Effect of Lu AF35700 in Patients With Treatment-resistant Schizophrenia

NCT ID: NCT02717195

Last Updated: 2019-11-25

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1098 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-04-30

Study Completion Date

2018-10-08

Brief Summary

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To evaluate the efficacy of 10 and 20 mg/day of Lu AF35700 on schizophrenia symptoms in patients with treatment-resistant schizophrenia (TRS)

Detailed Description

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The study consists of a Screening Period (3 weeks), a single-blind Prospective Confirmation (PC) Period (6 weeks), a Double-blind Treatment (DBT) Period (10 weeks), and a Safety Follow-up Period (6 weeks).

Patients who did not fulfil the randomization criteria for the DBT Period, were withdrawn from the study after the PC period.

Patients who fulfilled the randomization criteria for the DBT Period, continued into the DBT Period and were randomized into one of 3 treatment arms (1:1:1) with either Lu AF35700 10 mg/day, Lu AF35700 20 mg/day or to continue the treatment allocated in PC Period (olanzapine or risperidone) at the dose set at last visit of PC Period. This mean that approximately one third of the confirmed treatment-resistant patients were randomised back to the failed treatment used in the PC Period.

Data was not collected separately for the DBT Olanzapine and DBT Risperidone participants, and there was no intent to compare Lu AF35700 to each drug separately.

Conditions

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Schizophrenia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Prospective Confirmation (PC) Period

Single (patient)-blinded treatment period with risperidone or olanzapine for 6 weeks

Group Type EXPERIMENTAL

Risperidone

Intervention Type DRUG

4-6 mg/day, encapsulated tablets, orally

Olanzapine

Intervention Type DRUG

15-20 mg/day, encapsulated tablets, orally

Double-blind Treatment (DBT) Period, Lu AF35700 10 mg

Eligible patients from PC Period (based on criteria to which investigator and patient are blinded), will be randomly assigned (1:1:1) double-blind treatment in DBT Period, 10 weeks

Group Type EXPERIMENTAL

Lu AF35700

Intervention Type DRUG

10 mg/day, encapsulated tablets, orally

DBT Period, Lu AF35700 20 mg

Eligible patients from PC Period (based on criteria to which investigator and patient are blinded), will be randomly assigned (1:1:1) double-blind treatment in DBT Period, 10 weeks

Group Type EXPERIMENTAL

Lu AF35700

Intervention Type DRUG

20 mg/day, encapsulated tablets, orally

DBT Period, Continued treatment from PC Period

Eligible patients from PC Period (based on criteria to which investigator and patient are blinded), will be randomly assigned (1:1:1) double-blind treatment in DBT Period,10 weeks. Patients in this arm will continue with same the treatment and dose as at last visit of PC Period

Group Type EXPERIMENTAL

Risperidone

Intervention Type DRUG

4-6 mg/day, encapsulated tablets, orally

Olanzapine

Intervention Type DRUG

15-20 mg/day, encapsulated tablets, orally

Interventions

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Risperidone

4-6 mg/day, encapsulated tablets, orally

Intervention Type DRUG

Olanzapine

15-20 mg/day, encapsulated tablets, orally

Intervention Type DRUG

Lu AF35700

10 mg/day, encapsulated tablets, orally

Intervention Type DRUG

Lu AF35700

20 mg/day, encapsulated tablets, orally

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* The patient has schizophrenia, diagnosed according to DSM-5(TM) (Diagnostic and Statistical Manual of Mental Disorders) and confirmed by the Mini International Neuropsychiatric Interview for Schizophrenia and Psychotic Disorders
* The patient is either an inpatient at a psychiatric setting or outpatient consulting a psychiatrist.
* Patients should be treated with adequate dose(s) and agent(s) of antipsychotic treatment for at least 2 weeks prior to Screening
* The patient has failed to show an adequate response in the level of psychotic symptoms despite at least one documented treatment trial with an adequate dose of an antipsychotic agent prescribed for an adequate time (at least lasting for 6 weeks) during 2 years prior to Screening. The failure to respond to the current antipsychotic treatment trial may be considered a retrospective failed treatment, if the patient was treated for 6 weeks with adequate dose(s) and agent(s)
* The patient has a PANSS total score of ≥80 and a score of ≥4 on at least 2 of the following PANSS items (at Screening and at the first visit of Period A)
* The patient has a CGI-S score of ≥4 at Screening and at the first visit of Period A

