ACTH Treatment of APOL1- Associated Nephropathy

NCT ID: NCT02006849

Last Updated: 2017-11-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

WITHDRAWN

Clinical Phase

NA

Study Classification

INTERVENTIONAL

Study Start Date

2014-01-31

Study Completion Date

2019-01-31

Brief Summary

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The purpose of this research study is to determine if the study drug H.C. Acthar gel slows the progression of your kidney disease. This drug is a steroid-based medicine with fewer side effects than other steroids used for treatment of kidney diseases similar to APOL1 nephropathy.

Detailed Description

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Conditions

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Kidney Disease

Keywords

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AfricanAmericans Hypertension Proteinuria ApoL1 gene

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Acthar 40 units

Acthar 40 units subcutaneously three times a week for patients with sub-nephrotic proteinuria.

Group Type OTHER

Acthar

Intervention Type DRUG

FDA approved drug being used in this study for sub-nephrotic proteinuria. Given Investigational New Drug (IND) exemption by FDA.

Acthar 80 units

Acthar 80 units subcutaneously twice a week for patients with nephrotic proteinuria.

Group Type OTHER

Acthar

Intervention Type DRUG

FDA approved drug being used in this study for sub-nephrotic proteinuria. Given Investigational New Drug (IND) exemption by FDA.

Interventions

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Acthar

FDA approved drug being used in this study for sub-nephrotic proteinuria. Given Investigational New Drug (IND) exemption by FDA.

Intervention Type DRUG

Other Intervention Names

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Repository Corticotropin

Eligibility Criteria

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Inclusion Criteria

* Non-diabetic African-American with two APOL1-risk genotypes
* Age ≥21 years
* BMI \< 40 kg/m2
* Hemoglobin A1c \<6.5%
* eGFR ≥30 ml/min/1.73m2
* Historical urine protein: creatinine ratio ≥ 1.0 g/g
* Strong clinical suspicion of APOL1-associated nephropathy or history of biopsy proven focal segmental glomerulosclerosis (FSGS) or focal global glomerulosclerosis (FGGS)
* Women of childbearing potential: negative serum pregnancy test at Screening and agreement to follow a medically acceptable form of contraception for the duration of Acthar administration and 4 weeks thereafter

Exclusion Criteria

* Diagnosis of diabetes mellitus and/or on pharmacologic treatment for diabetes
* Medical condition that could cause secondary FSGS
* History of sensitivity to steroids (psychosis, steroid-induced diabetes)
* Contraindication to Acthar per package insert: scleroderma, osteoporosis, systemic fungal infections, ocular herpes simplex, recent surgery (within previous 6 months), history of or the presence of peptic ulcer (within 6 months prior to Screening), adrenal insufficiency or hyperfunction.
* Acute glaucoma diagnosed ≤3 months prior to Screening
* Biopsy proven glomerular disease other than FSGS or FGGS
* Live or live attenuated vaccine received within 1 month prior to screening, or planned administration once enrolled in the study
* Uncontrolled hypertension (HTN) (≥ 180/110 mmHg) and frequent admissions (≥1 admission per 6 months interval) for hypertensive urgency or hypertensive emergency
* Unstable cardiovascular disease: history of congestive heart failure (NYHA Functional Class III-IV); history of dilated cardiomyopathy with ejection fraction \< 40%; any of the following events within 3 months of screening: unstable angina, myocardial infarction, coronary artery bypass graft or percutaneous transluminal coronary angioplasty, transient ischemic attack or cerebrovascular accident, unstable arrhythmia
* Uncontrolled volume overload: history of moderate or severe peripheral edema; on loop diuretics ≥ 120 mg daily of furosemide or ≥ 3.0 mg daily of bumetanide or ≥ 150 mg daily of ethacrynic acid or ≥ 60 mg daily of torsemide;
* History of secondary hypertension (i.e., renal artery stenosis, primary aldosteronism or pheochromocytoma)
* Significant comorbidities (e.g., advanced malignancy, advanced liver disease) with a life expectancy of less than 1 year
* Subject is expected to initiate dialysis within 6 months
* Previous treatment on a drug being investigated for the treatment of FSGS
* Known diagnosis of Human Immunodeficiency Virus, Hepatitis B, or Hepatitis C
* Known history of a primary immunodeficiency or an underlying condition such as splenectomy that predisposes the subject to infections
* Systemic hematologic disease (e.g., hematologic malignancy, sickle cell anemia, myelodysplastic syndrome)
* Current malignancy or history of malignancy within 5 years of screening, with the exception of non-melanoma skin cancers and cervical intraepithelial neoplasia
* Treatment for any malignancy (e.g., radiation, chemotherapy, hormone therapy, or biologics) within 5 years of screening, with the exception of locally excised non-melanoma skin cancer or cervical intraepithelial neoplasia
* Pregnant or breast feeding, or might become pregnant during the study or within 4 weeks after the end of treatment
* Female of reproductive potential not willing to use highly effective methods of birth control during treatment and for 4 weeks after the end of treatment
* Currently receiving systemic antibiotics for treatment of an active infection; or history of frequent infections (more than one event per 6 months)
* History of any organ transplant
* Bipolar disorder, or Major Depressive Disorder characterized by severe depression requiring hospitalization, or history of suicidal ideation/attempts
* Currently enrolled in another interventional study, or less than 4 weeks since ending another interventional study(s) or receiving investigational agents(s)
* Subject has a disorder that, in the opinion of the investigator, may compromise the ability of the subject to give written informed consent and/or comply with all required study procedures.
Minimum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Wake Forest University Health Sciences

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mariana Murea, MD

Role: PRINCIPAL_INVESTIGATOR

Wake Forest University Health Sciences

Locations

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Wake Forest Baptist Medical Center

Winston-Salem, North Carolina, United States

Site Status

Countries

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United States

Other Identifiers

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IRB00024943

Identifier Type: -

Identifier Source: org_study_id