Study to Evaluate the Efficacy and Safety of Fenebrutinib Compared With Teriflunomide in Relapsing Multiple Sclerosis (RMS)

NCT ID: NCT04586023

Last Updated: 2025-12-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

751 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-24

Study Completion Date

2027-07-09

Brief Summary

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A study to evaluate the efficacy and safety of fenebrutinib on disability progression and relapse rate in adult participants with RMS. Eligible participants will be randomized 1:1 to either fenebrutinib or teriflunomide. At the end of the DBT phase (after disclosure of the DBT results), the Sponsor will determine whether or not to initiate the open-label extension phase of the study.

Detailed Description

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Conditions

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Relapsing Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
Sponsor will also be blinded.

Study Groups

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Fenebrutinib

Participants will receive oral fenebrutinib with teriflunomide-matching placebo.

Group Type EXPERIMENTAL

Fenebrutinib

Intervention Type DRUG

Participants will receive fenebrutinib.

Placebo

Intervention Type DRUG

Participants will receive teriflunomide-matching placebo or fenebrutinib-matching placebo.

Teriflunomide

Participants will receive oral teriflunomide with fenebrutinib-matching placebo in a blinded fashion.

Group Type ACTIVE_COMPARATOR

Teriflunomide

Intervention Type DRUG

Participants will receive teriflunomide.

Placebo

Intervention Type DRUG

Participants will receive teriflunomide-matching placebo or fenebrutinib-matching placebo.

Interventions

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Fenebrutinib

Participants will receive fenebrutinib.

Intervention Type DRUG

Teriflunomide

Participants will receive teriflunomide.

Intervention Type DRUG

Placebo

Participants will receive teriflunomide-matching placebo or fenebrutinib-matching placebo.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Expanded Disability Status Scale (EDSS) score of 0 - 5.5 at screening.
* A diagnosis of RMS in accordance with the revised 2017 McDonald Criteria.
* Ability to complete the 9-Hole Peg Test (9-HPT) for each hand in \< 240 seconds.
* Ability to perform the Timed 25-Foot Walk Test (T25FWT) in \<150 seconds.
* For female participants of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive measures, and refrain from donating eggs.
* For male participants: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive measures, and refrain from donating sperm.


* Completed the Double-Blind Treatment (DBT) phase of the study (remaining on study treatment; no other Disease-Modifying Therapy (DMT) administered) and who, in the opinion of the investigator, may benefit from treatment with fenebrutinib.
* Participants randomized to the teriflunomide treatment arm during the DBT phase must undergo the accelerated teriflunomide elimination procedure (ATEP) prior to the first administration of open-label fenebrutinib.
* For female participants of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive measures, and refrain from donating eggs.
* For male participants: agreement to remain abstinent (refrain from heterosexual intercourse) or use contraceptive measures, and refrain from donating sperm.

Exclusion Criteria

* Disease duration of \> 10 years from the onset of symptoms and an EDSS score at screening \< 2.0.
* Female participants who are pregnant or breastfeeding, or intending to become pregnant.
* Male participants who intend to father a child during the study.
* A diagnosis of primary progressive MS (PPMS) or non-active secondary progressive MS (SPMS).
* Any known or suspected active infection at screening, including but not limited to a positive screening tests for Hepatitis B and C, an active or latent or inadequately treated infection with tuberculosis (TB), a confirmed or suspected progressive multifocal leukoencephalopathy (PML).
* History of cancer including hematologic malignancy and solid tumors within 10 years of screening.
* Known presence of other neurological disorders, that could interfere with the diagnosis of MS or assessments of efficacy or safety during the study and clinically significant cardiovascular, psychiatric, pulmonary, renal, hepatic, endocrine, metabolic or gastrointestinal disease.
* Rare hereditary problems of galactose intolerance, total lactase deficiency, or glucose-galactose malabsorption.
* Hypoproteinemia.
* Acute liver disease
* Chronic liver disease unless considered stable for \> 6 months.
* Presence of cirrhosis (Child-Pugh Class A, B, or C) or Gilbert's Syndrome.
* Participants with significantly impaired bone marrow function or significant anemia, leukopenia, neutropenia or thrombocytopenia.
* Any concomitant disease that may require chronic treatment with systemic corticosteroids or immunosuppressants during the course of the study.
* History of alcohol or other drug abuse within 12 months prior to screening.
* History of or currently active primary or secondary (non-drug-related) immunodeficiency, including known history of human immunodeficiency virus (HIV) infection.
* Inability to complete an MRI scan.
* Adrenocorticotropic hormone or systemic corticosteroid therapy within 4 weeks prior to screening (inhaled and topical corticosteroids are allowed).
* Receipt of a live-attenuated vaccine within 6 weeks prior to randomization.
* Any previous treatment with immunomodulatory or immunosuppressive medication without an appropriate washout period.


