A Study of Cobimetinib Plus Atezolizumab Versus Pembrolizumab in Participants With Previously Untreated Advanced BRAFv600 Wild-Type Melanoma

NCT ID: NCT03273153

Last Updated: 2022-09-21

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

446 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-12-11

Study Completion Date

2021-02-19

Brief Summary

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This is a Phase III, multicenter, open-label, randomized study designed to evaluate the efficacy, safety, and pharmacokinetics of cobimetinib plus atezolizumab compared with pembrolizumab in treatment-naive participants with advanced BRAFV600 wild-type melanoma.

Detailed Description

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Conditions

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Advanced BRAFV600 Wild-type Melanoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cobimetinib and Atezolizumab

Participants will receive 60 mg of cobimetinib orally from Days 1 to 21 along with 840 mg of atezolizumab by intravenous (IV) infusion on Days 1 and 15 of each 28-day cycle until investigator-determined disease progression, unacceptable toxicity, death, patient or physician decision to withdraw, or pregnancy, whichever occurs first. There will be no cobimetinib administration for 7 days (Days 22-28) in each cycle.

Group Type EXPERIMENTAL

Cobimetinib

Intervention Type DRUG

Cobimetinib 60 mg tablets orally once daily on a 21 days on, 7 days off schedule.

Atezolizumab

Intervention Type DRUG

Atezolizumab 840 mg as IV infusion once in every 2 weeks.

Pembrolizumab

Participants will receive 200 mg of pembrolizumab administered by IV infusion every 3 weeks (Q3W) until investigator-determined disease progression, unacceptable toxicity, death, patient or physician decision to withdraw, or pregnancy, whichever occurs first.

Group Type ACTIVE_COMPARATOR

Pembrolizumab

Intervention Type DRUG

Pembrolizumab 200 mg as IV infusion once in every 3 weeks.

Interventions

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Cobimetinib

Cobimetinib 60 mg tablets orally once daily on a 21 days on, 7 days off schedule.

Intervention Type DRUG

Atezolizumab

Atezolizumab 840 mg as IV infusion once in every 2 weeks.

Intervention Type DRUG

Pembrolizumab

Pembrolizumab 200 mg as IV infusion once in every 3 weeks.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed locally advanced and unresectable or metastatic melanoma
* Naive to prior systemic anti-cancer therapy for melanoma
* Documentation of BRAFV600 wild-type status in melanoma tumor tissue through use of a clinical mutation test approved by the local health authority
* A representative, formalin-fixed, paraffin-embedded (FFPE) tumor specimen in a paraffin block (preferred) or 20 slides containing unstained, freshly cut, serial sections must be submitted along with an associated pathology report prior to study entry. If 20 slides are not available or the tissue block is not of sufficient size, the patient may still be eligible for the study, after discussion with and approval by the Medical Monitor
* Measurable disease according to Response Evaluation Criteria in Solid Tumors (RECIST) v1.1
* Age \>=18 years at time of signing Informed Consent Form
* Ability to comply with the study protocol, in the investigator's judgment
* Histologically or cytologically confirmed BRAFV600 wild-type melanoma
* Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 or 1
* Life expectancy \>=3 months
* Adequate hematologic and end-organ function
* For women of childbearing potential: agreement to remain abstinent or use at least two forms of effective contraceptive with a failure rate of \< 1% per year during the treatment period and for at least 3 months after the last dose of cobimetinib and at least 5 months after the last dose of atezolizumab or pembrolizumab
* For men: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive measures (e.g. condom), and agreement to refrain from donating sperm, for at least 3 months after the last dose of cobimetinib
* Willingness and ability of patients to report selected study outcomes (e.g., GHS and HRQoL) using an electronic device or paper backup questionnaires.

