Dysport® Treatment of Urinary Incontinence in Adults Subjects With Neurogenic Detrusor Overactivity (NDO) Due to Spinal Cord Injury or Multiple Sclerosis - Study 1

NCT ID: NCT02660138

Last Updated: 2022-09-28

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

227 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-03-31

Study Completion Date

2019-02-14

Brief Summary

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The purpose of this study is to provide confirmatory evidence of the safety and efficacy of two Dysport® (AbobotulinumtoxinA) doses (600 units \[U\] and 800 U), compared to placebo in reducing urinary incontinence (UI) in adult subjects treated for neurogenic detrusor overactivity (NDO) due to spinal cord injury (SCI) or multiple sclerosis (MS).

Detailed Description

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Conditions

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Urinary Incontinence Overactive Bladder

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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600 U Dysport® Group

Group Type EXPERIMENTAL

Botulinum toxin type A

Intervention Type BIOLOGICAL

600 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

600 U Dysport® Placebo Group

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

AbobotulinumtoxinA Placebo 600 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

800 U Dysport® Group

Group Type EXPERIMENTAL

Botulinum toxin type A

Intervention Type BIOLOGICAL

800 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

800 U Dysport® Placebo Group

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

AbobotulinumtoxinA Placebo 800 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

Interventions

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Botulinum toxin type A

600 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

Intervention Type BIOLOGICAL

Botulinum toxin type A

800 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

Intervention Type BIOLOGICAL

Placebo

AbobotulinumtoxinA Placebo 600 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

Intervention Type DRUG

Placebo

AbobotulinumtoxinA Placebo 800 U intra detrusor injection in two treatment periods (Initial and Retreatment phase) delivered at 30 injection points

Intervention Type DRUG

Other Intervention Names

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AbobotulinumtoxinA (Dysport®) Clostridium BTX-A-haemagglutinin complex AbobotulinumtoxinA (Dysport®) Clostridium BTX-A-haemagglutinin complex

Eligibility Criteria

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Inclusion Criteria

* Urinary Incontinence for at least 3 months prior to Screening as a result of Neurogenic Detrusor Overactivity due to Spinal Cord Injury or Multiple Sclerosis.
* Subjects with Spinal Cord Injury must have a stable neurological injury at T1 level or below which occurred at least 6 months prior to Screening.
* Subjects with Multiple Sclerosis must be clinically stable in the investigator's opinion, with no exacerbation (relapse) of MS for at least 3 months prior to Screening.
* Subjects must have had an inadequate response after at least 4 weeks of oral medications used in the treatment of NDO (e.g. anticholinergics, beta-3 agonists) and/or have intolerable side-effects.
* Routinely performing Clean Intermittent Catheterization (CIC) to ensure adequate bladder emptying.
* An average of at least two episodes per day of Urinary Incontinence recorded on the screening bladder diary.

Exclusion Criteria

* Any current condition (other than NDO) that may impact on bladder function.
* Previous or current, tumour or malignancy affecting the spinal column or spinal cord, or any other unstable cause of SCI.
* Any condition that will prevent cystoscopic treatment administration or CIC usage, e.g. urethral strictures.
* Current indwelling bladder catheter, or removal of indwelling bladder catheter less than 4 weeks prior to Screening.
* BTX-A treatment within 9 months prior to Screening for any urological condition (e.g. detrusor or urethral sphincter treatments).
* Any neuromodulation/electrostimulation usage for urinary symptoms/incontinence within 4 weeks prior to Screening. Any implanted neuromodulation device must be switched off at least 4 weeks prior to Screening.
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ipsen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ipsen Medical Director

Role: STUDY_DIRECTOR

Ipsen

Locations

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UAB School of Medicine Spain Rehabilitation Center (SRC)

Birmingham, Alabama, United States

Site Status

Urological Associates of Southern Arizona, P.C.

Tucson, Arizona, United States

Site Status

Atlantic Urology Medical Group

Long Beach, California, United States

Site Status

USC Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

UC Davis Medical Center

Sacramento, California, United States

Site Status

University of Colorado Denver

Aurora, Colorado, United States

Site Status

Women's Health Specialty Care

Farmington, Connecticut, United States

Site Status

Gousse Urology - The Bladder Heath and Reconstructive Urology Institute

Miramar, Florida, United States

Site Status

The Iowa Clinic, PC

West Des Moines, Iowa, United States

Site Status

Chesapeake Urology Associates, PA

Owings Mills, Maryland, United States

Site Status

University of Michigan Hospital

Ann Arbor, Michigan, United States

Site Status

Weill Cornell Medical College

Denville, New Jersey, United States

Site Status

Delaware Valley Urology,IIC

Voorhees Township, New Jersey, United States

Site Status

Urology Group of New Mexico, PC

Albuquerque, New Mexico, United States

Site Status

New York University Langone Medical Center and School of Medicine

New York, New York, United States

Site Status

New York-Presbyterian Hospital/Weill Cornell Medical Center

New York, New York, United States

Site Status

Advanced Urology Centers of New York

Plainview, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

University of North Carolina School of Medicine

Chapel Hill, North Carolina, United States

Site Status

Levine Cancer Institute

Charlotte, North Carolina, United States

Site Status

Louis Stokes Cleveland Veterans Affairs Medical Center

Cleveland, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Lancaster Urology

Lancaster, Pennsylvania, United States

Site Status

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, United States

Site Status

Medical University of South Carolina (MUSC)

Charleston, South Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Urology Clinics of North Texas

Dallas, Texas, United States

Site Status

Houston Methodist Hospital

Houston, Texas, United States

Site Status

Lahey Hospital & Medical Center

Burlington, Vermont, United States

Site Status

Urology of Virginia, PLLC

Virginia Beach, Virginia, United States

Site Status

Integrity Medical Research

Mountlake Terrace, Washington, United States

Site Status

Medical College of Wisconsin - Freodert Hospital

Milwaukee, Wisconsin, United States

Site Status

CHUS - Hôpital Fleurimont

Sherbrooke, , Canada

Site Status

Sunnybrook Health Sciences Centre

Toronto, , Canada

Site Status

UBC Hospital - Koerner Pavilion

Vancouver, , Canada

Site Status

Spinal Cord Research Centre, University of Manitoba

Winnipeg, , Canada

Site Status

Fakultní Nemocnice Brno

Brno, , Czechia

Site Status

Karlovarska krajska nemocnice, a.s.

