ASA404 or Placebo in Combination With Paclitaxel and Carboplatin as First-Line Treatment for Stage IIIb/IV Non-Small Cell Lung Cancer

NCT ID: NCT00662597

Last Updated: 2020-12-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

1285 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-04-30

Study Completion Date

2010-05-31

Brief Summary

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The purpose of this study is to determine if adding ASA404 to standard chemotherapy makes the cancer treatment more effective in patients with advanced lung cancer.

Detailed Description

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Conditions

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Non-Small Cell Lung Cancer

Keywords

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Tumor vascular disrupting agent VDA ASA404 non-small cell lung cancer NSCLC

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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ASA404

Group Type EXPERIMENTAL

ASA404

Intervention Type DRUG

carboplatin

Intervention Type DRUG

Paclitaxel

Intervention Type DRUG

ASA40 Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

carboplatin

Intervention Type DRUG

Paclitaxel

Intervention Type DRUG

Interventions

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ASA404

Intervention Type DRUG

Placebo

Intervention Type DRUG

carboplatin

Intervention Type DRUG

Paclitaxel

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Histologically confirmed non-small cell carcinoma of the lung. (Histological or cytological specimens must be collected via surgical biopsy, brushing, washing or core needle aspiration of a defined lesion. Sputum cytology is not acceptable.)
2. Newly diagnosed Stage IIIb disease (malignant pleural effusion or pericardial effusion that have been confirmed cytologically) or Stage IV disease
3. No prior systemic antineoplastic treatment for Stage IIIb/IV non-small cell carcinoma of the lung (Prior neoadjuvant or adjuvant chemotherapy for earlier stage I/II NSCLC is allowed if 12 months or more prior to Baseline visit.)
4. Age ≥ 18 years old
5. WHO Performance Status of 0-1
6. Measurable or non-measurable disease per RECIST criteria (Post-text supplement 1)
7. Lab values within the range, as defined below, within 2 weeks of randomization:

* Absolute neutrophils count (ANC) \> 2.0 x 109/L
* Platelets ≥ 100 x109/L
* Hemoglobin ≥ 10 g/dL
* Serum creatinine ≤ 1.5 x ULN (≤ 120 micro mol/L)
* Serum bilirubin ≤ 1.5 x ULN (≤ 25 micro mol/L)
* Aspartate transaminase (AST) and alanine transaminase (ALT) ≤ 2.5 x ULN (≤ 5 x ULN if liver metastases)
* International Normalized Ratio (INR) or Prothrombin Time (PT) ≤ 1.5 x IULN (Sections 6.9.1 and 7.3.4.2)
* Electrolyte values (potassium, calcium, magnesium) within \> 1 x LLN and \< 1 x ULN. Patients with corrected electrolyte values are eligible. See Sections 6.8.1 and 7.3.4.3.
* Females of child-bearing potential must have negative serum pregnancy test (confirmation of negative urine pregnancy test within 72 hours prior to initial dosing).
8. Life expectancy ≥ 12 weeks
9. Written informed consent obtained according to local guidelines

Exclusion Criteria

1. Patients having CNS metastases (Patients having any clinical signs of CNS metastases must have a CT or MRI of the brain performed to rule out CNS metastases in order to be eligible for study participation. Patients who have had brain metastases surgically removed or irradiated with no residual disease confirmed by imaging are allowed.).
2. Patients with a history of another primary malignancy ≤ 5 years, with the exception of non-melanoma skin cancer or cervical cancer in situ.
3. Radiotherapy ≤ 2 weeks prior to randomization. Patients must have recovered from all radiotherapy-related toxicities.
5. Concurrent use of other investigational agents and patients who have received investigational agents ≤ 4 weeks prior to randomization
6. Prior exposure to Tumor-VDAs or other vascular targeting agents (anti-VEGF, anti-VEGF receptor agents, anti-EGFR agents \[bevacizumab, cetuximab, etc.\])
7. Pleural effusion that causes ≥ CTC grade 2 dyspnea
8. Patients with systolic BP \> 160 mm Hg and/or diastolic BP \>90 mm Hg
9. Patients with recent hemoptysis associated with NSCLC (\> 1 teaspoon in a single episode within 4 weeks)
10. Patients with any one of the following:

