Study to Evaluate Safety, Tolerability and Efficacy of UCB7665 in Subjects With Primary Immune Thrombocytopenia

NCT ID: NCT02718716

Last Updated: 2024-01-29

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

66 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-03-02

Study Completion Date

2019-02-04

Brief Summary

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The primary objective of the study is to check if an subcutaneous (sc) infusion of UCB7665 is safe and tolerated in subjects with primary immune thrombocytopenia.

Detailed Description

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Conditions

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Thrombocytopenia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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UCB7665 4 mg/kg

Participants in this arm received 5 subcutaneous (sc) doses of UCB7665 (rozanolixizumab) 4 milligram per kilograms (mg/kg) at 1-week intervals.

Group Type EXPERIMENTAL

UCB7665

Intervention Type DRUG

* Intervention Type: Biological/Vaccine
* Pharmaceutical Form: Powder for solution for infusion
* Concentration: 100 mg/ml - Route of Administration:

Subcutaneous infusion

UCB7665 7 mg/kg

Participants in this arm received 3 sc doses of UCB7665 (rozanolixizumab) 7 mg/kg at 1-week intervals.

Group Type EXPERIMENTAL

UCB7665

Intervention Type DRUG

* Intervention Type: Biological/Vaccine
* Pharmaceutical Form: Powder for solution for infusion
* Concentration: 100 mg/ml - Route of Administration:

Subcutaneous infusion

UCB7665 10 mg/kg

Participants in this arm received 2 sc doses of UCB7665 (rozanolixizumab) 10 mg/kg at 1-week intervals.

Group Type EXPERIMENTAL

UCB7665

Intervention Type DRUG

* Intervention Type: Biological/Vaccine
* Pharmaceutical Form: Powder for solution for infusion
* Concentration: 100 mg/ml - Route of Administration:

Subcutaneous infusion

UCB7665 15 mg/kg

Participants in this arm received 1 sc dose of UCB7665 (rozanolixizumab) 15 mg/kg.

Group Type EXPERIMENTAL

UCB7665

Intervention Type DRUG

* Intervention Type: Biological/Vaccine
* Pharmaceutical Form: Powder for solution for infusion
* Concentration: 100 mg/ml - Route of Administration:

Subcutaneous infusion

UCB7665 20 mg/kg

Participants in this arm received 1 sc dose of UCB7665 (rozanolixizumab) 20 mg/kg.

Group Type EXPERIMENTAL

UCB7665

Intervention Type DRUG

* Intervention Type: Biological/Vaccine
* Pharmaceutical Form: Powder for solution for infusion
* Concentration: 100 mg/ml - Route of Administration:

Subcutaneous infusion

Interventions

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UCB7665

* Intervention Type: Biological/Vaccine
* Pharmaceutical Form: Powder for solution for infusion
* Concentration: 100 mg/ml - Route of Administration:

Subcutaneous infusion

Intervention Type DRUG

Other Intervention Names

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rozanolixizumab

Eligibility Criteria

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Inclusion Criteria

* Subject has a diagnosis of primary immune thrombocytopenia (ITP) for a minimum of 3 months prior to Screening Visit
* Subject has a platelet count \<30x10\^9/L at Screening and \<35x10\^9/L at Baseline (Visit 2)
* Subject has a current or history of a peripheral blood smear consistent with ITP
* Subject has responded to previous ITP therapy (according to the judgment of the investigator)

Exclusion Criteria

* Subject has an immunoglobulin G (IgG) level \<=6g/L at Screening Visit
* Subject has a partial thromboplastin time (PTT) \>=1.5x upper limit of normal (ULN) or International Normalized Ratio (INR) \>=1.5 at Screening Visit
* Subject has renal and/or liver impairment defined as:

