A Novel Approach to Infantile Spasms

NCT ID: NCT03347526

Last Updated: 2021-05-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

SUSPENDED

Clinical Phase

PHASE3

Total Enrollment

394 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-04-19

Study Completion Date

2021-08-31

Brief Summary

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This study proposes to assess the efficacy of Cosyntropin Injectable Suspension, 1 mg/mL compared to vigabatrin. Additionally, this study proposes to determine efficacy of combination therapy of Cosyntropin Injectable Suspension, 1 mg/mL and vigabatrin to monotherapy Cosyntropin Injectable Suspension, 1mg/mL in children with new onset infantile spasms (IS).

Detailed Description

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This is a prospective randomized trial comparing 3 treatment arms:

1. Cosyntropin Injectable Suspension, 1 mg/mL
2. Vigabatrin
3. Combination of both these therapies, Cosyntropin Injectable Suspension, 1 mg/mL and vigabatrin for treatment of new onset infantile spasms. Outcome measures include resolution of clinical spasms, improvement of hypsarrhythmia as well as longer term outcomes of development and subsequent seizures.

The data is expected to demonstrate greater efficacy with Cosyntropin Injectable Suspension, 1 mg/mL than vigabatrin for the treatment of IS.

Conditions

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Infantile Spasm

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Blinded outcome measure

Study Groups

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Cosyntropin Injectable Suspension, 1mg/mL + vigabatrin

Group Type EXPERIMENTAL

Cosyntropin Injectable Suspension 1 MG/ML + vigabatrin

Intervention Type DRUG

Injectable + oral solution

Cosyntropin Injectable Suspension, 1 mg/mL

Group Type EXPERIMENTAL

Cosyntropin Injectable Suspension, 1 mg/mL

Intervention Type DRUG

Injectable

Vigabatrin

Group Type ACTIVE_COMPARATOR

Vigabatrin

Intervention Type DRUG

oral

Interventions

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Cosyntropin Injectable Suspension, 1 mg/mL

Injectable

Intervention Type DRUG

Cosyntropin Injectable Suspension 1 MG/ML + vigabatrin

Injectable + oral solution

Intervention Type DRUG

Vigabatrin

oral

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* New onset infantile spasms
* Age \> 2 months
* Age\< 2 years
* Hypsarrhythmia on video-EEG
* Normal renal function

Exclusion Criteria

* Prior treatment given for infantile spasms
* Diagnosis of Ohtahara syndrome or Early Myoclonic Epilepsy
* Absence of hypsarrhythmia
* Inability for the parent or caregiver to provide consent
* Inability for the parent or caregiver to complete seizure diary
* Diagnosis of:

* scleroderma,
* osteoporosis,
* recent systemic fungal infections,
* ocular herpes simplex,
* recent surgery,
* history of or the presence of a peptic ulcer,
* congestive heart failure,
* uncontrolled hypertension
Minimum Eligible Age

2 Months

Maximum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pediatric Epilepsy Research Foundation

UNKNOWN

Sponsor Role collaborator

West Therapuetics, Inc

UNKNOWN

Sponsor Role collaborator

University of Colorado, Denver

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kelly G. Knupp, MD

Role: PRINCIPAL_INVESTIGATOR

University of Colorado, Denver

Locations

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Children's Hospital Los Angeles

Los Angeles, California, United States

Site Status

UCSF Medical Center

San Francisco, California, United States

Site Status

University of Colorado Anschutz Medical Campus

Aurora, Colorado, United States

Site Status

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

Children's Healthcare of Atlanta at Scottish Rite

Atlanta, Georgia, United States

Site Status

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

C.S. Mott Children's Hospital

Ann Arbor, Michigan, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Atrium Health

Charlotte, North Carolina, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Cook Children's Medical Center

Fort Worth, Texas, United States

Site Status

Countries

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United States

Other Identifiers

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17-0222

Identifier Type: -

Identifier Source: org_study_id

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