Non-interventional Study to Evaluate Long Term Safety, Prescription Management Patterns of Esmya in a Long Term Setting

NCT ID: NCT02748460

Last Updated: 2025-09-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

1527 participants

Study Classification

OBSERVATIONAL

Study Start Date

2015-12-22

Study Completion Date

2024-04-11

Brief Summary

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This is a multi-centre, multinational, prospective, non-interventional study in females with a diagnosis of moderate to severe uterine fibroids, and for whom a treatment with Esmya in a long term manner is planned, and in subjects who were previously exposed to UPA in the long term Phase III studies.

Detailed Description

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This is a multi-centre, multinational, prospective, non-interventional study in females with a diagnosis of moderate to severe uterine fibroids, and for whom a treatment with Esmya in a long term manner is planned, and in subjects who were previously exposed to UPA in the long term Phase III studies. It is planned to enrol approximately 1,500 patients. Consecutive, eligible, patients will be invited to enrol from approximately 100-150 European Union (EU) clinical practice sites in approximately 15 countries. Patients will be followed for an observation period of 60 months (5 years) from treatment start. Investigators are to manage and treat patients according to their standard medical practice.

Conditions

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Uterine Fibroids

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

PROSPECTIVE

Study Groups

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Patients treated with Esmya

Any patient who was confirmed as receiving one dose of Esmya

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Adult women of reproductive age with a diagnosis of moderate to severe symptoms of uterine fibroids who are not eligible for surgery and for whom a intermittent treatment with Esmya in a long term manner (at least 2 courses), is planned or subjects who were exposed to UPA 5 or 10 mg during long term Phase III trials PGL09-027 (PEARL III extension, including patients (PEARL extension 2)) or PGL11-006 (PEARL IV), and
* Patient is willing and able to attend visits which are scheduled by her treating physician for the regular follow-up, provide the required medical data, and
* Patient has personally signed and dated the informed consent document indicating that she has been informed of all pertinent aspects of the study.

Exclusion Criteria

* Patient is prescribed Esmya for pre-operative treatment
* Patient has a contraindication to receive Esmya as per SmPC
* Patient is using an investigational drug/therapy or has discontinued the use of an investigational drug/therapy within 30 days prior to study enrolment,
* Patient has hypersensitivity to the active substance of Esmya or to one of its excipients,
* Not applicable to long term phase III previous subjects who are not planning to receive Esmya during this study:

* Patient is pregnant or plans to become pregnant within the next 12 months from treatment start,
* Patient is breastfeeding,
* Patient has genital bleeding of unknown aetiology or not due to uterine fibroids,
* Patient has been diagnosed with uterine, cervical, ovarian or breast cancer.
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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PregLem SA

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pablo Arriagada

Role: STUDY_DIRECTOR

PregLem SA

Locations

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Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

Centre Hospitalier Regional De La Citadelle

Liège, , Belgium

Site Status

Clinique Universitaire de Mont Godinne

Yvoir, , Belgium

Site Status

Dr Dvorak

Brno, , Czechia

Site Status

Gyn-Porodnicka Klinika Fn Brno

Brno, , Czechia

Site Status

Gyn -Fsro

Králová, , Czechia

Site Status

G-Centrum Olomouc S.R.O.

Olomouc, , Czechia

Site Status

Private Practice 2

Prague, , Czechia

Site Status

Private Practice

Prague, , Czechia

Site Status

Uherskohradistska Nemocnice A.S

Uherské Hradiště, , Czechia

Site Status

Aarhus University Hospital

Aarhus, , Denmark

Site Status

Gastroenheden Herlev-Gentofte

Herlev, , Denmark

Site Status

Centre Hospitalier Universitaire d'Angers

Angers, , France

Site Status

Centre Hospitalier de Bethune

Béthune, , France

Site Status

Groupement Hospitalier Universitaire Sud CHU Bicetre

Le Kremlin-Bicêtre, , France

Site Status

Hopital Bichat - Claude-Bernard

Paris, , France

Site Status

Centre Hospitalier Regional Universitaire de Tours (CHRU de Tours) - Hopital Bretonneau

