Brief Title: Study of Efficacy and Safety of Canakinumab as Adjuvant Therapy in Adult Subjects With Stages AJCC/UICC v. 8 II-IIIA and IIIB (T>5cm N2) Completely Resected Non-small Cell Lung Cancer Acronym: CANOPY-A

NCT ID: NCT03447769

Last Updated: 2024-10-09

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

1382 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-03-16

Study Completion Date

2023-02-07

Brief Summary

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The primary purpose of the study was to compare the efficacy and safety of canakinumab versus placebo as adjuvant therapy in adult subjects with stages II -IIIA according to the 8th edition of the American Joint Committee on Cancer (AJCC)/Union for International Cancer Control (UICC) and the subset of IIIB (T\>5cm N2 disease) completely resected (R0) non-small cell lung cancer (NSCLC).

Detailed Description

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This was a phase III, multicenter, randomized, double-blind study to evaluate the efficacy and safety of canakinumab as adjuvant therapy in adult patients with stages AJCC/UICC v.8 II-IIIA and IIIB (T\>5 cm N2) completely resected (R0) NSCLC.

Approximately 1500 patients were planned to be randomized 1:1 to canakinumab, 200 mg subcutaneously (s.c.) every 3 weeks or matching placebo s.c. every 3 weeks. Patients were planned to continue their assigned treatment until they completed 18 cycles (cycle= 21 days) or experienced any one of the following: non-small cell lung cancer (NSCLC) disease recurrence as determined by Investigator; unacceptable toxicity that precluded further treatment; treatment discontinuation at the discretion of the Investigator or patient; start of a new antineoplastic therapy; death, or loss to follow-up, whichever occurred first. All patients who discontinued from the study treatment were to be followed up every 12 weeks for survival until the final OS analysis or death, loss to follow-up or withdrawal of consent for survival follow-up.

Conditions

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Non-Small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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canakinumab

Participants received 200mg of canakinumab subcutaneously every 3 weeks for up to 18 cycles (approximately 54 weeks)

Group Type EXPERIMENTAL

Canakinumab

Intervention Type DRUG

200 mg of canakinumab administered subcutaneously on day 1 of every 21-day cycle for 18 cycles. Canakinumab solution for injection was provided by Novartis as ready-to-use pre-filled syringes to be administered by study personnel.

Placebo

Participants received canakinumab placebo subcutaneously every 3 weeks for up to 18 cycles (approximately 54 weeks)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered subcutaneously on day 1 of every 21-day cycle for 18 cycles. Placebo solution for injection was provided by Novartis as ready-to-use pre-filled syringes to be administered by study personnel.

Interventions

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Canakinumab

200 mg of canakinumab administered subcutaneously on day 1 of every 21-day cycle for 18 cycles. Canakinumab solution for injection was provided by Novartis as ready-to-use pre-filled syringes to be administered by study personnel.

Intervention Type DRUG

Placebo

Placebo administered subcutaneously on day 1 of every 21-day cycle for 18 cycles. Placebo solution for injection was provided by Novartis as ready-to-use pre-filled syringes to be administered by study personnel.

Intervention Type DRUG

Other Intervention Names

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ACZ885

Eligibility Criteria

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Inclusion Criteria

* Had completely resected (R0) NSCLC AJCC/UICC v. 8 stage IIA-IIIA and IIIB (N2 disease only) OR had NSCLC Stage IIA-IIIA, IIIB (N2 disease only) and were candidates for complete resection surgery.
* Cisplatin-based chemotherapy was mandatory for all subjects (Exception: In subjects with stage IIA disease with no nodal involvement, cisplatin-based chemotherapy could be administered if recommended by the treating physician). When required, a minimum of two cycles of cisplatin-based chemotherapy was mandatory, after which additional therapies could be given based upon local clinical practice and/or guidelines. Typically, chemotherapy was initiated within 60 days of surgery.
* Radiation therapy was allowed if indicated as per local guidelines or practice.
* Had recovered from all toxicities related to prior systemic therapy to grade ≤ 1 (CTCAE v 5.0). Exception to this criterion: subjects with any grade of alopecia and grade 2 or less neuropathy were allowed to enter the study
* Had ECOG performance status (PS) of 0 or 1

Exclusion Criteria

* Had unresectable or metastatic disease, positive microscopic margins on the pathology report, and/or gross disease remaining at the time of surgery
* Had received any neoadjuvant therapy
* Had presence or history of a malignant disease, other than the resected NSCLC, that had been diagnosed and/or required therapy within the past 3 years Exceptions to this exclusion included the following: completely resected basal cell and squamous cell skin cancers, completely resected carcinoma in situ of any type and hormonal maintenance for breast and prostate cancer \> 3 years.
* Had a history of current diagnosis of cardiac disease
* Had uncontrolled diabetes
* Had known active or recurrent hepatic disorder including cirrhosis, hepatitis B and C (positive or indeterminate central laboratory results)
* Subjects had to be evaluated for tuberculosis as per local treatment guidelines or clinical practice. Subjects with active tuberculosis were not eligible.
* Had suspected or proven immunocompromised state as described in the protocol
* Had live and attenuated vaccination within 3 months prior to first dose of study drug (e.g. MMR, Yellow Fever, Rotavirus, Smallpox, etc.).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Highlands Oncology Group .

