Randomized Trial of Crenolanib in Subjects With D842V Mutated GIST

NCT ID: NCT02847429

Last Updated: 2021-01-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

120 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-08-31

Study Completion Date

2021-08-31

Brief Summary

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This is a multicenter, randomized, double-blinded, placebo-controlled, trial of oral crenolanib versus oral placebo in combination with best supportive care in subjects with advanced or metastatic GIST with a D842V mutation in the PDGFRA gene. Approximately 120 subjects will be randomized in a 2:1 ratio to receive either crenolanib 100 mg or matching placebo orally (PO) 3 times daily (TID) in combination with best supportive care.

Detailed Description

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Conditions

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GIST With D842V Mutated PDGFRA Gene

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Crenolanib Arm

Investigational product (crenolanib)

Group Type EXPERIMENTAL

Crenolanib

Intervention Type DRUG

Placebo Arm

Matching placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Interventions

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Crenolanib

Intervention Type DRUG

Placebo

Intervention Type DRUG

Other Intervention Names

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Crenolanib Besylate

Eligibility Criteria

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Inclusion Criteria

1. Histologically or cytologically-confirmed advanced or metastatic GIST with a D842V mutation in the PDGFRA gene as determined by central laboratory testing
2. Measurable disease as per modified RECIST 1.1

• A lesion in an area that was previously treated with local therapy (e.g. radiation, surgery, or cryotherapy) can be considered measurable disease as long as there is objective evidence of progression of the lesion prior to randomization
3. Subjects (male or female) ≥ 18 years of age
4. Female subjects with reproductive potential must have negative serum or urine pregnancy test
5. Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2

Exclusion Criteria

1. Severe liver disease (e.g. cirrhosis, non-alcoholic steatohepatitis, sclerosing cholangitis)
2. Known, active infection with hepatitis B virus (HBV) or hepatitis C virus (HCV)
3. Female subject who is pregnant or breastfeeding, or planning to become pregnant within 30 days after ending treatment
4. Systemic anti-cancer treatment (e.g. chemotherapy, tyrosine kinase inhibitors, immunotherapy, or investigational agents) or investigational device within 3 weeks or 5 half-lives (if the drug's half-life in subject is known) prior to randomization, whichever is shorter
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Centre Leon Berard

OTHER

Sponsor Role collaborator

Fox Chase Cancer Center

OTHER

Sponsor Role collaborator

Arog Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jean-Yves Blay, MD

Role: PRINCIPAL_INVESTIGATOR

Centre Leon Berard

Margaret von Mehren, MD

Role: PRINCIPAL_INVESTIGATOR

Fox Chase Cancer Center

Locations

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Sarcoma Oncology Center

Santa Monica, California, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Duke Cancer Institute

Durham, North Carolina, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Institut Bergonie

Bordeaux, , France

Site Status

Centre Leon Berard

Lyon, , France

Site Status

La Timone University Hospital

Marseille, , France

Site Status

Centre Hospitalier Universitaire (CHU) de Reims

Reims, , France

Site Status

HELIOS Klinikum Berlin-Buch

Berlin, , Germany

Site Status

Mannheim University Medical Centre, University of Heidelberg

Mannheim, , Germany

Site Status

Universitätsklinikum München

Munich, , Germany

Site Status

Policlinico S. Orsola-Malpighi

Bologna, , Italy

Site Status

Istituto Nazionale Tumori

Milan, , Italy

Site Status

Institut Regina Elena / IFO

Rome, , Italy

Site Status

Candiolo Cancer Institute - FPO, IRCCS

Turin, , Italy

Site Status

University Hospital The Norwegian Radium Hospital

Oslo, , Norway

Site Status

M Sklodowska-Curie Memorial Cancer Centre and Institute of Oncology

Warsaw, , Poland

Site Status

Vall d'Hebron University Hospital

Barcelona, , Spain

Site Status

Hospital Universitario Puerta de Hierro

Madrid, , Spain

Site Status

Hospital Virgen del Rocio

Seville, , Spain

Site Status

Fundación Instituto Valenciano de Oncología

Valencia, , Spain

Site Status

Countries

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United States France Germany Italy Norway Poland Spain

Other Identifiers

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2015-000287-34

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ARO-012

Identifier Type: -

Identifier Source: org_study_id

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