Tours, , France

Site Status

Private practice

Aachen, , Germany

Site Status

Klinikum Bayreuth GmbH

Bayreuth, , Germany

Site Status

Charite -Universitatsmedizin Berlin - Campus Benjamin Franklin

Berlin, , Germany

Site Status

Praxis fuer Gynaekologie & Geburtshilfe Prof. Dr. Dr. A. Ebert

Berlin, , Germany

Site Status

Gynakologische Praxis Klinik

Bonn, , Germany

Site Status

PAN-Klinik am Neumarkt-Gemeinschaftspraxis fur Urologie

Cologne, , Germany

Site Status

Gemeinschaftspraxis der Frauenarztpraxis

Deggendorf, , Germany

Site Status

Private Practice

Dortmund, , Germany

Site Status

Private Practice

Frankfurt, , Germany

Site Status

Frauenarztpraxis

Frankfurt am Main, , Germany

Site Status

Hellweg gynakologie/DOCX

Geseke, , Germany

Site Status

Universitaetsklinikum Giessen und Marburg GmbH

Giessen, , Germany

Site Status

Frauenarztpraxis Gluckstadt

Glückstadt, , Germany

Site Status

Frauenarzt Bergedorf

Hamburg, , Germany

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Frauenarztpraxis Wandsbek

Hamburg, , Germany

Site Status

Praxisklinik Harburg

Hamburg, , Germany

Site Status

Private Practice

Hamburg, , Germany

Site Status

Unversitaetsklinikum Hamburg Eppendorf - Klinik und Poliklinik fur Gynakologie

Hamburg, , Germany

Site Status

Private practice

Ilsede, , Germany

Site Status

Frauenarztpraxis

Köthen, , Germany

Site Status

Medplus Krefeld

Krefeld, , Germany

Site Status

Endoskopie Und Endometriose-Zentrum Munchen

München, , Germany

Site Status

Private Practice

Plöcking, , Germany

Site Status

Private practice

Ribnitz-Damgarten, , Germany

Site Status

Private Practice

Stolberg, , Germany

Site Status

Ammerland Klinik GmbH

Westerstede, , Germany

Site Status

Rethy Pal Hospital-Clinic Bekescsaba

Békéscsaba, , Hungary

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Robert Karoly Maganklinika

Budapest, , Hungary

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Szent Anna Privat Surgery-Szent Anna Magae¡nrendela

Debrecen, , Hungary

Site Status

Josa Andras County Teaching Hospital

Nyíregyháza, , Hungary

Site Status

Szegedi Tudomanyegyetem, Szuleszeti es Nogyogyaszati Klinika

Szeged, , Hungary

Site Status

Csongrad Megyei Dr. Bugyi Istvan Korhaz

Szentes, , Hungary

Site Status

Woman's Health Sciences Department, Gynecologic Section, Hsopital G. Salesi- Polytechnic University of Marche

Ancona, , Italy

Site Status

University of Bari Policlinico

Bari, , Italy

Site Status

Azienda Usl Di Bologna

Bologna, , Italy

Site Status

Policlinico S. Orsola Malpighi

Bologna, , Italy

Site Status

A.O.Spedali Civili di Brescia

Brescia, , Italy

Site Status

University ""Magna Graecia"" Of Catanzaro

Catanzaro, , Italy

Site Status

Amyloidosis Research & Treatment Center, Fondazione Irccs Policlinico San Matteo

Pavia, , Italy

Site Status

Azienda Ospedaliera Universitaria Senese - Policlinico Santa Maria Alle Scotte

Siena, , Italy

Site Status

University of Torino, S. Anna Hospital- City of Health and Science

Torino, , Italy

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ARS

Riga, , Latvia

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Latvian Maritime Medicine Centre

Riga, , Latvia

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N. Lietuviete Private Practice

Riga, , Latvia

Site Status

Private Practice

Riga, , Latvia

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RiGa 1st Hospital

Riga, , Latvia

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Jsc Kardiolita

Vilnius, , Lithuania

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Medical Center Maxmeda

Vilnius, , Lithuania

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Radboud Universitair Medical Center

Nijmegen, , Netherlands

Site Status

Gabinet Lekarski Specjalistyczny "Sonus" Lemieszczuk Boguslaw

Warsaw, , Poland

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Centro hospitalar do Baixo vouga, EPE

