An Observational Study of Presentation, Treatment Patterns, and Outcomes in Multiple Myeloma Participants

NCT ID: NCT02761187

Last Updated: 2025-02-24

Study Results

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Basic Information

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Recruitment Status

TERMINATED

Total Enrollment

4253 participants

Study Classification

OBSERVATIONAL

Study Start Date

2016-07-01

Study Completion Date

2021-09-30

Brief Summary

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The purpose of this study is to describe contemporary, real-world patterns of participant characteristics, clinical disease presentation, therapeutic regimen chosen, and clinical outcomes in participants with newly diagnosed \[ND\] multiple myeloma (MM) and participants with relapsed/refractory \[R/R\] MM.

Detailed Description

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This is a prospective, non-interventional, observational study. This study will look at contemporary, real-world patterns of participant characteristics, clinical disease presentation, therapeutic regimen chosen, and clinical outcomes in participants with MM. Participants will not be asked to change their routine clinical treatment. Participants will have to complete patient reported outcomes (PROs) surveys during on-site routine office visits.

The study will enroll approximately 4200 participants. Participants will be assigned to one of the following cohorts based upon the diagnosis of MM:

* ND MM within 3 months from initiation of treatment
* R/R MM who have received 1 to 3 prior lines of therapy

This multi-center trial will be conducted worldwide. The overall time to participate in this study is up to 8 years. Participants will be evaluated and followed-up for a period of at least 5 years, until death, are lost to follow-up, or the end of the study, whichever comes first.

Conditions

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Multiple Myeloma

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

PROSPECTIVE

Study Groups

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Newly Diagnosed Multiple Myeloma

Participants newly diagnosed with MM within 3 months from initiation of treatment were enrolled for 3 years, and followed for at least 2 years, until death, or the end of the study, whichever comes first (up to approximately 5 years).

No Intervention

Intervention Type OTHER

As this was an observational study, no intervention was administered.

Relapsed/Refractory Multiple Myeloma

Participants diagnosed with RRMM who previously received 1 to 3 prior lines of therapy were enrolled for 3 years, and followed for at least 2 years, until death, or the end of the study, whichever comes first (up to approximately 5 years).

No Intervention

Intervention Type OTHER

As this was an observational study, no intervention was administered.

Interventions

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No Intervention

As this was an observational study, no intervention was administered.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

Is 18 years of age or older.

Is experiencing the following:

1. Newly diagnosed MM within 3 months from initiation of treatment with documented month and year of diagnosis, criteria met for diagnosis, stage, and MM-directed treatment history, including duration, or
2. Relapsed/refractory MM who have received 1 to 3 prior lines of therapy with documented data in the medical record regarding diagnosis (month and year), the regimens used in 1st, 2nd, and 3rd line as applicable, whether stem cell transplant was part of 1st, 2nd, and 3rd line of therapy, whether consolidation/maintenance was part of 1st, 2nd, and 3rd line of therapy, also whether investigational therapy/treated on a clinical trial was part of any of these regimens.

Is willing and able to sign informed consent to participate. Is willing and able to complete patient-reported outcomes (PROs) in accordance with local regulatory and data protection requirements.

Exclusion Criteria

Is reporting to a site in this study for a second opinion (consultation only) or participants whose frequency of consult and follow-up are not adequate for quarterly electronic case report form (eCRF) completion.

Has participated in another study (observational or interventional) that prohibits participation in this study.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Takeda

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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CARTI Cancer Center

