Study of Weekly ALTU-238 Compared With Daily Nutropin AQ in Prepubertal Children With Growth Hormone Deficiency

NCT ID: NCT00837863

Last Updated: 2009-05-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-03-31

Brief Summary

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The purpose of the study is to evaluate the safety and effectiveness of ALTU-238 in the treatment of children with growth hormone deficiency who have not yet reached puberty who lack the normal ability to make growth hormone themselves. This study will also test if ALTU-238 works as a weekly treatment.

Detailed Description

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Conditions

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Growth Hormone Deficiency

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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1

ALTU-238

Group Type EXPERIMENTAL

Somatropin

Intervention Type DRUG

ALTU-238 0.3 mg/kg daily

2

ALTU-238

Group Type EXPERIMENTAL

Somatropin

Intervention Type DRUG

ALTU-238 0.6 mg/kg daily

3

ALTU-238

Group Type EXPERIMENTAL

Somatropin

Intervention Type DRUG

ALTU-238 0.9 mg/kg daily

4

Nutropin AQ

Group Type ACTIVE_COMPARATOR

Somatropin

Intervention Type DRUG

Nutropin AQ 0.043 mg/kg daily

Interventions

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Somatropin

ALTU-238 0.3 mg/kg daily

Intervention Type DRUG

Somatropin

ALTU-238 0.6 mg/kg daily

Intervention Type DRUG

Somatropin

ALTU-238 0.9 mg/kg daily

Intervention Type DRUG

Somatropin

Nutropin AQ 0.043 mg/kg daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Assent of subject, if applicable, and written informed consent of parent or legal guardian
2. Diagnosis of GHD as defined by a maximum stimulated GH \< 7 ng/mL (μg/L) on two stimulation tests (using any two distinct agents from the following list: arginine, L-dopa, clonidine, insulin, or glucagon); if two documented historical tests are not available,test(s) must be performed during Screening period
3. Available results from one or more historical CT or MRI scans of the head obtained at or following the diagnosis of GHD
4. Chronologic age at Screening of 3 to 13 years (inclusive) for boys and 3 to 12 years(inclusive) for girls
5. Bone age at Screening of ≤ 11 years for boys and ≤ 10 years for girls
6. Pre-pubertal at Screening (Tanner stage 1 for both breast/genitalia and pubic hair
7. For subjects with idiopathic GHD, a Screening height SDS ≤ -2.0 (standardized for chronologic age and sex) there is no height SDS requirement if the subject has organic GHD (as defined by a CNS lesion or insult on a historical CT or MRI scan)
8. Pre-treatment annualized height velocity ≤ median (50th percentile) for chronologic age and sex (based on values for delayed maturers provided in Appendix 4), utilizing Screening height and height obtained 52 ± 13 weeks (i.e. 39 to 65 weeks) prior to Screening
9. Screening IGF-1 SDS for chronologic age and sex \< -1
10. If on thyroid hormone replacement therapy, the dose must be stable for at least 6 weeks prior to Screening and the free thyroxine level (T4), TSH, and cortisol must be within the normal range at the Screening visit

Exclusion Criteria

1. History of any prior rhGH, rhIGF-1, or sex steroid treatment
2. History of treatment with any medications that may affect growth
3. Evidence of active intracranial neoplasm per recent serial CT or MRI scans of the head or other criteria
4. Surgery/chemotherapy/radiation therapy for intracranial neoplasm within the prior 52 weeks
5. Any history of non-intracranial neoplasm
6. History of or active benign intracranial hypertension
7. High-dose chronic systemic corticosteroid treatment (oral or injected) within prior 13 weeks
8. Acute or severe illness within prior 26 weeks
9. History of diabetes mellitus, anorexia nervosa, cystic fibrosis, chronic severe kidney or liver disease, chronic infectious disease, inborn errors of metabolism, chromosomal disorders, intrauterine growth retardation, or other childhood disease associated with growth failure
10. History of congenital syndromes associated with abnormal growth, including Turner syndrome, Noonan syndrome, Prader-Willi syndrome, etc.
11. History of severe associated pathology affecting growth, including malnutrition,malabsorption, or bone dysplasia
12. History of autoimmune disease
13. Serum ALT or AST ≥ 1.5X ULN
14. Participation in another clinical trial or treatment with any investigational agent (drug or biologic) within 30 days prior to Baseline if the half-life of the agent is known to be ≤ 6 days or within 6 weeks prior to Baseline if the half-life is \> 6 days or not known
15. History of any allergic or abnormal reaction to any of the components of the study drugs
16. Any previous or ongoing clinically significant illness, PE findings, or laboratory abnormality that, in the opinion of the Investigator or the Medical Monitor, could prevent the subject from completing the protocol-specified requirements successfully
17. Poor likelihood, in the Investigator's opinion, that the subject will comply with protocol requirements (e.g., uncooperative attitude, inability to return for follow-up visits, history of medical noncompliance) and/or poor likelihood of completing the study
Minimum Eligible Age

3 Years

Maximum Eligible Age

13 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Altus Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Altus Pharmaceuticals

Locations

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Arkansas Children's Hospital

Little Rock, Arkansas, United States

Site Status RECRUITING

Nemours Children's Clinic

Orlando, Florida, United States

Site Status RECRUITING

Baystate Medical Centre

Springfield, Massachusetts, United States

Site Status RECRUITING

UMass Memorial Medical Center

Worcester, Massachusetts, United States

Site Status RECRUITING

Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status RECRUITING

Morristown Memorial Hospital

Morristown, New Jersey, United States

Site Status RECRUITING

Schneider Children's Hospital

New Hyde Park, New York, United States

Site Status RECRUITING

Children's Hospital Medical Centre

Cincinnati, Ohio, United States

Site Status RECRUITING

Cook Children's Hospital

Fort Worth, Texas, United States

Site Status RECRUITING

Seattle Children's Hospital

Seattle, Washington, United States

Site Status RECRUITING

Swedish Medical Center

Seattle, Washington, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Dr. Kenneth Attie, Medical Monitor

Role: CONTACT

781-373-6481

Facility Contacts

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Dr Stephen Kemp

Role: primary

Dr. Jorge Daaboul

Role: primary

407-650-7210

Dr Edward Reiter

Role: primary

413-794-5060

Dr. Leslie Soyka

Role: primary

508-856-6289

Dr. Finen Ugrasbul

Role: primary

816-234-3973

Dr. Lawrence Silverman

Role: primary

973-971-6340

Dr. Phyllis Speiser

Role: primary

718-470-3290

Dr Susan Rose

Role: primary

513-636-4744

Dr. Paul Thornton

Role: primary

682-885-7960

Dr Patricia Fetchner

Role: primary

Dr. Gad Kletter

Role: primary

206-215-2700

Other Identifiers

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0001194

Identifier Type: -

Identifier Source: org_study_id

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