Efficacy and Safety of Ofatumumab Compared to Teriflunomide in Patients With Relapsing Multiple Sclerosis

NCT ID: NCT02792218

Last Updated: 2021-10-01

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

930 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-09-20

Study Completion Date

2020-07-20

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

To compare the efficacy and safety of ofatumumab administered subcutaneously (sc) every 4 weeks versus teriflunomide administered orally once daily in patients with relapsing multiple sclerosis

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This was a randomized, double-blind, double-dummy, active comparator-controlled, parallel-group, multi-center study with variable treatment duration in approximately 900 patients with relapsing multiple sclorosis (RMS). The maximal treatment duration in the study for an individual patient was 2.5 years.

Eligible patients were randomized to receive either experimental ofatumumab subcutaneous (s.c.) injections every 4 weeks or active comparator teriflunomide orally once daily. The dose regimen for ofatumumab for this study was a loading dose regimen of 20 mg at Day 1, Day 7 and Day 14, followed by a maintenance dose regimen of 20 mg administered every 4 weeks starting at Week 4. In order to blind for the different formulations, double-dummy masking was used i.e. all patients will take injections (containing either active ofatumumab or placebo) and oral capsules (containing either active teriflunomide or placebo).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Relapsing Multiple Sclerosis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

OMB 20 mg

Ofatumumab 20 mg pre-filled syringes for subcutaneous injectionon on days 1 ,7 ,14, week 4 and every 4 weeks thereafter and a teriflunomide- matching placebo, taken orally once daily

Group Type EXPERIMENTAL

Ofatumumab subcutaneous injection

Intervention Type DRUG

Ofatumumab 20 mg pre-filled syringes for subcutaneous injection on days 1, 7, 14, week 4 and every 4 weeks thereafter

Teriflunomide-matching placebo capsules

Intervention Type DRUG

Placebo capsule, matching in appearance to teriflunomide, taken orally once daily

TER 14 mg

Teriflunomide 14 mg oral capsule taken once daily and matching placebo for subcutaneous injections to ofatumumab on days 1, 7, 14, week 4 and every 4 weeks thereafter

Group Type ACTIVE_COMPARATOR

Teriflunomide capsule

Intervention Type DRUG

Teriflunomide 14 mg oral capsule taken once daily

Matching placebo of ofatumumab subcutaneous injections

Intervention Type DRUG

Matching placebo of ofatumumab subcutaneous injections on days 1, 7, 14, week 4 and every 4 weeks thereafter

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Ofatumumab subcutaneous injection

Ofatumumab 20 mg pre-filled syringes for subcutaneous injection on days 1, 7, 14, week 4 and every 4 weeks thereafter

Intervention Type DRUG

Teriflunomide-matching placebo capsules

Placebo capsule, matching in appearance to teriflunomide, taken orally once daily

Intervention Type DRUG

Teriflunomide capsule

Teriflunomide 14 mg oral capsule taken once daily

Intervention Type DRUG

Matching placebo of ofatumumab subcutaneous injections

Matching placebo of ofatumumab subcutaneous injections on days 1, 7, 14, week 4 and every 4 weeks thereafter

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* 18 to 55 years of age
* Diagnosis of multiple sclerosis (MS)
* Relapsing MS: relapsing-remitting MS (RRMS) or secondary progressive MS (SPMS)
* At least 1 relapse during the previous 1 year or 2 relapses during the previous 2 years or a positive gadolinium-enhancing MRI scan in previous year
* Expanded disability status scale (EDSS) score of 0 to 5.5

Exclusion Criteria

* Primary progressive MS
* Disease duration of more than 10 years in patients with an EDSS score of 2 or less
* Patients with an active chronic disease of the immune system other than MS
* Patients at risk of developing or having reactivation of hepatitis
* Patients with active systemic infections or with neurological findings consistent with PML
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Novartis Investigative Site