Exclusion Criteria

* Inability to swallow medications
* Malabsorption condition that would alter the absorption of orally administered medications
* Pregnancy, breastfeeding, or intention of becoming pregnant during the study
* History of severe hypersensitivity reactions to components of the cobimetinib, atezolizumab, or pembrolizumab formulations
* Current or recent treatment with therapeutic antibiotics, live attenuated vaccines or systemic immunostimulatory/immunosuppresive medication
* Ocular melanoma
* Major surgery or radiotherapy within 21 days prior to Day 1 of Cycle 1 or anticipation of needing such procedure while receiving study treatment
* Uncontrolled tumor-related pain
* Uncontrolled pleural effusion, pericardial effusion, or ascites requiring repeated drainage more than once every 28 days
* Active or untreated central nervous system (CNS) metastases Exclusions Related to Cardiovascular Disease
* Unstable angina, new-onset angina within last 3 months, myocardial infarction within the last 6 months prior to Day 1 of Cycle 1, or current congestive heart failure classified as New York Heart Association Class II or higher
* Left ventricular ejection fraction (LVEF) below institutional lower limit of normal or \<50%, whichever is lower
* Poorly controlled hypertension, defined as sustained, uncontrolled, non-episodic baseline hypertension consistently above 159/99 mmHg despite optimal medical management
* History or presence of an abnormal electrocardiogram (ECG) that is clinically significant in the investigator's opinion, including complete left bundle branch block, second- or third degree heart block, or evidence of prior myocardial infarction Exclusions Related to Infections
* HIV infection
* Active tuberculosis infection
* Severe infections within 4 weeks prior to Day 1 of Cycle 1, including, but not limited to, hospitalization for complications of infection, bacteremia, or severe pneumonia
* Signs or symptoms of clinically relevant infection within 2 weeks prior to Day 1 of Cycle 1
* Treatment with oral or IV antibiotics within 2 weeks prior to Day 1 of Cycle 1
* Active or chronic viral hepatitis B or C infection Exclusions Related to Ocular Disease
* Known risk factors for ocular toxicity Exclusions Related to Autoimmune Conditions and Immunomodulatory Drugs
* Active or history of autoimmune disease or immune deficiency
* Prior allogeneic stem cell or solid organ transplantation
* History of idiopathic pulmonary fibrosis, organizing pneumonia, drug-induced or idiopathic pneumonitis, or evidence of active pneumonitis on screening chest CT scan
* Treatment with systemic immunosuppressive medications within 2 weeks prior to Day 1, Cycle 1 Exclusions Related to Other Medical Conditions or Medications
* Active malignancy (other than melanoma) or a prior malignancy within the past 3 years
* Any Grade \>=3 hemorrhage or bleeding event within 28 days of Day 1 of Cycle 1
* History of stroke, reversible ischemic neurological defect, or transient ischemic attack within 6 months prior to Day 1
* Proteinuria \>3.5 gm/24 hr
* Consumption of foods, supplements, or drugs that are strong or moderate CYP3A4 enzyme inducers or inhibitors at least 7 days prior to Day 1 of Cycle 1 and during study treatment
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_CHAIR

Hoffmann-La Roche

Locations

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University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

City of Hope Comprehensive Cancer Center

Duarte, California, United States

Site Status

USC Norris Cancer Center

Los Angeles, California, United States

Site Status

USC Norris Cancer Center; USC Oncology Hematology Newport Beach

Newport Beach, California, United States

Site Status

University of California at Irvine Medical Center; Department of Oncology

Orange, California, United States

Site Status

Stanford Comprehensive Cancer Center

Stanford, California, United States

Site Status

UF Health Cancer Center at Orlando Health

Orlando, Florida, United States

Site Status

Florida Cancer Specialist, North Region

St. Petersburg, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Florida Cancer Specialists

West Palm Beach, Florida, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Massachusetts General Hospital;Hematology/ Oncology

Boston, Massachusetts, United States

Site Status

University of Michigan; Michigan Institute for Clinical and Health Research (MICHR)

