Efficacy and Safety of Elagolix in Combination With Estradiol/Norethindrone Acetate for the Management of Heavy Menstrual Bleeding Associated With Uterine Fibroids in Premenopausal Women

NCT ID: NCT02654054

Last Updated: 2020-06-29

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

413 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-12-22

Study Completion Date

2018-12-12

Brief Summary

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This study seeks to evaluate the efficacy, safety and tolerability of elagolix alone and in combination with estradiol/norethindrone acetate for the management of heavy menstrual bleeding associated with uterine fibroids in premenopausal women.

Detailed Description

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Conditions

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Uterine Fibroids Heavy Menstrual Bleeding

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Placebo for both elagolix twice daily (BID) and norethindrone acetate (E2/NETA) once daily (QD)

Group Type PLACEBO_COMPARATOR

Placebo for Estradiol/Norethindrone Acetate

Intervention Type DRUG

Placebo capsules

Placebo for Elagolix

Intervention Type DRUG

Film-coated placebo tablets

Elagolix

Elagolix 300 mg BID and placebo for E2/NETA (estradiol 1.0 mg/norethindrone acetate 0.5 mg) QD

Group Type EXPERIMENTAL

Elagolix

Intervention Type DRUG

Film-coated tablets

Placebo for Estradiol/Norethindrone Acetate

Intervention Type DRUG

Placebo capsules

Elagolix + E2/NETA

Elagolix 300 mg BID and E2/NETA (estradiol 1.0 mg/norethindrone acetate 0.5 mg) QD

Group Type EXPERIMENTAL

Elagolix

Intervention Type DRUG

Film-coated tablets

Estradiol/Norethindrone Acetate

Intervention Type DRUG

Commercially-available E2/NETA tablets were over-encapsulated to maintain study blinding.

Interventions

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Elagolix

Film-coated tablets

Intervention Type DRUG

Placebo for Estradiol/Norethindrone Acetate

Placebo capsules

Intervention Type DRUG

Estradiol/Norethindrone Acetate

Commercially-available E2/NETA tablets were over-encapsulated to maintain study blinding.

Intervention Type DRUG

Placebo for Elagolix

Film-coated placebo tablets

Intervention Type DRUG

Other Intervention Names

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ABT-620 elagolix sodium E2/NETA

Eligibility Criteria

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Inclusion Criteria

* Subject is a premenopausal female at the time of Screening.
* Subject has a diagnosis of uterine fibroids documented by a pelvic ultrasound (transabdominal ultrasound/transvaginal ultrasound).
* Subject has heavy menstrual bleeding associated with uterine fibroids as evidenced by menstrual blood loss \> 80 mL during each of two screening menses as measured by the alkaline hematin method.
* Subject has negative urine and/or serum pregnancy test in Screening and just prior to first dose.
* Subject has an adequate endometrial biopsy performed during Screening, the results of which show no clinically significant endometrial pathology.

Exclusion Criteria

* Subject has screening pelvic ultrasound or saline infusion sonohysterography results that show a clinically significant gynecological disorder.
* Subject has history of osteoporosis or other metabolic bone disease.
* Subject has clinically significant abnormalities in clinical chemistry, hematology, or urinalysis.
* Subject has a history of major depression or post-traumatic stress disorder (PTSD) within 2 years of screening, OR a history of other major psychiatric disorder at any time (e.g., schizophrenia, bipolar disorder).
* Subject is using any systemic corticosteroids for over 14 days within 3 months prior to Screening or is likely to require treatment with systemic corticosteroids during the course of the study. Over the counter and prescription topical, inhaled, intranasal or injectable (for occasional use) corticosteroids are allowed.
Minimum Eligible Age

18 Years

Maximum Eligible Age

51 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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AbbVie Inc.