Exclusion Criteria

* The patient has any current primary psychiatric disorder other than schizophrenia as assessed by the Mini International Neuropsychiatric Interview (MINI)
* The patient is experiencing an acute exacerbation of his/her psychotic symptoms
* The patient has not responded to treatment with clozapine
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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H. Lundbeck A/S

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Email contact via H. Lundbeck A/S

Role: STUDY_DIRECTOR

[email protected]

Locations

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US1018

Bellflower, California, United States

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US1041

Cerritos, California, United States

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US1062

Costa Mesa, California, United States

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US1463

Culver City, California, United States

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US1104

Garden Grove, California, United States

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US1118

Glendale, California, United States

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US1114

National City, California, United States

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US1452

Oceanside, California, United States

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US1459

Oceanside, California, United States

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US1399

Orange, California, United States

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US1368

Orange, California, United States

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US1391

San Bernardino, California, United States

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US1464

Santa Ana, California, United States

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US1384

Sherman Oaks, California, United States

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US1392

Torrance, California, United States

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US1396

Washington D.C., District of Columbia, United States

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US1395

Bradenton, Florida, United States

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US1253

Jacksonville, Florida, United States

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US1130

Miami, Florida, United States

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US1318

North Miami, Florida, United States

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US1129

North Miami, Florida, United States

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US1402

Oakland Park, Florida, United States

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US1229

Orange City, Florida, United States

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US1453

Tampa, Florida, United States

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US1403

Atlanta, Georgia, United States

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US1009

Atlanta, Georgia, United States

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US1442

Decatur, Georgia, United States

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US1046

Chicago, Illinois, United States

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US1423

Hoffman Estates, Illinois, United States

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US1398

Shreveport, Louisiana, United States

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US1404

Shreveport, Louisiana, United States

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US1086

Flowood, Mississippi, United States

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US1444

Las Vegas, Nevada, United States

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US1426

Berlin, New Jersey, United States

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US1454

Marlton, New Jersey, United States

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US1405

Glen Oaks, New York, United States

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US1244

Jamaica, New York, United States

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US1394

New York, New York, United States

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US1416

New York, New York, United States

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US1171

Rochester, New York, United States

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US1190

Staten Island, New York, United States

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US1390

Charlotte, North Carolina, United States

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US1401

Charlotte, North Carolina, United States

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US1441

Hickory, North Carolina, United States

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US1124

Norristown, Pennsylvania, United States

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US1319

Charleston, South Carolina, United States

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US1451

Austin, Texas, United States

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US1065

Dallas, Texas, United States

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US1443

Fort Worth, Texas, United States

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BG1030

Burgas, , Bulgaria

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BG1028

Kazanlak, , Bulgaria

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BG1003

Lovech, , Bulgaria

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BG1032

Pazardzhik, , Bulgaria

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BG1008

Plovdiv, , Bulgaria

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BG1024

Sofia, , Bulgaria

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BG1026

Sofia, , Bulgaria

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BG1022

Tserova Koria, , Bulgaria

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BG1033

Varna, , Bulgaria

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BG1034

Varna, , Bulgaria

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BG1029

Veliko Tarnovo, , Bulgaria

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BG1027

Vratsa, , Bulgaria

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CA1017

Chatham, , Canada

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CA1034

Kingston, , Canada

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CA1003

Montreal, , Canada

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CA1033

Montreal, , Canada

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CA1029

Penticton, , Canada

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CA1039

Québec, , Canada

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CZ1023

Brno, , Czechia

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CZ1032

Brno, , Czechia

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CZ1037

Hostivice, , Czechia

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CZ1013

Lnáře, , Czechia

