Efficacy and Safety of Elagolix in Combination With Estradiol/Norethindrone Acetate for the Management of Heavy Menstrual Bleeding Associated With Uterine Fibroids in Premenopausal Women (Replicate Study)

NCT ID: NCT02691494

Last Updated: 2021-07-13

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

378 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-02-03

Study Completion Date

2019-01-23

Brief Summary

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This study seeks to evaluate the efficacy, safety and tolerability of elagolix alone and in combination with estradiol/norethindrone acetate for the management of heavy menstrual bleeding associated with uterine fibroids in premenopausal women.

Detailed Description

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Conditions

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Uterine Fibroids Heavy Menstrual Bleeding

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Placebo for both elagolix twice daily (BID) and norethindrone acetate (E2/ NETA) once daily (QD)

Group Type PLACEBO_COMPARATOR

Placebo for Estradiol/Norethindrone Acetate

Intervention Type DRUG

Placebo capsules

Placebo for Elagolix

Intervention Type DRUG

Film-coated placebo tablets

Elagolix

Elagolix 300 mg BID and placebo for E2/NETA (estradiol 1.0 mg/norethindrone acetate 0.5 mg) QD

Group Type EXPERIMENTAL

Elagolix

Intervention Type DRUG

Film-coated tablets

Placebo for Estradiol/Norethindrone Acetate

Intervention Type DRUG

Placebo capsules

Elagolix + E2/NETA

Elagolix 300 mg BID and E2/NETA (estradiol 1.0 mg/norethindrone acetate 0.5 mg) QD

Group Type EXPERIMENTAL

Elagolix

Intervention Type DRUG

Film-coated tablets

Estradiol/Norethindrone Acetate

Intervention Type DRUG

Commercially-available E2/NETA tablets were over-encapsulated to maintain study blinding.

Interventions

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Elagolix

Film-coated tablets

Intervention Type DRUG

Placebo for Estradiol/Norethindrone Acetate

Placebo capsules

Intervention Type DRUG

Estradiol/Norethindrone Acetate

Commercially-available E2/NETA tablets were over-encapsulated to maintain study blinding.

Intervention Type DRUG

Placebo for Elagolix

Film-coated placebo tablets

Intervention Type DRUG

Other Intervention Names

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ABT-620 elagolix sodium E2/NETA

Eligibility Criteria

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Inclusion Criteria

* Subject is a premenopausal female at the time of Screening.
* Subject has a diagnosis of uterine fibroids documented by a pelvic ultrasound (transabdominal ultrasound/transvaginal ultrasound).
* Subject has heavy menstrual bleeding associated with uterine fibroids as evidenced by menstrual blood loss \> 80 mL during each of two screening menses as measured by the alkaline hematin method.
* Subject has negative urine and/or serum pregnancy test in Screening and just prior to first dose.
* Subject has an adequate endometrial biopsy performed during Screening, the results of which show no clinically significant endometrial pathology.

Exclusion Criteria

* Subject has screening pelvic ultrasound or saline infusion sonohysterography results that show a clinically significant gynecological disorder.
* Subject has history of osteoporosis or other metabolic bone disease.
* Subject has clinically significant abnormalities in clinical chemistry, hematology, or urinalysis.
* Subject has a history of major depression or post-traumatic stress disorder (PTSD) within 2 years of screening, OR a history of other major psychiatric disorder at any time (e.g., schizophrenia, bipolar disorder).
* Subject is using any systemic corticosteroids for over 14 days within 3 months prior to Screening or is likely to require treatment with systemic corticosteroids during the course of the study. Over the counter and prescription topical, inhaled, intranasal or injectable (for occasional use) corticosteroids are allowed.
Minimum Eligible Age

18 Years

Maximum Eligible Age

51 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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AbbVie Inc.

