A Study of ASA404 or Placebo in Combination With Docetaxel in Second-line Treatment for (Stage IIIb/IV) Non-small Cell Lung Cancer

NCT ID: NCT00738387

Last Updated: 2020-12-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

900 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-12-31

Brief Summary

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The purpose of this study is to determine if adding ASA404 to docetaxel chemotherapy makes the cancer treatment more effective in patients with locally advanced or metastatic non-small cell lung cancer

Detailed Description

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Conditions

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Non-Small Cell Lung Cancer

Keywords

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Tumor vascular disrupting agent VDA ASA404 non-small cell lung cancer NSCLC

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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ASA404 + docetaxel

1800 mg/m2 of ASA404 intravenous (IV) on day 1 of each 21 day cycle

75 mg/m2 of docetaxel intravenous (IV) an hour for 1st 6 cycles; cycle: every 21 days

Group Type EXPERIMENTAL

ASA404

Intervention Type DRUG

1800 mg/m2 of ASA404 i.v. on day 1 of each 21 day cycle

docetaxel

Intervention Type DRUG

75 mg/m2 of docetaxel intravenous (IV) an hour for 1st 6 cycles; cycle: every 21 days

Placebo + docetaxel

Placebo i.v. on day 1 of each 21 day cycle

75 mg/m2 of docetaxel intravenous (IV) an hour for 1st 6 cycles; cycle: every 21 days

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo i.v. on day 1 of each 21 day cycle

docetaxel

Intervention Type DRUG

75 mg/m2 of docetaxel intravenous (IV) an hour for 1st 6 cycles; cycle: every 21 days

Interventions

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ASA404

1800 mg/m2 of ASA404 i.v. on day 1 of each 21 day cycle

Intervention Type DRUG

Placebo

Placebo i.v. on day 1 of each 21 day cycle

Intervention Type DRUG

docetaxel

75 mg/m2 of docetaxel intravenous (IV) an hour for 1st 6 cycles; cycle: every 21 days

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Histologically confirmed non-small cell carcinoma of the lung of all histologies. (Histological or cytological specimens must be collected via surgical biopsy, brushing, washing or core needle aspiration of a defined lesion. Sputum cytology is not acceptable.)
2. Patients who have progressed while on or following a first-line chemotherapy regimen for Stage IIIb disease (malignant pleural effusion or pericardial effusion that have been confirmed cytologically) or Stage IV disease. Patients who have received bevacizumab and/or EGFR inhibitors in first-line will be eligible
3. Age ≥ 18 years old
4. WHO Performance Status of 0-2
5. Not applicable per amendment#2
6. Central laboratory values within the range, as defined below, within 2 weeks of randomization:

* Absolute neutrophils count (ANC) ≥ 2.0 x 109/L
* Platelets ≥ 100 x109/L
* Hemoglobin ≥ 10 g/dL
* Serum creatinine ≤ 1.5 x ULN
* Serum bilirubin ≤ 1.5 x ULN
* Aspartate transaminase (AST) and alanine transaminase (ALT) ≤2.5 x ULN (≤5 x ULN if liver metastases)
* International Normalized Ratio (INR) or Prothrombin Time (PT) ≤1.5 x ULN
* Electrolyte values (sodium, potassium, calcium, magnesium) within ≥1 x LLN and ≤1 x ULN. Patients with corrected electrolyte values are eligible
* Females of child-bearing potential must have negative serum pregnancy test (confirmation of negative urine pregnancy test within 72 hours prior to initial dosing). Any female presenting with a positive or borderline pregnancy test may undergo a gynecological exam and ultra sound to rule out pregnancy and if found to be negative may be included in the trial.
7. Life expectancy ≥ 12 weeks
8. Written informed consent obtained according to local guidelines