Little Rock, Arkansas, United States

Site Status

University of Arkansas For Medical Sciences

Little Rock, Arkansas, United States

Site Status

University of California San Diego

La Jolla, California, United States

Site Status

St Joseph Heritage Healthcare

Santa Rosa, California, United States

Site Status

Rocky Mountain Cancer Centers (Williams) - USOR

Denver, Colorado, United States

Site Status

Poudre Valley Health System

Fort Collins, Colorado, United States

Site Status

George Washington University

Washington D.C., District of Columbia, United States

Site Status

SCRI Florida Cancer Specialists East

Daytona Beach, Florida, United States

Site Status

SCRI Florida Cancer Specialists South

Fort Myers, Florida, United States

Site Status

SCRI Florida Cancer Specialists North

St. Petersburg, Florida, United States

Site Status

Illinois Cancer Specialists (Niles) - USOR

Niles, Illinois, United States

Site Status

Indiana University

Indianapolis, Indiana, United States

Site Status

East Jefferson General Hospital

Metairie, Louisiana, United States

Site Status

Central Maine Medical Center

Lewiston, Maine, United States

Site Status

Maryland Oncology Hematology (Columbia) - USOR

Columbia, Maryland, United States

Site Status

Barbara Ann Karmanos Cancer Center

Detroit, Michigan, United States

Site Status

Park Nicollet Institute

Saint Louis Park, Minnesota, United States

Site Status

Central Care Cancer Center

Bolivar, Missouri, United States

Site Status

Kansas City VA Medical Center

Kansas City, Missouri, United States

Site Status

Washington University in St. Louis

St Louis, Missouri, United States

Site Status

Hunterdon Hematology Oncology

Flemington, New Jersey, United States

Site Status

San Juan Oncology Associates

Farmington, New Mexico, United States

Site Status

Saint Francis Hospital

East Hills, New York, United States

Site Status

Mount Sinai Medical Center

New York, New York, United States

Site Status

Levine Cancer Center

Charlotte, North Carolina, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Hematology Oncology Associates - USOR

Medford, Oregon, United States

Site Status

Northwest Cancer Specialists (Broadway) - USOR

Portland, Oregon, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Veterans Affairs Pittsburgh Healthcare System

Pittsburgh, Pennsylvania, United States

Site Status

Greenville Health System Cancer Institute

Greenville, South Carolina, United States

Site Status

SCRI Tennessee Oncology Nashville

Nashville, Tennessee, United States

Site Status

Texas Oncology (Loop) - USOR

Amarillo, Texas, United States

Site Status

Texas Oncology (Loop) - USOR

Dallas, Texas, United States

Site Status

Texas Oncology (Loop) - USOR

El Paso, Texas, United States

Site Status

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Texas Oncology (Loop) - USOR

Round Rock, Texas, United States

Site Status

Texas Oncology (Loop) - USOR

San Antonio, Texas, United States

Site Status

Yakima Valley Memorial Hospital North Star Lodge - USOR

Yakima, Washington, United States

Site Status

Berkeley Medical Center

Martinsburg, West Virginia, United States

Site Status

St Vincent Hospital

Green Bay, Wisconsin, United States

Site Status

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States

Site Status

Aurora Health Care, Aurora Cancer Care

Milwaukee, Wisconsin, United States

Site Status

Grand Hopital de Charleroi asbl

Charleroi, , Belgium

Site Status

UZ Gent

Ghent, , Belgium

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Hopital de Jolimont

Haine-Saint-Paul, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

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CHU de Liege

Liège, , Belgium

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CHU UCL Namur asbl - Site Godinne

Yvoir, , Belgium

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Unicamp Universidade Estadual de Campinas

Campinas, , Brazil

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Centro de Pesquisas Oncologicas

Florianópolis, , Brazil

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Hospital Das Clinicas Da Universidade Federal de Goias

Goiânia, , Brazil

Site Status

Universidade Federal Do Rio de Janeiro Hospital Universitario Clementino Fraga Filho

Rio de Janeiro, , Brazil

Site Status

CEHON - Centro de Hematologia e Oncologia da Bahia Ltda

Salvador, , Brazil

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Clinica Sao Germano

São Paulo, , Brazil

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Hospital Israelita Albert Einstein

São Paulo, , Brazil

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Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo

São Paulo, , Brazil

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Peking Union Medical College Hospital

Beijing, , China

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Peking University Peoples Hospital

Beijing, , China

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The First Affiliated Hospital of College of Medicine, Zhejiang University

Hangzhou, , China

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First Affiliated Hospital of Soochow University

Suzhou, , China

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Fundacion Santa Fe de Bogota

Bogotá, , Colombia

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Fundacion Oftalmologica de Santander Foscal

Floridablanca, , Colombia

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Hospital Pablo Tobon Uribe

Medellín, , Colombia

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Oncomedica SA

Montería, , Colombia

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Centre Hospitalier de La Cote Basque

Bayonne, , France

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Centre Hospitalier Departemental de Vendee

La Roche-sur-Yon, , France

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Centre Hospitalier Le Mans

Le Mans, , France

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Centre Hospitalier de Perigueux

