Acthar for Treatment-Resistant or Treatment-Intolerant Proteinuria

NCT ID: NCT02633046

Last Updated: 2021-08-04

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

63 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-10-10

Study Completion Date

2020-08-27

Brief Summary

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Focal segmental glomerulosclerosis (FSGS) is a condition that harms the kidney "filters" that remove waste from the blood. Proteins are supposed to stay in the blood. Damaged "filters" let protein get into the kidney.

FSGS is a serious condition that can lead to kidney failure. The only treatment for kidney failure is dialysis or kidney transplant.

Proteinuria means too much protein came through the kidneys into the urine.

If the doctor cannot figure out what is causing the problem, it is primary (idiopathic) FSGS. This kind of FSGS is very hard to treat.

This study will test Acthar in patients with this condition who have not responded to other treatments. It primarily investigates how well the therapy is tolerated by the patients and how well they respond to this treatment.

Detailed Description

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Conditions

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Idiopathic Focal Segmental Glomerulosclerosis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Acthar Gel

Acthar Gel, 1 mL (80 U) by subcutaneous injection (SC) 3x/week will be administered to all participants from Week 0 to 50. Tapering of dose to 1 mL SC 2x/week will be allowed for safety and/ tolerability issues. Once the dose is tapered to 1 mL SC 2x/week it must remain at this level. Participants unable to tolerate 1 mL SC 2x/week will be discontinued. All participants will have an End of Study/Early Termination Visit 4 weeks after discontinuing Investigational Medicinal Product (IMP).

Group Type OTHER

Acthar Gel

Intervention Type DRUG

Acthar Gel 80 U/mL solution for subcutaneous injection

Interventions

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Acthar Gel

Acthar Gel 80 U/mL solution for subcutaneous injection

Intervention Type DRUG

Other Intervention Names

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Acthar

Eligibility Criteria

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Inclusion Criteria

Potential participants must meet the following summary criteria for inclusion in the study:

* Is male or non-pregnant, non-lactating female
* Has primary FSGS, is nephrotic and did not achieve at least partial proteinuria response with prior therapy
* Has been treated with an angiotensin converting enzyme inhibitor or receptor blocker (or have documented intolerance), for at least 4 weeks before screening
* Has blood pressure no higher than 150/90 mmHg

Exclusion Criteria

Potential participants will not be eligible for the the study if they meet the following summary criteria:

* Has hepatitis B or C, tuberculosis, or other contraindication listed on the United States (US) Prescribing Information for Acthar
* Has Type 1 or Type 2 diabetes mellitus or any clinically significant infection
* Has received specific treatments at exclusionary time points per protocol
* Has been involved in a therapeutic drug/device trial (other than for FSGS) within 4 weeks before screening
* Has any other condition that might, per protocol or in the opinion of the investigator, compromise:

1. the safety and well-being of the participant or their offspring
2. the safety of study staff
3. analysis of results
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Mallinckrodt ARD LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Team Leader

Role: STUDY_DIRECTOR

Mallinckrodt

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

AKDHC Medical Research Services, LLC

Tucson, Arizona, United States

Site Status

California Institute of Renal Research

Chula Vista, California, United States

Site Status

Stanford University

Stanford, California, United States

Site Status

VERITAS Research Corp

Miami Lakes, Florida, United States

Site Status

Genesis Clinical Research Corp

Tampa, Florida, United States

Site Status

GA Nephrology

Lawrenceville, Georgia, United States

Site Status

NANI Research

Hinsdale, Illinois, United States

Site Status

University of Louisville Research Foundation, Inc.

Louisville, Kentucky, United States

Site Status

Ochsner Clinic Foundation, Baton Rouge

Baton Rouge, Louisiana, United States

Site Status

NKDHC Medical Research Services, LLC

Las Vegas, Nevada, United States

Site Status

Icahn School of Medicine-Mt. Sinai

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Metrolina Nephrology Associates

Charlotte, North Carolina, United States

Site Status

Brookview Hills Research Associates, LLC

Winston-Salem, North Carolina, United States

Site Status

University of Cincinnati Physicians Company, LLC

Cincinnati, Ohio, United States

Site Status

Cincinnati VA Medical Center

Cincinnati, Ohio, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Texas Tech University Health Science Center

Amarillo, Texas, United States

Site Status

Texas Kidney Institute (Neprhotex Research Group)

Dallas, Texas, United States

Site Status

University of Wisconsin Wisconsin Dialysis Institute

Madison, Wisconsin, United States

Site Status

Centro de Salud Renal Junín SRL

Junín, Buenos Aires, Argentina

Site Status

Centro de Investigaciones Médicas

Mar del Plata, Buenos Aires, Argentina

Site Status

Sanatorio Allende

Córdoba, , Argentina

Site Status

Renal Research Group

Gosford, New South Wales, Australia

Site Status

Liverpool Hospital

Liverpool, New South Wales, Australia

Site Status

Westmead Hospita

Westmead, New South Wales, Australia

Site Status

Royal Brisbane and Women's Hospital

Herston, Queensland, Australia

Site Status

Launceston Hospital

Launceston, Tasmania, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Sunshine Hopital - Western Health

St Albans, Victoria, Australia

Site Status

Hospital Dr. Hernán Henríquez Aravena

Temuco, Región de la Araucanía, Chile

Site Status

Clinica Davila

Santiago, RM, Chile

Site Status

Investigación Nefrológica SC

Cuernavaca, Morelos, Mexico

Site Status

Hospital y Clínica OCA S.A de C.V

Monterrey, Nuevo León, Mexico

Site Status

Hospital Nacional Cayetano Heredia

San Martín de Porres, Lima region, Peru

Site Status

Hospital Nacional Alberto Sabogal

Lima, , Peru

Site Status

Hospital Nacional Arzobispo Loayza

Lima, , Peru

Site Status

Hospital Nacional Hospital Maria Auxiliadora

Lima Lima, , Peru

Site Status

Şişli Etfal Hamidiye Training and Research Hospital

Istanbul, Sisli, Turkey (Türkiye)

Site Status

İstanbul University Faculty of Medicine

Istanbul, Topkapi, Turkey (Türkiye)

Site Status

Ankara NumuneTraining and Research Hospital

Ankara, , Turkey (Türkiye)

Site Status

Ankara Training and Research Hospital

Ankara, , Turkey (Türkiye)

Site Status

İstanbul University Faculty of Medicine

Istanbul, , Turkey (Türkiye)

Site Status

Kocaeli University Faculty of Medicine

Kocaeli, , Turkey (Türkiye)

Site Status

Marmara University Faculty of Medicine

Maltepe, , Turkey (Türkiye)

Site Status

Mersin University Faculty of Medicine

Mersin, , Turkey (Türkiye)

Site Status

Countries

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United States Argentina Australia Chile Mexico Peru Turkey (Türkiye)

References

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Hodson EM, Sinha A, Cooper TE. Interventions for focal segmental glomerulosclerosis in adults. Cochrane Database Syst Rev. 2022 Feb 28;2(2):CD003233. doi: 10.1002/14651858.CD003233.pub3.

Reference Type DERIVED
PMID: 35224732 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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MNK14224049

Identifier Type: -

Identifier Source: org_study_id

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