* Chronic liver disease unless considered stable for \> 6 months
* Acute liver disease
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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North Central Neurology Associates

Cullman, Alabama, United States

Site Status

Xenoscience

Phoenix, Arizona, United States

Site Status

Los Angeles Biomedical Research Institute at Harbor-UCLA

Torrance, California, United States

Site Status

KI Health Partners, LLC

Stamford, Connecticut, United States

Site Status

Georgetown University Medical Center

Washington D.C., District of Columbia, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

American Health Network Institute, LLC

Avon, Indiana, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Neuro Institute of New England P.C.

Foxborough, Massachusetts, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Hope Neurology

Knoxville, Tennessee, United States

Site Status

Integrated Neurology Services PLLC

Falls Church, Virginia, United States

Site Status

Medical College of Wisconsin, Inc.

Milwaukee, Wisconsin, United States

Site Status

Kepler Universitätskliniken GmbH - Med Campus III

Linz, , Austria

Site Status

L2 Ip Instituto de Pesquisas Clinicas Ltda ME

Brasília, Federal District, Brazil

Site Status

Santa Casa de Misericordia

Belo Horizonte, Minas Gerais, Brazil

Site Status

Instituto de Neurologia de Curitiba

Curitiba, Paraná, Brazil

Site Status

IMV Pesquisa Neurológica

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Núcleo de Pesquisa do Rio Grande do Sul

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital Sao Lucas - PUCRS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Clinica Neurologica

Joinville, Santa Catarina, Brazil

Site Status

Praxis Pesquisa Médica

Santo André, São Paulo, Brazil

Site Status

CEMEC - Centro Multidisciplinar de Estudos Clínicos

São Bernardo do Campo, São Paulo, Brazil

Site Status

Centro de Pesquisas Clinicas

São Paulo, São Paulo, Brazil

Site Status

Hospital Santa Marcelina

São Paulo, São Paulo, Brazil

Site Status

Jordy Sinapse Medicina LTDA ME

São Paulo, , Brazil

Site Status

UMHAT Dr. Georgi Stranski

Pleven, , Bulgaria

Site Status

MHATNP Sveti Naum EAD

Sofia, , Bulgaria

Site Status

University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

The Ottawa Hospital - General Campus

Ottawa, Ontario, Canada

Site Status

CIUSSS du Saguenay Lac-Saint-Jean, Chicoutimi Hospital

Chicoutimi, Quebec, Canada

Site Status

MUCH - Montreal Neurological Institute & Hospital

Montreal, Quebec, Canada

Site Status

CHU de Québec

Québec, Quebec, Canada

Site Status

Sydvestjysk Sygehus Esbjerg

Esbjerg, , Denmark

Site Status

Hjerne- og nervesygdomme, Ambulatorium, Skleroseklinikken

Sønderborg, , Denmark

Site Status

Hopital Gabriel Montpied CHU de Clermont-Ferrand

Clermont-Ferrand, , France

Site Status

Hôpital Pasteur

Nice, , France

Site Status

Hôpital Charles Nicolle

Rouen, , France

Site Status

CHU toulouse - Hôpital Purpan

Toulouse, , France

Site Status

Hospital Eginition

Athens, , Greece

Site Status

University General Hospital of Larisa

Larissa, , Greece

Site Status

AHEPA Univ. General Hospital of Thessaloniki

Thessaloniki, , Greece

Site Status

Nucare

Guatemala City, , Guatemala

Site Status

Zydus Hospital

Ahmedabad, Gujarat, India

Site Status

Seth G.S Medical College K.E.M Hospital

Mumbai, Maharashtra, India

Site Status

Deenanath Mangeshkar Hospital & Research Centre

Pune, Maharashtra, India

Site Status

Sahyadri Superspeciality Hospital

Pune, Maharashtra, India

Site Status

Max Super Speciality Hospital

New Delhi, National Capital Territory of Delhi, India

Site Status

Sir Gangaram Hospital

New Delhi, National Capital Territory of Delhi, India

Site Status

Christian Medical College and Hospital

Ludhiana, Punjab, India

Site Status

SRM Institute of Medical Sciences

Vadapalani, Tamil Nadu, India

Site Status

Postgraduate Institute of Medical Education and Research

Chandigarh, , India

Site Status

Universita? G. D'Annunzio

Chieti, Abruzzo, Italy

Site Status

Azienda Ospedaliero-Universitaria Consorziale Pol. di Bari

Bari, Apulia, Italy

Site Status

A. O. U. Federico II

Napoli, Campania, Italy

Site Status

Ospedale S.Camillo Forlanini

Rome, Lazio, Italy

Site Status

Policlinico Universitario A. Gemelli

Rome, Lazio, Italy

Site Status

NCL Institute Neuroscience

Rome, Lazio, Italy

Site Status

Irccs A.O.U.San Martino Ist

Genoa, Liguria, Italy

Site Status

Fond. Istituto Neurologico C.Besta

Milan, Lombardy, Italy

Site Status

Ospedale Civile di Montichiari

Montichiari, Lombardy, Italy

Site Status

IRCCS Istituto Neurologico C. Mondino?Dip. Neurologia Neuroriabilitazione S.S. Sclerosi Multipla

Pavia, Lombardy, Italy

Site Status

IRCCS Istituto Neurologico Neuromed

Pozzilli, Molise, Italy

Site Status

Ospedale Binaghi

Cagliari, Sardinia, Italy

Site Status

AOU Policlinico Giaccone

Palermo, Sicily, Italy

Site Status

Mexico Centre for Clinical Research

Mexico City, Mexico CITY (federal District), Mexico

Site Status

Clinstile S.A de C.V.

