Study Evaluating Efficacy and Safety of FFX Versus Combination of CPI-613 With mFFX in Patients With Metastatic Adenocarcinoma of the Pancreas

NCT ID: NCT03504423

Last Updated: 2023-01-03

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

528 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-11-09

Study Completion Date

2022-01-02

Brief Summary

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A prospective, multicenter, open label, randomized phase III study to evaluate efficacy and safety of FFX versus CPI-613 + mFFX in patients with metastatic adenocarcinoma of the pancreas with age range of 18 to 75 years

Detailed Description

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Conditions

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Pancreatic Cancer Metastatic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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CPI-613, mFolfirinox

CPI-613, mFolfirinox

CPI-613 at 500 mg/m2 IV infusion at a rate of 4mL/min via a central venous port on day 1 and 3 of a 14-day cycle.

mFolfirinox (given immediately after CPI-613 administration): Oxaliplatin (Eloxatin) at 65 mg/m2 given as a 2 hr IV infusion, Folinic acid at 400 mg/m2 given as a 90 min (1.5hr) infusion immediately after Oxaliplatin, and concurrently with Irinotecan (irinotecan at 140mg/m2 given as a 90 min IV infusion) via a Y-connector, Flurouracil at 400 mg/m2 as bolus followed by a 46 hr infusion at 2400mg/m2 starting immediately after completion of folinic acid and Irinotecan.

Group Type EXPERIMENTAL

CPI 613, mFolfirinox

Intervention Type DRUG

CPI-613: 500mg/m2, IV infusion at a rate of 4mL/min via a central venous port. mFolfirinox: given immediately after CPI-613 administration

Folfirinox

Folfirinox

Folfirinox: Oxaliplatin (Eloxatin) at 85 mg/m2 given as a 2 hr IV infusion, Folinic acid at 400 mg/m2 given as a 90 min (1.5hr) infusion immediately after Oxaliplatin, and concurrently with Irinotecan (irinotecan at 180mg/m2 given as a 90 min IV infusion) via a Y-connector, Flurouracil at 400 mg/m2 as bolus followed by a 46 hr infusion at 2400mg/m2 starting immediately after completion of folinic acid and Irinotecan.

Group Type ACTIVE_COMPARATOR

Folfirinox

Intervention Type DRUG

Folfirinox

Interventions

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CPI 613, mFolfirinox

CPI-613: 500mg/m2, IV infusion at a rate of 4mL/min via a central venous port. mFolfirinox: given immediately after CPI-613 administration

Intervention Type DRUG

Folfirinox

Folfirinox

Intervention Type DRUG

Other Intervention Names

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CPI-613,Oxaliplatin, folinic acid, irinotecan, flurouracil Oxaliplatin, folinic acid, irinotecan, flurouracil

Eligibility Criteria

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Inclusion Criteria

1. Histologically or cytologically confirmed metastatic Stage IV adenocarcinoma of the pancreas
2. No prior treatments for stage IV pancreatic adenocarcinoma (prior adjuvant or neoadjuvant treatment is allowed provided completed \> 6 months prior to disease recurrence)
3. Eastern Cooperative Oncology Group (ECOG) performance status 0 - 1
4. Male and female patients 18 - 75 years of age
5. Measurable disease determined using guidelines of Response Evaluation Criteria In Solid Tumors (RECIST version 1.1)
6. Expected survival \>3 months
7. Women of child-bearing potential (i.e., women who are pre-menopausal or not surgically sterile) must use accepted highly effective contraceptive methods (abstinence, intrauterine device \[IUD\], oral contraceptive(s), intrauterine hormone releasing system (IUS), bilateral tubal occlusion or vasectomized partner) during and for 6 months after last study dose and must have a negative serum or urine pregnancy test within 1 week prior to treatment initiation, at monthly interval (day 1 of every even numbered cycle), at the end of systemic exposure, and at 30 days after the systemic exposure
8. Males with female partners (of childbearing potential) and female partners (of child bearing potential) with male partners must agree to use double barrier contraceptive measure (a combination of male condom with either cap, diaphragm or sponge with spermicide) in addition to oral contraception or avoidance of intercourse during the study and for 6 months after last study dose is received
9. At least 2 weeks must have elapsed from any prior surgery with resolution of any sequela for randomization
10. Laboratory values ≤2 weeks prior to randomization must be:

* Adequate hematologic values

* Platelet count ≥100,000 cells/mm3 or ≥100 bil/L;
* Absolute neutrophil count \[ANC\] ≥1,500 cells/mm3 or ≥1.5 bil/L;
* Hemoglobin ≥9 g/dL or ≥90 g/L)
* Adequate hepatic function