Exclusion Criteria

1. Patients having CNS metastases (patients having any clinical signs of CNS metastases must have a CT or MRI of the brain performed to rule out CNS metastases in order to be eligible for study participation. Patients who have had brain metastases surgically removed or irradiated with no residual disease confirmed by imaging are allowed).
2. Patients with concurrent malignancy, or history or prior malignancy within the past two years, except for basal cell or squamous cell skin cancer, carcinoma in situ of the cervix, treated early stage (T1a) prostate cancer or treated early stage (DCIS or LCIS) breast cancer.
3. Radiotherapy ≤ 2 weeks prior to randomization. Patients must have recovered from all acute radiotherapy-related toxicities.
4. Major surgery must be completed 4 weeks prior to starting study treatment. Major surgery is defined at the investigator's discretion. Insertion of a vascular access device is not considered major or minor surgery. Patients must have recovered from all acute surgery-related complications.
5. Treatment with all prior anticancer therapies ≤ 3 weeks prior to randomization (≤ 6 weeks for bevacizumab, mitomycin and nitrosoureas)
6. Concurrent use of other investigational agents and patients who have received investigational agents ≤ 4 weeks prior to randomization
7. Prior treatment with docetaxel for NSCLC in the locally advanced or metastatic first-line setting
8. Prior treatment with VDAs or tumor - VDAs
9. Any medical condition resulting in ≥ CTC grade 2 dyspnea
10. Patients with systolic BP \> 160 mm Hg and/or diastolic BP \> 90 mm Hg while on medication for hypertension
11. Patients with recent hemoptysis associated with NSCLC (\>1 teaspoon in a single episode within 4 weeks)
12. Patients with any one of the following:

* Patients with long QT syndrome
* Patients with a Baseline 12-lead ECG QTcF of \> 450 msec for men or \>470 msec for women using the Fridericia \[QTcF formula\] measurement determined per central ECG evaluation report
* Congestive heart failure (NY Heart Association class III or IV)
* Patients with a myocardial infarction within 12 months of starting study treatment or with implanted cardiac pacemaker
* Unstable or poorly controlled angina pectoris, including Prinzmetal variant angina pectoris
* History of poorly-controlled hypertension or poor compliance with anti-hypertensive regimen
* History of a sustained ventricular tachycardia
* Presence of atrial tachycardia (e.g., atrial fibrillation, atrial flutter, multifocal atrial tachycardia, supraventricular tachycardia) if not effectively rate-controlled
* History of ventricular fibrillation or Torsades de Pointes (TdP)
* Right bundle branch block (RBBB) and either left anterior hemiblock or left posterior hemiblock (bifasicular block)
* Bradycardia defined as heart rate \<50 beats per minute
* \[For China only: Patients older than 70 years with evidence of myocardial ischemia by coronary artery angiography or cardiac radionucleotide imaging examination\]
* \[For China only: Patients with LVEF \<=40%\]
* Any clinically significant cardiac abnormality as assessed by the investigator
13. Patients who are currently receiving treatment with any medications that have the potential to prolong QT interval or are known to have a risk of causing Torsades de Pointes (See Section 6.8.5.1 and Appendix 2) which cannot be either safely discontinued or switched to a different medication prior to starting study drug administration must be discussed with and approved by the Novartis Global Clinical team prior to randomization.
14. Known allergy or hypersensitivity to docetaxel or drugs formulated with polysorbate 80
15. Peripheral sensory neuropathy with functional impairment (CTC grade 2 neuropathy, regardless of causality)
16. Pregnant or breast feeding females

• Pregnant or nursing (lactating) women, where pregnancy is defined as the state of a female after conception and until the termination of gestation, confirmed by a positive hCG laboratory test (\> 5 mIU/ml)
17. Women of child bearing potential or sexually active males, unwilling or unable to use the required highly effective method(s) of contraception for both sexes while receiving treatment and for at least 6 months after the discontinuation of study treatment. (Adequate forms of contraception include IUD, oral or depot contraceptive or the barrier method plus spermicide.)