Phoenix, Arizona, United States

Site Status

Novartis Investigative Site

Berkeley, California, United States

Site Status

Novartis Investigative Site

Fullerton, California, United States

Site Status

Novartis Investigative Site

Sacramento, California, United States

Site Status

Novartis Investigative Site

Washington D.C., District of Columbia, United States

Site Status

Novartis Investigative Site

Atlantis, Florida, United States

Site Status

Novartis Investigative Site

Delray Beach, Florida, United States

Site Status

Novartis Investigative Site

Hollywood, Florida, United States

Site Status

Novartis Investigative Site

Loxahatchee Groves, Florida, United States

Site Status

Novartis Investigative Site

Miami, Florida, United States

Site Status

Novartis Investigative Site

Miami, Florida, United States

Site Status

Novartis Investigative Site

Naples, Florida, United States

Site Status

Novartis Investigative Site

North Palm Beach, Florida, United States

Site Status

Novartis Investigative Site

Pensacola, Florida, United States

Site Status

Novartis Investigative Site

Port Charlotte, Florida, United States

Site Status

Novartis Investigative Site

Sunrise, Florida, United States

Site Status

Novartis Investigative Site

Vero Beach, Florida, United States

Site Status

Novartis Investigative Site

West Palm Beach, Florida, United States

Site Status

Novartis Investigative Site

Savannah, Georgia, United States

Site Status

Novartis Investigative Site

Honolulu, Hawaii, United States

Site Status

Novartis Investigative Site

Chicago, Illinois, United States

Site Status

Novartis Investigative Site

Northbrook, Illinois, United States

Site Status

Novartis Investigative Site

Indianapolis, Indiana, United States

Site Status

Novartis Investigative Site

Des Moines, Iowa, United States

Site Status

Novartis Investigative Site

Kansas City, Kansas, United States

Site Status

Novartis Investigative Site

Overland Park, Kansas, United States

Site Status

Novartis Investigative Site

Alexandria, Louisiana, United States

Site Status

Novartis Investigative Site

Baton Rouge, Louisiana, United States

Site Status

Novartis Investigative Site

Clinton Township, Michigan, United States

Site Status

Novartis Investigative Site

Detroit, Michigan, United States

Site Status

Novartis Investigative Site

Golden Valley, Minnesota, United States

Site Status

Novartis Investigative Site

Chesterfield, Missouri, United States

Site Status

Novartis Investigative Site

Ozark, Missouri, United States

Site Status

Novartis Investigative Site

St Louis, Missouri, United States

Site Status

Novartis Investigative Site

Las Vegas, Nevada, United States

Site Status

Novartis Investigative Site

Latham, New York, United States

Site Status

Novartis Investigative Site

Charlotte, North Carolina, United States

Site Status

Novartis Investigative Site

Raleigh, North Carolina, United States

Site Status

Novartis Investigative Site

Winston-Salem, North Carolina, United States

Site Status

Novartis Investigative Site

Winston-Salem, North Carolina, United States

Site Status

Novartis Investigative Site

Cleveland, Ohio, United States

Site Status

Novartis Investigative Site

Oklahoma City, Oklahoma, United States

Site Status

Novartis Investigative Site

Spartanburg, South Carolina, United States

Site Status

Novartis Investigative Site

Johnson City, Tennessee, United States

Site Status

Novartis Investigative Site

Knoxville, Tennessee, United States

Site Status

Novartis Investigative Site

Dallas, Texas, United States

Site Status

Novartis Investigative Site

El Paso, Texas, United States

Site Status

Novartis Investigative Site

Houston, Texas, United States

Site Status

Novartis Investigative Site

Round Rock, Texas, United States

Site Status

Novartis Investigative Site

San Antonio, Texas, United States

Site Status

Novartis Investigative Site

San Antonio, Texas, United States

Site Status

Novartis Investigative Site

Virginia Beach, Virginia, United States

Site Status

Novartis Investigative Site

Green Bay, Wisconsin, United States

Site Status

Novartis Investigative Site

Madison, Wisconsin, United States

Site Status

Novartis Investigative Site

Milwaukee, Wisconsin, United States

Site Status

Novartis Investigative Site

Neenah, Wisconsin, United States

Site Status

Novartis Investigative Site

Rosario, Santa Fe Province, Argentina

Site Status

Novartis Investigative Site

Buenos Aires, , Argentina

Site Status

Novartis Investigative Site

Córdoba, , Argentina

Site Status

Novartis Investigative Site

