Evaluating the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of BIIB054 in Participants With Parkinson's Disease

NCT ID: NCT03318523

Last Updated: 2022-02-28

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

357 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-01-10

Study Completion Date

2021-04-29

Brief Summary

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The primary objective of the study is to evaluate the clinical efficacy of BIIB054 via dose response using the change from baseline in Movement Disorder Society-Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Total Score.

The secondary objectives of the study are to evaluate the dose-related safety of BIIB054, to evaluate the clinical efficacy of BIIB054 via MDS-UPDRS total score, to assess the pharmacokinetic (PK) profile of BIIB054, to evaluate the clinical efficacy of BIIB054 based on MDS-UPDRS subparts, to evaluate the pharmacodynamic effects of BIIB054 on the integrity of nigrostriatal dopaminergic nerve terminals and to evaluate the immunogenicity of BIIB054.

Detailed Description

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Conditions

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Parkinson's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Year 1: Participants will receive matching placebo to BIIB054 on Day 1 and then every 4 weeks.

Year 2: Participants who received placebo in year 1 will be randomized into one of the active treatment arms in year 2 and will receive BIIB054 intravenous (IV) infusion on Week 52 and then every 4 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered as specified in the treatment arm

BIIB054 250 mg

Participants will receive BIIB054 250 milligrams (mg) intravenous (IV) infusion on Day 1 and then every 4 weeks.

Group Type EXPERIMENTAL

BIIB054

Intervention Type DRUG

Administered as specified in the treatment arm.

BIIB054 1250 mg

Participants will receive BIIB054 1250 mg IV infusion on Day 1 and then every 4 weeks.

Group Type EXPERIMENTAL

BIIB054

Intervention Type DRUG

Administered as specified in the treatment arm.

BIIB054 3500 mg

Participants will receive BIIB054 3500 mg IV infusion on Day 1 and then every 4 weeks.

Group Type EXPERIMENTAL

BIIB054

Intervention Type DRUG

Administered as specified in the treatment arm.

Interventions

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Placebo

Administered as specified in the treatment arm

Intervention Type DRUG

BIIB054

Administered as specified in the treatment arm.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosed with Parkinson's disease (PD) within a maximum of 3 years prior to Screening.
* Score of ≤2.5 on the Modified Hoehn and Yahr Scale.
* Has not received any medication for the treatment of the motor symptoms of PD for at least 12 weeks prior to Day 1 and, in the opinion of the Investigator, is not expected to require PD treatment for at least 6 months following Day 1. Maximum total duration of prior PD regimens should not exceed 30 days. Stable (at least 8 weeks) dosages of medications that are used to treat conditions other than PD tremor are allowed. Further guidance will be provided by the study's Medical Monitor on a case by case basis.
* Screening dopamine transporter (DaT)/ single-photon emission computed tomography (SPECT) results consistent with neurodegenerative Parkinsonism (central reading).
* All women of childbearing potential and all men must practice highly effective contraception during the study and for 6 months after their last dose of study treatment.

Exclusion Criteria

* Presence of freezing of gait.
* Montreal cognitive assessment (MOCA) score \<23 or other significant cognitive impairment or clinical dementia that, in the opinion of the Investigator, would interfere with study evaluation.
* History of or screening brain magnetic resonance imaging (MRI) scan indicative of clinically significant abnormality, as read by central reader.
* History of severe allergic or anaphylactic reactions, or history of hypersensitivity to BIIB054 or any of the inactive ingredients in the drug product or to radioligands or iodine used in the study.
* Participation in any active immunotherapy study targeting alpha-synuclein.
* Use of allowed medications not previously specified at doses that have not been stable for at least 8 weeks before Day 1, and/or that are not expected to remain stable for the duration of the study.
* Clinically significant abnormal laboratory test values at Screening, as determined by the Investigator.
* Blood donation (1 unit or more) within 8 weeks before Day 1 (must also refrain from donating blood for the duration of the study).
Minimum Eligible Age

40 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Biogen

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

St. Joseph's Hopsital & Medical Center- Barrow Neurological Institute

Phoenix, Arizona, United States

Site Status

Research Site

La Jolla, California, United States

Site Status

Cedars Sinai

Los Angeles, California, United States

Site Status

University of California San Francisco Medical Center

San Francisco, California, United States

Site Status

Research Site

Stanford, California, United States

Site Status

University of Colorado Health

Aurora, Colorado, United States

Site Status

Rocky Mountain Movement Disorders Center, PC

Englewood, Colorado, United States

Site Status

Parkinson's Disease and Movement Disorders Centerf

Boca Raton, Florida, United States

Site Status

Mayo Clinic Hospital

Jacksonville, Florida, United States

Site Status

Bioclinica Research

Orlando, Florida, United States

Site Status

USF Health Byrd Institute

Tampa, Florida, United States

Site Status

Northwestern University PD and Movement Disorders Center

Chicago, Illinois, United States

Site Status

Research Site

Chicago, Illinois, United States

Site Status

University of Kansas Medical Center Research Institute

Kansas City, Kansas, United States

Site Status

Ochsner Health System

New Orleans, Louisiana, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Boston University Medical Center

Boston, Massachusetts, United States

Site Status

Quest Research Institute

Farmington Hills, Michigan, United States

Site Status

NYU Langone Health Center

New York, New York, United States

Site Status

Research Site

New York, New York, United States

Site Status

Research Site

Durham, North Carolina, United States

Site Status

Wake Forest Baptist Health

Winston-Salem, North Carolina, United States

Site Status

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Research Site

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center Health System

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Research Site

Nashville, Tennessee, United States

Site Status

Research Site

Houston, Texas, United States

Site Status

Booth Gardner Parkinson's Care Center at Evergreen Health

Kirkland, Washington, United States

Site Status

Inland Northwest Research

Spokane, Washington, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Research Site