* Aspartate aminotransferase \[AST/SGOT\] ≤3x upper normal limit \[UNL\] (≤5x UNL if liver metastases present)
* Alanine aminotransferase \[ALT/SGPT\] ≤3x UNL (≤5x UNL if liver metastases present)
* Bilirubin (≤1.5x UNL); bilirubin ≤ 2.5 x ULN for subjects with Gilbert's syndrome
* Serum albumin \> 3.0 g/dL
* Adequate renal function serum creatinine clearance CLcr \> 30 mL/min). (Cocroft-Gault Formula should be used for CrCl calculation)
* Adequate coagulation function • International Normalized Ratio or INR must be \<1.5 unless on therapeutic blood thinners)
11. No evidence of active infection and no serious infection within the past 30 days.
12. Mentally competent, ability to understand and willingness to sign the informed consent form.

25. Prior malignancy except for the following: adequately treated basal or squamous cell skin cancer, in situ cervical cancer, adequately treated cancer from which the patient has been disease-free for at least 3 years prior to screening
26. Unwilling or unable to avoid the concomitant use of strong CYP3A4 inducers or inhibitors during treatment with irinotecan
27. A marked baseline prolongation of QT/QTc interval (e.g., repeated demonstration of a QTc interval \> 480 milliseconds (ms) (CTCAE grade 1) using Fredericia's QT correction formula (i.e. QTcF)
28. A history of additional risk factors for TdP (e.g., heart failure, hypokalemia, family history of long QT syndrome)
29. The use of concomitant medications that prolong the QT/QTc intervals
30. Contraindications to any of the FFX treatment as follows:

Folinic Acid

* Calcium Folinate is contraindicated in patients who have previously shown hypersensitivity to folinate or any of the excipients.
* Calcium Folinate Injection is contraindicated in the treatment of pernicious anemia or other megaloblastic anemias where vitamin B12 is deficient. Its use can lead to an apparent response of the hematopoietic system, but neurological damage may occur or progress if already present.
* Patients with rare hereditary problems of galactose intolerance, the Lapp lactase deficiency or glucose-galactose malabsorption should not take calcium folinate tablets.

Fluorouracil/5FU

* Fluorouracil is contraindicated in patients who have any known hypersensitivity to fluorouracil, are seriously debilitated or are suffering from bone marrow depression after radiotherapy or treatment with other antineoplastic agents, or who are suffering from a potentially serious infection.
* Fluorouracil is strictly contraindicated in pregnant or breast-feeding women.
* Flourouracil should not be used in the management of non-malignant disease.
* Fluorouracil must not be taken or used concomitantly with brivudin, sorivudine and analogues. Brivudin, sorivudine and analogues are potent inhibitors of the enzyme dihydropyrimidine dehydrogenase (DPD) which degrades fluorouracil
* In patients with known complete absence of dihydropyrimidine dehydrogenase (DPD) activity

Oxaliplatin

* Oxaliplatin is contraindicated in patients who have a known history of hypersensitivity to oxaliplatin or to any of the excipients
* are breast-feeding.
* have myelosuppression prior to starting first course, as evidenced by baseline neutrophils \<2x109/l and/or platelet count of \<100x109l.
* have a peripheral sensitive neuropathy with functional impairment prior to first course.
* have a severely impaired renal function (creatinine clearance less than 30 ml /min)

Irinotecan

* Chronic inflammatory bowel disease and/or bowel obstruction
* History of severe hypersensitivity reactions to Irinotecan hydrochloride trihydrate or to any of the excipients
* Bilirubin \> 3 times the ULN
* Severe bone marrow failure.
* WHO performance status \> 2.
* Concomitant use with St John's wort

