAL DE BOIS-GUILLAUME

Rouen, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Charite Universitaetsmedizin Berlin - Campus Charite Mitte

Berlin, , Germany

Site Status

Elbe Klinikum Buxtehude

Buxtehude, , Germany

Site Status

Helios Klinikum Erfurt

Erfurt, , Germany

Site Status

Universitatsklinikum Essen

Essen, , Germany

Site Status

Universitatsklinikum Schleswig-Holstein

Kiel, , Germany

Site Status

Universitatsklinikum Giessen Und Marburg Gmbh, Klinik Für Innere Medizin

Marburg, , Germany

Site Status

University Hospital Regensburg

Regensburg, , Germany

Site Status

Universitaetsklinikum in Tubingen

Tübingen, , Germany

Site Status

National Institute of Oncology

Budapest, , Hungary

Site Status

Debreceni Egyetem Klinikai Kozpon Belgyogy Klinika

Debrecen, , Hungary

Site Status

Szte Borgyogyszati Es Allergologiai Klinika

Szeged, , Hungary

Site Status

Istituto Tumori Giovanni Paolo Ii Irccs Ospedale Oncologico Bari

Bari, , Italy

Site Status

Fondazione Del Piemonte Per L'Oncologia Ircc Candiolo

Candiolo, , Italy

Site Status

Irccs Azienda Ospedaliera Universitaria San Martino

Genova, , Italy

Site Status

Fondazione Irccs Istituto Nazionale Dei Tumori

Milan, , Italy

Site Status

European Institute of Oncology

Milan, , Italy

Site Status

A.O.U. Di Modena - Policlinico

Modena, , Italy

Site Status

Istituto Nazionale Tumori Irccs Fondazione Pascale

Naples, , Italy

Site Status

Iov - Istituto Oncologico Veneto Irccs

Padua, , Italy

Site Status

ONCOLOGIA � IDI IRCCS ISTITUTO DERMOPATICO DELL'IMMACOLATA

Rome, , Italy

Site Status

Azienda Ospedaliera Universitaria Senese Policlinico Santa Maria Alle Scotte

Siena, , Italy

Site Status

Centrum Onkologii - Instytut Im. Marii Sklodowskiej - Curie

Warsaw, , Poland

Site Status

Hospital General Universitario Vall D Hebron

Barcelona, , Spain

Site Status

Hospital Clinic I Provincial

Barcelona, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Centre Hospitalier Universitaire Vaudois (Chuv)

Lausanne, , Switzerland

Site Status

Universitatsspital Zurich

Zurich, , Switzerland

Site Status

Castle Hill Hospital

Cottingham, , United Kingdom

Site Status

Royal Free London Nhs Foundation Trust

London, , United Kingdom

Site Status

The Royal Marsden Nhs Foundation Trust

London, , United Kingdom

Site Status

The Royal Marsden Nhs Foundation Trust - Sutton

Sutton, , United Kingdom

Site Status

Royal Cornwall Hospital Truro Sunrise Centre

Truro, , United Kingdom

Site Status

Countries

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United States Australia Canada Czechia France Germany Hungary Italy Poland Spain Switzerland United Kingdom

References

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Grignani G, Rutkowski P, Lebbe C, Guida M, Gaudy-Marqueste C, Spagnolo F, Burgess M, Morano F, Montaudie H, Depenni R, Spada F, Yeung CCS, Pulini J, Cornfeld M, Tian C, Bhatia S. Phase II study of retifanlimab in patients with recurrent locally advanced or metastatic Merkel cell carcinoma (POD1UM-201). J Immunother Cancer. 2025 Aug 11;13(8):e012478. doi: 10.1136/jitc-2025-012478.

Reference Type DERIVED
PMID: 40796223 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-001627-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCMGA 0012-201

Identifier Type: -

Identifier Source: org_study_id

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