Innsbruck, , Austria

Site Status

University Health Network

Toronto, Ontario, Canada

Site Status

Montreal Neurological Institute Clinical Research Unit

Montreal, Quebec, Canada

Site Status

Research Name

Toulouse, Haute Garonne, France

Site Status

CHU Nantes - Hopital Nord Laënnec

Nantes, Loire Atlantique, France

Site Status

Hopital Roger Salengro - CHU Lille

Lille, Nord, France

Site Status

Hôpital Henri Mondor

Créteil, Val De Marne, France

Site Status

Research Site

Paris, , France

Site Status

Universitaetsklinikum Ulm

Ulm, Baden-Wurttemberg, Germany

Site Status

Klinikum rechts der Isar der TU Muenchen

Munich, Bavaria, Germany

Site Status

Universitaetsklinikum Wuerzburg

Würzburg, Bavaria, Germany

Site Status

Paracelsus-Elena-Klinik

Kassel, Hesse, Germany

Site Status

Universitaetsklinikum Aachen AOeR

Aachen, North Rhine-Westphalia, Germany

Site Status

Research Site

Bochum, North Rhine-Westphalia, Germany

Site Status

Research Site

Haifa, , Israel

Site Status

Research Site

Tel Aviv, , Israel

Site Status

I.R.C.C.S. Neuromed-Istituto Neurologico Mediterraneo

Pozzilli, Isernia, Italy

Site Status

Ospedale Bellaria

Bologna, , Italy

Site Status

Azienda Ospedaliero Univ. Policlinico Gaspare Rodolico

Catania, , Italy

Site Status

Research Site

Milan, , Italy

Site Status

Ospedale San Raffaele

Milan, , Italy

Site Status

Research Site

Milan, , Italy

Site Status

Seconda Università degli Studi di Napoli

Napoli, , Italy

Site Status

Research Site

Pisa, , Italy

Site Status

IRCCS San Raffaele

Roma, , Italy

Site Status

Azienda Ospedaliera Universitaria OO. RR. S. Giovanni di Dio e Ruggi D'Aragona

Salerno, , Italy

Site Status

Azienda Ospedaliera Santa Maria di Terni

Terni, , Italy

Site Status

Hospital General de Catalunya

Sant Cugat Del Vallés, Barcelona, Spain

Site Status

Research Site

Móstoles, Madrid, Spain

Site Status

Clinica Universidad de Navarra

Pamplona, Navarre, Spain

Site Status

Biocruces Health Research Institute

Barakaldo, Vizcaya, Spain

Site Status

Hospital Clinic De Barcalona

Barcelona, , Spain

Site Status

Hospital Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Research Site

Madrid, , Spain

Site Status

Research Site

Madrid, , Spain

Site Status

Research Site

Madrid, , Spain

Site Status

Research Site

Seville, , Spain

Site Status

Research Site

Cambridge, Cambridgeshire, United Kingdom

Site Status

Salford Royal

Salford, Greater Manchester, United Kingdom

Site Status

Research Site

Oxford, Oxfordshire, United Kingdom

Site Status

Clinical Ageing Research Unit

Newcastle upon Tyne, Tyne & Wear, United Kingdom

Site Status

Royal Hallamshire Hospital

Sheffield, West Midlands, United Kingdom

Site Status

Research Site

London, , United Kingdom

Site Status

Countries

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United States Austria Canada France Germany Israel Italy Spain United Kingdom

References

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Hutchison RM, Fraser K, Yang M, Fox T, Hirschhorn E, Njingti E, Scott D, Bedell BJ, Kistner KM, Cedarbaum JM, Evans KC, Graham D, Martarello L, Mollenhauer B, Lang AE, Dam T, Beaver J. Cinpanemab in Early Parkinson Disease: Evaluation of Biomarker Results From the Phase 2 SPARK Clinical Trial. Neurology. 2024 Mar 12;102(5):e209137. doi: 10.1212/WNL.0000000000209137. Epub 2024 Feb 5.

Reference Type DERIVED
PMID: 38315945 (View on PubMed)

Lang AE, Siderowf AD, Macklin EA, Poewe W, Brooks DJ, Fernandez HH, Rascol O, Giladi N, Stocchi F, Tanner CM, Postuma RB, Simon DK, Tolosa E, Mollenhauer B, Cedarbaum JM, Fraser K, Xiao J, Evans KC, Graham DL, Sapir I, Inra J, Hutchison RM, Yang M, Fox T, Budd Haeberlein S, Dam T; SPARK Investigators. Trial of Cinpanemab in Early Parkinson's Disease. N Engl J Med. 2022 Aug 4;387(5):408-420. doi: 10.1056/NEJMoa2203395.

Reference Type DERIVED
PMID: 35921450 (View on PubMed)

Hutchison RM, Evans KC, Fox T, Yang M, Barakos J, Bedell BJ, Cedarbaum JM, Brys M, Siderowf A, Lang AE. Evaluating dopamine transporter imaging as an enrichment biomarker in a phase 2 Parkinson's disease trial. BMC Neurol. 2021 Nov 23;21(1):459. doi: 10.1186/s12883-021-02470-8.

Reference Type DERIVED
PMID: 34814867 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2016-004610-95

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

228PD201

Identifier Type: -

Identifier Source: org_study_id

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