Role: STUDY_DIRECTOR

AbbVie

Locations

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Alabama Clinical Therapeutics, LLC /ID# 152258

Birmingham, Alabama, United States

Site Status

Choice Research, LLC /ID# 150988

Dothan, Alabama, United States

Site Status

Brown, Pearson, Guepet Gynecology /ID# 151020

Fairhope, Alabama, United States

Site Status

Mobile, Ob-Gyn, P.C. /ID# 144294

Mobile, Alabama, United States

Site Status

Mesa Obstetricians and Gynecol /ID# 149139

Mesa, Arizona, United States

Site Status

Visions Clinical Research-Tucs /ID# 151017

Tucson, Arizona, United States

Site Status

Core Healthcare Group /ID# 151016

Cerritos, California, United States

Site Status

Diagnamics Inc. /ID# 152469

Encinitas, California, United States

Site Status

HCP Clinical Research LLC /ID# 154434

Huntington Beach, California, United States

Site Status

Alliance Research Centers /ID# 149752

Laguna Hills, California, United States

Site Status

University of California, Los Angeles /ID# 149760

Los Angeles, California, United States

Site Status

Futura Research, Inc. /ID# 149759

Norwalk, California, United States

Site Status

Farid Yasharpour MD Medical Co /ID# 149770

San Fernando, California, United States

Site Status

Clinical Trial Investigators /ID# 152470

Tustin, California, United States

Site Status

Bayview Research Group LLC /ID# 153799

Valley Village, California, United States

Site Status

Emerson Clinical Research Inst /ID# 152348

Washington D.C., District of Columbia, United States

Site Status

Ideal Clinical Research Inc. /ID# 149757

Aventura, Florida, United States

Site Status

Seffner Premier Health Care, P /ID# 167480

Brandon, Florida, United States

Site Status

Olympian Clinical Research /ID# 149756

Clearwater, Florida, United States

Site Status

KO Clinical Research, LLC /ID# 144299

Fort Lauderdale, Florida, United States

Site Status

University of Florida /ID# 149751

Gainesville, Florida, United States

Site Status

Solutions Through Adv Rch /ID# 151021

Jacksonville, Florida, United States

Site Status

Meridien Research /ID# 167100

Kenneth City, Florida, United States

Site Status

Invictus Clinical Research Group,LLC /ID# 141859

Miami, Florida, United States

Site Status

Precision Research Org, LLC /ID# 144335

Miami Lakes, Florida, United States

Site Status

Suncoast Clinical Research /ID# 149765

New Port Richey, Florida, United States

Site Status

All Wmns HC of West Broward /ID# 144298

Plantation, Florida, United States

Site Status

Oncova Clinical Research, Inc. /ID# 149764

Saint Cloud, Florida, United States

Site Status

Physician Care Clin. Res., LLC /ID# 149766

Sarasota, Florida, United States

Site Status

Qps-Mra, Llc /Id# 144325

South Miami, Florida, United States

Site Status

Martin Health System Center /ID# 152263

Stuart, Florida, United States

Site Status

University of South Florida /ID# 149754

Tampa, Florida, United States

Site Status

Axcess Medical Research /ID# 149769

Wellington, Florida, United States

Site Status

Virtus Research Consultant,LLC /ID# 144296

Wellington, Florida, United States

Site Status

Paramount Research Solutions /ID# 149291

Alpharetta, Georgia, United States

Site Status

Agile Clinical Research Trials /ID# 167074

Atlanta, Georgia, United States

Site Status

Mount Vernon Clinical Res, LLC /ID# 144297

Atlanta, Georgia, United States

Site Status

Atlanta Women's Research Inst /ID# 144303

Atlanta, Georgia, United States

Site Status

Masters of Clinical Research, Inc. /ID# 167400

Augusta, Georgia, United States

Site Status

Georgia Regents University /ID# 144295

Augusta, Georgia, United States

Site Status

Meridian Clinical Research, LLC /ID# 149144

Savannah, Georgia, United States

Site Status

Gyn-Care, Inc. /ID# 149341

Smyrna, Georgia, United States

Site Status

Atlanta Gynecology Research Institute /ID# 151014

Suwanee, Georgia, United States

Site Status

Womens Healthcare Assoc, DBA /ID# 149762

Idaho Falls, Idaho, United States

Site Status

Advanced Clinical Research /ID# 149767