Périgueux, , France

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CHRU de Poitiers La Miletrie

Poitiers, , France

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CHU de Nancy-Hopital Brabois Adulte

Vandœuvre-lès-Nancy, , France

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Klinikum Chemnitz gGmbH

Chemnitz, , Germany

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Gefos - Gesellschaft fur onkologische Studien mbH

Dortmund, , Germany

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Universitatsklinikum Heidelberg

Heidelberg, , Germany

Site Status

Internistisch Hamatologische und Internistische Praxis

Herrsching am Ammersee, , Germany

Site Status

Institut fur Versorgungsforschung in der Onkologie GbR

Koblenz, , Germany

Site Status

Universitatsmedizin der Johannes Gutenberg-Universitat Mainz

Mainz, , Germany

Site Status

Mannheimer Onkologie Praxis

Mannheim, , Germany

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OnkoNet Marburg GmbH

Marburg, , Germany

Site Status

Onkologische Gemeinschaftspraxis Siegburg

Siegburg, , Germany

Site Status

Universitatsklinikum Tubingen

Tübingen, , Germany

Site Status

University Hospital of Alexandroupolis

Alexandroupoli, , Greece

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Evangelismos General Hospital of Athens

Athens, , Greece

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Alexandra Hospital

Athens, , Greece

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University General Hospital of Ioannina

Ioannina, , Greece

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University General Hospital of Larissa

Larissa, , Greece

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University General Hospital of Patras

Pátrai, , Greece

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HaEmek Medical Center

Afula, , Israel

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Lady Davis Carmel Medical Center

Haifa, , Israel

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Shaare Zedek Medical Center

Jerusalem, , Israel

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Meir Medical Center

Kefar Sava, , Israel

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Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

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Assuta Medical Centers

Tel Aviv, , Israel

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Azienda Ospedaliero Universitaria Ospedali Riuniti di Ancona-Umberto I G.M. Lancisi G. Salesi

Ancona, , Italy

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Azienda Ospedaliero Universitaria Di Bologna - Policlinico S Orsola Malpighi

Bologna, , Italy

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Azienda Ospedaliero Universitaria Policlinico Vittorio Emanuele

Catania, , Italy

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Azienda Ospedaliera Universitaria Careggi

Florence, , Italy

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Azienda Ospedaliera Universitaria Federico II

Napoli, , Italy

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Azienda Policlinico Umberto I

Roma, , Italy

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Azienda Ospedaliera Citta della Salute e della Scienza di Torino

Torino, , Italy

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Azienda Sanitaria Universitaria Integrata di Udine

Udine, , Italy

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Nucleo Oncologico de Occidente S.C.

Guadalajara, , Mexico

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Hematologica Alta Especialidad S.C.

Huixquilucan, , Mexico

Site Status

Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran

Mexico City, , Mexico

Site Status

Hospital Universitario Dr. Jose Eleuterio Gonzalez

Monterrey, , Mexico

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Hospital Clinic de Barcelona

Barcelona, , Spain

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Hospital Universitario Virgen de Las Nieves

Granada, , Spain

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Complejo Asistencial Universitario de Leon

León, , Spain

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Hospital Universitario 12 de Octubre

Madrid, , Spain

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Hospital Universitario de Salamanca

Salamanca, , Spain

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Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

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Chang Gung Medical Foundation Chiayi Chang Gung Memorial Hospital

Buzi, Chiayi County, Taiwan

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Kaohsiung Medical University Hospital

Kaohsiung City, , Taiwan

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Chang Gung Medical Foundation Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

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China Medical University Hospital

Taichung, , Taiwan

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National Cheng Kung University Hospital

Tainan City, , Taiwan

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National Taiwan University Hospital

Taipei, , Taiwan

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Cukurova Universitesi Tip Fakultesi Balcali Hastanesi

Adana, , Turkey (Türkiye)

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Ankara University Medical Faculty Cebeci Hospital

Ankara, , Turkey (Türkiye)

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Akdeniz University Medical Faculty

Antalya, , Turkey (Türkiye)

Site Status

Johns Hopkins Medicine - Anadolu Saglik Merkezi

Gebze, , Turkey (Türkiye)

Site Status

Ege Universitesi Tip Fakultesi Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status

Istanbul Universitesi Istanbul Tip Fakultesi Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status