* Patients with long QT syndrome
* Patients with a Baseline 12-lead ECG QTc of \> 450 msec per central evaluation
* Congestive heart failure (NY Heart Association class III or IV)
* Patients with a myocardial infarction within 12 months of study entry
* Unstable or poorly controlled angina pectoris, including Prinzmetal variant angina pectoris
* History of labile hypertension or poor compliance with anti-hypertensive regimen
* History of a sustained ventricular tachycardia
* Any history of ventricular fibrillation or Torsades de Pointes
* Right bundle branch block and left anterior hemiblock (bifasicular block)
* Bradycardia defined as heart rate \< 50 beats per minute
11. Concomitant use of drugs with a risk of causing Torsades de Pointes (See Table 6-3)
12. Known allergy or hypersensitivity to platinum-containing drugs, taxanes, other drugs formulated in Cremophor EL (polyoxyethylated castor oil) or any known excipients of these drugs.
13. Peripheral sensory neuropathy with functional impairment (CTC grade 2 neuropathy, regardless of causality)
14. Pregnant or breast feeding females

• Pregnant or nursing (lactating) women, where pregnancy is defined as the state of a female after conception and until the termination of gestation, confirmed by a positive hCG laboratory test (\> 5 mIU/ml)
15. Women of child bearing potential or sexually active males, unwilling or unable to use the required highly effective method(s) of contraception for both sexes while receiving treatment and for at least 6 months after the discontinuation of study treatment. (Adequate forms of contraception include IUD, oral or depot contraceptive or the barrier method plus spermicide.)

• Oral, implantable, or injectable contraceptives may be affected by cytochrome P450 interactions while taking paclitaxel and therefore are not considered effective contraceptive methods for this study when used as a single agent. Therefore, it is highly recommended that a concomitant barrier method be used with oral, implantable, or injectable contraceptives. The investigator shall counsel the patient accordingly. Women of childbearing potential must have a negative pregnancy test (serum or urine) 72 hours prior to administration of study treatment. For a list of substrates of human liver microsomal P450 enzymes, visit website (http://medicine.iupui.edu/flockhart/)
16. Concurrent severe and/or uncontrolled medical disease (i.e. uncontrolled diabetes, chronic renal disease, chronic liver disease, confirmed diagnosis of HIV infection or active uncontrolled infection).
17. Significant neurologic or psychiatric disorder which could compromise participation in the study Patient unwilling or unable to comply with the protocol
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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University of South Alabama/Mitchell Cancer Institute

Mobile, Alabama, United States

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Arizona Oncology Associates

Tucson, Arizona, United States

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University of Arizona Cancer Center

Tucson, Arizona, United States

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Highlands Oncology Group

Bentonville, Arkansas, United States

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Genesis Cancer Center

Hot Springs, Arkansas, United States

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Alta Bates Summit Medical Center

Berkeley, California, United States

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Pacific Oncology and Hematology Association

Encinitas, California, United States

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Cancer Care Associates

Fresno, California, United States

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Ronald Yanagihara - Private Practice

Gilroy, California, United States

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California Cancer Care

Greenbrae, California, United States

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Moores UCSD Cancer Center

La Jolla, California, United States

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Loma Linda University Cancer Center

Loma Linda, California, United States

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Cedars Sinai Medical Center

Los Angeles, California, United States

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University of California Irvine Comprhensive Center

Orange, California, United States

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Loma Linda Oncology Medical Group, Inc.