Karlovy Vary, , Czechia

Site Status

Krajská Nemocnice Liberec, a.s.

Liberec, , Czechia

Site Status

Uromedical Center s.r.o.

Olomouc, , Czechia

Site Status

Fakultní nemocnice Královské Vinohrady

Prague, , Czechia

Site Status

Všeobecná fakultní nemocnice v Praze

Prague, , Czechia

Site Status

Thomayerova nemocnice

Prague, , Czechia

Site Status

Fakultní Nemocnice v Motole

Prague, , Czechia

Site Status

Urologicka Ordinace s.r.o.

Sternberk, , Czechia

Site Status

Azienda Ospedaliero-Universitaria Careggi - Dipartimento Di Neuro-Urologia

Florence, , Italy

Site Status

Farmacia Istituto Ospedaliero ICOT "Marco Pasquali"

Latina, , Italy

Site Status

Azienda Ospedaliera di Perugia - Ospedale Santa Maria della Misericordia

Perugia, , Italy

Site Status

Viale Oxford, 81

Roma, , Italy

Site Status

Ospedale "Bolognini" di Seriate

Seriate, , Italy

Site Status

Azienda Ospedaliera di Perugia - Ospedale Santa Maria della Misericordia

Udine, , Italy

Site Status

VU University Medical Center

Amsterdam, , Netherlands

Site Status

Radboud UMC

Nijmegen, , Netherlands

Site Status

Erasmus MC

Rotterdam, , Netherlands

Site Status

Wojewódzki Szpital Zespolony w Elblągu

Elblag, , Poland

Site Status

Nzoz Neuro-Medic Poradnia Wielospecjalistyczna

Katowice, , Poland

Site Status

NZOZ Heureka

Piaseczno, , Poland

Site Status

Szpital Kliniczny Dzieciątka Jezus w Warszawie

Warsaw, , Poland

Site Status

EuroMediCare Szpital Specjalistyczny z Przychodnią we Wrocławiu

Wroclaw, , Poland

Site Status

Hospital de Braga

Braga, , Portugal

Site Status

Centro Hospitalar do Alto Ave, EPE

Guimarães, , Portugal

Site Status

British Hospital

Lisbon, , Portugal

Site Status

Centro Hospitalar do Porto, EPE - Hospital Geral de Santo António

Porto, , Portugal

Site Status

Centro Hospitalar de São João, EPE - Hospital de São João

Porto, , Portugal

Site Status

Gnosis Evomed

Bucharest, , Romania

Site Status

Spitalul Clinic Colentina

Bucharest, , Romania

Site Status

Spitalul Clinic Fundeni Bucureşti

Bucharest, , Romania

Site Status

Hifu Terramed Conformal S.R.L

Bucharest, , Romania

Site Status

Spitalul Clinic Judeţean Mureş

Târgu Mureş, , Romania

Site Status

88 Olympic-ro 43-gil, Songpa-gu

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Ulsan University Hospital (UUH)

Ulsan, , South Korea

Site Status

Ankara Üniversitesi Tıp Fakültesi

Ankara, , Turkey (Türkiye)

Site Status

Medipol Mega University Hospital

Bağcılar, , Turkey (Türkiye)

Site Status

Uludag Universitesi Tip Fakultesi, Uroloji Anabilim Dali, Gorukle

Bursa, , Turkey (Türkiye)

Site Status

Marmara Üniversitesi Eğitim ve Araştırma Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status

Istanbul Medeniyet Universitesi Goztepe Egitim ve Arastirma Hastanesi Merdivenköy Mah

Istanbul, , Turkey (Türkiye)

Site Status

Erciyes Üniversitesi Tıp Fakültesi

Kayseri, , Turkey (Türkiye)

Site Status

Kocaeli Üniversitesi Tıp Fakültesi

Kocaeli, , Turkey (Türkiye)

Site Status

Celal Bayar Universitesi Hafsa Sultan Hastanesi

Manisa, , Turkey (Türkiye)

Site Status

Ondokuz Mayıs Üniversitesi Tıp Fakültesi

Samsun, , Turkey (Türkiye)

Site Status

Countries

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United States Canada Czechia Italy Netherlands Poland Portugal Romania South Korea Turkey (Türkiye)

References

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Kennelly M, Cruz F, Herschorn S, Abrams P, Onem K, Solomonov VK, Del Rosario Figueroa Coz E, Manu-Marin A, Giannantoni A, Thompson C, Vilain C, Volteau M, Denys P; Dysport CONTENT Program Group. Efficacy and Safety of AbobotulinumtoxinA in Patients with Neurogenic Detrusor Overactivity Incontinence Performing Regular Clean Intermittent Catheterization: Pooled Results from Two Phase 3 Randomized Studies (CONTENT1 and CONTENT2). Eur Urol. 2022 Aug;82(2):223-232. doi: 10.1016/j.eururo.2022.03.010. Epub 2022 Apr 7.

Reference Type DERIVED
PMID: 35400537 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2015-003471-30

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D-FR-52120-222

Identifier Type: -

Identifier Source: org_study_id

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