A Study of Nilotinib Versus Imatinib in GIST Patients

NCT ID: NCT00785785

Last Updated: 2016-06-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

644 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-03-31

Study Completion Date

2014-10-31

Brief Summary

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This study will evaluate efficacy and safety of nilotinib versus imatinib in adult patients with unresectable or metastatic gastrointestinal stromal tumors (GIST).

Detailed Description

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Conditions

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Gastrointestinal Stromal Tumor (GIST)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Nilotinib

nilotinib 400 mg twice a day

Group Type EXPERIMENTAL

Nilotinib (AMN107)

Intervention Type DRUG

Imatinib

imatinib 400 mg once daily

Group Type ACTIVE_COMPARATOR

imatinib (STI571)

Intervention Type DRUG

Interventions

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Nilotinib (AMN107)

Intervention Type DRUG

imatinib (STI571)

Intervention Type DRUG

Other Intervention Names

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Glivec/Gleevec

Eligibility Criteria

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Inclusion Criteria

1. Histologically confirmed diagnosis of GIST which is unresectable and/or metastatic and either:

* have not received any prior anti-neoplastic therapy other than adjuvant imatinib. Note: newly diagnosed patients may have received up to 14 days of treatment with imatinib for disease management while awaiting entry to the study or
* recurrent GIST after stopping adjuvant treatment with imatinib and no subsequent treatment with any other therapies.
2. At least one measurable site of disease on CT/MRI scan
3. Performance status ≤ 2 (capable of self-care but unable to carry out any work)
4. Normal organ, electrolyte and marrow function

Exclusion Criteria

1. Any prior anti-neoplastic therapy with the exception of patients who have received adjuvant imatinib or patients with newly diagnosed metastatic/ unresectable GIST whose disease requires therapy while awaiting entry to the study.
2. Disease progression during adjuvant therapy with imatinib
3. History of active malignancy (other than GIST) within 10 years prior to study entry with the exception of previous or concomitant basal cell skin cancer, previous cervical carcinoma in situ.
4. Impaired cardiac function
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Birmingham Hematology and Oncology Associates

Birmingham, Alabama, United States

Site Status

Northern Arizona Hematology/Oncology Associates, P.C. Dept. of No. AZ Hem-Onc

Flagstaff, Arizona, United States

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City of Hope National Medical Center Dept.ofCityofHopeMedicalCtr(4)

Duarte, California, United States

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City of Hope National Medical Center Regulatory Document

Duarte, California, United States

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University of California San Diego - Moores Cancer Center Dept of Moores Cancer Ctr (2)

La Jolla, California, United States

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University of California at Los Angeles GI Oncology Program

Los Angeles, California, United States

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Stanford University Medical Center Stanford Cancer Center

Stanford, California, United States

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University of Colorado Dept. of Univ. of Colorado

Aurora, Colorado, United States

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Rocky Mountain Cancer Centers Dept. of Rocky Mountain Cancer

Greenwood Village, Colorado, United States

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Washington Hospital Center Wash Hospital

Washington D.C., District of Columbia, United States

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Ocala Oncology Center Dept. of Ocala Oncology Center

Ocala, Florida, United States

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Kootenai Medical Center Dept.ofKootenai Med.Ctr.

Coeur d'Alene, Idaho, United States

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Northwestern University Clinical Research Office (2)

Chicago, Illinois, United States

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Dana Farber Cancer Institute Centerfor Sarcoma&BoneOncology

Boston, Massachusetts, United States

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University of Michigan Comprehensive Cancer Center DeptofMichiganCancerCenter(6)

Ann Arbor, Michigan, United States

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Minnesota Oncology Hematology, P.A. SC

Minneapolis, Minnesota, United States

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Mayo Clinic - Rochester Division of Hematology

Rochester, Minnesota, United States

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New York Oncology Hematology, P.C. NYOH Amsterdam

Troy, New York, United States

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New York Oncology Hematology, P.C. NYOH@AlbanyMedicalCenter(2)

Troy, New York, United States

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University of Pennsylvania Medical Center CAMN107G2301

Philadelphia, Pennsylvania, United States

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Vanderbilt Univeristy Ingram Cancer Ctr.

Nashville, Tennessee, United States

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Texas Oncology, P.A. Tex Onc (2)

Bedford, Texas, United States

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Texas Oncology Wichita Falls

Dallas, Texas, United States

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University of Texas Southwestern Medical Center DeptofSimmons Cancer Center(3)

Dallas, Texas, United States

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University of Texas/MD Anderson Cancer Center Dept. of MD Anderson (13)

Houston, Texas, United States

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Cancer Care Centers of South Texas / HOAST CCC of So. TX- San Antonio(2)

San Antonio, Texas, United States

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Tyler Cancer Center Dept.ofTylerCancerCtr. (2)

Tyler, Texas, United States

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University of Utah / Huntsman Cancer Institute Dept.ofHuntsmanCancerInst.(3)

Salt Lake City, Utah, United States

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Novartis Investigative Site

Buenos Aires, Buenos Aires, Argentina

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Caba, Buenos Aires, Argentina

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Rosario, Santa Fe Province, Argentina

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Innsbruck, Tyrol, Austria

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Graz, , Austria

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Leoben, , Austria

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Vienna, , Austria

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Wels, , Austria

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Uberlândia, Minas Gerais, Brazil

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Florianópolis, Santa Catarina, Brazil

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Campinas, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Sofia, , Bulgaria