Redlands, California, United States

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UC Davis Comprehensive Cancer Center

Sacramento, California, United States

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California Pacific Medical Research Institute

San Francisco, California, United States

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Redwood Regional Cancer Center

Santa Rosa, California, United States

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Georgetown University Hospital

Washington D.C., District of Columbia, United States

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Palm Beach Institute of Hematology & Oncology

Boynton Beach, Florida, United States

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Florida Cancer Specialists

Bradenton, Florida, United States

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Cancer Centers of Central Florida, PA

Leesburg, Florida, United States

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Advanced Medical Specialties (ACORN)

Miami, Florida, United States

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Northwest Georgia Oncology Centers

Marietta, Georgia, United States

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Cancer Research Center of Hawaii

Honolulu, Hawaii, United States

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Kootenai Cancer Center (ACORN)

Coeur d'Alene, Idaho, United States

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Advocate Illinois Masonic Medical Center

Chicago, Illinois, United States

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Illinois Oncology/Warren Billhartz Cancer Ctr.

Maryville, Illinois, United States

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Loyola University Medical Center

Maywood, Illinois, United States

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Hematology/Oncology of North Shore

Skokie, Illinois, United States

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Loyola Cancer Care & Research Ctr. at Central Dupage Hospital

Winfield, Illinois, United States

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Ft. Wayne Oncology and Hematology

Fort Wayne, Indiana, United States

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Siouxland Hematology-Oncology Assoc., LLC

Sioux City, Iowa, United States

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Kansas City Cancer Center, Southwest

Overland Park, Kansas, United States

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University of Louisville - James Graham Brown Cancer Center

Louisville, Kentucky, United States

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Hematology Oncology Specialists

Metairie, Louisiana, United States

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Louisiana State University Health Sciences Center - Feist-Weiller Cancer Center

Shreveport, Louisiana, United States

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St. Agnes Cancer Center

Baltimore, Maryland, United States

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Sinai Hospital of Baltimore - The Alvin & Lois Lapidus Cancer Institute

Baltimore, Maryland, United States

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The Harry and Jeanette Weinberg Cancer Institute at Franklin Square/MedStar Health

Baltimore, Maryland, United States

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Peninsula Regional Oncology and Hematology

Salisbury, Maryland, United States

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Boston VA Healthcare System

Boston, Massachusetts, United States

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Fallon Clinic

Worcester, Massachusetts, United States

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Breslin Cancer Center

Lansing, Michigan, United States

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Osteopathic Medical Oncology and Hematology PC

Woodhaven, Michigan, United States

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St. Luke's Hospital - St Luke's Cancer Center

Duluth, Minnesota, United States

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Kansas City Veterans Affair Medical Center

Kansas City, Missouri, United States

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St. Louis University Cancer Center

St Louis, Missouri, United States

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Center for Cancer Care and Research (US Oncology)

St Louis, Missouri, United States

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St. John's Mercy Medical Center

St Louis, Missouri, United States

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St. Louis Cancer and Breast Institute

St Louis, Missouri, United States

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Billings Clinic

Billings, Montana, United States

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Sletten Cancer Institute

Great Falls, Montana, United States

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University of Nebraska Medical Center

Omaha, Nebraska, United States

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Arena Oncology Associates

Lake Success, New York, United States

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New York Oncology Hematology

Latham, New York, United States

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Hematology Oncology Associates of Rockland

Nyack, New York, United States

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Rochester General Hospital - Lipson Cancer Center

Rochester, New York, United States

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Syracuse VA Medical Center

Syracuse, New York, United States

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Eastchester Center for Cancer Care

The Bronx, New York, United States

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Alamance Regional Medical Center-Cancer Ctr.

Burlington, North Carolina, United States

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Carolina Cancer Mgmt/Cape Fear Valley Health System/Med Onc

Fayetteville, North Carolina, United States

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Akron City Hospital

Akron, Ohio, United States

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Oncology Hematology Care Research

Cincinnati, Ohio, United States

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University Hospitals of Cleveland

Cleveland, Ohio, United States

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Medical Oncology Hematology Associates, Inc. - Dayton Clinical Oncology Program

Dayton, Ohio, United States

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Medical Oncology Hematology Associates, Inc.