Role: STUDY_DIRECTOR

AbbVie

Locations

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Summers, Birmingham, AL /ID# 139684

Birmingham, Alabama, United States

Site Status

University of South Alabama /ID# 148763

Mobile, Alabama, United States

Site Status

WCCT Global, LLC /ID# 145666

Costa Mesa, California, United States

Site Status

American Clinical Trials /ID# 147374

Hawaiian Gardens, California, United States

Site Status

Grossmont Ctr Clin Research /ID# 144011

La Mesa, California, United States

Site Status

Long Beach Clinical Trial Serv /ID# 152424

Long Beach, California, United States

Site Status

National Research Institute /ID# 151629

Los Angeles, California, United States

Site Status

University of California, Los Angeles /ID# 144107

Los Angeles, California, United States

Site Status

Beach OBGYN Medical Group /ID# 151414

Newport Beach, California, United States

Site Status

Advanced RX Clinical Research /ID# 149168

Westminster, California, United States

Site Status

Bluebird Clinical Trials, LLC /ID# 144843

Colorado Springs, Colorado, United States

Site Status

Advanced Women's Health Institution /ID# 144108

Greenwood Village, Colorado, United States

Site Status

Medstar Health Research Institute /ID# 145933

Washington D.C., District of Columbia, United States

Site Status

James A. Simon, MD, PC /ID# 139675

Washington D.C., District of Columbia, United States

Site Status

Helix Biomedics, LLC /ID# 147114

Boynton Beach, Florida, United States

Site Status

Brandon Premier Health Care, PA /ID# 153130

Brandon, Florida, United States

Site Status

Florida Clin Res Group /ID# 139811

Ckearwater, Florida, United States

Site Status

Universal Clinical Research A /ID# 139742

Doral, Florida, United States

Site Status

Clinical Physiology Associates /ID# 139736

Fort Myers, Florida, United States

Site Status

Meridien Research /ID# 139663

Kenneth City, Florida, United States

Site Status

Altus Research, Inc /ID# 139662

Lake Worth, Florida, United States

Site Status

South Florida Wellness & Clinic /ID# 143558

Margate, Florida, United States

Site Status

LCC Medical Research Institute /ID# 143551

Miami, Florida, United States

Site Status

Healthcare Clinical Data, Inc /ID# 139650

Miami, Florida, United States

Site Status

Ocean Blue Med Research Ctr /ID# 139826

Miami, Florida, United States

Site Status

Salom Tangir, LLC /ID# 151732

Miramar, Florida, United States

Site Status

Advanced Research Institute /ID# 143554

New Port Richey, Florida, United States

Site Status

Clinical Associates of Orlando /ID# 148123

Orlando, Florida, United States

Site Status

Omega Research Consultants /ID# 139648

Orlando, Florida, United States

Site Status

Unified Womens Clin Research /ID# 145169

Panama City, Florida, United States

Site Status

Comprehensive Clinical Trials /ID# 139644

West Palm Beach, Florida, United States

Site Status

Atlanta Medical Research Insti /ID# 147117

Alpharetta, Georgia, United States

Site Status

Paramount Research Solutions /ID# 139645

Alpharetta, Georgia, United States

Site Status

Agile Clinical Research Trials /ID# 143563

Atlanta, Georgia, United States

Site Status

Perimeter Inst Clinical Resear /ID# 148298

Atlanta, Georgia, United States

Site Status

Masters of Clinical Research, Inc. /ID# 139658

Augusta, Georgia, United States

Site Status

Fellows Research Alliance, Inc /ID# 139655

Savannah, Georgia, United States

Site Status

Boise Family Medical Center /ID# 139844

Boise, Idaho, United States

Site Status

Women's Health Practice, LLC /ID# 143569

Champaign, Illinois, United States

Site Status

Great Lakes Clinical Trials /ID# 148135

Chicago, Illinois, United States

Site Status

Affinity Clinical Research /ID# 150980

Oak Brook, Illinois, United States

Site Status

American Health Network of IN /ID# 139822

Avon, Indiana, United States

Site Status

GTC Research /ID# 141854

Kansas City, Kansas, United States

Site Status

Cypress Medical Research Ctr /ID# 147116

Wichita, Kansas, United States

Site Status

Research Integrity, LLC /ID# 139727

Owensboro, Kentucky, United States

Site Status

Clinical Trials Management, LLC - Covington /ID# 139651

Covington, Louisiana, United States

Site Status

Ochsner Baptist Medical Center /ID# 139740

New Orleans, Louisiana, United States

Site Status

Omni Fertility and Laser Insti /ID# 139836

Shreveport, Louisiana, United States

Site Status