Exclusion Criteria

1. Endocrine or acinar pancreatic carcinoma
2. Known cerebral metastases, central nervous system (CNS), or epidural tumor
3. Prior treatment with any chemotherapy for metastatic adenocarcinoma of the pancreas
4. Completion of a gemcitabine-based adjuvant chemotherapy regimen within less than 6 months at the time of screening.
5. Receipt of neoadjuvant or adjuvant FOLFIRINOX therapy if \<6 months prior to disease recurrence
6. Patients with hypersensitivity to devimistat, FFX treatment or any of their excipients
7. Presence of clinically significant abdominal ascites
8. Patients receiving any other standard or investigational treatment for their cancer, or any other investigational agent for any indication within the past 2 weeks prior to initiation of devimistat treatment
9. Serious medical illness that would potentially increase patients' risk for toxicity
10. Any active uncontrolled bleeding, and any patients with a bleeding diathesis (e.g., active peptic ulcer disease)
11. Female patients who are pregnant or breastfeeding or planning to become pregnant or breastfeed during treatment and for an additional 6 months after the last dose of study treatment
12. Female patients of childbearing potential with a positive pregnancy test assessed by a serum pregnancy test at screening
13. Female patients of childbearing potential unwilling to use 1 highly effective method of contraception during treatment and for 6 months after the last dose of study treatment
14. Male patients with a pregnant partner who are unwilling to practice abstinence or use a condom during treatment and for 6 months after completion of study treatment
15. Male patients unwilling to abstain from donating sperm during treatment and for 6 months after completion of study treatment
16. Life expectancy less than 3 months
17. Any condition or abnormality which may, in the opinion of the investigator, compromise the safety of patients
18. Unwilling or unable to follow protocol requirements
19. Active heart disease including but not limited to symptomatic congestive heart failure (NYHA class 3 or 4), symptomatic coronary artery disease, symptomatic angina pectoris, or symptomatic myocardial infarction
20. Patients with a history of myocardial infarction that is \<3 months prior to registration
21. Evidence of active infection, or serious infection within the past 30 days.
22. Patients with known HIV infection
23. Patients who have received cancer immunotherapy of any type within the past 2 weeks prior to initiation of devimistat treatment (steroids given for supportive care or in response to allergic reactions are allowed at any time)
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Cornerstone Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Philip A Philip, MD, PhD, FRCP

Role: PRINCIPAL_INVESTIGATOR

Karmanos Cancer Institute at Wayne State University

Locations

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Banner MD Anderson Cancer Center

Gilbert, Arizona, United States

Site Status

The University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

City of Hope

Duarte, California, United States

Site Status

USC Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

UCLA Medical Center

Los Angeles, California, United States

Site Status

Pacific Hematology Oncology Associates

San Francisco, California, United States

Site Status

Smilow Cancer Hospital at Yale-New Haven

New Haven, Connecticut, United States

Site Status

Georgetown University Medical Center

Washington D.C., District of Columbia, United States

Site Status

Mayo Clinic Hospital

Jacksonville, Florida, United States

Site Status

Mount Sinai Medical Center

Miami Beach, Florida, United States

Site Status

Northwestern Memorial Hospital - Arkes Family Pavilion

Chicago, Illinois, United States

Site Status

University of Chicago

Harvey, Illinois, United States

Site Status

The University of Kansas Cancer Center - Clinical Research Center - Fairway Office Park

Fairway, Kansas, United States

Site Status

University of Massachusetts Memorial Medical Center

Worcester, Massachusetts, United States

Site Status

University of Micihgan

Ann Arbor, Michigan, United States

Site Status

Karmanos cancer Center

Detroit, Michigan, United States

Site Status

Mayo Clinic Cancer Center (MCCC)

Rochester, Minnesota, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Comprehensive Cancer centers of Nevada

Las Vegas, Nevada, United States

Site Status

Englewood Hospital and Medical Center

Englewood, New Jersey, United States

Site Status

Atlantic Health System

Morristown, New Jersey, United States

Site Status

University of New Mexico Cancer Center

Albuquerque, New Mexico, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

New York University Langone Medical Center

New York, New York, United States

Site Status

Stony Brook University Hospital

Stony Brook, New York, United States

Site Status

UNC Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, United States

Site Status

Levine cancer Institute

Charlotte, North Carolina, United States

Site Status

Wake Forest Baptist Health

Winston-Salem, North Carolina, United States

Site Status

University of Cincinnati Cancer Institute

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic - Taussig Cancer Center

Cleveland, Ohio, United States

Site Status

University Hospitals - Seidman Cancer Center

Cleveland, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

University of Pittsburgh-Hillman cancer ceter

Pittsburgh, Pennsylvania, United States

Site Status

Vanderbilt University Medical Center-Vanderbilt-Ingram Cancer Center-Henry-Joyce Cancer Clinic

