Study of BIIB092 in Participants With Progressive Supranuclear Palsy

NCT ID: NCT03068468

Last Updated: 2020-12-21

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

490 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-06-01

Study Completion Date

2020-02-07

Brief Summary

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The Primary objective of the study is to evaluate the efficacy of BIIB092, compared to placebo, as measured by a change from baseline in the PSP Rating Scale (PSPRS) at Week 52 and to assess the safety and tolerability of BIIB092, relative to placebo, by measuring the frequency of deaths, SAEs, AEs leading to discontinuation, and Grade 3 \& 4 laboratory abnormalities.

The Secondary objective of the study is to evaluate the efficacy of BIIB092, compared to placebo, as measured by a change in baseline in the Movement Disorder Society (MDS)-sponsored revision of the Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Part II at Week 52, to evaluate the efficacy of BIIB092, compared to placebo, as measured by the Clinical Global Impression of Change (CGI-C) at Week 52, to evaluate the efficacy of BIIB092, compared to placebo, as measured by a change in baseline in the Repeatable Battery for the Assessment of Neuropsychological Disease Severity (RBANS) at Week 52 and to assess the impact of BIIB092 on quality of life, relative to placebo, as measured by change from baseline on the Progressive Supranuclear Palsy Quality of Life scale (PSP-QoL) at Week 52.

Detailed Description

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This study, previously posted by Bristol-Myers Squibb, has transitioned to Biogen under a licensing agreement.

Conditions

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Supranuclear Palsy, Progressive

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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BIIB092

Participants will receive BIIB092 50 mg/ml intravenous (IV) infusion once every 4 weeks for 48 weeks in double blind treatment period followed by BIIB092 50 mg/ml IV infusion once every 4 weeks starting at Week 52 up to Week 208.

Group Type EXPERIMENTAL

BIIB092

Intervention Type DRUG

BIIB092 intravenous infusion on specified days

Placebo

Participants will receive BIIB092 matching placebo IV infusion once every 4 weeks for 48 weeks in double blind treatment period followed by BIIB092 50 mg/ml IV infusion once every 4 weeks starting at Week 52 up to Week 208.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo intravenous infusion on specified days

Interventions

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BIIB092

BIIB092 intravenous infusion on specified days

Intervention Type DRUG

Placebo

Placebo intravenous infusion on specified days

Intervention Type DRUG

Other Intervention Names

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BMS-986168

Eligibility Criteria

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Inclusion Criteria

* Participants with probable or possible PSP
* Able to ambulate independently or with assistance
* Able to tolerate MRI
* Have reliable caregiver to accompany participant to all study visits
* Score greater or equal to 20 on the Mini Mental State Exam (MMSE) at screening
* Participant must reside outside a skilled nursing facility or dementia care facility at the time of screening and admission to such a facility must not be planned

Exclusion Criteria

* Presence of other significant neurological or psychiatric disorders
* Diagnosis of amyotrophic lateral sclerosis (ALS) or other motor neuron disease
* History of early, prominent rapid eye movement (REM) sleep behavior disorder
* History of or screening brain MRI scan indicative of significant abnormality
* Known history of serum or plasma progranulin level less than one standard deviation below the normal patient mean for the laboratory performing the assay
Minimum Eligible Age

41 Years

Maximum Eligible Age

86 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Biogen

Locations

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Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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Sun City, Arizona, United States

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Fountain Valley, California, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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San Francisco, California, United States

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Boca Raton, Florida, United States

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Gainesville, Florida, United States

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Tampa, Florida, United States

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Chicago, Illinois, United States

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Chicago, Illinois, United States

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Chicago, Illinois, United States

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Indianapolis, Indiana, United States

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Kansas City, Kansas, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Burlington, Massachusetts, United States

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Farmington Hills, Michigan, United States

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Minneapolis, Minnesota, United States

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New Brunswick, New Jersey, United States

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Albany, New York, United States

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New York, New York, United States

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New York, New York, United States

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New York, New York, United States

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Hershey, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Charleston, South Carolina, United States

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Dallas, Texas, United States

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Charlottesville, Virginia, United States

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Seattle, Washington, United States

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North Melbourne, Victoria, Australia

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Innsbruck, Tyrol, Austria

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Vienna, , Austria

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London, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Bordeaux, , France

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Lille, , France

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Marseille, , France

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Nîmes, , France

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Paris, , France

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Rennes, , France

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Toulouse, , France

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Munich, Bavaria, Germany

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Marburg, Hesse, Germany

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Rostock, Mecklenburg-Western-Pommerania, Germany

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Düsseldorf, North Rhine-Westphalia, Germany

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Dresden, Saxony, Germany

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Kiel, Schleswig-Holstein, Germany

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Lübeck, Schleswig-Holstein, Germany

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Beelitz-Heilstätten, , Germany

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Bochum, , Germany

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Bonn, , Germany

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Essen, , Germany

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Kassel, , Germany

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Ulm, , Germany

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Athens, Marousi, Greece

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Salerno, Campania, Italy

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Pisa, , Italy

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Venice-Lido, , Italy

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Nagoya, Aichi-ken, Japan

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Kamagaya, Chiba, Japan

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Sapporo, Hokkaido, Japan

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Sagamihara, Kanagawa, Japan

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Kodaira, Tokyo, Japan

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Yonago, Tottori, Japan

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Shizuoka, , Japan

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Krasnoyarsk, , Russia

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Moscow, , Russia

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Seoul, , South Korea

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Pamplona, Navarre, Spain

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Barakaldo, Vizcaya, Spain

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Barcelona, , Spain

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Madrid, , Spain

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Seville, , Spain

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Valencia, , Spain

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Cambridge, Cambridgeshire, United Kingdom

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Brighton, East Sussex, United Kingdom

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Southampton, Hampshire, United Kingdom

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Liverpool, Merseyside, United Kingdom

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Newcastle upon Tyne, Tyne and Wear, United Kingdom

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Newport, Wales, United Kingdom

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London, , United Kingdom

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Countries

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United States Australia Austria Canada France Germany Greece Italy Japan Russia South Korea Spain United Kingdom

References

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Jaeger J, Yang L, Li Y, Castrillo-Viguera C, Haeberlein SB, Dam T, O'Gorman J. Development of a cognitive composite for measuring change in progressive supranuclear palsy. Parkinsonism Relat Disord. 2021 Nov;92:94-100. doi: 10.1016/j.parkreldis.2021.10.007. Epub 2021 Oct 12.

Reference Type DERIVED
PMID: 34736158 (View on PubMed)

Dam T, Boxer AL, Golbe LI, Hoglinger GU, Morris HR, Litvan I, Lang AE, Corvol JC, Aiba I, Grundman M, Yang L, Tidemann-Miller B, Kupferman J, Harper K, Kamisoglu K, Wald MJ, Graham DL, Gedney L, O'Gorman J, Haeberlein SB; PASSPORT Study Group. Safety and efficacy of anti-tau monoclonal antibody gosuranemab in progressive supranuclear palsy: a phase 2, randomized, placebo-controlled trial. Nat Med. 2021 Aug;27(8):1451-1457. doi: 10.1038/s41591-021-01455-x. Epub 2021 Aug 12.

Reference Type DERIVED
PMID: 34385707 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-002554-21

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CN002-012

Identifier Type: OTHER

Identifier Source: secondary_id

251PP301

Identifier Type: -

Identifier Source: org_study_id