Meridian, Idaho, United States

Site Status

University of Chicago /ID# 152257

Chicago, Illinois, United States

Site Status

Affinity Clinical Research /ID# 167119

Oak Brook, Illinois, United States

Site Status

Center for Women's Research, Inc /ID# 144300

Palos Heights, Illinois, United States

Site Status

Women's Health Advantage /ID# 144301

Fort Wayne, Indiana, United States

Site Status

The Iowa Clinic /ID# 150105

West Des Moines, Iowa, United States

Site Status

PRN Professional Research Network of Kansas, LLC /ID# 152265

Wichita, Kansas, United States

Site Status

Bluegrass Clinical Research /ID# 150103

Louisville, Kentucky, United States

Site Status

Clinical Trials Management, LLC - Covington /ID# 144314

Covington, Louisiana, United States

Site Status

Women Under Study, LLC /ID# 144312

New Orleans, Louisiana, United States

Site Status

Baltimore Suburban Health /ID# 154638

Baltimore, Maryland, United States

Site Status

Womens Health Center /ID# 154209

Glen Burnie, Maryland, United States

Site Status

Maryland Ctr for Sexual Health /ID# 149778

Lutherville, Maryland, United States

Site Status

NECCR Fall River LLC /ID# 149584

Fall River, Massachusetts, United States

Site Status

Saginaw Valley Med Res Group /ID# 149768

Saginaw, Michigan, United States

Site Status

Accent Clinical Trials /ID# 149753

Las Vegas, Nevada, United States

Site Status

Jersey Shore University Medical Center /ID# 149779

Neptune City, New Jersey, United States

Site Status

Rowan University SOM /ID# 152697

Stratford, New Jersey, United States

Site Status

SUNY Downstate Medical Center /ID# 144311

Brooklyn, New York, United States

Site Status

Manhattan Medical Research /ID# 167077

New York, New York, United States

Site Status

Weill Cornell Medicine /ID# 149585

New York, New York, United States

Site Status

Montefiore Medical Center /ID# 149582

The Bronx, New York, United States

Site Status

Duplicate_Unified Women's Clinical Research-Fayetteville /ID# 149587

Fayetteville, North Carolina, United States

Site Status

Unified Women's Clinical Research-Greensboro /ID# 149588

Greensboro, North Carolina, United States

Site Status

Pinewest Ob-Gyn, Inc. /ID# 145671

High Point, North Carolina, United States

Site Status

Eastern Carolina Women's Centr /ID# 144309

New Bern, North Carolina, United States

Site Status

Wake Research Associates, LLC /ID# 144307

Raleigh, North Carolina, United States

Site Status

Clinical Inquest Center Ltd /ID# 148728

Beavercreek, Ohio, United States

Site Status

CTI Clinical Research Center /ID# 149761

Cincinnati, Ohio, United States

Site Status

The Christ Hospital /ID# 150104

Cincinnati, Ohio, United States

Site Status

Alpha Research Associates LLC /ID# 152471

Dayton, Ohio, United States

Site Status

Comprehensive Womens Care /ID# 144306

Westerville, Ohio, United States

Site Status

Family Medical Associates /ID# 145668

Levittown, Pennsylvania, United States

Site Status

University of Pennsylvania /ID# 149586

Philadelphia, Pennsylvania, United States

Site Status

Clinical Research of Philadelphia, LLC /ID# 151015

Philadelphia, Pennsylvania, United States

Site Status

Reading Hosp Clncl Trials Ofc /ID# 149583

West Reading, Pennsylvania, United States

Site Status

Holston Medical Group /ID# 149763

Bristol, Tennessee, United States

Site Status

Chattanooga Medical Research /ID# 145667

Chattanooga, Tennessee, United States

Site Status

Chattanooga Women for Women /ID# 167051

Hixson, Tennessee, United States

Site Status

The Jackson Clinic, PA /ID# 145670

Jackson, Tennessee, United States

Site Status

The Womens Physician Group /ID# 144317

Memphis, Tennessee, United States

Site Status

Access Clinical Trials, Inc. /ID# 167333

Nashville, Tennessee, United States

Site Status

Lotus Gynecology /ID# 149140

Austin, Texas, United States

Site Status

Inquest Clinical Research /ID# 149755

Baytown, Texas, United States

Site Status

Texas Health Presbyterian Hosp /ID# 149142

Dallas, Texas, United States

Site Status

Baylor College of Medicine /ID# 149141