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CZ1038

Prague, , Czechia

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EE1016

Pärnu, , Estonia

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EE1007

Tallinn, , Estonia

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EE1017

Viljandi, , Estonia

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FI1032

Espoo, , Finland

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FI1030

Kuopio, , Finland

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FI1027

Turku, , Finland

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MX1024

Durango, , Mexico

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MX1011

Guadalajara, , Mexico

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MX1021

Guadalajara, , Mexico

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MX1022

Guadalajara, , Mexico

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MX1020

México, , Mexico

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MX1005

Monterrey, , Mexico

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MX1007

Monterrey, , Mexico

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MX1015

Monterrey, , Mexico

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MX1016

Monterrey, , Mexico

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MX1018

San Luis Potosí City, , Mexico

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PL1025

Bełchatów, , Poland

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PL1043

Bialystok, , Poland

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PL1026

Gorlice, , Poland

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PL1060

Lodz, , Poland

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PL1027

Lublin, , Poland

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PL1058

Pruszcz Gdański, , Poland

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PL1061

Pruszków, , Poland

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PL1059

Torun, , Poland

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PL1051

Wroclaw, , Poland

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RO1024

Bucharest, , Romania

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RO1022

Campulung Muscel, , Romania

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RO1025

Sibiu, , Romania

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RO1004

Târgu Mureş, , Romania

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RU1021

Nikol’skoye, Gatchinckiy District, Russia

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RU1009

Arkhangelsk, , Russia

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RU1006

Moscow, , Russia

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RU1051

Moscow, , Russia

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RU1055

Moscow, , Russia

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RU1023

Saint Petersburg, , Russia

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RU1028

Saint Petersburg, , Russia

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RU1030

Saint Petersburg, , Russia

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RU1031

Saint Petersburg, , Russia

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RU1049

Saint Petersburg, , Russia

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RU1052

Saint Petersburg, , Russia

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RU1053

Saint Petersburg, , Russia

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RU1056

Saint Petersburg, , Russia

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RU1050

Yaroslavl, , Russia

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RS1008

Belgrade, , Serbia

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RS1010

Belgrade, , Serbia

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RS1012

Belgrade, , Serbia

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RS1011

Kragujevac, , Serbia

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RS1016

Kragujevac, , Serbia

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RS1017

Kragujevac, , Serbia

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RS1003

Niš, , Serbia

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RS1009

Novi Kneževac, , Serbia

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SK1014

Bratislava, , Slovakia

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SK1024

Bratislava, , Slovakia

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SK1015

Rožňava, , Slovakia

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SK1025

Svidník, , Slovakia

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SK1026

Zlaté Moravce, , Slovakia

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ES1047

Barcelona, , Spain

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ES1012

Madrid, , Spain

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ES1008

Málaga, , Spain

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ES1048

Oviedo, , Spain

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ES1049

Zamora, , Spain

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UA1019

Dnipropetrovsk, , Ukraine

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UA1017

Kharkiv, , Ukraine

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UA1022

Kharkiv, , Ukraine

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UA1031

Kharkiv, , Ukraine

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UA1035

Kharkiv, , Ukraine

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UA1028

Kherson, , Ukraine

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UA1029

Kherson, , Ukraine

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UA1027

Kiev, , Ukraine

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UA1030

Kiev, , Ukraine

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UA1033

Lviv, , Ukraine

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UA1020

Odesa, , Ukraine

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UA1032

Odesa, , Ukraine

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UA1001

Poltava, , Ukraine

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UA1036

Vinnitsa, , Ukraine

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Countries

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United States Bulgaria Canada Czechia Estonia Finland Mexico Poland Romania Russia Serbia Slovakia Spain Ukraine

References

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Kane JM, Kinon BJ, Forray C, Such P, Mittoux A, Lemming OM, Hertel P, Howes OD; DayBreak and Debut study investigators. Efficacy and safety of Lu AF35700 in treatment-resistant schizophrenia: A randomized, active-controlled trial with open-label extension. Schizophr Res. 2022 Oct;248:271-278. doi: 10.1016/j.schres.2022.09.012. Epub 2022 Sep 14.

Reference Type DERIVED
PMID: 36115192 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2014-003569-12

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

16159A

Identifier Type: -

Identifier Source: org_study_id

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