• Oral, implantable, or injectable contraceptives may be affected by cytochrome P450 interactions while taking docetaxel and therefore are not considered effective contraceptive methods for this study when used as a single agent. Therefore, it is highly recommended that a concomitant barrier method be used with oral, implantable, or injectable contraceptives. The investigator shall counsel the patient accordingly. Women of childbearing potential must have a negative pregnancy test (serum or urine) 72 hours prior to administration of study treatment. For a list of substrates of human liver microsomal P450 enzymes, visit website (http://medicine.iupui.edu/flockhart/)
18. Concurrent severe and/or uncontrolled medical disease (i.e. uncontrolled diabetes, chronic renal disease, chronic liver disease, confirmed diagnosis of HIV infection or active uncontrolled infection).
19. Significant neurologic or psychiatric disorder which could compromise participation in the study
20. Patient unwilling or unable to comply with the protocol
21. Patients receiving full-dose therapeutic oral or parenteral anticoagulation are ineligible. Patients receiving thrombolytic therapy within 10 days of starting are also ineligible.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Hemer, , Germany

Site Status

Novartis Investigative Site

Leipzig, , Germany

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Novartis Investigative Site

Magdeburg, , Germany

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Novartis Investigative Site

München, , Germany

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Novartis Investigative Site

Münster, , Germany

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Novartis Investigative Site

Oldenburg, , Germany

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Novartis Investigative Site

Ulm, , Germany

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Oncology Specialist, P.c.

Huntsville, Alabama, United States

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Arizona Oncology

Tucson, Arizona, United States

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Highlands Oncology Group

Bentonville, Arkansas, United States

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Central Hematology Oncology Medical Group

Alhambra, California, United States

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Comprehensive Blood and Cancer Center

Bakersfield, California, United States

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Compassionate Cancer Care Medical Group

Corona, California, United States

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Compassionate Cancer Care Medical Group

Fountain Valley, California, United States

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St. Jude Heritage Healthcare

Fullerton, California, United States

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Beaver Medical Group, L.P.

Highland, California, United States

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Scripps Clinic

La Jolla, California, United States

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University of Southern Californa

Los Angeles, California, United States

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Cedars-Sinai Medical Center

Los Angeles, California, United States

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UCLA

Los Angeles, California, United States

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North Valley Hematology/Oncology Medical Group

Northridge, California, United States

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University of California Irvine Medical Center

Orange, California, United States

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Ventura County Hematology/Oncology Specialists

Oxnard, California, United States

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Palo Alto Medical Foundation - Camino Div.

Palo Alto, California, United States

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Bay Area Cancer Research Group

Pleasant Hill, California, United States

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Loma Linda Oncology Medical Group, Inc.

Redlands, California, United States

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Compassionate Cancer Care Medical Group

Riverside, California, United States

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California Pacific Medical Research Institute

San Francisco, California, United States

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University of California - SF

San Francisco, California, United States

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Stanford Cancer Center

Stanford, California, United States

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Rocky Mountain Cancer Center

Denver, Colorado, United States

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Georgetown University Hospital

Washington D.C., District of Columbia, United States

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Advanced Medical Specialties

Miami, Florida, United States

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Florida Cancer Institute

New Port Richey, Florida, United States

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Ocala Oncology Center

Ocala, Florida, United States

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Florida Hospital Cancer Institute

Orlando, Florida, United States

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Cancer Centers of Florida, PA

Orlando, Florida, United States

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Hematology/Oncology Associates of Treasure Coast

Port Saint Lucie, Florida, United States

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Suburban Hematology-Oncology

Lawrenceville, Georgia, United States

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Cancer Care Specialists of Central Illinois

Decatur, Illinois, United States

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Comprehensive Cancer Program

Harvey, Illinois, United States

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Cancer Care & Hematology Specialists of Chicagoland

Niles, Illinois, United States

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OSF Center for Cancer Care

Rockford, Illinois, United States

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Loyola Cancer Care and Research Center

Winfield, Illinois, United States

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Central Indiana Cancer Centers

