Safety and Efficacy Following Repeat-Dose of Evinacumab (Anti-ANGPTL3) in Patients With Severe Hypertriglyceridemia (sHTG) at Risk for Acute Pancreatitis

NCT ID: NCT03452228

Last Updated: 2023-02-16

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

52 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-06-07

Study Completion Date

2020-07-23

Brief Summary

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The primary objective is to determine the change in Triglyceride (TG) levels following 12 weeks of repeated Intravenous (IV) doses of evinacumab.

Detailed Description

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Conditions

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Severe Hypertriglyceridemia (sHTG)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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evinacumab

Group Type EXPERIMENTAL

evinacumab

Intervention Type DRUG

Administered by Intravenous (IV)

Placebo

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Administered by Intravenous (IV)

Interventions

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evinacumab

Administered by Intravenous (IV)

Intervention Type DRUG

Placebo

Administered by Intravenous (IV)

Intervention Type DRUG

Other Intervention Names

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REGN1500

Eligibility Criteria

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Inclusion Criteria

1. Previous documentation in the patient's medical records of a fasting serum TG measurement ≥ 1000 mg/dL (11.3 mmol/L) on more than 1 occasion, and all fasting TG values ≥500 mg/dL (5.6 mmol/L) at screening
2. History of a hospitalization and diagnosis of acute pancreatitis in the past 10 years
3. On stable lipid-modifying diet with or without medications (eg, statins, niacin, omega-3 fatty acids). Lipid-modifying diet and doses of medications should be stable for at least 4 weeks (6 weeks for fibrates, 8 weeks for PCSK9 inhibitors) prior to screening
4. Body mass index (BMI) of 18-40 kg/m2

Exclusion Criteria

1. A hospital or clinic discharge diagnosis of acute pancreatitis within 12 weeks of screening
2. Lipid apheresis or plasma exchange treatment within the last 4 weeks or plans to undergo apheresis or plasma exchange during the time frame of the study
3. History of class 3/4 heart failure at any time in the past, or hospitalization for heart failure, diagnosis of a myocardial infarction, stroke, Transient ischemic attack (TIA), unstable angina, Coronary artery bypass surgery (CABG), Percutaneous coronary intervention (PCI), carotid surgery/stenting within 3 months before the screening visit
4. History of bleeding disorders, esophageal varices, heparin induced thrombocytopenia, or contraindications to receiving heparin (eg, allergic reaction to heparin)
5. Previous treatment with Glybera® in the past 5 years or treatment with lomitapide or mipomersen in the past 6 months
6. Pregnant or breast feeding women
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Regeneron Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trial Management

Role: STUDY_DIRECTOR

Regeneron Pharmaceuticals

Locations

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Regeneron Research Facility

Boca Raton, Florida, United States

Site Status

Regeneron Research Facility

Atlanta, Georgia, United States

Site Status

Regeneron Research Facility

Kansas City, Kansas, United States

Site Status

Regeneron Research Facility

New York, New York, United States

Site Status

Regeneron Research Facility

Philadelphia, Pennsylvania, United States

Site Status

Regeneron Research Facility

Pittsburgh, Pennsylvania, United States

Site Status

Regeneron Research Facility

Dallas, Texas, United States

Site Status

Regeneron Research Facility

Houston, Texas, United States

Site Status

Regeneron Research Facility

Milwaukee, Wisconsin, United States

Site Status

Regeneron Research Facility

Chicoutimi, Quebec, Canada

Site Status

Regeneron Research Facility

Québec, Quebec, Canada

Site Status

Regeneron Research Facility

Napoli, Campania, Italy

Site Status

Regeneron Research Facility

Rome, , Italy

Site Status

Regeneron Research Facility

Birmingham, , United Kingdom

Site Status

Regeneron Research Facility

London, , United Kingdom

Site Status

Regeneron Research Facility

London, , United Kingdom

Site Status

Regeneron Research Facility

Manchester, , United Kingdom

Site Status

Countries

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United States Canada Italy United Kingdom

References

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Rosenson RS, Gaudet D, Ballantyne CM, Baum SJ, Bergeron J, Kershaw EE, Moriarty PM, Rubba P, Whitcomb DC, Banerjee P, Gewitz A, Gonzaga-Jauregui C, McGinniss J, Ponda MP, Pordy R, Zhao J, Rader DJ. Evinacumab in severe hypertriglyceridemia with or without lipoprotein lipase pathway mutations: a phase 2 randomized trial. Nat Med. 2023 Mar;29(3):729-737. doi: 10.1038/s41591-023-02222-w. Epub 2023 Mar 6.

Reference Type DERIVED
PMID: 36879129 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-003307-62

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

R1500-HTG-1522

Identifier Type: -

Identifier Source: org_study_id

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