A Phase 1 Study of Fisogatinib (BLU-554) in Patients With Hepatocellular Carcinoma

NCT ID: NCT02508467

Last Updated: 2024-04-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

146 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-07-31

Study Completion Date

2024-02-28

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a Phase 1, open-label, first-in-human (FIH) study designed to evaluate the safety, tolerability, pharmacokinetics (PK), pharmacodynamics (PD), and preliminary antineoplastic activity of fisogatinib (formerly known as BLU- 554) administered orally in patients with FGF19 IHC+ hepatocellular carcinoma (HCC). The study consists of 3 parts, a dose-escalation part (Part 1), an expansion part (Part 2) exploring a once daily (qd) dosing schedule at the recommended Phase 2 dose (RP2D), and a Part 3 expansion of the qd dosing schedule at the RP2D in TKI naive patients.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Hepatocellular Carcinoma (HCC)

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Fisogatinib (BLU-554)

Fisogatinib (BLU-554) capsules for oral administration.

Group Type EXPERIMENTAL

Fisogatinib (BLU-554)

Intervention Type DRUG

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Fisogatinib (BLU-554)

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

BLU-554

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Confirmed diagnosis of HCC by histological examination or by non-invasive criteria according to European Association for the Study of the Liver (EASL) or American Association for the Study of Liver Disease (AASLD) guidelines (Part 1, 2 and 3).
* For Part 1 and 2, the patient has unresectable disease and has been previously treated with sorafenib, has declined treatment with sorafenib, or does not have access to sorafenib.
* For Part 3, the patient has not received prior treatment with a TKI.
* Child-Pugh class A with no clinically apparent ascites
* Eastern Cooperative Oncology Group (ECOG) performance status of 0-1
* For Part 1, willing to provide archived tumor tissue (if available) and willing to undergo pre- and on-treatment tumor biopsy (if considered safe and medically feasible by the treating investigator)
* For Part 2 and 3, all patients must have an FGF19 IHC result available. Only FGF19 IHC+ HCC patients will be eligible for Part 3.

Exclusion Criteria

* Central nervous system metastases
* Platelet count \<75,000/mL
* Absolute neutrophil count \<1000/mL
* Hemoglobin \<8 g/dL
* Aspartate aminotransferase (AST) or alanine aminotransferase (ALT) \>5x the upper limit of normal (ULN)
* Total bilirubin \>2.5 mg/dL
* International normalized ratio (INR) \>2.3 or prothrombin time (PT) \>6 seconds above control
* Estimated (Cockroft-Gault formula) or measured creatinine clearance \<40 mL/min
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Blueprint Medicines Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Inland Empire Liver Foundation

Rialto, California, United States

Site Status

University of Miami - Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status

H. Lee Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Ochsner Cancer Institute

New Orleans, Louisiana, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Mount Sinai Medical Center

New York, New York, United States

Site Status

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status

Zhejiang Cancer Hospital

Hangzhou, Gongshu District, China

Site Status

Nanfang Hospital

Guangzhou, Guangdong, China

Site Status

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, China

Site Status

Henan Cancer Hospital

Zhengzhou, Henan, China

Site Status

Hunan Cancer Hospital, Radioactive Interventional Department

Changsha, Hunan, China

Site Status

The Chinese People's Liberation Army 81 Hospital

Nanjing, Jiangsu, China

Site Status

Nantong Tumor Hospital

Nantong, Jiangsu, China

Site Status

Jilin Cancer Hospital

Changchun, Jilin, China

Site Status

Jilin University the First Affiliated Hospital

Changchun, Jilin, China

Site Status

Fudan University Zhongshan Hospital

Xuhui, Shanghai City, China

Site Status

West China Hospital, Sichuan University

Chengdu, Sichuan, China

Site Status

Tianjin Medical University Cancer Institute & Hospital, Hepatobiliary Oncology Department

Tianjin, West Lake District, China

Site Status

Fudan University Shanghai Cancer Center

Shanghai, Xuhui District, China

Site Status

The First Affiliated Hospital, College of Medicine, Zhejiang University

Hangzhou, Zhejiang, China

Site Status

Hospital Beaujon

Clichy, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Johannes Gutenberg University Mainz - University Medical Center

Mainz, Rhineland-Palatine, Germany

Site Status

University of Frankfurt

Frankfurt, , Germany

Site Status

Prince of Wales Hospital

Hong Kong, , Hong Kong

Site Status

Queen Mary Hospital

Hong Kong, , Hong Kong

Site Status

IRCCS Foundation - National Institute of Tumors

Milan, , Italy

Site Status

National Cancer Centre

Singapore, , Singapore

Site Status

National Cancer Center

Gyeonggi-do, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Vall d'Hebron Institute of Oncology

Barcelona, , Spain

Site Status

Inselspital Bern

Bern, , Switzerland

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

University of Liverpool - Clatterbridge Cancer Centre

Bebington, , United Kingdom

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

Guy's Hospital

London, , United Kingdom

Site Status

University College London

London, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States China France Germany Hong Kong Italy Singapore South Korea Spain Switzerland Taiwan United Kingdom

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2015-001662-26

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

BLU-554-1101

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.