Indianapolis, Indiana, United States

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Horizon Oncology Center

Lafayette, Indiana, United States

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Providence Medical Group

Terre Haute, Indiana, United States

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Siouxland Hematology-Oncology Associates

Sioux City, Iowa, United States

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Kansas City Cancer care, Southwest

Overland Park, Kansas, United States

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University of Kansas Medical Center

Westwood, Kansas, United States

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Cancer Center of Texas

Wichita, Kansas, United States

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James Graham Brown Cancer Center

Louisville, Kentucky, United States

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Western Kentucky Hematology & Oncology

Paducah, Kentucky, United States

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Harry & Jeannette Weinberg Cancer Institute

Baltimore, Maryland, United States

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Missouri Cancer Associates

Columbia, Missouri, United States

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St. John's Mercy Medical Center

St Louis, Missouri, United States

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Comprehensive Cancer Centers of Nevada

Henderson, Nevada, United States

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Nevada Cancer Institute

Las Vegas, Nevada, United States

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New Mexico Cancer Center

Albuquerque, New Mexico, United States

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Advanced Oncology Associates

Armonk, New York, United States

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Arena Oncology Associates, P.C.

Lake Success, New York, United States

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NY Oncology/Hematology - Latham

Latham, New York, United States

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Winthrop Hematology/Oncology

Mineola, New York, United States

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SUNY Upstate Medical University

Syracuse, New York, United States

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Duke University Medical Center

Durham, North Carolina, United States

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Cancer Center of North Carolina

Raleigh, North Carolina, United States

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MetroHealth Medical Center

Cleveland, Ohio, United States

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Hematology Oncology Consultants, Inc.

Columbus, Ohio, United States

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Signal Point Hematology/Oncology, Inc.

Middletown, Ohio, United States

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Kaiser Permanante, Northwest Region

Portland, Oregon, United States

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St. Luke's Hospital & Healtth Network

Bethlehem, Pennsylvania, United States

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Temple University Hospital

Philadelphia, Pennsylvania, United States

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Hollings Cancer Center

Charleston, South Carolina, United States

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Sarah Cannon Research Institute

Nashville, Tennessee, United States

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Texas Cancer center - Abilene

Abilene, Texas, United States

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Texas Oncology - Arlington South

Arlington, Texas, United States

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Mamie McFadden Ward Cancer Ctr, Texas Oncology

Beaumont, Texas, United States

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Texas Cancer Center at Medical City

Dallas, Texas, United States

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Texas Oncology at Presbyterian Hospital

Dallas, Texas, United States

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Methodist Charlton Cancer Center

Dallas, Texas, United States

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UT Southwester Med Ctr at Dallas

Dallas, Texas, United States

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Texas Cancer Center - Denton

Denton, Texas, United States

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Longview Cancer Center

Longview, Texas, United States

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Texas Oncology - Allison Cancer Center

Midland, Texas, United States

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Paris Regional Cancer Center

Paris, Texas, United States

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Texas Cancer Center - Sherman

Sherman, Texas, United States

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Tyler Cancer Center

Tyler, Texas, United States

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Blood and Cancer Center of East Texas

Tyler, Texas, United States

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Texas Oncology Cancer Care Center & Research Center

Waco, Texas, United States

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Puget Sound Cancer Centers

Edmonds, Washington, United States

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Fred Hutchinson Cancer Reseach Center

Seattle, Washington, United States

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Puget Sound Cancer Center

Seattle, Washington, United States

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Evergreen Hematology and Oncology

Spokane, Washington, United States

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MultiCare Health System

Tacoma, Washington, United States

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Northwest Cancer Specialists