Ann Arbor, Michigan, United States

Site Status

Dartmouth-Hitchcock Medical Center; Hematology/Oncology

Lebanon, New Hampshire, United States

Site Status

Morristown Medical Center

Morristown, New Jersey, United States

Site Status

Forsythe Memorial Hospital Inc., dba Novant Health Oncology Specialists

Winston-Salem, North Carolina, United States

Site Status

TriHealth Hatton Institute; Surgical Education

Cincinnati, Ohio, United States

Site Status

St. Luke's University Health network

Bethlehem, Pennsylvania, United States

Site Status

Thomas Jefferson University Hospital;Medical Oncology

Philadelphia, Pennsylvania, United States

Site Status

SCRI Tennessee Oncology Chattanooga

Chattanooga, Tennessee, United States

Site Status

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

M.D Anderson Cancer Center; Uni of Texas At Houston

Houston, Texas, United States

Site Status

West Virginia University Hospitals Inc

Morgantown, West Virginia, United States

Site Status

Cairns Base Hospital

Cairns, Queensland, Australia

Site Status

Townsville General Hospital

Douglas, Queensland, Australia

Site Status

Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status

Royal Hobart Hospital

Hobart, Tasmania, Australia

Site Status

Fiona Stanley Hospital

Murdoch, Western Australia, Australia

Site Status

Cliniques Universitaires St-Luc

Brussels, , Belgium

Site Status

AZ Groeninge

Kortrijk, , Belgium

Site Status

UZ Leuven Gasthuisberg

Leuven, , Belgium

Site Status

Instituto Nacional de Cancer - INCa; Oncologia

Rio de Janeiro, Rio de Janeiro, Brazil

Site Status

Hospital das Clinicas - UFRGS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hopital Avicenne; Dermatologie

Bobigny, , France

Site Status

Hopital Saint Andre CHU De Bordeaux; Dermatologie

Bordeaux, , France

Site Status

Chu Site Du Bocage;Dermatologie

Dijon, , France

Site Status

CHU de Grenoble - Hôpital Nord

Grenoble, , France

Site Status

Centre Hospitalier Le Mans; Dermatologie

Le Mans, , France

Site Status

Hopital Claude Huriez; Sce Dermatologie

Lille, , France

Site Status

Hopital Timone Adultes; Dermatologie

Marseille, , France

Site Status

CHU de Nantes; Cancéro-dermatologie

Nantes, , France

Site Status

Hopital l Archet 2; Ginestriere, Service de; Dermatologie

Nice, , France

Site Status

Groupe Hospitalier Bichat Claude Bernard

Paris, , France

Site Status

Hopital Saint Louis; Dermatologie 1

Paris, , France

Site Status

Hopital Robert Debre; DERMATOLOGIE

Reims, , France

Site Status

Centre Eugene Marquis; Service d'oncologie

Rennes, , France

Site Status

Hopital Charles Nicolle; Dermatologie Serv.

Rouen, , France

Site Status

Institut Universitaire du Cancer - Oncopole Toulouse (IUCT-O)

Toulouse, , France

Site Status

Institut Gustave Roussy; Dermatologie

Villejuif, , France

Site Status

Universitätsklinikum "Carl Gustav Carus"; Klinik und Poliklinik für Dermatologie

Dresden, , Germany

Site Status

HELIOS Klinikum Erfurt; Klinik für Dermatologie & Allergologie

Erfurt, , Germany

Site Status

Universitatsklinikum Essen; Klinik für Dermatologie

Essen, , Germany

Site Status

Klinik Johann Wolfgang von Goethe Uni; Klinik für Dermatologie, Venerologie und Allergologie

Frankfurt, , Germany

Site Status

SRH Wald-Klinikum Gera; Klinik für Hautkrankheiten und Allergologie

Gera, , Germany

Site Status

Medizinische Hochschule Hannover; Klinik für Dermatologie, Allergologie und Venerologie