Dayton, Ohio, United States

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Cleo Craig Memorial Cancer Ctr. & Research Clinic

Lawton, Oklahoma, United States

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University of Oklahoma Health Science Center

Oklahoma City, Oklahoma, United States

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Kaiser Permanente, Northwest Region

Portland, Oregon, United States

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Allegheny General Hospital/Allegheny Cancer Center

Pittsburgh, Pennsylvania, United States

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South Carolina Oncology Associate

Columbia, South Carolina, United States

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Lowcountry Hematology & Oncology PA

Mt. Pleasant, South Carolina, United States

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Chattanooga Oncology Hematology Associates

Chattanooga, Tennessee, United States

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The West Clinic

Memphis, Tennessee, United States

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Tennessee Oncology

Nashville, Tennessee, United States

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Texas Oncology Cancer Center of the High Plains

Amarillo, Texas, United States

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Arlington Cancer Center

Arlington, Texas, United States

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Patient's Comprehensive Cancer Center

Carrollton, Texas, United States

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South Texas Cancer Institute

Corpus Christi, Texas, United States

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Cancer Care Centers of South Texas

Dallas, Texas, United States

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Texas Oncology at Presbyterian Hospital

Dallas, Texas, United States

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University of Texas Southwestern Medical Center/Simmons Comprehensive Cancer Center

Dallas, Texas, United States

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Texas Oncology at Garland

Garland, Texas, United States

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HOPE Oncology

Richardson, Texas, United States

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Tyler Cancer Center

Tyler, Texas, United States

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UT Health Center

Tyler, Texas, United States

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Deke Slayton Cancer Center

Webster, Texas, United States

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Texoma Cancer Center

Wichita Falls, Texas, United States

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Northern Utah Associates

Ogden, Utah, United States

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Danville Hematology & Oncology

Danville, Virginia, United States

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Medical Oncology & Hematology Associates of Northern Virginia

Fairfax, Virginia, United States

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Virginia Oncology Associates

Norfolk, Virginia, United States

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Virginia Cancer Institute

Richmond, Virginia, United States

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Highline Medical Oncology

Burien, Washington, United States

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Providence Everett Medical Center/Providence regional Cancer Partnership

Everett, Washington, United States

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Northwest Cancer Specialists

Vancouver, Washington, United States

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University of Wisconsin

Madison, Wisconsin, United States

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Medical Consultants

Milwaukee, Wisconsin, United States

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Medical College of Wisconsin/Division of Neoplastic & Related Disorders

Milwaukee, Wisconsin, United States

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Novartis Investigative Site

Buenos Aires, , Argentina

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Capital Federal, , Argentina