Capital Women's Care /ID# 144109

Frederick, Maryland, United States

Site Status

Genesis Clinical Research - Fall River /ID# 148449

Fall River, Massachusetts, United States

Site Status

Great Lakes Research Group,Inc /ID# 139659

Bay City, Michigan, United States

Site Status

Grand Rapids Womens Health /ID# 139705

Grand Rapids, Michigan, United States

Site Status

Wayne State University Physician Group - Southfield /ID# 139802

Southfield, Michigan, United States

Site Status

Office of Edmond E. Pack, MD /ID# 139792

Las Vegas, Nevada, United States

Site Status

Mabey, Las Vegas, NV /ID# 148138

Las Vegas, Nevada, United States

Site Status

Lawrence OB/GYN /ID# 143567

Lawrenceville, New Jersey, United States

Site Status

Bosque Women's Care /ID# 145934

Albuquerque, New Mexico, United States

Site Status

Manhattan Medical Research /ID# 144471

New York, New York, United States

Site Status

Cwrwc /Id# 139664

Durham, North Carolina, United States

Site Status

Unified Women's Clinical Research-Greensboro /ID# 139829

Greensboro, North Carolina, United States

Site Status

Unified Women's Clinical Resea /ID# 139774

Raleigh, North Carolina, United States

Site Status

PMG Research of Wilmington LLC /ID# 152563

Wilmington, North Carolina, United States

Site Status

Unified Women's Clinical Resea /ID# 144721

Winston-Salem, North Carolina, United States

Site Status

University of Cincinnati /ID# 139820

Cincinnati, Ohio, United States

Site Status

Univ Hosp Cleveland /ID# 139741

Cleveland, Ohio, United States

Site Status

Complete Healthcare for Women /ID# 139673

Columbus, Ohio, United States

Site Status

Miami Valley Hospital /ID# 144430

Dayton, Ohio, United States

Site Status

University of Toledo /ID# 139787

Toledo, Ohio, United States

Site Status

Legacy Medical Group-Portland /ID# 148807

Portland, Oregon, United States

Site Status

Main Line Fertility Center /ID# 150295

Bryn Mawr, Pennsylvania, United States

Site Status

Penn State University and Milton S. Hershey Medical Center /ID# 139733

Hershey, Pennsylvania, United States

Site Status

Thomas Jefferson University /ID# 139812

Philadelphia, Pennsylvania, United States

Site Status

Temple University Hospital /ID# 151429

Philadelphia, Pennsylvania, United States

Site Status

Clinical Trials Research Svcs /ID# 139707

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina /ID# 148754

Charleston, South Carolina, United States

Site Status

Vista Clinical Research /ID# 139797

Columbia, South Carolina, United States

Site Status

WR-ClinSearch /ID# 143538

Chattanooga, Tennessee, United States

Site Status

Research Memphis Associates, LLC /ID# 139674

Memphis, Tennessee, United States

Site Status

Access Clinical Trials, Inc. /ID# 139730

Nashville, Tennessee, United States

Site Status

UT Southwestern Medical Center /ID# 143537

Dallas, Texas, United States

Site Status

Advances in Health, Inc. /ID# 139672

Houston, Texas, United States

Site Status

Victorium Clinical Research /ID# 149630

San Antonio, Texas, United States

Site Status

Discovery Clinical Trials-San Antonio /ID# 139776

San Antonio, Texas, United States

Site Status

Houston Ctr for Clin Research /ID# 149149

Sugar Land, Texas, United States

Site Status

Center of Reproductive Medicin /ID# 139813

Webster, Texas, United States

Site Status

Eastern Virginia Med School /ID# 139647

Norfolk, Virginia, United States

Site Status

Clinical Research Partners, LL /ID# 143999

North Chesterfield, Virginia, United States

Site Status

Clinical Trials Virginia, Inc. /ID# 139801

Richmond, Virginia, United States

Site Status

Emerson Clinical Research /ID# 147373

Vienna, Virginia, United States

Site Status

Seattle Women's Health, Research, Gynecology /ID# 139768

Seattle, Washington, United States

Site Status

Premier Clinical Research /ID# 148145

Spokane, Washington, United States

Site Status

Froedtert and Medical College /ID# 143566

Milwaukee, Wisconsin, United States

Site Status

IWK Health Center /ID# 149066

Halifax, Nova Scotia, Canada

Site Status

The Ottawa Hospital /ID# 148695

Ottawa, Ontario, Canada

Site Status

Rodriguez-Ginorio, San Juan /ID# 139847

San Juan, , Puerto Rico

Site Status

School of Medicine University of Puerto Rico-Medical Sciences Campus /ID# 139848

San Juan, , Puerto Rico

Site Status

Countries

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United States Canada Puerto Rico