Vancouver, Washington, United States

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Novartis Investigative Site

Antwerp, , Belgium

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Novartis Investigative Site

Arlon, , Belgium

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Novartis Investigative Site

Brussels, , Belgium

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Novartis Investigative Site

Genk, , Belgium

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Novartis Investigative Site

Ghent, , Belgium

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Novartis Investigative Site

Leuven, , Belgium

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Novartis Investigative Site

Liège, , Belgium

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Novartis Investigative Site

Namur, , Belgium

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Novartis Investigative Site

Edmonton, , Canada

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Novartis Investigative Site

Greenfield Park, , Canada

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Novartis Investigative Site

Laval, , Canada

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Novartis Investigative Site

Montreal, , Canada

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Novartis Investigative Site

Toronto, , Canada

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Novartis Investigative Site

Trois-Rivières, , Canada

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Novartis Investigative Site

Vancouver, , Canada

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Novartis Investigative Site

Weston, , Canada

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Novartis Investigative Site

Winnepeg, , Canada

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Novartis Investigative Site

Avignon, , France

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Novartis Investigative Site

Brest, , France

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Novartis Investigative Site

Caen, , France

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Novartis Investigative Site

La Chaussée-Saint-Victor, , France

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Novartis Investigative Site

Le Mans, , France

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Novartis Investigative Site

Lille, , France

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Novartis Investigative Site

Nîmes, , France

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Novartis Investigative Site

Paris, , France

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Novartis Investigative Site

Perpignan, , France

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Novartis Investigative Site

Rennes, , France

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Novartis Investigative Site

Vandœuvre-lès-Nancy, , France

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Novartis Investigative site

Bamberg, , Germany

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Novartis Investigative Site

Berlin, , Germany

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Novartis Investigative Site

Cologne, , Germany

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Novartis Investigative Site

Coswig, , Germany

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Novartis Investigative Site

Eschweiler, , Germany

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Novartis Investigative Site

Essen, , Germany

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Novartis Investigative Site

Freiburg im Breisgau, , Germany

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Novartis Investigative Site

Großhansdorf, , Germany

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Novartis Investigative Site

Güstrow, , Germany

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Novartis Investigative Site

Halle, , Germany

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Novartis Investigative Site

Hamburg, , Germany

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Novartis Investigative Site

Hanover, , Germany

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Novartis Investigative site

Deszk, , Hungary

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Novartis Investigative Site

Gyula, , Hungary

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Novartis Investigative Site

Székesfehérvár, , Hungary

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Novartis Investigative Site

Törökbálint, , Hungary

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Novartis Investigative Site

Zalaegerszeg-Pozva, , Hungary

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Novartis Investigative Site

Ancona, , Italy

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Novartis Investigative Site

Aviano, , Italy

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Novartis Investigative Site

Bologna, , Italy

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Novartis Investigative Site

Cosenza, , Italy

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Novartis Investigative Site

Cremona, , Italy

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Novartis Investigative Site

Milan, , Italy

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Novartis Investigative Site

Mirano, , Italy

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Novartis Investigative Site

Monza, , Italy

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Novartis Investigative Site

Napoli, , Italy

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Novartis Investigative Site

Palermo, , Italy

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Novartis Investigative Site

Reggio Emilia, , Italy

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Novartis Investigative Site

Sassari, , Italy

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Novartis InvestigativeSite

Udine, , Italy

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Novartis Investigative Site

Bialystok, , Poland

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Novartis Investigative Site

Lonza, , Poland

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Novartis Investigative Site

Szczecin, , Poland

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Novartis Investigative Site

Warsaw, , Poland

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Novartis Investigative Site

Mataró, , Spain

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Novartis investigative Site

Sabadell, , Spain

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Novartis Investigative Site

Santander, , Spain

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Novartis Investigative Site

Geneva, , Switzerland

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Novartis Investigative site

Sankt Gallen, , Switzerland

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Countries

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United States Belgium Canada France Germany Hungary Italy Poland Spain Switzerland

Related Links

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https://www.novctrd.com/ctrdweb/trialresult/trialresults/pdf?trialResultId=4927

Results for CASA404A2302 from the Novartis Clinical Trials Website

Other Identifiers

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EUDRACT number: 2008-002309-38

Identifier Type: -

Identifier Source: secondary_id

CASA404A2302

Identifier Type: -

Identifier Source: org_study_id