Trial of Afatinib in Pediatric Tumours

NCT ID: NCT02372006

Last Updated: 2021-03-04

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

56 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-04-29

Study Completion Date

2020-08-05

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Open-label, dose escalation, monotherapy, basket trial with biomarker specific MTD expansion cohort/Phase II part.

The trial will consist of 2 parts:

1. Dose finding part to determine the MTD
2. Biomarker specific MTD expansion cohort/Phase II part to assess clinical anti-tumour activity in included tumour types

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Neuroectodermal Tumors Rhabdomyosarcoma

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

afatinib

dose escalation

Group Type EXPERIMENTAL

afatinib

Intervention Type DRUG

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

afatinib

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Paediatric patients aged 1 year to \<18 years at the time of informed consent
* diagnosis of HGG, DIPG, low grade astrocytoma, medulloblastoma/PNET, ependymoma, neuroblastoma, RMS and tumours with ErbB deregulation
* recurrent/refractory disease after they received at least one prior standard treatment regimen
* no effective conventional therapy exists
* Performance status \>= 50% (Lansky for =\<12ys; Karnofsky for \>12ys)

Exclusion Criteria

* relevant toxicity from previous treatment
* known pre-existing relevant cardiac , hepatic, renal, bone marrow dysfunction, ILD, keratitis
Minimum Eligible Age

1 Year

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Boehringer Ingelheim

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Boehringer Ingelheim

Role: STUDY_CHAIR

Boehringer Ingelheim

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

University of Wisconsin

Madison, Wisconsin, United States

Site Status

Sydney Childrens Hospital

Randwick, New South Wales, Australia

Site Status

AKH - Medical University of Vienna

Vienna, , Austria

Site Status

St. Anna Children-Hospital, Children's Cancer Research, Wien

Vienna, , Austria

Site Status

The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

Rigshospitalet, København, Børneonkologisk Afsnit 5002

København Ø, , Denmark

Site Status

HOP Toulouse, Pédiat, Toulouse

Toulouse, , Faroe Islands

Site Status

HOP Pellegrin

Bordeaux, , France

Site Status

CTR Oscar Lambret

Lille, , France

Site Status

CTR Leon Berard

Lyon, , France

Site Status

INS Curie

Paris, , France

Site Status

INS Gustave Roussy

Villejuif, , France

Site Status

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Universitätsklinikum Essen AöR

Essen, , Germany

Site Status

Universitätsklinikum Tübingen

Tübingen, , Germany

Site Status

Istituto G. Gaslini

Genova, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

Azienda Ospedaliera Universitaria di Padova

Padua, , Italy

Site Status

Osp. Pediatrico Bambin Gesù

Roma, , Italy

Site Status

Erasmus MC - Sophia Kinderziekenhuis

Rotterdam, , Netherlands

Site Status

Hospital Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Infantil Universitario Niño Jesus

Madrid, , Spain

Site Status

Birmingham Children's Hospital

Birmingham, , United Kingdom

Site Status

Great Ormond Street Hospital

London, , United Kingdom

Site Status

Royal Manchester Children's Hospital

Manchester, , United Kingdom

Site Status

The Royal Marsden Hospital

Sutton, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Austria Canada Denmark Faroe Islands France Germany Italy Netherlands Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Geoerger B, Marshall LV, Nysom K, Makin G, Bouffet E, Defachelles AS, Amoroso L, Aerts I, Leblond P, Barahona P, Van-Vlerken K, Fu E, Solca F, Lorence RM, Ziegler DS. Afatinib in paediatric patients with recurrent/refractory ErbB-dysregulated tumours: Results of a phase I/expansion trial. Eur J Cancer. 2023 Jul;188:8-19. doi: 10.1016/j.ejca.2023.04.007. Epub 2023 Apr 20.

Reference Type DERIVED
PMID: 37178647 (View on PubMed)

Andrade RC, Boroni M, Amazonas MK, Vargas FR. New drug candidates for osteosarcoma: Drug repurposing based on gene expression signature. Comput Biol Med. 2021 Jul;134:104470. doi: 10.1016/j.compbiomed.2021.104470. Epub 2021 May 7.

Reference Type DERIVED
PMID: 34004576 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2014-002123-10

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

1200.120

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.