Aveiro, , Portugal

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Private Practice

Coimbra, , Portugal

Site Status

Clinica Jardim das Amoreiras

Lisbon, , Portugal

Site Status

Centrul Medical Euromed

Bucharest, , Romania

Site Status

Genesys Fertility Center

Bucharest, , Romania

Site Status

Spitalul Clinic Dr. Ioan Cantacuzino

Bucharest, , Romania

Site Status

Elena Doamna Obstetrics and Gynecology Clinical Hospital

Iași, , Romania

Site Status

Complejo Hospitalario Universitario A Coruna

A Coruña, , Spain

Site Status

Hospital Universitario de Cruces

Barakaldo, , Spain

Site Status

ASSIR OSONA (Atencio a la Salut Sexual i Reproductiva) - ICS (Institut Catala de la Salut)

Barcelona, , Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital General Hospitalet CSI

Barcelona, , Spain

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Hospital Universitari Quiron Dexeus Barcelona

Barcelona, , Spain

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Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Institut Clinic de Nefrologia i Urologia - ICNU, Hospital Clinic i Provincial de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario de Guadalajara (HUG)

Guadalajara, , Spain

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Hospital Clinico San Carlos

Madrid, , Spain

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Hospital General Universitario Gregorio Maranon

Madrid, , Spain

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Hospital Universitario 12 de Octubre

Madrid, , Spain

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Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

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Hospital Universitario La Paz

Madrid, , Spain

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Hospital Universitario Ramon y Cajal

Madrid, , Spain

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Instituto Palacios, Salud y Medicina de la Mujer

Madrid, , Spain

Site Status

Hospital Universitario Puerta de Hierro

Majadahonda, , Spain

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Hospital Regional Universitario Carlos Haya

Málaga, , Spain

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Hospital Quironsalud Toledo

Toledo, , Spain

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Hospital Universitario y Politecnico La Fe

Valencia, , Spain

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Danderyds Sjukhus AB

Stockholm, , Sweden

Site Status

Karolinska Institutet, Karolinska University Hospital Huddinge

Stockholm, , Sweden

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Royal United Hospital, Bath - Royal United Hospital Bath NHS Trust

Bath, , United Kingdom

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Royal Bolton Hospital

Bolton, , United Kingdom

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University Hospital of North Durham

Durham, , United Kingdom

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London North West Healthcare NHS Trust

Harrow, , United Kingdom

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Hull Royal Infirmary - Hull and East Yorkshire Hospitals NHS Trust

Hull, , United Kingdom

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Hinchingbrooke Health Care NHS Trust - Hinchingbrooke Hospital

Huntingdon, , United Kingdom

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Leicester General Hospital

Leicester, , United Kingdom

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North Middlesex University Hospital

London, , United Kingdom

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Queen Charlotte's & Chelsea Hospital

London, , United Kingdom

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Royal Manchester Children's Hospital - Manchester University NHS Foundation Trust

Manchester, , United Kingdom

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Arrowe Park Hospital

Metropolitan Borough of Wirral, , United Kingdom

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Royal Victoria Infirmary - The Newcastle Upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, , United Kingdom

Site Status

Norfolk and Norwich University Hospital

Norwich, , United Kingdom

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Rosemere Cancer Centre - Royal Preston Hospital

Preston, , United Kingdom

Site Status

Sheffield Teaching Hospitals NHS Foundation Trust - Jessop Wing

Sheffield, , United Kingdom

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University Hospital Southampton NHS Foundation Trust

Southampton, , United Kingdom

Site Status

University Hospital Of North Tees - North Tees And Hartlepool Nhs Foundation Trust

Stockton-on-Tees, , United Kingdom

Site Status

Royal Stoke University Hospital - University Hospital of North Midlands NHS Trust

Stoke-on-Trent, , United Kingdom

Site Status

Countries

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Belgium Czechia Denmark France Germany Hungary Italy Latvia Lithuania Netherlands Poland Portugal Romania Spain Sweden United Kingdom

Other Identifiers

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PGL14-001 (PREMIUM)

Identifier Type: -

Identifier Source: org_study_id

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