Study of Leuprolide Acetate Injectable Suspension in the Treatment of Central Precocious Puberty

NCT ID: NCT02452931

Last Updated: 2020-06-02

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

64 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-08-31

Study Completion Date

2018-09-05

Brief Summary

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This study determines the effectiveness of leuprolide acetate 45 mg for injectable suspension for treatment of children with Central Precocious Puberty.

Detailed Description

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Leuprolide acetate is a GnRH agonist that inhibits pituitary gonadotropin secretion by binding to the GnRH receptors and blocking downstream hormone synthesis. The steady decrease in hormone synthesis (LH and FSH) leads to a suppression of testicular and ovarian steroidogenesis. In children with CPP, this steady decrease in hormone synthesis disrupts the progression of puberty.

Conditions

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Precocious Puberty, Central

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Assigned Intervention

Leuprolide acetate 45 mg will be administered as a subcutaneous injection at 6-month intervals for the 12 month study period.

Group Type EXPERIMENTAL

Leuprolide Acetate 45 mg

Intervention Type DRUG

Subcutaneous injection

Interventions

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Leuprolide Acetate 45 mg

Subcutaneous injection

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Females age 2 to 8 years (inclusive) or males age 2 to 9 years (inclusive)
* Confirmed diagnosis of CPP within 12 months of Baseline Visit (Day 0) but have not received prior GnRH agonist treatment for CPP
* Pubertal-type LH response following an abbreviated GnRHa stimulation test before treatment initiation
* Clinical evidence of puberty, defined as Tanner stage ≥ 2 for breast development in females or testicular volume ≥ 4 mL in males
* Difference between bone age (Greulich and Pyle method) and chronological age ≥ 1 year

Exclusion Criteria

* Gonadotropin-independent (peripheral) precocious puberty
* Prior or current GnRH treatment for CPP
* Prior or current therapy with medroxyprogesterone acetate, growth hormone or insulin-like growth factor-1 (IGF-1)
* Diagnosis of short stature (ie, 2.25 standard deviations (SD) below the mean height for age)
* Known history of seizures, epilepsy, and/or central nervous system disorders that may be associated with seizures or convulsions
* Any other medical condition or serious intercurrent illness that, in the opinion of the Investigator, may make it undesirable for the subject to participate in the study
Minimum Eligible Age

2 Years

Maximum Eligible Age

9 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Tolmar Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Peggy Schorr

Role: STUDY_DIRECTOR

orphan reach USA, LLC

Locations

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University of California, San Diego

San Diego, California, United States

Site Status

Joe DiMaggio Children's Hospital

Hollywood, Florida, United States

Site Status

Nemours Children's Clinic

Jacksonville, Florida, United States

Site Status

Nemours Children's Hospital

Orlando, Florida, United States

Site Status

Riley Hospital for Children at Indiana University Health

Indianapolis, Indiana, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Cincinnati Children's Hospital Medical Center, Endocrine

Cincinnati, Ohio, United States

Site Status

University of Oklahoma College of Medicine

Tulsa, Oklahoma, United States

Site Status

Seattle Children's

Seattle, Washington, United States

Site Status

MultiCare Institute for Research and Innovation

Tacoma, Washington, United States

Site Status

Hospital de Ninos

Buenos Aires, , Argentina

Site Status

University of Calgary, Alberta Children's Hospital

Calgary, Alberta, Canada

Site Status

McGill University Health Centre

Montreal, Quebec, Canada

Site Status

CHU de Quebec-Universite Laval

Québec, , Canada

Site Status

Pontificia Universidad Catolica de Chile

Santiago, Santiago Metropolitan, Chile

Site Status

Instituto de Investigaciones Materno Infantil (IDIMI)

Santiago, Santiago Metropolitan, Chile

Site Status

Hospital Regional de Antofagasta Leonardo Guzman

Antofagasta, Second Region, Chile

Site Status

Hospital Unversitario "Dr. Jose Eleuterio Gonzalez"

Monterrey, Nuevo León, Mexico

Site Status

Instituto de Investigaciones Aplicadas a la Neurociencia, A.C.

Durango, , Mexico

Site Status

The Liggins Institute, University of Auckland

Auckland, , New Zealand

Site Status

Countries

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United States Argentina Canada Chile Mexico New Zealand

References

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Klein KO, Freire A, Gryngarten MG, Kletter GB, Benson M, Miller BS, Dajani TS, Eugster EA, Mauras N. Phase 3 Trial of a Small-volume Subcutaneous 6-Month Duration Leuprolide Acetate Treatment for Central Precocious Puberty. J Clin Endocrinol Metab. 2020 Oct 1;105(10):e3660-71. doi: 10.1210/clinem/dgaa479.

Reference Type DERIVED
PMID: 32738042 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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TOL2581A

Identifier Type: -

Identifier Source: org_study_id

NCT02811471

Identifier Type: -

Identifier Source: nct_alias

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