New Lambton Heights, New South Wales, Australia

Site Status

Novartis Investigative Site

St Leonards, New South Wales, Australia

Site Status

Novartis Investigative Site

Brasschaat, , Belgium

Site Status

Novartis Investigative Site

Bruges, , Belgium

Site Status

Novartis Investigative Site

Liège, , Belgium

Site Status

Novartis Investigative Site

Overpelt, , Belgium

Site Status

Novartis Investigative Site

Plovdiv, , Bulgaria

Site Status

Novartis Investigative Site

Sofia, , Bulgaria

Site Status

Novartis Investigative Site

Sofia, , Bulgaria

Site Status

Novartis Investigative Site

Vancouver, British Columbia, Canada

Site Status

Novartis Investigative Site

Gatineau, Quebec, Canada

Site Status

Novartis Investigative Site

Montreal, Quebec, Canada

Site Status

Novartis Investigative Site

Québec, Quebec, Canada

Site Status

Novartis Investigative Site

Rijeka, HRV, Croatia

Site Status

Novartis Investigative Site

Zagreb, , Croatia

Site Status

Novartis Investigative Site

Praha 4 Krc, Czech Republic, Czechia

Site Status

Novartis Investigative Site

Hradec Králové, CZE, Czechia

Site Status

Novartis Investigative Site

Olomouc, CZE, Czechia

Site Status

Novartis Investigative Site

Jihlava, , Czechia

Site Status

Novartis Investigative Site

Pardubice, , Czechia

Site Status

Novartis Investigative Site

Prague, , Czechia

Site Status

Novartis Investigative Site

Aarhus, , Denmark

Site Status

Novartis Investigative Site

Copenhagen, , Denmark

Site Status

Novartis Investigative Site

Odense C, , Denmark

Site Status

Novartis Investigative Site

Tallinn, , Estonia

Site Status

Novartis Investigative Site

Tartu, , Estonia

Site Status

Novartis Investigative Site

Nancy, Cedex, France

Site Status

Novartis Investigative Site

Lille, , France

Site Status

Novartis Investigative Site

Nantes, , France

Site Status

Novartis Investigative Site

Nîmes, , France

Site Status

Novartis Investigative Site

Barsinghausen, , Germany

Site Status

Novartis Investigative Site

Bayreuth, , Germany

Site Status

Novartis Investigative Site

Bielefeld, , Germany

Site Status

Novartis Investigative Site

Hamburg, , Germany

Site Status

Novartis Investigative Site

Marburg, , Germany

Site Status

Novartis Investigative Site

München, , Germany

Site Status

Novartis Investigative Site

München, , Germany

Site Status

Novartis Investigative Site

Neuburg an der Donau, , Germany

Site Status

Novartis Investigative Site

Potsdam, , Germany

Site Status

Novartis Investigative Site

Ulm, , Germany

Site Status

Novartis Investigative Site

Wiesbaden, , Germany

Site Status

Novartis Investigative Site

Athens, GR, Greece

Site Status

Novartis Investigative Site

Athens, , Greece

Site Status

Novartis Investigative Site

Thessaloniki, , Greece

Site Status

Novartis Investigative Site

Budapest, HUN, Hungary

Site Status

Novartis Investigative Site

Budapest, , Hungary

Site Status

Novartis Investigative Site

Kistarcsa, , Hungary

Site Status

Novartis Investigative Site

Szeged, , Hungary

Site Status

Novartis Investigative Site

Bangalore, Karnataka, India

Site Status

Novartis Investigative Site

Kochi, Kerala, India

Site Status

Novartis Investigative Site

New Delhi, National Capital Territory of Delhi, India

Site Status

Novartis Investigative Site

Chandigarh, Punjab, India

Site Status

Novartis Investigative Site

Kolkata, West Bengal, India

Site Status

Novartis Investigative Site

Mangalore, , India

Site Status

Novartis Investigative Site

Ashkelon, , Israel

Site Status

Novartis Investigative Site

Haifa, , Israel

Site Status

Novartis Investigative Site

Sefad, , Israel

Site Status

Novartis Investigative Site

Tel Aviv, , Israel

Site Status

Novartis Investigative Site

Milan, MI, Italy

Site Status

Novartis Investigative Site

Roma, RM, Italy

Site Status

Novartis Investigative Site

Gallarate, VA, Italy

Site Status

Novartis Investigative Site

Napoli, , Italy

Site Status

Novartis Investigative Site

Mexico City, Mexico City, Mexico

Site Status

Novartis Investigative Site

Sittard-Geleen, BG, Netherlands

Site Status

Novartis Investigative Site

Amsterdam, , Netherlands

Site Status

Novartis Investigative Site

Rotterdam, , Netherlands

Site Status

Novartis Investigative Site

Bydgoszcz, , Poland

Site Status

Novartis Investigative Site

Gdansk, , Poland

Site Status

Novartis Investigative Site

Gdansk, , Poland

Site Status

Novartis Investigative Site

Gdansk, , Poland

Site Status

Novartis Investigative Site

Katowice, , Poland

Site Status

Novartis Investigative Site

