LIBERTY 1: Efficacy & Safety Study of Relugolix in Women With Heavy Menstrual Bleeding Associated With Uterine Fibroids

NCT ID: NCT03049735

Last Updated: 2022-04-19

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

388 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-04-26

Study Completion Date

2020-08-24

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to determine the benefit of relugolix 40 milligrams (mg) once a day co-administered with estradiol (E2) 1 mg and norethindrone acetate (NETA) 0.5 mg compared with placebo for 24 weeks on heavy menstrual bleeding associated with uterine fibroids.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This study is an international phase 3 randomized, double-blind, placebo-controlled efficacy and safety study to evaluate 24 weeks of oral daily relugolix 40 mg co-administered with low-dose E2 and NETA (Group A) and 12 weeks of daily oral relugolix 40 mg alone followed by 12 weeks of daily oral relugolix 40 mg co-administered with low-dose E2 and NETA (Group B) compared with 24 weeks of placebo (Group C).

All participants completing the Week 24 visit, including women randomized to placebo, were offered the opportunity to enroll in an open-label extension study in which all eligible participants will receive relugolix co-administered with low-dose E2 and NETA. Participants who did not enroll into the extension study had a follow-up visit approximately 30 days after the end of treatment (that is, after the participant's last dose of study medication).

Safety will be assessed throughout the study by monitoring adverse events, vital signs, physical examinations, clinical laboratory tests, 12-lead electrocardiograms, and assessments of bone mineral density.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Heavy Menstrual Bleeding Uterine Fibroid

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Relugolix plus E2/NETA (Group A)

Relugolix co-administered with E2/NETA for 24 weeks.

Group Type EXPERIMENTAL

Relugolix

Intervention Type DRUG

Relugolix (40 mg) tablet administered orally once daily.

Estradiol/norethindrone acetate

Intervention Type DRUG

E2 (1.0 mg)/NETA (0.5 mg) co-formulated capsule administered orally once daily.

Relugolix plus Delayed E2/NETA (Group B)

Relugolix co-administered with E2/NETA placebo for 12 weeks, followed by relugolix co-administered with E2/NETA for 12 weeks.

Group Type EXPERIMENTAL

Relugolix

Intervention Type DRUG

Relugolix (40 mg) tablet administered orally once daily.

Estradiol/norethindrone acetate

Intervention Type DRUG

E2 (1.0 mg)/NETA (0.5 mg) co-formulated capsule administered orally once daily.

Estradiol/norethindrone acetate placebo

Intervention Type DRUG

E2 (0 mg)/NETA (0 mg) placebo capsule administered orally once daily and designed to match the capsule containing E2/NETA in size, shape, color, and odor.

Placebo (Group C)

Relugolix placebo co-administered with E2/NETA placebo for 24 weeks.

Group Type PLACEBO_COMPARATOR

Estradiol/norethindrone acetate placebo

Intervention Type DRUG

E2 (0 mg)/NETA (0 mg) placebo capsule administered orally once daily and designed to match the capsule containing E2/NETA in size, shape, color, and odor.

Relugolix placebo

Intervention Type DRUG

Relugolix (0 mg) placebo tablet administered orally once daily and manufactured to match the relugolix tablet in size, shape, color, and odor.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Relugolix

Relugolix (40 mg) tablet administered orally once daily.

Intervention Type DRUG

Estradiol/norethindrone acetate

E2 (1.0 mg)/NETA (0.5 mg) co-formulated capsule administered orally once daily.

Intervention Type DRUG

Estradiol/norethindrone acetate placebo

E2 (0 mg)/NETA (0 mg) placebo capsule administered orally once daily and designed to match the capsule containing E2/NETA in size, shape, color, and odor.