Mexico City, Mexico CITY (federal District), Mexico

Site Status

Grupo Médico Camino S.C.

México, Mexico CITY (federal District), Mexico

Site Status

Unidad de Investigación en Salud

Chihuahua City, , Mexico

Site Status

Unidad de investigacion en salud (UIS)

Mexico City, , Mexico

Site Status

NZOZ Vitamed

Bydgoszcz, , Poland

Site Status

Neurocentrum Bydgoszcz sp. z o.o

Bydgoszcz, , Poland

Site Status

COPERNICUS Podmiot Leczniczy Sp. z o. o. Szpital im. M. Kopernika

Gdansk, , Poland

Site Status

RESMEDICA Spolka z o.o.

Kielce, , Poland

Site Status

Centrum Neurologii Klinicznej

Krakow, , Poland

Site Status

Malopolskie Centrum Diagnostyczne MEDICAL Sp. z o. o.

Krakow, , Poland

Site Status

Centrum Neurologii Krzysztof Selmaj

Lodz, , Poland

Site Status

Instytut Zdrowia Dr Boczarska-Jedynak Sp. z o.o. Sp. k.

Oświęcim, , Poland

Site Status

Neurologiczny Niepubliczny ZOZ Centrum Leczenia SM Osrodek Bada? Klinicznych

Plewiska, , Poland

Site Status

MedPolonia

Poznan, , Poland

Site Status

NZOZ NEURO-KARD Ilkowski i Partnerzy Sp. Partn. Lek

Późna, , Poland

Site Status

Wojewódzki Szpital Specjalistyczny Nr 3

Rybnik, , Poland

Site Status

Klinika Neurologii I Wydzialu Lekarskiego WUM w Warszawie

Warsaw, , Poland

Site Status

Wro Medica

Wroc?aw, , Poland

Site Status

IBISMED Wielospecjalistyczne Centrum Medyczne

Zabrze, , Poland

Site Status

Krasnoyarsk State Medical Academy

Krasnoyarsk, Krasnoyarsk Krai, Russia

Site Status

FSBHI Siberian Clinical Center of the Federal Medical and Biological Agency

Krasnoyarsk, Krasnoyarsk Krai, Russia

Site Status

Federal center of brain research and neurotechnologies

Moskva, Moscow Oblast, Russia

Site Status

Regional Clinical Hospital N.A. Semashko

Nizhny Novgorod, Niznij Novgorod, Russia

Site Status

National Center of Social Significant Disease

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

Regional clinical hospital named after prof. S.V. Ochapovsky

Krasnodar, , Russia

Site Status

Nebbiolo Center for Clinical Trials

Tomsk, , Russia

Site Status

Keimyung University Dongsan Medical Center

Daegu, , South Korea

Site Status

National Cancer Center

Goyang-si, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Gazi University Medical Faculty

Ankara, , Turkey (Türkiye)

Site Status

Baskent Universitesi Ankara Hastanesi

Çankaya, , Turkey (Türkiye)

Site Status

Bakirkoy State Mental Hospital

Istanbul, , Turkey (Türkiye)

Site Status

Sancaktepe Training and Research Hospital

Istanbul, , Turkey (Türkiye)

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Selcuk University Medical Faculty

Istanbul, , Turkey (Türkiye)

Site Status

Kocaeli University Hospital

Kocaeli, , Turkey (Türkiye)

Site Status

Ege Üniversitesi Tip Fakültesi

Lzmir, , Turkey (Türkiye)

Site Status

Mersin University Medical Faculty

Mersin, , Turkey (Türkiye)

Site Status

Ondokuz Mayis University School of Medicine

Samsun, , Turkey (Türkiye)

Site Status

Karadeniz Tecnical Uni. Med. Fac.

Trabzon, , Turkey (Türkiye)

Site Status

Van Yuzuncu Yil University Hospital

Van, , Turkey (Türkiye)

Site Status

Salford Royal NHS Foundation Trust

Salford, , United Kingdom

Site Status

Countries

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United States Austria Brazil Bulgaria Canada Denmark France Greece Guatemala India Italy Mexico Poland Russia South Korea Turkey (Türkiye) United Kingdom

Other Identifiers

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2020-001168-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2022-502618-95-00

Identifier Type: CTIS

Identifier Source: secondary_id

GN42272

Identifier Type: -

Identifier Source: org_study_id