Kielce, , Poland

Site Status

Novartis Investigative Site

Lodz, , Poland

Site Status

Novartis Investigative Site

Guaynabo, , Puerto Rico

Site Status

Novartis Investigative Site

Kemerovo, , Russia

Site Status

Novartis Investigative Site

Moscow, , Russia

Site Status

Novartis Investigative Site

Nizhny Novgorod, , Russia

Site Status

Novartis Investigative Site

Novosibirsk, , Russia

Site Status

Novartis Investigative Site

Saint Petersburg, , Russia

Site Status

Novartis Investigative Site

Saransk, , Russia

Site Status

Novartis Investigative Site

Sestroretsk, , Russia

Site Status

Novartis Investigative Site

Tyumen, , Russia

Site Status

Novartis Investigative Site

Banská Bystrica, , Slovakia

Site Status

Novartis Investigative Site

Bratislava, , Slovakia

Site Status

Novartis Investigative Site

Bratislava, , Slovakia

Site Status

Novartis Investigative Site

Nitra, , Slovakia

Site Status

Novartis Investigative Site

Trnava, , Slovakia

Site Status

Novartis Investigative Site

Cadiz, Andalusia, Spain

Site Status

Novartis Investigative Site

Barcelona, Catalonia, Spain

Site Status

Novartis Investigative Site

Barcelona, Catalonia, Spain

Site Status

Novartis Investigative Site

Barcelona, Catalonia, Spain

Site Status

Novartis Investigative Site

L'Hospitalet de Llobregat, Catalonia, Spain

Site Status

Novartis Investigative Site

Salt, Catalonia, Spain

Site Status

Novartis Investigative Site

El Palmar, Murcia, Spain

Site Status

Novartis Investigative Site

Barcelona, , Spain

Site Status

Novartis Investigative Site

Valencia, , Spain

Site Status

Novartis Investigative Site

Gothenburg, , Sweden

Site Status

Novartis Investigative Site

Stockholm, , Sweden

Site Status

Novartis Investigative Site

Basel, , Switzerland

Site Status

Novartis Investigative Site

Khon Kaen, THA, Thailand

Site Status

Novartis Investigative Site

Istanbul, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Izmir, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Kocaeli, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Samsun, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Headington, Oxfordshire, United Kingdom

Site Status

Novartis Investigative Site

Glasgow, , United Kingdom

Site Status

Novartis Investigative Site

London, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Belgium Bulgaria Canada Croatia Czechia Denmark Estonia France Germany Greece Hungary India Israel Italy Mexico Netherlands Poland Puerto Rico Russia Slovakia Spain Sweden Switzerland Thailand Turkey (Türkiye) United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Williams MJ, Amezcua L, Cohan SL, Cohen JA, Delgado SR, Hua LH, Lucassen EB, Piccolo RS, Koulouris CR, Stankiewicz J. Efficacy of Ofatumumab and Teriflunomide in Patients With Relapsing MS From Racial/Ethnic Minority Groups: ASCLEPIOS I/II Subgroup Analyses. Neurology. 2024 Aug 13;103(3):e209610. doi: 10.1212/WNL.0000000000209610. Epub 2024 Jul 17.

Reference Type DERIVED
PMID: 39018512 (View on PubMed)

Bhan V, Clift F, Baharnoori M, Thomas K, Patel BP, Blanchette F, Adlard N, Vudumula U, Gudala K, Dutta N, Grima D, Mouallif S, Farhane F. Cost-consequence analysis of ofatumumab for the treatment of relapsing-remitting multiple sclerosis in Canada. J Comp Eff Res. 2023 Sep;12(9):e220175. doi: 10.57264/cer-2022-0175. Epub 2023 Aug 22.

Reference Type DERIVED
PMID: 37606897 (View on PubMed)

Gartner J, Hauser SL, Bar-Or A, Montalban X, Cohen JA, Cross AH, Deiva K, Ganjgahi H, Haring DA, Li B, Pingili R, Ramanathan K, Su W, Willi R, Kieseier B, Kappos L. Efficacy and safety of ofatumumab in recently diagnosed, treatment-naive patients with multiple sclerosis: Results from ASCLEPIOS I and II. Mult Scler. 2022 Sep;28(10):1562-1575. doi: 10.1177/13524585221078825. Epub 2022 Mar 10.

Reference Type DERIVED
PMID: 35266417 (View on PubMed)

Hauser SL, Bar-Or A, Cohen JA, Comi G, Correale J, Coyle PK, Cross AH, de Seze J, Leppert D, Montalban X, Selmaj K, Wiendl H, Kerloeguen C, Willi R, Li B, Kakarieka A, Tomic D, Goodyear A, Pingili R, Haring DA, Ramanathan K, Merschhemke M, Kappos L; ASCLEPIOS I and ASCLEPIOS II Trial Groups. Ofatumumab versus Teriflunomide in Multiple Sclerosis. N Engl J Med. 2020 Aug 6;383(6):546-557. doi: 10.1056/NEJMoa1917246.

Reference Type DERIVED
PMID: 32757523 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2015-005418-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

COMB157G2301

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Effects of Ocrevus in Relapsing Multiple Sclerosis
NCT04387734 ACTIVE_NOT_RECRUITING PHASE4