Intervention Type DRUG

Relugolix placebo

Relugolix (0 mg) placebo tablet administered orally once daily and manufactured to match the relugolix tablet in size, shape, color, and odor.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

TAK-385 MVT-601 E2/NETA low-dose hormonal add-back

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Premenopausal female aged 18 to 50 years old (inclusive) on the day of signing and dating the informed consent form.
2. Has regularly occurring menstrual periods of ≤ 14 days duration with a cycle of 21 to 38 days from the start of 1 menstrual period until the start of the next, by participant history for at least 3 months prior to the first screening visit.
3. Has a diagnosis of uterine fibroids that is confirmed by a transvaginal and/or transabdominal ultrasound performed during the screening period.
4. Has heavy menstrual bleeding associated with uterine fibroids as evidenced by an MBL of ≥ 160 milliliter (mL) during 1 cycle or ≥ 80 mL per cycle for 2 menstrual cycles as measured by the alkaline hematin method during the screening period.

Exclusion Criteria

1. Has transvaginal and/or transabdominal ultrasound during the screening period demonstrating pathology other than uterine fibroids that could be responsible for or contributing to the patient's heavy menstrual bleeding.
2. Has known rapidly enlarging uterine fibroids in the opinion of the investigator.
3. Has a weight that exceeds the weight limit of the DXA scanner or has a condition that precludes an adequate DXA measurement at the lumbar spine and proximal femur.
4. Has a history of or currently has osteoporosis, or other metabolic bone disease, hyperparathyroidism, hyperprolactinemia, hyperthyroidism, anorexia nervosa, or low traumatic (from the standing position) or atraumatic fracture (toe, finger, skull, face and ankle fractures are allowed). A history of successfully treated hyperparathyroidism, hyperprolactinemia, or hyperthyroidism is allowed if the participant's bone mineral density is within normal limits.
5. Has a history of the use of bisphosphonates, calcitonin, calcitriol, ipriflavone, teriparatide, denosumab, or any medication other than calcium and vitamin D preparations to treat bone mineral density loss.
6. Has been a participant in an investigational drug or device study within the 1 month prior to the first screening visit.
Minimum Eligible Age

18 Years

Maximum Eligible Age

50 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Myovant Sciences GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Myovant Medical Monitor

