A Study of Pirtobrutinib in Participants With Immune Thrombocytopenia

NCT ID: NCT06721013

Last Updated: 2026-02-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

58 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-07-30

Study Completion Date

2027-02-28

Brief Summary

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The purpose of the phase 1 part of this study is to evaluate how well pirtobrutinib is tolerated and what side effects may occur. The phase 2 part of the study will further investigate efficacy and safety of multiple pirtobrutinib dosages versus placebo.

The study drug will be administered orally in participants with Primary Immune Thrombocytopenia (ITP). Blood tests will be performed to check how much pirtobrutinib gets into the bloodstream and how long it takes the body to eliminate it.

The study will last up to approximately 16 weeks for phase 1 dose-escalation and 28 weeks for phase 2 dose-optimization, excluding screening.

Detailed Description

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Conditions

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Immune Thrombocytopenia (ITP)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Phase 1-Open label Sequential, Phase 2-Double-blind Parallel
Primary Study Purpose

BASIC_SCIENCE

Blinding Strategy

DOUBLE

Participants Investigators
Phase 1-Open label, Phase 2-Double-blind

Study Groups

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Pirtobrutinib Phase 1

Pirtobrutinib administered orally

Group Type EXPERIMENTAL

Pirtobrutinib

Intervention Type DRUG

Administered orally

Pirtobrutinib Phase 2

Pirtobrutinib administered orally

Group Type EXPERIMENTAL

Pirtobrutinib

Intervention Type DRUG

Administered orally

Placebo Phase 2

Placebo administered orally

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered orally

Interventions

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Pirtobrutinib

Administered orally

Intervention Type DRUG

Placebo

Administered orally

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Have a diagnosis of primary ITP, defined as isolated thrombocytopenia not associated with another known disease process
* Have documented history of response, defined as 2 or more platelet counts greater than or equal to 50,000/microliter (μL), to at least 1 prior line of therapy. Splenectomy is considered a line of therapy
* Have relapsed or treatment-resistant primary ITP, with no available therapies known to provide clinical benefit
* Have a platelet count less than 30,000/μL on 2 occasions more than 5 days apart in the 15 days before randomization
* Have adequate liver, renal, and hematologic functions as defined by a table
* Are willing to follow contraception requirements

Exclusion Criteria

* Have a history of any thrombotic or embolic event within 12 months before screening
* Had a transfusion with blood or blood products or plasmapheresis within 14 days (Phase 1) or within 28 days (Phase 2) of randomization
* Have significant cardiovascular disease
* Have a diagnosis or history of hematologic malignancy
* Have hepatitis B virus (HBV) defined as positive for antigen of hepatitis B (HBsAg) or polymerase chain reaction (PCR) positive for HBV deoxyribonucleic acid (DNA)
* Have hepatitis C virus (HCV) defined as positive for anti-HCV antibodies and PCR positive for HCV ribonucleic acid (RNA)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eli Lilly and Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 8 AM - 8 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

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USC Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status RECRUITING

Stanford University

Stanford, California, United States

Site Status NOT_YET_RECRUITING

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status RECRUITING

University of Miami Hospital and Clinics Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status NOT_YET_RECRUITING

Bleeding and Clotting Disorders Institute

Peoria, Illinois, United States

Site Status NOT_YET_RECRUITING

Ochsner Medical Center - New Orleans

New Orleans, Louisiana, United States

Site Status NOT_YET_RECRUITING

Mayo Clinic

Rochester, Minnesota, United States

Site Status NOT_YET_RECRUITING

Clinical Research Alliance

Westbury, New York, United States

Site Status RECRUITING

Texas Oncology-Central Austin

Austin, Texas, United States

Site Status NOT_YET_RECRUITING

MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Texas Oncology Gulf Coast

The Woodlands, Texas, United States

Site Status NOT_YET_RECRUITING

Nanfang Hospital of Southern Medical University

Guangzhou, , China

Site Status NOT_YET_RECRUITING

Qilu Hospital of Shandong University

Jinan, , China

Site Status NOT_YET_RECRUITING

Hematology Hospital of the Chinese Academy of Medical Sciences

Tianjin, , China

Site Status NOT_YET_RECRUITING

Union Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, , China

Site Status NOT_YET_RECRUITING

OUH

Odense C, , Denmark

Site Status RECRUITING

Hôpital Henri Mondor

Créteil, , France

Site Status RECRUITING

CHU Dijon - Hopital du Bocage

Dijon, , France

Site Status RECRUITING

CHU Bordeaux - Hôpital Haut-Lévêque

Pessac, , France

Site Status RECRUITING

Azienda Ospedaliera Universitaria Policlinico Sant'Orsola Malpighi IRCCS

Bologna, , Italy

Site Status RECRUITING

Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status NOT_YET_RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Roma, , Italy

Site Status RECRUITING

Azienda Sanitaria Universitaria Giuliano Isontina (ASU GI)

Trieste, , Italy

Site Status NOT_YET_RECRUITING

Haukeland University Hospital

Bergen, , Norway

Site Status NOT_YET_RECRUITING

Sykehuset Ostfold, Kalnes

Grålum, , Norway

Site Status NOT_YET_RECRUITING

St. Olavs Hospital Hf, Universitetssykehuset i Trondheim

Trondheim, , Norway

Site Status NOT_YET_RECRUITING

Pratia Onkologia Katowice

Katowice, , Poland

Site Status RECRUITING

Pratia MCM Krakow

Krakow, , Poland

Site Status RECRUITING

Aidport sp z o.o.

Skorzewo, , Poland

Site Status RECRUITING

MICS Centrum Medyczne Torun

Torun, , Poland

Site Status RECRUITING

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wroclawiu

Wroclaw, , Poland

Site Status NOT_YET_RECRUITING

Pusan National University Hospital

Busan, , South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, , South Korea

Site Status NOT_YET_RECRUITING

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status RECRUITING

Asan Medical Center

Seoul, , South Korea

Site Status NOT_YET_RECRUITING

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, , South Korea

Site Status RECRUITING

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario de Burgos

Burgos, , Spain

Site Status RECRUITING

Hospital General Universitario Morales Meseguer

Murcia, , Spain

Site Status RECRUITING

Clinica Universidad de Navarra

Pamplona, , Spain

Site Status RECRUITING

Bristol Haematology and Oncology Centre

Bristol, , United Kingdom

Site Status RECRUITING

St James's University Hospital

Leeds, , United Kingdom

Site Status RECRUITING

Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status RECRUITING

Royal London Hospital

London, , United Kingdom

Site Status NOT_YET_RECRUITING

Hammersmith Hospital

London, , United Kingdom

Site Status NOT_YET_RECRUITING

Countries

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United States China Denmark France Italy Norway Poland South Korea Spain United Kingdom

Central Contacts

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Trial questions or participation questions: 1-877-CTLILLY (1-877-285-4559) or

Role: CONTACT

1-317-615-4559

Physicians interested in becoming principal investigators please contact

Role: CONTACT

Related Links

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Other Identifiers

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27294

Identifier Type: -

Identifier Source: org_study_id

J2N-MC-JZNZ

Identifier Type: OTHER

Identifier Source: secondary_id

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