References

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Simon JA, Stewart EA, Jewell S, Li M, Snabes MC. Impact of demographic and clinical factors on elagolix plus add-back therapy effects on patient-reported nonbleeding symptoms in women with heavy menstrual bleeding and uterine fibroids: a post hoc analysis of data from two clinical trials. F S Rep. 2024 Jun 14;5(3):285-295. doi: 10.1016/j.xfre.2024.06.002. eCollection 2024 Sep.

Reference Type DERIVED
PMID: 39381651 (View on PubMed)

Beck D, Winzenborg I, Liu M, Degner J, Mostafa NM, Noertersheuser P, Shebley M. Population Pharmacokinetics of Elagolix in Combination with Low-Dose Estradiol/Norethindrone Acetate in Women with Uterine Fibroids. Clin Pharmacokinet. 2022 Apr;61(4):577-587. doi: 10.1007/s40262-021-01096-w. Epub 2021 Dec 8.

Reference Type DERIVED
PMID: 34878624 (View on PubMed)

Stewart EA, Archer DF, Owens CD, Barnhart KT, Bradley LD, Feinberg EC, Gillispie-Bell V, Imudia AN, Liu R, Kim JH, Al-Hendy A. Reduction of Heavy Menstrual Bleeding in Women Not Designated as Responders to Elagolix Plus Add Back Therapy for Uterine Fibroids. J Womens Health (Larchmt). 2022 May;31(5):698-705. doi: 10.1089/jwh.2021.0152. Epub 2021 Sep 28.

Reference Type DERIVED
PMID: 34582715 (View on PubMed)

Muneyyirci-Delale O, Archer DF, Owens CD, Barnhart KT, Bradley LD, Feinberg E, Gillispie V, Hurtado S, Kim JH, Wang A, Wang H, Stewart EA. Efficacy and safety of elagolix with add-back therapy in women with uterine fibroids and coexisting adenomyosis. F S Rep. 2021 May 26;2(3):338-346. doi: 10.1016/j.xfre.2021.05.004. eCollection 2021 Sep.

Reference Type DERIVED
PMID: 34553161 (View on PubMed)

Beck D, Winzenborg I, Gao W, Mostafa NM, Noertersheuser P, Chiuve SE, Owens C, Shebley M. Integrating real-world data and modeling to project changes in femoral neck bone mineral density and fracture risk in premenopausal women. Clin Transl Sci. 2021 Jul;14(4):1452-1463. doi: 10.1111/cts.13006. Epub 2021 Apr 8.

Reference Type DERIVED
PMID: 33650259 (View on PubMed)

Al-Hendy A, Bradley L, Owens CD, Wang H, Barnhart KT, Feinberg E, Schlaff WD, Puscheck EE, Wang A, Gillispie V, Hurtado S, Muneyyirci-Delale O, Archer DF, Carr BR, Simon JA, Stewart EA. Predictors of response for elagolix with add-back therapy in women with heavy menstrual bleeding associated with uterine fibroids. Am J Obstet Gynecol. 2021 Jan;224(1):72.e1-72.e50. doi: 10.1016/j.ajog.2020.07.032. Epub 2020 Jul 20.

Reference Type DERIVED
PMID: 32702363 (View on PubMed)

Schlaff WD, Ackerman RT, Al-Hendy A, Archer DF, Barnhart KT, Bradley LD, Carr BR, Feinberg EC, Hurtado SM, Kim J, Liu R, Mabey RG Jr, Owens CD, Poindexter A, Puscheck EE, Rodriguez-Ginorio H, Simon JA, Soliman AM, Stewart EA, Watts NB, Muneyyirci-Delale O. Elagolix for Heavy Menstrual Bleeding in Women with Uterine Fibroids. N Engl J Med. 2020 Jan 23;382(4):328-340. doi: 10.1056/NEJMoa1904351.

Reference Type DERIVED
PMID: 31971678 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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M12-815

Identifier Type: -

Identifier Source: org_study_id

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