Role: STUDY_DIRECTOR

Myovant Sciences

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Andalusia

Andalusia, Alabama, United States

Site Status

Mobile

Mobile, Alabama, United States

Site Status

Little Rock

Little Rock, Arkansas, United States

Site Status

La Mesa

La Mesa, California, United States

Site Status

Lomita

Lomita, California, United States

Site Status

Norwalk

Norwalk, California, United States

Site Status

Oceanside

Oceanside, California, United States

Site Status

San Diego

San Diego, California, United States

Site Status

San Diego

San Diego, California, United States

Site Status

Denver

Denver, Colorado, United States

Site Status

Aventura

Aventura, Florida, United States

Site Status

Brandon

Brandon, Florida, United States

Site Status

Clearwater

Clearwater, Florida, United States

Site Status

Clermont

Clermont, Florida, United States

Site Status

Fort Myers

Fort Myers, Florida, United States

Site Status

Hialeah

Hialeah, Florida, United States

Site Status

Hialeah

Hialeah, Florida, United States

Site Status

Jacksonville

Jacksonville, Florida, United States

Site Status

Lauderdale Lakes

Lauderdale Lakes, Florida, United States

Site Status

Margate

Margate, Florida, United States

Site Status

Miami

Miami, Florida, United States

Site Status

Miami

Miami, Florida, United States

Site Status

Miami

Miami, Florida, United States

Site Status

Orlando

Orlando, Florida, United States

Site Status

Orlando

Orlando, Florida, United States

Site Status

Palm Harbor

Palm Harbor, Florida, United States

Site Status

South Miami

South Miami, Florida, United States

Site Status

Tampa

Tampa, Florida, United States

Site Status

West Palm Beach

West Palm Beach, Florida, United States

Site Status

Weston

Weston, Florida, United States

Site Status

Atlanta

Atlanta, Georgia, United States

Site Status

Atlanta

Atlanta, Georgia, United States

Site Status

Augusta

Augusta, Georgia, United States

Site Status

College Park

College Park, Georgia, United States

Site Status

Richland

Richland, Georgia, United States

Site Status

Oakbrook

Oakbrook Terrace, Illinois, United States

Site Status

Lafayette

Lafayette, Indiana, United States

Site Status

Covington

Covington, Louisiana, United States

Site Status

Shreveport

Shreveport, Louisiana, United States

Site Status

St. Louis

St Louis, Missouri, United States

Site Status

Lincoln

Lincoln, Nebraska, United States

Site Status

Omaha

Omaha, Nebraska, United States

Site Status

Las Vegas

Las Vegas, Nevada, United States

Site Status

Las Vegas

Las Vegas, Nevada, United States

Site Status

Lawrenceville

Lawrenceville, New Jersey, United States

Site Status

Albuquerque

Albuquerque, New Mexico, United States

Site Status

Williamsville

Williamsville, New York, United States

Site Status

Durham

Durham, North Carolina, United States

Site Status

Morehead City

Morehead City, North Carolina, United States

Site Status

Raleigh

Raleigh, North Carolina, United States

Site Status

Bismarck

Bismarck, North Dakota, United States

Site Status

Fargo

Fargo, North Dakota, United States

Site Status

Minot

Minot, North Dakota, United States

Site Status

Cincinnati

Cincinnati, Ohio, United States

Site Status

Cincinnati

Cincinnati, Ohio, United States

Site Status

Dayton

Dayton, Ohio, United States

Site Status

Englewood

Englewood, Ohio, United States

Site Status

Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Bluffton

Bluffton, South Carolina, United States

Site Status

Charleston

Charleston, South Carolina, United States

Site Status

Columbia

Columbia, South Carolina, United States

Site Status

Greenville

Greenville, South Carolina, United States

Site Status

Chattanooga

Chattanooga, Tennessee, United States

Site Status

Memphis

Memphis, Tennessee, United States

Site Status

Memphis

Memphis, Tennessee, United States

Site Status

Fort Worth

Fort Worth, Texas, United States

Site Status

Houston

Houston, Texas, United States

Site Status

Houston

Houston, Texas, United States

Site Status

Irving

Irving, Texas, United States

Site Status

San Antonio

San Antonio, Texas, United States

Site Status

Sugar Land

Sugar Land, Texas, United States

Site Status

Webster

Webster, Texas, United States

Site Status

Salt Lake City

Salt Lake City, Utah, United States

Site Status

Salt Lake City

Salt Lake City, Utah, United States

Site Status

Norfolk

Norfolk, Virginia, United States

Site Status

Seattle

Seattle, Washington, United States

Site Status

Curitiba

Curitiba, , Brazil

Site Status

Porto Alegre

Porto Alegre, , Brazil

Site Status

Ribeirao Preto

Ribeirão Preto, , Brazil

Site Status

Santo Andre

Santo André, , Brazil

Site Status

Sao Paulo

São Paulo, , Brazil

Site Status

Bologna

Bologna, , Italy

Site Status

Catanzaro

Catanzaro, , Italy

Site Status

Fiernze

Florence, , Italy

Site Status

Genova

Genova, , Italy

Site Status

Milano

Milan, , Italy

Site Status

Modena

Modena, , Italy

Site Status

Monserrato

Monserrato, , Italy

Site Status

Napoli

Napoli, , Italy

Site Status

Roma

Roma, , Italy

Site Status

Roma

Roma, , Italy

Site Status

Siena

Siena, , Italy

Site Status

Torino

Torino, , Italy

Site Status

Katowice

Katowice, , Poland

Site Status

Lodz

Lodz, , Poland

Site Status

Lodz

Lodz, , Poland

Site Status

Lublin

Lublin, , Poland

Site Status

Lublin

Lublin, , Poland

Site Status

Poznan

Poznan, , Poland

Site Status

Szczecin

Szczecin, , Poland

Site Status

Warszawa

Warsaw, , Poland

Site Status

Warszawa

Warsaw, , Poland

Site Status

Durban

Durban, , South Africa

Site Status

Durban

Durban, , South Africa

Site Status

Port Elizabeth

Port Elizabeth, , South Africa

Site Status

Roodepoort

Roodepoort, , South Africa

Site Status

Birmingham

Birmingham, , United Kingdom

Site Status

Isleworth

Isleworth, , United Kingdom

Site Status

London

London, , United Kingdom

Site Status

Nottingham

Nottingham, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Brazil Italy Poland South Africa United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Stewart EA, Lukes AS, Venturella R, Ferreira JA, Li Y, Hunsche E, Wagman RB, Al-Hendy A. A plain language summary describing changes in pain associated with uterine fibroids among women receiving relugolix combination therapy. Pain Manag. 2024 Sep;14(9):469-476. doi: 10.1080/17581869.2024.2408114. Epub 2024 Oct 28.