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Córdoba, , Argentina

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La Plata, , Argentina

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Mendoza, , Argentina

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Rosario, , Argentina

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Heidelberg, , Australia

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Herston, , Australia

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South Brisbane, , Australia

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Duffel, , Belgium

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Jette, , Belgium

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Liège, , Belgium

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Barretos, , Brazil

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Belo Horizonte, , Brazil

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Goiânia, , Brazil

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Jaù, , Brazil

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Jaú, , Brazil

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Porto Alegre, , Brazil

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Santo André, , Brazil

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São Paulo, , Brazil

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Calgary, , Canada

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Greenfield Park, , Canada

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Kitchener, , Canada

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London, , Canada

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Moncton, , Canada

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Montreal, , Canada

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Rimouski, , Canada

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Sainte-Foy, , Canada

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Sherbrooke, , Canada

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Sult Ste-Marie, , Canada

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Beijing, , China

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Guangzhou, , China

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Shanghai, , China

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Wuhan, , China

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Xi'an, , China

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Brno, , Czechia

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Ostrava Poruba, , Czechia

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Prague, , Czechia

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Bobigny, , France

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Boujan-sur-Libron, , France

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Clamart, , France

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Le Mans, , France

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Limoges, , France

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Lyon, , France

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Marseille, , France

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Nice, , France

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Paris, , France

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Saint-Herblain, , France

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Toulon Armées, , France

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Tours, , France

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Aschaffenburg, , Germany

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Bad Berka, , Germany

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Berlin, , Germany

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Cologne, , Germany

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Donaustauf, , Germany

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Ebensberg, , Germany

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Essen, , Germany

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Freiburg im Breisgau, , Germany

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Gerlingen, , Germany

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Göttingen, , Germany

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Grosshandsdorf, , Germany

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Heidenheim, , Germany

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Leipzig, , Germany

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Merseburg, , Germany

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München, , Germany

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Nuremberg, , Germany

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Athens, , Greece

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Heraklion Crete, , Greece

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Thessaloniki, , Greece

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Hong Kong, , Hong Kong

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Budapest, , Hungary

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Deszk, , Hungary

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Mátraháza, , Hungary

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Kfar Saba, , Israel

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Rehovot, , Israel

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Tel Aviv, , Israel

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Tel Litwinsky, , Israel

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Zrifin, , Israel

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Avellino, , Italy

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Milan, , Italy

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Modena, , Italy

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Napoli, , Italy

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Orbassano, , Italy

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Parma, , Italy

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Perugia, , Italy

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Roma, , Italy

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Akashi, , Japan

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Fukuoka, , Japan

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Habikino, , Japan

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Hiroshima, , Japan

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Kashiwa, , Japan

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Kobe, , Japan

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Kōtō City, , Japan

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Kumamoto, , Japan

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Kurashiki, , Japan

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Matsuyama, , Japan

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Nagoya, , Japan

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Niigata, , Japan

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Okayama, , Japan

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Osaka, , Japan

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Ōsaka-sayama, , Japan

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Sapporo, , Japan

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Sendai, , Japan

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Ube, , Japan

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Yokohama, , Japan

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's-Hertogenbosch, , Netherlands

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Amsterdam, , Netherlands

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Breda, , Netherlands

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Eindhoven, , Netherlands

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Harderwijk, , Netherlands

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Zwolle, , Netherlands

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Auckland, , New Zealand

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Christchurch, , New Zealand

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Hamilton, , New Zealand

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Wellington, , New Zealand

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Lodz, , Poland

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Lublin, , Poland

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Otwock, , Poland

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Poznan, , Poland

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Singapore, , Singapore

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Seoul, , South Korea

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Seungnam, , South Korea

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Suwon, , South Korea

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Barakaldo, , Spain

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Barcelona, , Spain

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Córdoba, , Spain

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Granada, , Spain

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Jaén, , Spain

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Madrid, , Spain

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Pontevedra, , Spain

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Seville, , Spain

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Zaragoza, , Spain

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Umeå, , Sweden

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Kaoshiung, , Taiwan

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Lin-Ko, , Taiwan

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Taichung, , Taiwan

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Tainan City, , Taiwan

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Taipei, , Taiwan

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Altunizade, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Aberdeen, , United Kingdom

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Cambridge, , United Kingdom

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Leicester, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Sutton, , United Kingdom

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Countries

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United States Argentina Australia Belgium Brazil Canada China Czechia France Germany Greece Hong Kong Hungary Israel Italy Japan Netherlands New Zealand Poland Singapore South Korea Spain Sweden Taiwan Turkey (Türkiye) United Kingdom

Related Links

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https://www.novctrd.com/ctrdweb/trialresult/trialresults/pdf?trialResultId=4609

Results for CASA404A2301 from the Novartis Clinical Trials website

Other Identifiers

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CASA404A2301

Identifier Type: -

Identifier Source: org_study_id