Pulmonary and Upper Limb Functions in Duchenne Muscular Dystrophy

NCT ID: NCT03552874

Last Updated: 2018-06-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

47 participants

Study Classification

OBSERVATIONAL

Study Start Date

2017-01-01

Study Completion Date

2018-03-31

Brief Summary

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Although it is known that the functions of pulmonary and upper limb is affected in late stage of Duchenne Muscular Dystrophy (DMD) negatively, the investigators do not have clear information about its early stage. The aim of this study was to investigate the differences in pulmonary and upper limb functions between children with DMD in early stage and healthy peers.

Detailed Description

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Conditions

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Duchenne Muscular Dystrophy Upper Limb Function Respiratory Function Test

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Patient Group

Children whose ages between 5-10 years with Duchenne Muscular Dystrophy.

The Performance of Upper Limb Questionnaire (PUL)

Intervention Type OTHER

Healthy Group

Healthy peers

The Performance of Upper Limb Questionnaire (PUL)

Intervention Type OTHER

Interventions

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The Performance of Upper Limb Questionnaire (PUL)

Intervention Type OTHER

Other Intervention Names

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Pulmonary Function Test (PFT)

Eligibility Criteria

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Inclusion Criteria

children with DMD was;

* age between 5-10 years
* being on treatment with corticosteroids for more than 6 months
* being at Level I according to Brooke Upper and Lower Extremity Classification Systems

Healthy peers;

* age between 5-10 years
* not having any diagnosed disease

Exclusion Criteria

• Children has undergo surgery and disease affect upper extremity or pulmonary function in last six months.
Minimum Eligible Age

5 Years

Maximum Eligible Age

10 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

Yes

Sponsors

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Hacettepe University

OTHER

Sponsor Role lead

Responsible Party

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Numan Bulut

Department of Physiotherapy and Rehabilitation, Principal Investigator, Research Assistant

Responsibility Role PRINCIPAL_INVESTIGATOR

Other Identifiers

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GO 16/773

Identifier Type: -

Identifier Source: org_study_id

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