Hanover, , Germany

Site Status

UKSH Kiel; Klinik für Dermatologie, Venerologie und Allergologie

Kiel, , Germany

Site Status

Universitatsklinikum Mainz; Klinik und Poliklinik fur Dermatologie

Mainz, , Germany

Site Status

Klinikum Mannheim Klinik fuer Dermatologie, Venerologie und Allergologie

Mannheim, , Germany

Site Status

Johannes Wesling Klinikum Minden; Hämatologie, Onkologie, Hämostaseologie und Palliativmedizin

Minden, , Germany

Site Status

Klinikum der Ludwigs-Maximilians-Universität München; Dermatologie

München, , Germany

Site Status

Fachklinik Hornheide; Dermatologie

Münster, , Germany

Site Status

Zentrum für Dermatoonkologie, Universitäts-Hautklinik Tübingen

Tübingen, , Germany

Site Status

Anticancer Hospital Ag. Savas ; 2Nd Dept. of Oncology - Internal Medicine

Athens, , Greece

Site Status

Laiko General Hospital Athen

Athens, , Greece

Site Status

Metropolitan Hospital; Dept. of Oncology

Pireaus, , Greece

Site Status

Bioclinic Thessaloniki

Thessaloniki, , Greece

Site Status

Orszagos Onkologiai Intezet; Borgyogyaszati Osztaly

Budapest, , Hungary

Site Status

Pecsi Tudomanyegyetem AOK; Borgyogyaszati Klinika

Pécs, , Hungary

Site Status

University of Szeged Szent-Györgyi Albert Clinical Center; Department of Dermatology and Allergology

Szeged, , Hungary

Site Status

A.O.U. Cons. Policlinico Bari - Consorzlale Policlinico; Scienze Biomediche e Oncologia Umana

Bari, Apulia, Italy

Site Status

Azienda Osp Uni Seconda Università Degli Studi Di Napoli; Unità Operativa Oncologia Medica

Napoli, Campania, Italy

Site Status

IRCCS Istituto Nazionale Tumori Fondazione Pascale; Oncologia Medica B

Napoli, Campania, Italy

Site Status

A.O. Universitaria Policlinico Di Modena; Ematologia

Modena, Emilia-Romagna, Italy

Site Status

IFO - Istituto Regina Elena; Oncologia Medica

Rome, Lazio, Italy

Site Status

IRCCS Istituto Nazionale Per La Ricerca Sul Cancro (IST); Oncologia Medica A

Genoa, Liguria, Italy

Site Status

Irccs Istituto Nazionale Dei Tumori (Int);S.C. Medicina Oncologica 2

Milan, Lombardy, Italy

Site Status

Irccs Istituto Europeo Di Oncologia (IEO); Oncologia Medica

Milan, Lombardy, Italy

Site Status

Fondazione Del Piemonte Per L'oncologia Ircc Di Candiolo; Dipartimento Oncologico

Candiolo, Piedmont, Italy

Site Status

Azienda Ospedaliero - Universitaria Pisana U.O. Oncologia Medica 2 Universitaria - Polo Oncologico

Pisa, Tuscany, Italy

Site Status

IOV - Istituto Oncologico Veneto IRCCS

Padua, Veneto, Italy

Site Status

Antoni Van Leeuwenhoek Ziekenhuis; Inwendige Geneeskunde

Amsterdam, , Netherlands

Site Status

Amphia Ziekenhuis, locatie Langendijk;Oncology

Breda, , Netherlands

Site Status

Erasmus Mc - Daniel Den Hoed Kliniek; Interne Oncologie

Rotterdam, , Netherlands

Site Status

Zuyderland ziekenhuis locatie Geleen

Sittard-Geleen, , Netherlands

Site Status

Copernicus Podmiot Medyczny Sp. z o.o. Wojewodzkie Centrum Onkologii

Gdansk, , Poland

Site Status

COZL Oddzial Onkologii Klinicznej z pododdzialem Chemioterapii Dziennej

Lublin, , Poland

Site Status

Szpital Kliniczny im. Heliodora Święcickiego UM w Poznaniu.

