A Study Evaluating Venetoclax Alone and in Combination With Azacitidine in Participants With Relapsed/Refractory Myelodysplastic Syndromes (MDS)

NCT ID: NCT02966782

Last Updated: 2023-05-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

70 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-03-07

Study Completion Date

2023-04-05

Brief Summary

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This is a Phase 1b, open-label, multicenter study designed to evaluate the safety and pharmacokinetics of venetoclax as a single-agent and in combination with azacitidine in participants with relapsed/refractory Myelodysplastic Syndromes (MDS).

Detailed Description

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Conditions

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Myelodysplastic Syndromes (MDS)

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Venetoclax monotherapy (Cohort 1)

Group Type EXPERIMENTAL

venetoclax

Intervention Type DRUG

Tablet

Venetoclax + azacitidine (Cohort 2)

Group Type EXPERIMENTAL

venetoclax

Intervention Type DRUG

Tablet

azacitidine

Intervention Type DRUG

Powder for injection, subcutaneously or intravenous

Safety Expansion (Cohort 3)

Group Type EXPERIMENTAL

venetoclax

Intervention Type DRUG

Tablet

azacitidine

Intervention Type DRUG

Powder for injection, subcutaneously or intravenous

Interventions

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venetoclax

Tablet

Intervention Type DRUG

azacitidine

Powder for injection, subcutaneously or intravenous

Intervention Type DRUG

Other Intervention Names

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ABT-199 GDC-0199 Vidaza

Eligibility Criteria

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Inclusion Criteria

* Subjects who have relapsed or refractory MDS.
* Subject enrolled in venetoclax monotherapy must have documented failure of prior therapy with a hypomethylating agent (HMA). HMA-failure is defined as:

1. Relapse after initial complete or partial response or hematological improvement after at least 4 cycles of azacitidine or at least 4 cycles of decitabine within the last 5 years, OR
2. Failure to achieve complete or partial response or hematological improvement after at least 4 cycles of azacitidine or at least 4 cycles of decitabine within the last 5 years
* Subjects must have presence of \< 20% bone marrow blasts per bone marrow biopsy/aspirate at screening.
* Subject is not a candidate to undergo allogenic hematopoietic stem cell transplantation (HSCT).
* Subject must have an Eastern Cooperative Oncology Group (ECOG) performance score of ≤2.
* Subject must have adequate hematologic, renal, and hepatic function.

Exclusion Criteria

* Subject has received prior therapy with a BH3 mimetic.
* Subject has MDS evolving from a pre-existing myeloproliferative neoplasm (MPN).
* Subject has MDS/MPN including chronic myelomonocytic leukemia (CMML), atypical chronic myeloid leukemia (CML), juvenile myelomonocytic leukemia (JMML) and unclassifiable MDS/MPN.
* Subject has received allogeneic HSCT or solid organ transplantation.
* Subject has received a live attenuated vaccine within 4 weeks prior to the first dose of study drug.
* Subject is pregnant or breastfeeding.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Celgene; Genentech, Inc.

UNKNOWN

Sponsor Role collaborator

AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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ABBVIE INC.

Role: STUDY_DIRECTOR

AbbVie

Locations

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University of Arizona Cancer Center - North Campus /ID# 157503

Tucson, Arizona, United States

Site Status

University of Colorado Hospital /ID# 155365

Aurora, Colorado, United States

Site Status

Yale University /ID# 162544

New Haven, Connecticut, United States

Site Status

Duplicate_University of Chicago /ID# 155364

Chicago, Illinois, United States

Site Status

Pediatric Endocrine Associates /ID# 171227

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute /ID# 155361

Boston, Massachusetts, United States

Site Status

University of Massachusetts - Worcester /ID# 155366

Worcester, Massachusetts, United States

Site Status

Columbia Univ Medical Center /ID# 156388

New York, New York, United States

Site Status

Oregon Health and Science University /ID# 155360

Portland, Oregon, United States

Site Status

University of Texas MD Anderson Cancer Center /ID# 155362

Houston, Texas, United States

Site Status

St George Hospital /ID# 156037

Kogarah, New South Wales, Australia

Site Status

Liverpool Hospital /ID# 155952

Liverpool, New South Wales, Australia

Site Status

St Vincent's Hospital Melbourne /ID# 155950

Fitzroy Melbourne, Victoria, Australia

Site Status

The Royal Melbourne Hospital /ID# 155949

Parkville, Victoria, Australia

Site Status

Royal Perth Hospital /ID# 155951

Perth, Western Australia, Australia

Site Status

Universitatsklinikum Mannheim /ID# 156038

Mannheim, Baden-Wurttemberg, Germany

Site Status

Universitaetsklinikum Koeln /ID# 155519

Cologne, North Rhine-Westphalia, Germany

Site Status

Universitaetsklinikum Duesseldorf /ID# 154899

Düsseldorf, North Rhine-Westphalia, Germany

Site Status

Marien Hospital Duesseldorf /ID# 155518

Düsseldorf, North Rhine-Westphalia, Germany

Site Status

Universitaetsklinikum Leipzig /ID# 154897

Leipzig, Saxony, Germany

Site Status

Universitaetsklinikum Carl Gustav Carus an der TU Dresden /ID# 154898

Dresden, , Germany

Site Status

Universitaetsklinikum Halle (Saale) /ID# 158643

Halle, , Germany

Site Status

Klinikum rechts der Isar - Technische Universitaet Muenchen /ID# 154896

Munich, , Germany

Site Status

Countries

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United States Australia Germany

References

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Zeidan AM, Borate U, Pollyea DA, Brunner AM, Roncolato F, Garcia JS, Filshie R, Odenike O, Watson AM, Krishnadasan R, Bajel A, Naqvi K, Zha J, Cheng WH, Zhou Y, Hoffman D, Harb JG, Potluri J, Garcia-Manero G. A phase 1b study of venetoclax and azacitidine combination in patients with relapsed or refractory myelodysplastic syndromes. Am J Hematol. 2023 Feb;98(2):272-281. doi: 10.1002/ajh.26771. Epub 2022 Nov 10.

Reference Type DERIVED
PMID: 36309981 (View on PubMed)

Franke GN, Luckemeier P, Platzbecker U. Allogeneic Stem-Cell Transplantation in Patients With Myelodysplastic Syndromes and Prevention of Relapse. Clin Lymphoma Myeloma Leuk. 2021 Jan;21(1):1-7. doi: 10.1016/j.clml.2020.10.008. Epub 2020 Oct 16.

Reference Type DERIVED
PMID: 33191169 (View on PubMed)

Other Identifiers

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2016-001904-46

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

M15-522

Identifier Type: -

Identifier Source: org_study_id

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