Reference Type DERIVED
PMID: 39466126 (View on PubMed)

Stewart EA, Al-Hendy A, Lukes AS, Madueke-Laveaux OS, Zhu E, Proehl S, Schulmann T, Marsh EE. Relugolix combination therapy in Black/African American women with symptomatic uterine fibroids: LIBERTY Long-Term Extension study. Am J Obstet Gynecol. 2024 Feb;230(2):237.e1-237.e11. doi: 10.1016/j.ajog.2023.10.030. Epub 2023 Oct 18.

Reference Type DERIVED
PMID: 37863160 (View on PubMed)

Al-Hendy A, Lukes AS, Venturella R, Villarroel C, McKain L, Li Y, Wagman RB, Stewart EA. A plain language summary of the long-term relugolix combination therapy study for uterine fibroids. J Comp Eff Res. 2023 Aug;12(8):e230069. doi: 10.57264/cer-2023-0069. Epub 2023 Jul 21.

Reference Type DERIVED
PMID: 37477173 (View on PubMed)

Al-Hendy A, Lukes AS, Poindexter AN 3rd, Venturella R, Villarroel C, Critchley HO, Li Y, McKain L, Arjona Ferreira JC, Langenberg AG, Wagman RB, Stewart EA. A plain language summary of the safety of relugolix combination therapy and improvement in symptoms in women with uterine fibroids from the LIBERTY 1 and LIBERTY 2 studies. Pain Manag. 2023 Apr;13(4):205-211. doi: 10.2217/pmt-2022-0085. Epub 2023 May 15.

Reference Type DERIVED
PMID: 37183454 (View on PubMed)

Al-Hendy A, Lukes AS, Poindexter AN 3rd, Venturella R, Villarroel C, McKain L, Li Y, Wagman RB, Stewart EA. Long-term Relugolix Combination Therapy for Symptomatic Uterine Leiomyomas. Obstet Gynecol. 2022 Dec 1;140(6):920-930. doi: 10.1097/AOG.0000000000004988. Epub 2022 Nov 2.

Reference Type DERIVED
PMID: 36357960 (View on PubMed)

Stewart EA, Lukes AS, Venturella R, Arjona Ferreira JC, Li Y, Hunsche E, Wagman RB, Al-Hendy A. Relugolix Combination Therapy for Uterine Leiomyoma-Associated Pain in the LIBERTY Randomized Trials. Obstet Gynecol. 2022 Jun 1;139(6):1070-1081. doi: 10.1097/AOG.0000000000004787. Epub 2022 May 2.

Reference Type DERIVED
PMID: 35675604 (View on PubMed)

Hunsche E, Rakov V, Scippa K, Witherspoon B, McKain L. The Burden of Uterine Fibroids from the Perspective of US Women Participating in Open-Ended Interviews. Womens Health Rep (New Rochelle). 2022 Mar 4;3(1):286-296. doi: 10.1089/whr.2021.0086. eCollection 2022.

Reference Type DERIVED
PMID: 35415708 (View on PubMed)

Al-Hendy A, Lukes AS, Poindexter AN 3rd, Venturella R, Villarroel C, Critchley HOD, Li Y, McKain L, Arjona Ferreira JC, Langenberg AGM, Wagman RB, Stewart EA. Treatment of Uterine Fibroid Symptoms with Relugolix Combination Therapy. N Engl J Med. 2021 Feb 18;384(7):630-642. doi: 10.1056/NEJMoa2008283.

Reference Type DERIVED
PMID: 33596357 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2016-003727-27

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MVT-601-3001

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.