Efficacy and Safety of Nilotinib (AMN107) Compared With Current Treatment Options in Patients With GIST Who Have Failed Both Imatinib and Sunitinib

NCT ID: NCT00471328

Last Updated: 2012-06-12

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

248 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-03-31

Study Completion Date

2011-06-30

Brief Summary

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The study evaluated the safety and efficacy of nilotinib versus current treatment in adults with gastrointestinal stromal tumors (GIST) who have either progressed or who were intolerant to the first and second line treatments.

Detailed Description

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Conditions

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Gastrointestinal Stromal Tumors

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Nilotinib

400mg twice daily in core and extension phases of the study.

Group Type EXPERIMENTAL

Nilotinib

Intervention Type DRUG

Nilotinib 400 mg twice daily (bid)

Control/cross-over to Nilotinib

In core study phase, patients in this arm received Best Supportive Care (BSC) with or without imatinib or sunitinib at the last tolerated dose or at the investigator's choice until documented disease progression followed by cross-over to nilotinib arm.

Patients entering the extension study on this control arm were permitted to cross over to nilotinib arm only upon documented disease progression.

Group Type ACTIVE_COMPARATOR

Nilotinib

Intervention Type DRUG

Nilotinib 400 mg twice daily (bid)

Best Supportive Care (BSC) +/- imatinib or sunitinib

Intervention Type OTHER

Can include pain medication, localized radiotherapy, nutritional support, and/or oxygen therapy and blood transfusions. Imatinib or sunitinib can be administered at the last tolerated dose and regimen or at the Investigator's choice.

Interventions

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Nilotinib

Nilotinib 400 mg twice daily (bid)

Intervention Type DRUG

Best Supportive Care (BSC) +/- imatinib or sunitinib

Can include pain medication, localized radiotherapy, nutritional support, and/or oxygen therapy and blood transfusions. Imatinib or sunitinib can be administered at the last tolerated dose and regimen or at the Investigator's choice.

Intervention Type OTHER

Other Intervention Names

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AMN107, Tasigna®

Eligibility Criteria

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Inclusion Criteria

* Age ≥18 years
* Radiological confirmation of disease progression during imatinib and sunitinib therapy OR intolerance to imatinib and/or sunitinib
* At least one measurable site of disease on CT/MRI scan
* Physically fit even if not able to work
* Normal organ, electrolyte, and bone marrow function


* Patients whose tumors had progressed on the control arm and had crossed over to the nilotinib arm.
* The study was stopped due to meeting the primary efficacy endpoint of PFS at the interim analysis.
* Patients who were still being treated at the close of the Core study on the control arm or nilotinib arm (whose tumors have not progressed at the time of the end of the Core study).
* Patients must have had documented, confirmed stable, partial or complete response as defined by the RECIST criteria at the time of entry into the Extension study with the exception of patients who had progressed on the control arm.

Exclusion Criteria

* Previous treatment with nilotinib or any other drug in this class or other targeted therapy
* Treatment with any cytotoxic and/or investigational cytotoxic drug ≤ 4 weeks prior to study entry
* Impaired cardiac function
* Use of coumarin derivatives (i.e. warfarin, acenocoumarol, phenprocoumon)
* Women who are pregnant or lactating


* Use of other anticancer treatments or investigational drugs (with exception of the study drugs)
* Patients with a history of noncompliance with study drug treatment in the Core study protocol.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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UCLA's Jonsson Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

Washington Hospital Center - Washington Cancer Institute

Washington D.C., District of Columbia, United States

Site Status

H. Lee Moffitt Cancer Center

Tampa, Florida, United States

Site Status

University of Chicago Hospital

Chicago, Illinois, United States

Site Status

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Wayne State University/Wertz Clinical Cancer Center

Detroit, Michigan, United States

Site Status

Washington University School of Medicine - Siteman Cancer Center

St Louis, Missouri, United States

Site Status

St. Vincent's Comprehensive Cancer Center

New York, New York, United States

Site Status

Wake Forest University Health Sciences

Winston-Salem, North Carolina, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

University of Texas/MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Novartis Investigative Site

Auchenflower, Queensland, Australia

Site Status

Novartis Investigative Site

East Melbourne, Victoria, Australia

Site Status

Novartis Investigative Site

Vienna, , Austria

Site Status

Novartis Investigative Site

Toronto, , Canada

Site Status

Novartis Investigative Site

Prague, , Czechia

Site Status

Novartis Investigative Site

Bordeaux, , France

Site Status

Novartis Investigative Site

Lyon, , France

Site Status

Novartis Investigative Site

Marseille, , France

Site Status

Novartis Investigative Site

Berlin, , Germany

Site Status

Novartis Investigative Site

Cologne, , Germany

Site Status

Novartis Investigative Site

Düsseldorf, , Germany

Site Status

Novartis Investigative Site

Essen, , Germany

Site Status

Novartis Investigative Site

Frankfurt, , Germany

Site Status

Novartis Investigative Site

Hanover, , Germany

Site Status

Novartis Investigative Site

Mannheim, , Germany

Site Status

Novartis Investigative Site

München, , Germany

Site Status

Novartis Investigative Site

Tübingen, , Germany

Site Status

Novrtis Investigative Site

Bologna, , Italy

Site Status

Novartis Investigative Site

Milan, , Italy

Site Status

Novartis Investigative Site

Leiden, , Netherlands

Site Status

Novartis Investigative Site

Warsaw, , Poland

Site Status

Novartis Investigative Site

Seoul, , South Korea

Site Status

Novartis Investigative Site

Madrid, , Spain

Site Status

Novartis Investigative Site

Chur, , Switzerland

Site Status

Countries

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United States Australia Austria Canada Czechia France Germany Italy Netherlands Poland South Korea Spain Switzerland

Other Identifiers

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2006-002267-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CAMN107A2201

Identifier Type: -

Identifier Source: org_study_id

NCT00488150

Identifier Type: -

Identifier Source: nct_alias

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