A Study to Evaluate Safety and Efficacy of AMZ002 Treatment, Compared With Vigabatrin in Participants With Infantile Spasms

NCT ID: NCT05128344

Last Updated: 2023-04-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

WITHDRAWN

Clinical Phase

PHASE3

Study Classification

INTERVENTIONAL

Study Start Date

2023-04-30

Study Completion Date

2025-12-31

Brief Summary

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The main purpose of this study is to evaluate the efficacy of AMZ002 compared to Vigabatrin in participants with newly diagnosed infantile spasms (IS).

Detailed Description

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Conditions

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Spasms, Infantile

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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AMZ002

Group Type EXPERIMENTAL

AMZ002 injectable solution, 0.5mg/mL

Intervention Type DRUG

Injectable solution

Vigabatrin

Group Type ACTIVE_COMPARATOR

Vigabatrin, oral

Intervention Type DRUG

Oral administration

Interventions

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AMZ002 injectable solution, 0.5mg/mL

Injectable solution

Intervention Type DRUG

Vigabatrin, oral

Oral administration

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participant has been diagnosed with IS within 6 weeks prior to Screening. Diagnostic criteria include both clinical spasms and an EEG pattern consistent with hypsarrhythmia or significant abnormality compatible with IS
* Participant has normal renal function as defined by an estimated glomerular filtration rate (eGFR) greater than \[\>\] 60 milliliter/minute (mL/min)/1.73 m\^2, calculated as eGFR = 0.413 × (height \[Centimeter (cm)\]/serum creatinine \[milligrams per deciliter {mg/dL}\])
* Participant's legally authorized representative (that is \[i.e.\], parent or guardian) must provide written informed consent obtained per Institutional Review Board (IRB) policy and requirements, consistent with the International Council for Harmonisation (ICH)
* Participant's parent/guardian is able to understand and willing to comply with study procedures and restrictions

Exclusion Criteria

* Participant has been diagnosed with tuberous sclerosis
* Participant has acute illness considered clinically significant by the Investigator within 30 days prior to Screening
* Participant has a diagnosis of recent systemic fungal infection; history of ocular herpes simplex; history of or current peptic ulcer; uncontrolled hypertension or congestive heart failure; or any other condition that would be significantly impacted by the study drug
* Participant has a preplanned surgery or procedure(s) that would interfere with the conduct of the study
* Participant has received any prior treatment for IS
* Participant has been previously treated with adrenocorticotropic hormone (ACTH), corticosteroids, or Vigabatrin for seizures;
* Participant has been previously treated with a course of corticosteroids for an indication other than seizures within 30 days prior to Screening
* Participant has a known or suspected allergy to ACTH or Vigabatrin or any component of AMZ002 or Vigabatrin
* Participant has used any other investigational drug within 30 days or 5 half-lives prior to the first dose of AMZ002 or Vigabatrin (whichever is longer)
* Participant' s parent/guardian is unable to provide written informed consent and/or to complete the daily diary
* Participant has any other disease, condition, or therapy that, in the opinion of the Investigator, might compromise safety or compliance, preclude the participant from successfully completing the study, or interfere with the interpretation of the results
Minimum Eligible Age

2 Months

Maximum Eligible Age

24 Months

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amzell

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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The Childrens Hospital Colorado

Aurora, Colorado, United States

Site Status

Miami Children's Hospital

Miami, Florida, United States

Site Status

Advent Health Orlando

Orlando, Florida, United States

Site Status

Arnold Palmer Hospital For Children

Orlando, Florida, United States

Site Status

Childrens Healthcare of Atlanta

Atlanta, Georgia, United States

Site Status

Ann and Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status

University of Kentucky Hospital

Lexington, Kentucky, United States

Site Status

Children's Brain Institute

Lexington, Massachusetts, United States

Site Status

Children's Hospital of Michigan

Detroit, Michigan, United States

Site Status

Staten Island University Hospital, North

Staten Island, New York, United States

Site Status

Wake Forest Baptist Medical Center - PPDS

Winston-Salem, North Carolina, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Fundacion para la Lucha contra las Enfermedades Neurologicas de la Infancia

Buenos Aires, , Argentina

Site Status

Hospital Italiano de Buenos Aires

Buenos Aires, , Argentina

Site Status

Paediatric Hospital Dr. Juan P. Garrahan

Buenos Aires, , Argentina

Site Status

CHU Bordeaux - Hopital des Enfants

Bordeaux, , France

Site Status

HFME-Hospices Civils de Lyon

Bron, , France

Site Status

Hopital Roger Salengro - CHU de Lille

Lille, , France

Site Status

Hopital Necker - Enfants Malades

Paris, , France

Site Status

Hopital de Hautepierre

Strasbourg, , France

Site Status

All India Institute of Medical Sciences

New Delhi, Dehli, India

Site Status

Indira Gandhi Institute of Child Health

Bangalore, Karnataka, India

Site Status

Amrita Advanced Centre for Epilepsy

Kochi, Kerala, India

Site Status

Bharati Vidyapeeth Deemed University - Bharati Hospital

Pune, Maharashtra, India

Site Status

Azienda Ospedaliero Universitaria

Ancona, , Italy

Site Status

Pediatric Hospital G. Salesi

Ancona, , Italy

Site Status

AOU Anna Meyer - Clinica di Neurologia Pediatrica

Florence, , Italy

Site Status

Istituto Pediatrico Giannina Gaslini

Genova, , Italy

Site Status

Ospedale dei Bambini Vittore Buzzi

Milan, , Italy

Site Status

Universita degli Studi di Napoli Federico II

Naples, , Italy

Site Status

Ospedale Pediatrico Bambino Gesu

Roma, , Italy

Site Status

Policlinico Universitario A.Gemelli

Roma, , Italy

Site Status

Azienda Ospedaliera Universitaria Integrata

Verona, , Italy

Site Status

Neurociencias Estudios Clinicos S.C.

Culiacán, , Mexico

Site Status

HSRT

Mexico City, , Mexico

Site Status

Tecnologico De Monterrey - Hospital Zambrano Hellion - Instituto de Neurologia y Neurocirugia

Nuevo León, , Mexico

Site Status

The University Clinical Center

Gdansk, Gdansk, Poland

Site Status

Provincial Specialist Children's Hospital st. Ludwika

Krakow, Krakow, Poland

Site Status

Medical University of Warsaw

Warsaw, , Poland

Site Status

Institute of Mother and Child

Warsaw, , Poland

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Countries

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United States Argentina France India Italy Mexico Poland Spain

Other Identifiers

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2021-003015-26

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

AMZ002-002

Identifier Type: -

Identifier Source: org_study_id

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