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Varna, , Bulgaria

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Vancouver, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Hamilton, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Beijing, Beijing Municipality, China

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Nanjing, Jiangsu, China

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Beijing, , China

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Guangzhou, , China

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Shanghai, , China

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Shanghai, , China

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Pereira, , Colombia

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Olomouc, , Czechia

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Århus C, , Denmark

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Herlev, , Denmark

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Alexandria, , Egypt

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Cairo, , Egypt

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Bordeaux, , France

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Chambray-lès-Tours, , France

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Lyon, , France

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Paris, , France

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Saint-Herblain Cédex, , France

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Toulouse, , France

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Vandœuvre-lès-Nancy, , France

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Villejuif, , France

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Bad Saarow, , Germany

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Düsseldorf, , Germany

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Essen, , Germany

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Hanover, , Germany

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Mannheim, , Germany

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München, , Germany

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Weiden, , Germany

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Hong Kong SAR, , Hong Kong

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Budapest, , Hungary

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Budapest, , Hungary

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Haifa, , Israel

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Ramat Gan, , Israel

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Bologna, BO, Italy

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San Giovanni Rotondo, FG, Italy

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Florence, FI, Italy

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Genova, GE, Italy

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Milan, MI, Italy

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Modena, MO, Italy

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Palermo, PA, Italy

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Aviano, PN, Italy

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Candiolo, TO, Italy

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Torino, TO, Italy

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Nagoya, Aichi-ken, Japan

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Kashiwa, Chiba, Japan

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Fukuoka, Fukuoka, Japan

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Gifu, Gifu, Japan

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Sapporo, Hokkaido, Japan

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Yokohama, Kanagawa, Japan

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Kumamoto, Kumamoto, Japan

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Sendai, Miyagi, Japan

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Niigata, Niigata, Japan

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Kurashiki, Okayama-ken, Japan

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Osaka, Osaka, Japan

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Suita, Osaka, Japan

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Sunto-gun, Shizuoka, Japan

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Chuo-ku, Tokyo, Japan

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Toyama, Toyama, Japan

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Chihuahua City, Chihuahua, Mexico

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León, Guanajuato, Mexico

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Mexico City, Mexico City, Mexico

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Leiden, , Netherlands

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Oslo, , Norway

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Krakow, , Poland

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Warsaw, , Poland

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Craiova, Dolj, Romania

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Iași, , Romania

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Kazan', Tatarstan Republic, Russia

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Moscow, , Russia

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Saint Petersburg, , Russia

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Yekaterinburg, , Russia

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Singapore, Singapore, Singapore

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Singapore, Singapore, Singapore

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Bratislava, Slovak Republic, Slovakia

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Cape Town, , South Africa

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Johannesburg, , South Africa

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Pretoria, , South Africa

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Pretoria, , South Africa

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Pretoria, , South Africa

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Suwon, Gyeonggi-do, South Korea

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Seoul, Korea, South Korea

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Seoul, Korea, South Korea

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Barcelona, Barcelona, Spain

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Sabadell, Barcelona, Spain

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Madrid, Madrid, Spain

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Oviedo, Principality of Asturias, Spain

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Gothenburg, , Sweden

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Linköping, , Sweden

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Lund, , Sweden

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Stockholm, , Sweden

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Umeå, , Sweden

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Uppsala, , Sweden

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Niaosong Township, Taiwan, Taiwan

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Taipei, Taiwan, Taiwan

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Taipei, Taiwan, ROC, Taiwan

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Linkou District, , Taiwan

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Bangkok, , Thailand

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Bangkok, , Thailand

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Khon Kaen, , Thailand

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Songkhla, , Thailand

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Adana, Turkey, Turkey (Türkiye)

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Ankara, Turkey, Turkey (Türkiye)

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Ankara, Turkey, Turkey (Türkiye)

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Izmir, Turkey, Turkey (Türkiye)

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Balcova / Izmir, , Turkey (Türkiye)

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Kartal, , Turkey (Türkiye)

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Newcastle upon Tyne, Newcastle-upon-Tyne, United Kingdom

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Cambridge, , United Kingdom

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Glasgow, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Caracas, Distrito Federal, Venezuela

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Countries

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United States Argentina Austria Brazil Bulgaria Canada China Colombia Czechia Denmark Egypt France Germany Hong Kong Hungary Israel Italy Japan Mexico Netherlands Norway Poland Romania Russia Singapore Slovakia South Africa South Korea Spain Sweden Taiwan Thailand Turkey (Türkiye) United Kingdom Venezuela

References

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Blay JY, Shen L, Kang YK, Rutkowski P, Qin S, Nosov D, Wan D, Trent J, Srimuninnimit V, Papai Z, Le Cesne A, Novick S, Taningco L, Mo S, Green S, Reichardt P, Demetri GD. Nilotinib versus imatinib as first-line therapy for patients with unresectable or metastatic gastrointestinal stromal tumours (ENESTg1): a randomised phase 3 trial. Lancet Oncol. 2015 May;16(5):550-60. doi: 10.1016/S1470-2045(15)70105-1. Epub 2015 Apr 14.

Reference Type DERIVED
PMID: 25882987 (View on PubMed)

Related Links

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http://www.novartisclinicaltrials.com/etrials/searchTrial.do?trialID=717

Visit NovartisClinicalTrials.com: Pre-qualify for a trial, and view a list of trials and participating study centers.

Other Identifiers

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2008-004758-34

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CAMN107G2301

Identifier Type: -

Identifier Source: org_study_id

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