Safety and Pharmacodynamic Effects of BIIB122 in Participants With LRRK2-Associated Parkinson's Disease (LRRK2-PD)

NCT ID: NCT06602193

Last Updated: 2025-11-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

50 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-10-24

Study Completion Date

2028-02-28

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This Phase 2a, multicenter, randomized, 12-week double-blind, placebo-controlled, parallel-group study, followed by an OLE, is designed to evaluate the safety, tolerability, and pharmacodynamic effects of BIIB122 in participants with LRRK2-PD. LRRK2-PD is defined as Parkinson's Disease (PD) in individuals who are heterozygous or homozygous carriers of a pathogenic LRRK2 variant that increases LRRK2 kinase activity.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Parkinson Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

BIIB122 225 mg

Oral 225 mg dose, once daily (QD)

Group Type EXPERIMENTAL

BIIB122 225 mg

Intervention Type DRUG

Administered as specified in the treatment arm

BIIB122 Matching Placebo

Oral BIIB122 matching placebo, once daily (QD)

Group Type PLACEBO_COMPARATOR

BIIB122-Matching Placebo

Intervention Type OTHER

Administered as specified in the treatment arm

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

BIIB122 225 mg

Administered as specified in the treatment arm

Intervention Type DRUG

BIIB122-Matching Placebo

Administered as specified in the treatment arm

Intervention Type OTHER

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

DNL151

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* For heterozygous pathogenic LRRK2 mutation carriers: ≥ 30 to ≤ 80 years
* For homozygous pathogenic LRRK2 mutation carriers: ≥ 30 years
* Have screening genetic test results verifying the presence of a pathogenic LRRK2 variant.
* Have a clinical diagnosis of PD meeting the Movement Disorder Society Clinical Diagnostic Criteria.

Exclusion Criteria

* Have a history of any clinically significant neurological disorder other than PD, including, but not limited to, stroke and dementia, in the opinion of the investigator, within 5 years of the screening visit.
* Have clinical evidence of atypical parkinsonism (eg, multiple-system atrophy or progressive supranuclear palsy) or evidence of drug-induced parkinsonism.
* Have previously participated or are currently participating in the BIIB122 LUMA study (Study 283PD201).
* Have previously participated or are currently participating in a gene therapy study for PD.
* Have a history of brain surgical intervention for PD (eg, deep-brain stimulation, pallidotomy).
* Have any physical condition that may confound the motor assessment (MDS-UPDRS) over time (eg, severe arthritis, severe dyskinesias, traumatic injuries with permanent physical disability).
* Abnormal vitals including Blood Pressure, Heart Rate, or Body Temperature
* Have abnormal PFT results at screening
Minimum Eligible Age

30 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Biogen

INDUSTRY

Sponsor Role collaborator

Denali Therapeutics Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Danna Jennings, MD

Role: STUDY_DIRECTOR

Denali Therapeutics

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Cedars-Sinai Department of Neurology

Los Angeles, California, United States

Site Status RECRUITING

University of California San Francisco

San Francisco, California, United States

Site Status RECRUITING

Parkinson's Disease and Movement Disorders Center

Boca Raton, Florida, United States

Site Status RECRUITING

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

Ichan School of Medicine at Mount Sinai/Beth Israel Downtown-Movement Disorder Center

New York, New York, United States

Site Status RECRUITING

Evergreen Health Laboratory

Kirkland, Washington, United States

Site Status RECRUITING

Inland Northwest Research

Spokane, Washington, United States

Site Status RECRUITING

Technische Universität Dresden

Dresden, , Germany

Site Status RECRUITING

University of Lübeck

Lübeck, , Germany

Site Status RECRUITING

University Hospital Tübingen

Tübingen, , Germany

Site Status RECRUITING

Hospital Universitari General de Catalunya

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Donostia

Donostia / San Sebastian, , Spain

Site Status RECRUITING

Universitary Hospital La Princesa

Madrid, , Spain

Site Status RECRUITING

IDIVAL/University Hospital Marques de Valdecilla

Santander, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Germany Spain

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Clinical Trials at Denali Therapeutics

Role: CONTACT

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Anne Tran

Role: primary

310-423-1697

Luisa Bolo Dave

Role: primary

Stuart Isaacson, MD

Role: primary

(561)392-1818

Jackie Forbes

Role: primary

617-667-9885

Ricardo Renvill

Role: primary

212-844-6055

EvergreenHealth Research Department

Role: primary

Jason Aldred, MD

Role: primary

509-960-2818

Marian Kollaske

Role: primary

Madita Grümmer

Role: primary

Susanne Solbrig

Role: primary

Susana Andrade

Role: primary

+3493175715

Alejandra Garcia Blanco

Role: primary

Ioana Croitoru

Role: primary

Pablo Sáinz-Ezquerra

Role: primary

Raquel Martinez

Role: primary

Cristina Gomez Rapela

Role: primary

Lorena Garrote

Role: backup

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

DNLI-C-0009

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

BIIB014 Phase 2a Monotherapy
NCT00451815 WITHDRAWN PHASE2
Pioglitazone in Early Parkinson's Disease
NCT01280123 COMPLETED PHASE2