Dokuz Eylul University Medical Faculty

Izmir, , Turkey (Türkiye)

Site Status

Erciyes Universitesi Tip Fakultesi Hastanesi

Kayseri, , Turkey (Türkiye)

Site Status

Ondokuz Mayis Universitesi Tip Fakultesi Hastanesi

Samsun, , Turkey (Türkiye)

Site Status

Karadeniz Technical University Faculty of Medicine

Trabzon, , Turkey (Türkiye)

Site Status

Leeds Teaching Hospitals NHS Trust

Leeds, West Yorkshire, United Kingdom

Site Status

Royal United Hospital

Bath, , United Kingdom

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University Hospital Birmingham

Birmingham, , United Kingdom

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Birmingham Heartlands Hospital

Birmingham, , United Kingdom

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Royal Bournemouth Hospital

Bournemouth, , United Kingdom

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Ninewells Hospital - PPDS

Dundee, , United Kingdom

Site Status

Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status

Nottingham University Hospitals NHS Trust

Nottingham, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

Sutton, , United Kingdom

Site Status

Pinderfields General Hospital

Wakefield, , United Kingdom

Site Status

Countries

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United States Belgium Brazil China Colombia France Germany Greece Israel Italy Mexico Spain Taiwan Turkey (Türkiye) United Kingdom

References

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Rifkin RM, Costello CL, Birhiray RE, Kambhampati S, Richter J, Abonour R, Lee HC, Stokes M, Ren K, Stull DM, Cherepanov D, Bogard K, Noga SJ, Girnius S. In-class transition from bortezomib-based therapy to IRd is an effective approach in newly diagnosed multiple myeloma. Future Oncol. 2024 Jan;20(3):131-143. doi: 10.2217/fon-2023-0272. Epub 2023 Oct 9.

Reference Type DERIVED
PMID: 37807952 (View on PubMed)

Thompson MA, Boccadoro M, Leleu X, Vela-Ojeda J, van Rhee F, Weisel KC, Rifkin RM, Usmani SZ, Hajek R, Cook G, Abonour R, Armour M, Morgan KE, Yeh SP, Costello CL, Berdeja JG, Davies FE, Zonder JA, Lee HC, Omel J, Spencer A, Terpos E, Hungria VTM, Puig N, Fu C, Ferrari RH, Ren K, Stull DM, Chari A. Rates of Influenza and Pneumococcal Vaccination and Correlation With Survival in Multiple Myeloma Patients. Clin Lymphoma Myeloma Leuk. 2023 Mar;23(3):e171-e181. doi: 10.1016/j.clml.2022.12.003. Epub 2022 Dec 7.

Reference Type DERIVED
PMID: 36641358 (View on PubMed)

Hajek R, Minarik J, Straub J, Pour L, Jungova A, Berdeja JG, Boccadoro M, Brozova L, Spencer A, van Rhee F, Vela-Ojeda J, Thompson MA, Abonour R, Chari A, Cook G, Costello CL, Davies FE, Hungria VT, Lee HC, Leleu X, Puig N, Rifkin RM, Terpos E, Usmani SZ, Weisel KC, Zonder JA, Barinova M, Kuhn M, Silar J, Capkova L, Galvez K, Lu J, Elliott J, Stull DM, Ren K, Maisnar V. Ixazomib-lenalidomide-dexamethasone in routine clinical practice: effectiveness in relapsed/refractory multiple myeloma. Future Oncol. 2021 Jul;17(19):2499-2512. doi: 10.2217/fon-2020-1225. Epub 2021 Mar 26.

Reference Type DERIVED
PMID: 33769076 (View on PubMed)

Costello C, Davies FE, Cook G, Vela-Ojeda J, Omel J, Rifkin RM, Berdeja J, Puig N, Usmani SZ, Weisel K, Zonder JA, Terpos E, Spencer A, Leleu X, Boccadoro M, Thompson MA, Romanus D, Stull DM, Hungria V. INSIGHT MM: a large, global, prospective, non-interventional, real-world study of patients with multiple myeloma. Future Oncol. 2019 May;15(13):1411-1428. doi: 10.2217/fon-2019-0013. Epub 2019 Feb 28.

Reference Type DERIVED
PMID: 30816809 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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NSMM-5001

Identifier Type: -

Identifier Source: org_study_id

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