Fayetteville, Arkansas, United States

Site Status

Cancer and Blood Specialty Clinic

Los Alamitos, California, United States

Site Status

University of California at Los Angeles

Los Angeles, California, United States

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VA Palo Alto Health Care System CRLX030A2301

Palo Alto, California, United States

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Sansum Clinic

Santa Barbara, California, United States

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Rocky Mountain Cancer Centers Denver-Mdtn(Bone&MarrowTransp)

Longmont, Colorado, United States

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Florida Cancer Specialists

Fort Myers, Florida, United States

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Advanced Medical Specialties Drug Ship - 2

Miami, Florida, United States

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Florida Cancer Affiliates of Ocala

Ocala, Florida, United States

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Florida Cancer Specialists North

St. Petersburg, Florida, United States

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Florida Cancer Specialists

West Palm Beach, Florida, United States

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Rush University Medical Center Regulatory

Chicago, Illinois, United States

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Cancer Center of Kansas Dept.ofCancerCtr.ofKansas

Wichita, Kansas, United States

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VA Nebraska-W IA Health Care System .

Omaha, Nebraska, United States

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Louis Stokes Cleveland Department of Veterans Affairs MC .

Cleveland, Ohio, United States

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Oncology Associates of Oregon, PC

Eugene, Oregon, United States

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Chattanooga Oncology and Hematology Associates PC Chattanooga Oncology

Chattanooga, Tennessee, United States

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Sarah Cannon Research Institute

Nashville, Tennessee, United States

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Texas Oncology MamieMcFaddenWardCtr

Dallas, Texas, United States

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Virginia Cancer Specialists Fairfax Northern Virginia

Fairfax, Virginia, United States

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Oncology and Hematology Associates of Southwest Virginia Inc .

Salem, Virginia, United States

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Novartis Investigative Site

CABA, Buenos Aires, Argentina

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Mar del Plata, Buenos Aires, Argentina

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Rosario, Santa Fe Province, Argentina

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Rosario, Sante Fe, Argentina

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Córdoba, , Argentina

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Graz, , Austria

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Klagenfurt, , Austria

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Krems, , Austria

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Vienna, , Austria

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Londrina, Paraná, Brazil

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Teresina, Piauí, Brazil

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Barretos, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Edmonton, Alberta, Canada

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Moncton, New Brunswick, Canada

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Halifax, Nova Scotia, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Santiago, , Chile

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Hefei, Anhui, China

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Beijing, Beijing Municipality, China

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Ostrava Vitkovice, , Czechia

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Prague, , Czechia

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Marseille, Bouches Du Rhone, France

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Le Mans, Cedex 09, France

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Heidelberg, Baden-Wurttemberg, Germany

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Gauting, Bavaria, Germany

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Georgsmarienhütte, , Germany

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Gerlingen, , Germany

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Großhansdorf, , Germany

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Halle, , Germany

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Leipzig, , Germany

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Nuremberg, , Germany

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Solingen, , Germany

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Ulm, , Germany

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Würzburg, , Germany

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Athens, Attica, Greece

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Athens, GR, Greece

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Thessaloniki, , Greece

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Hong Kong, , Hong Kong

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Kowloon, , Hong Kong

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Tuenmen, , Hong Kong

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Törökbálint, Pest County, Hungary

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Veszprém, , Hungary

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Reykjavik, , Iceland

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Mumbai, Maharashtra, India

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Nashik, Maharashtra, India

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Kolkata, West Bengal, India

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Delhi, , India

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Haifa, , Israel

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Holon, , Israel

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Ancona, AN, Italy

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Bari, BA, Italy

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Meldola, FC, Italy

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Monza, MB, Italy

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Milan, MI, Italy

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Milan, MI, Italy

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Padua, PD, Italy

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Perugia, PG, Italy

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Aviano, PN, Italy

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Ravenna, RA, Italy

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Roma, RM, Italy

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Orbassano, TO, Italy

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Nagoya, Aichi-ken, Japan

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Nagoya, Aichi-ken, Japan

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Hirosaki, Aomori, Japan

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Matsuyama, Ehime, Japan

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Iizuka, Fukuoka, Japan

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Asahikawa, Hokkaido, Japan

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Sapporo, Hokkaido, Japan

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Himeji, Hyōgo, Japan

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Kanazawa, Ishikawa-ken, Japan