Nashville, Tennessee, United States

Site Status

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Huntsman cancer Institute

Salt Lake City, Utah, United States

Site Status

University of Virginia Cancer Center - Emily Couric Clinical Cancer Center

Charlottesville, Virginia, United States

Site Status

VCU Massey Cancer Center

Richmond, Virginia, United States

Site Status

Blue Ridge Cancer Care

Roanoke, Virginia, United States

Site Status

Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

Hôpital Erasme

Brussels, Brussels Capital, Belgium

Site Status

UZ Leuven

Leuven, VBR, Belgium

Site Status

CHRU Brest - Hôpital Morvan

Brest, , France

Site Status

Hôpital Beaujon

Clichy, , France

Site Status

Centre Hospitalier Départemental Vendée - Hôpital de la Roche-sur-Yon

La Roche-sur-Yon, , France

Site Status

L'ICM, Institut régional du Cancer de Montpellier

Montpellier, , France

Site Status

CHU de Nantes - Hôpital Nord Laennec

Nantes, , France

Site Status

CHU Hopitaux de Bordeaux - Hôpital Saint-André

Pessac, , France

Site Status

CHU de Poitiers

Poitiers, , France

Site Status

Centre Eugène Marquis

Rennes, , France

Site Status

Institut de Cancérologie de Lorraine

Vandœuvre-lès-Nancy, , France

Site Status

Gustave Roussy Cancer Campus Grand Paris (Institut de Cancerologie Gustave-Roussy)

Villejuif, , France

Site Status

SLK-Kliniken Heilbronn GmbH

Heilbronn, Baden-Wurttemberg, Germany

Site Status

Universitätsklinikum Knappschaftskrankenhaus Bochum GmbH

Bochum, , Germany

Site Status

Universitaetsklinikum Tuebingen

Tübingen, , Germany

Site Status

Hillel Yaffe Medical Center

Hadera, Haifa District, Israel

Site Status

Rambam Medical Center

Haifa, , Israel

Site Status

Shaare Zedek Medical Center

Jerusalem, , Israel

Site Status

Sanz Medical Center - Laniado Hospital

Netanya, , Israel

Site Status

The Chaim Sheba Medical Center - Sheba Cancer Research Center (SCRC)

Ramat Gan, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Assaf-Harofeh Medical Center

Ẕerifin, , Israel

Site Status

The Catholic University of Korea - Seoul St. Mary's Hospital (Kangnam St. Mary's Hospital)

Seocho, Seoul, South Korea

Site Status

Seoul National University Hospital

Busan, , South Korea

Site Status

Kyungpook National University Chilgok Hospital

Daegu, , South Korea

Site Status

Gachon University Gil Hospital

Incheon, , South Korea

Site Status

Inha University Hospital

Incheon, , South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam-si, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Korea University Anam Hospital

Seoul, , South Korea

Site Status

Severance Hospital - Yonsei Cancer Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

National Cancer Center

Seoul, , South Korea

Site Status

Ajou University Hospital

Suwon, , South Korea

Site Status

Countries

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United States Belgium France Germany Israel South Korea

References

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Philip PA, Sahai V, Bahary N, Mahipal A, Kasi A, Rocha Lima CMS, Alistar AT, Oberstein PE, Golan T, Metges JP, Lacy J, Fountzilas C, Lopez CD, Ducreux M, Hammel P, Salem M, Bajor D, Benson AB, Luther S, Pardee T, Van Cutsem E. Devimistat (CPI-613) With Modified Fluorouarcil, Oxaliplatin, Irinotecan, and Leucovorin (FFX) Versus FFX for Patients With Metastatic Adenocarcinoma of the Pancreas: The Phase III AVENGER 500 Study. J Clin Oncol. 2024 Nov;42(31):3692-3701. doi: 10.1200/JCO.23.02659. Epub 2024 Aug 1.

Reference Type DERIVED
PMID: 39088774 (View on PubMed)

Liu N, Yan M, Tao Q, Wu J, Chen J, Chen X, Peng C. Inhibition of TCA cycle improves the anti-PD-1 immunotherapy efficacy in melanoma cells via ATF3-mediated PD-L1 expression and glycolysis. J Immunother Cancer. 2023 Sep;11(9):e007146. doi: 10.1136/jitc-2023-007146.

Reference Type DERIVED
PMID: 37678921 (View on PubMed)

Philip PA, Buyse ME, Alistar AT, Rocha Lima CM, Luther S, Pardee TS, Van Cutsem E. A Phase III open-label trial to evaluate efficacy and safety of CPI-613 plus modified FOLFIRINOX (mFFX) versus FOLFIRINOX (FFX) in patients with metastatic adenocarcinoma of the pancreas. Future Oncol. 2019 Oct;15(28):3189-3196. doi: 10.2217/fon-2019-0209. Epub 2019 Sep 12.

Reference Type DERIVED
PMID: 31512497 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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PANC003

Identifier Type: -

Identifier Source: org_study_id

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