* Serum creatinine level of \>=1.4 mg/dL for females and \>=1.5 mg/dL for males at Screening Visit
* Subject has planned an elective surgical procedure in the coming 6 months
* Subject has evidence of a secondary cause of primary immune thrombocytopenia purpura
* Subject has a history of clinically relevant ongoing chronic infections
* Subject has a family history of primary immunodeficiency
* Subject has a clinically relevant active infection or has had a serious infection within 6 weeks prior to the first dose of IMP
* Subject has a history of known inflammatory bowel disease, diverticular disease, and gastric or esophageal ulceration
* Subject has experienced gastrointestinal bleed in the last 6 months prior to Screening Visit and/or has current gastritis or esophagitis
* Subject has a medical history of thrombosis
* Subject has a history of coagulopathy disorders other than ITP
* Subject has received a live vaccination within 8 weeks prior to the Baseline Visit; or intends to have a live vaccination during the course of the study or within 7 weeks following the final dose of IMP
* Subject has had prior treatment with rituximab in the 6 months prior to the Baseline Visit
* Subject has not completed the washout period for the immunosuppressants, biologics and other therapies
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Parexel

INDUSTRY

Sponsor Role collaborator

UCB Biopharma SRL

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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UCB Cares

Role: STUDY_DIRECTOR

001 844 599 2273 (UCB)

Locations

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Tp0001 1101

Adelaide, , Australia

Site Status

Tp0001 1302

Pleven, , Bulgaria

Site Status

Tp0001 1301

Sofia, , Bulgaria

Site Status

Tp0001 203

Olomouc, , Czechia

Site Status

Tp0001 201

Prague, , Czechia

Site Status

Tp0001 1201

Tbilisi, , Georgia

Site Status

Tp0001 401

Berlin, , Germany

Site Status

Tp0001 403

Düsseldorf, , Germany

Site Status

Tp0001 404

München, , Germany

Site Status

Tp0001 502

Florence, , Italy

Site Status

Tp0001 506

Torino, , Italy

Site Status

Tp0001 503

Udine, , Italy

Site Status

Tp0001 505

Vicenza, , Italy

Site Status

Tp0001 601

Chisinau, , Moldova

Site Status

Tp0001 702

Bialystok, , Poland

Site Status

Tp0001 703

Gdansk, , Poland

Site Status

Tp0001 701

Lodz, , Poland

Site Status

Tp0001 704

Poznan, , Poland

Site Status

Tp0001 705

Warsaw, , Poland

Site Status

Tp0001 802

Brasov, , Romania

Site Status

Tp0001 801

Bucharest, , Romania

Site Status

Tp0001 803

Craiova, , Romania

Site Status

Tp0001 902

Madrid, , Spain

Site Status

Tp0001 903

Madrid, , Spain

Site Status

Tp0001 901

Valencia, , Spain

Site Status

Tp0001 1001

London, , United Kingdom

Site Status

Tp0001 1002

London, , United Kingdom

Site Status

Tp0001 1003

London, , United Kingdom

Site Status

Tp0001 1004

Truro, , United Kingdom

Site Status

Countries

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Australia Bulgaria Czechia Georgia Germany Italy Moldova Poland Romania Spain United Kingdom

References

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Robak T, Kazmierczak M, Jarque I, Musteata V, Trelinski J, Cooper N, Kiessling P, Massow U, Woltering F, Snipes R, Ke J, Langdon G, Bussel JB, Jolles S. Phase 2 multiple-dose study of an FcRn inhibitor, rozanolixizumab, in patients with primary immune thrombocytopenia. Blood Adv. 2020 Sep 8;4(17):4136-4146. doi: 10.1182/bloodadvances.2020002003.

Reference Type RESULT
PMID: 32886753 (View on PubMed)

Smith B, Kiessling A, Lledo-Garcia R, Dixon KL, Christodoulou L, Catley MC, Atherfold P, D'Hooghe LE, Finney H, Greenslade K, Hailu H, Kevorkian L, Lightwood D, Meier C, Munro R, Qureshi O, Sarkar K, Shaw SP, Tewari R, Turner A, Tyson K, West S, Shaw S, Brennan FR. Generation and characterization of a high affinity anti-human FcRn antibody, rozanolixizumab, and the effects of different molecular formats on the reduction of plasma IgG concentration. MAbs. 2018 Oct;10(7):1111-1130. doi: 10.1080/19420862.2018.1505464. Epub 2018 Sep 12.

Reference Type DERIVED
PMID: 30130439 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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TP0001

Identifier Type: -

Identifier Source: org_study_id

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