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Shiwa-gun, Iwate, Japan

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Yokohama, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Natori-shi, Miyagi, Japan

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Hirakata, Osaka, Japan

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Osaka, Osaka, Japan

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Sakai, Osaka, Japan

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Hidaka, Saitama, Japan

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Sunto Gun, Shizuoka, Japan

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Bunkyo Ku, Tokyo, Japan

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Chuo Ku, Tokyo, Japan

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Minato Ku, Tokyo, Japan

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Ube, Yamaguchi, Japan

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Fukuoka, , Japan

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Osaka, , Japan

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Wakayama, , Japan

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Amman, , Jordan

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Beirut, , Lebanon

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El Achrafiyé, , Lebanon

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Saida, , Lebanon

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Tripoli, , Lebanon

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Kuching, Sarawak, Malaysia

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Kuala Lumpur, , Malaysia

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Pulau Pinang, , Malaysia

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Bergen, , Norway

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Drammen, , Norway

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Oslo, , Norway

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Tromsø, , Norway

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Panama City, , Panama

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San Borja, Lima region, Peru

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Surquillo, Lima region, Peru

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Makati City, , Philippines

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Krakow, Ma3opolska, Poland

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Konin, , Poland

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Olsztyn, , Poland

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Poznan, , Poland

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Rzeszów, , Poland

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Warsaw, , Poland

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Lisbon, , Portugal

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Matosinhos Municipality, , Portugal

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Porto, , Portugal

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Floreşti, Cluj, Romania

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Cluj-Napoca, , Romania

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Arkhangelsk, , Russia

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Kaliningrad, , Russia

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Moscow Region Istra Village, , Russia

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Obninsk, , Russia

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Pushkin Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Yaroslavl, , Russia

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Ljubljana, , Slovenia

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Jeollanam-do, Korea, South Korea

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Seoul, Korea, South Korea

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Cheongju-si, North Chungcheong, South Korea

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Busan, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Córdoba, Andalusia, Spain

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Seville, Andalusia, Spain

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Santander, Cantabria, Spain

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Badalona, Catalonia, Spain

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L'Hospitalet de Llobregat, Catalonia, Spain

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Santiago de Compostela, Galicia, Spain

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San Cristóbal de La Laguna, Santa Cruz De Tenerife, Spain

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Valencia, Valencia, Spain

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Madrid, , Spain

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Madrid, , Spain

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Bern, , Switzerland

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Taichung, Taiwan ROC, Taiwan

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Changhua, , Taiwan

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Hualien City, , Taiwan

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Kaohsiung City, , Taiwan

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Kaohsiung City, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Songkhla, Hat Yai, Thailand

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Khon Kaen, THA, Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chaingmai, , Thailand

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Pendik Istanbul, Turkey, Turkey (Türkiye)

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Ankara, Yenimahalle, Turkey (Türkiye)

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Adana, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Cambridge, Cambrigdeshire, United Kingdom

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Truro, Cornwall, United Kingdom

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Cheltenham, Gloucestershire, United Kingdom

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Metropolitan Borough of Wirral, Merseyside, United Kingdom

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Ipswich, Suffolk, United Kingdom

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Guildford, Surrey, United Kingdom

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Birmingham, , United Kingdom

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Bristol, , United Kingdom

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Leicester, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Nottingham, , United Kingdom

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Oxford, , United Kingdom

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Preston, , United Kingdom

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Stoke-on-Trent, , United Kingdom

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Hanoi, , Vietnam

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Countries

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United States Argentina Austria Brazil Bulgaria Canada Chile China Colombia Czechia France Georgia Germany Greece Hong Kong Hungary Iceland India Israel Italy Japan Jordan Lebanon Malaysia Norway Panama Peru Philippines Poland Portugal Romania Russia Slovenia South Korea Spain Switzerland Taiwan Thailand Turkey (Türkiye) United Kingdom Vietnam

References

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Garon EB, Lu S, Goto Y, De Marchi P, Paz-Ares L, Spigel DR, Thomas M, Yang JC, Ardizzoni A, Barlesi F, Orlov S, Yoshioka H, Mountzios G, Khanna S, Bossen C, Carbini M, Turri S, Myers A, Cho BC. Canakinumab as Adjuvant Therapy in Patients With Completely Resected Non-Small-Cell Lung Cancer: Results From the CANOPY-A Double-Blind, Randomized Clinical Trial. J Clin Oncol. 2024 Jan 10;42(2):180-191. doi: 10.1200/JCO.23.00910. Epub 2023 Oct 3.

Reference Type DERIVED
PMID: 37788412 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://www.novctrd.com/ctrdweb/patientsummary/patientsummaries?patientSummaryId=1875

A Plain Language Trial Summary is available on www.novctrd.com

Other Identifiers

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2017-004011-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CACZ885T2301

Identifier Type: -

Identifier Source: org_study_id

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