Poznan, , Poland

Site Status

Zachodniopomorskie Centrum Onkologii, Osrodek Innowacyjnosci, Rozwoju i Badan Klinicznych

Szczecin, , Poland

Site Status

Narodowy Instytut Onkologii im. Marii Skłodowskiej-Curie - Państwowy Instytut Badawczy

Warsaw, , Poland

Site Status

Dolnośląskie Centrum Onkologii, Pulmonologii i Hematologii

Wroclaw, , Poland

Site Status

Moscow City Oncology Hospital #62

Moscovskaya Oblast, Moscow Oblast, Russia

Site Status

FSBSI "Russian Oncological Scientific Center n.a. N.N. Blokhin"

Moscow, , Russia

Site Status

St. Petersburg Oncology Hospital

Saint Petersburg, , Russia

Site Status

FBI "Scientific Research Institute of Oncology n. a. N. N. Petrov"

Saint Petersburg, , Russia

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Hospital Universitario Son Espases; Servicio de Oncologia

Palma de Mallorca, Balearic Islands, Spain

Site Status

Hospital Universitari Germans Trias i Pujol; Servicio de Oncologia

Badalona, Barcelona, Spain

Site Status

Complejo Hospitalario Universitario de Santiago (CHUS) ; Servicio de Oncologia

Santiago de Compostela, LA Coruña, Spain

Site Status

Hospital Universitario Materno Infantil de Gran Canaria; Servicio de Oncologia

Las Palmas de Gran Canaria, LAS Palmas, Spain

Site Status

Clinica Universitaria de Navarra; Servicio de oncología

Pamplona, Navarre, Spain

Site Status

Hospital Univ Vall d'Hebron; Servicio de Oncologia

Barcelona, , Spain

Site Status

Hospital Clínic i Provincial; Servicio de Oncología

Barcelona, , Spain

Site Status

Hospital General Universitario Gregorio Marañon; Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Ramon y Cajal; Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre; Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Universitario La Paz; Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Universitario Virgen Macarena; Servicio de Oncologia

Seville, , Spain

Site Status

Instituto Valenciano Oncologia; Oncologia Medica

Valencia, , Spain

Site Status

Hospital General Universitario de Valencia; Servicio de oncologia

Valencia, , Spain

Site Status

Hospital Universitario Miguel Servet; Servicio Oncologia

Zaragoza, , Spain

Site Status

BRISTOL ONCOLOGY CENTRE; CLINICAL TRIALS UNIT; R & D department

Bristol, , United Kingdom

Site Status

Western General Hospital; Edinburgh Cancer Center

Edinburgh, , United Kingdom

Site Status

Leicester Royal Infirmary; Dept. of Medical Oncology

Leicester, , United Kingdom

Site Status

University College London Hospital

London, , United Kingdom

Site Status

Guys & St Thomas Hospital; Department of Oncology

London, , United Kingdom

Site Status

University Hospitals of North Midlands NHS Trust-Royal Stoke University Hospital

Stoke-on-Trent, , United Kingdom

Site Status

Singleton Hospital; Pharmacy

Swansea, , United Kingdom

Site Status

Royal Cornwall Hospital

Truro, , United Kingdom

Site Status

Countries

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United States Australia Belgium Brazil France Germany Greece Hungary Italy Netherlands Poland Russia South Korea Spain United Kingdom

References

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de Azevedo SJ, de Melo AC, Roberts L, Caro I, Xue C, Wainstein A. First-line atezolizumab monotherapy in patients with advanced BRAFV600 wild-type melanoma. Pigment Cell Melanoma Res. 2021 Sep;34(5):973-977. doi: 10.1111/pcmr.12960. Epub 2021 Feb 15.

Reference Type DERIVED
PMID: 33476492 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-004387-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CO39722

Identifier Type: -

Identifier Source: org_study_id

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