Houston, Texas, United States

Site Status

The Woman's Hospital of Texas /ID# 144319

Houston, Texas, United States

Site Status

Centex Studies, Inc. - Houston /ID# 150106

Houston, Texas, United States

Site Status

BI Research Center /ID# 149143

Houston, Texas, United States

Site Status

FMC Science /ID# 151802

Lampasas, Texas, United States

Site Status

Willowbend Health and Wellness /ID# 144318

Plano, Texas, United States

Site Status

Clinical Trials of Texas,Inc. /ID# 144322

San Antonio, Texas, United States

Site Status

Center of Reproductive Medicin /ID# 167235

Webster, Texas, United States

Site Status

Southampton Women's Health /ID# 152325

Franklin, Virginia, United States

Site Status

Tidewater Physicians for Women /ID# 144321

Norfolk, Virginia, United States

Site Status

Clinical Research Partners, LLC /ID# 144310

Richmond, Virginia, United States

Site Status

Alliance Womens Health /ID# 152468

Richmond, Virginia, United States

Site Status

Zain Research /ID# 151018

Richland, Washington, United States

Site Status

Virginia Mason Medical Center /ID# 149758

Seattle, Washington, United States

Site Status

Medicor Research Inc. /ID# 153406

Greater Sudbury, Ontario, Canada

Site Status

Victory Reproductive Care /ID# 150247

Windsor, Ontario, Canada

Site Status

Countries

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United States Canada

References

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Simon JA, Stewart EA, Jewell S, Li M, Snabes MC. Impact of demographic and clinical factors on elagolix plus add-back therapy effects on patient-reported nonbleeding symptoms in women with heavy menstrual bleeding and uterine fibroids: a post hoc analysis of data from two clinical trials. F S Rep. 2024 Jun 14;5(3):285-295. doi: 10.1016/j.xfre.2024.06.002. eCollection 2024 Sep.

Reference Type DERIVED
PMID: 39381651 (View on PubMed)

Beck D, Winzenborg I, Liu M, Degner J, Mostafa NM, Noertersheuser P, Shebley M. Population Pharmacokinetics of Elagolix in Combination with Low-Dose Estradiol/Norethindrone Acetate in Women with Uterine Fibroids. Clin Pharmacokinet. 2022 Apr;61(4):577-587. doi: 10.1007/s40262-021-01096-w. Epub 2021 Dec 8.

Reference Type DERIVED
PMID: 34878624 (View on PubMed)

Stewart EA, Archer DF, Owens CD, Barnhart KT, Bradley LD, Feinberg EC, Gillispie-Bell V, Imudia AN, Liu R, Kim JH, Al-Hendy A. Reduction of Heavy Menstrual Bleeding in Women Not Designated as Responders to Elagolix Plus Add Back Therapy for Uterine Fibroids. J Womens Health (Larchmt). 2022 May;31(5):698-705. doi: 10.1089/jwh.2021.0152. Epub 2021 Sep 28.

Reference Type DERIVED
PMID: 34582715 (View on PubMed)

Muneyyirci-Delale O, Archer DF, Owens CD, Barnhart KT, Bradley LD, Feinberg E, Gillispie V, Hurtado S, Kim JH, Wang A, Wang H, Stewart EA. Efficacy and safety of elagolix with add-back therapy in women with uterine fibroids and coexisting adenomyosis. F S Rep. 2021 May 26;2(3):338-346. doi: 10.1016/j.xfre.2021.05.004. eCollection 2021 Sep.

Reference Type DERIVED
PMID: 34553161 (View on PubMed)

Beck D, Winzenborg I, Gao W, Mostafa NM, Noertersheuser P, Chiuve SE, Owens C, Shebley M. Integrating real-world data and modeling to project changes in femoral neck bone mineral density and fracture risk in premenopausal women. Clin Transl Sci. 2021 Jul;14(4):1452-1463. doi: 10.1111/cts.13006. Epub 2021 Apr 8.

Reference Type DERIVED
PMID: 33650259 (View on PubMed)

Schlaff WD, Ackerman RT, Al-Hendy A, Archer DF, Barnhart KT, Bradley LD, Carr BR, Feinberg EC, Hurtado SM, Kim J, Liu R, Mabey RG Jr, Owens CD, Poindexter A, Puscheck EE, Rodriguez-Ginorio H, Simon JA, Soliman AM, Stewart EA, Watts NB, Muneyyirci-Delale O. Elagolix for Heavy Menstrual Bleeding in Women with Uterine Fibroids. N Engl J Med. 2020 Jan 23;382(4):328-340. doi: 10.1056/NEJMoa1904351.

Reference Type DERIVED
PMID: 31971678 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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M12-817

Identifier Type: -

Identifier Source: org_study_id

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