Erlotinib Versus Oral Etoposide in Patients With Recurrent or Refractory Pediatric Ependymoma

NCT ID: NCT01032070

Last Updated: 2024-12-12

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

25 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-09-27

Study Completion Date

2012-11-26

Brief Summary

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This is a phase 2 study to evaluate the efficacy of single-agent erlotinib versus oral etoposide in patients with recurrent or refractory pediatric ependymoma.

Detailed Description

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This is a phase 2 study involving a 1:1 randomization of 40 patients with recurrent or refractory pediatric ependymoma who will receive either erlotinib or oral etoposide.

Conditions

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Recurrent or Refractory Pediatric Ependymoma

Keywords

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pediatric etoposide erlotinib phase 2 ependymoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Erlotinib

Erlotinib was administered orally at a dose of 85 mg/m\^2 per day continuously until either progression, death, patient request or investigator decision to discontinue study drug or intolerable toxicity.

Group Type EXPERIMENTAL

erlotinib

Intervention Type DRUG

oral

Etoposide

Etoposide 50 mg/m\^2 per day was administered orally for 21 days followed by a 7-day rest period until either progression, death, patient request or investigator decision to discontinue study drug or intolerable toxicity.

Group Type ACTIVE_COMPARATOR

etoposide

Intervention Type DRUG

oral

Interventions

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erlotinib

oral

Intervention Type DRUG

etoposide

oral

Intervention Type DRUG

Other Intervention Names

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OSI-774 Tarceva VP-16

Eligibility Criteria

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Inclusion Criteria

* Recurrent of refractory ependymoma or subependymoma
* Performance Status (PS): Lansky ≥ 50% for patients ≤ 10 years of age or Karnofsky ≥ 50% for patients \>10 years of age
* Measurable disease, defined as 1 measurable lesion that can be accurately measured in 2 planes that has not received radiation therapy within 12 weeks
* Recovered from the acute toxic effects of all prior chemotherapy, immunotherapy, or radiotherapy
* ≥ 1 year to ≤ 21 years
* Serum creatinine for patients ≤ 5 years in age is ≤ 0.8 mg/dL or Creatinine Clearance/Glomerular Filtration Rate (GFR) ≥ 70 mL/min/m\^2
* Serum creatinine for patients \> 5 and ≤ 10 years in age is ≤ 1.0 mg/dL or Creatinine Clearance/GFR ≥ 70 mL/min/m\^2
* Serum creatinine for patients \> 10 and ≤ 15 years in age is ≤ 1.2 mg/dL or Creatinine Clearance/GFR ≥ 70 mL/min/m\^2
* Serum creatinine for patients \> 15 years in age is ≤ 1.5 mg/dL or Creatinine Clearance/GFR ≥ 70 mL/min/m\^2
* Total bilirubin is ≤ 1.5 x upper limit of normal for age
* Alanine aminotransferase (ALT) ≤ 3 x upper limit of normal
* Absolute neutrophil count \> 1000/µL
* Platelet count \> 100,000/µL
* Hemoglobin \> 8 gm/dL
* Neurologically stable for at least 7 days prior to randomization
* If receiving corticosteroids, patients must be on a stable or decreasing dose for at least 7 days before randomization
* Patients of reproductive potential must agree to proactive effective contraceptive measures for the duration of the study and for at least 90 days after completion of study drug

Exclusion Criteria

* Previously received epidermal growth factor receptor (EGFR)-targeted therapy
* Previously received oral etoposide
* Received craniospinal radiotherapy within 24 weeks prior to randomization
* Received field radiotherapy to the target lesion within 12 weeks prior to randomization
* Received symptomatic metastatic disease within 14 days prior to randomization
* Received myelosuppressive chemotherapy within 21 days before randomization
* Received growth factors within 7 days prior to randomization
* Participating in another investigational drug trial
* Received a biologic agent within 7 days prior to randomization
* Received a monoclonal antibody within 28 days prior to randomization
* Taking cytochrome P450 (CYP)3A4 or CYP1A2 inhibitors/inducers within 14 days prior to randomization
* Taking proton pump inhibitors within 14 days prior to randomization
* Smoking during treatment
* Pregnant or breast-feeding females
Minimum Eligible Age

1 Year

Maximum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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OSI Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Monitor

Role: STUDY_DIRECTOR

Astellas Pharma Global Development

Locations

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University of Alabama at Birmingham Dept. of Pediatric-Hematology/Oncology

Birmingham, Alabama, United States

Site Status

Center for Cancer and Blood Disorders-Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status

Children's Hospital of Orange County (CHOC)

Orange, California, United States

Site Status

Stanford University and Lucile Packard Children's Hospital

Palo Alto, California, United States

Site Status

Children's Hospital Center for Cancer and Blood Disorders

Aurora, Colorado, United States

Site Status

Children's National Medical Center - D.C. Center for Cancer and Blood Disorders

Washington D.C., District of Columbia, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Emory University Children's Healthcare of Atlanta Aflac Cancer Center & Blood Disorders

Atlanta, Georgia, United States

Site Status

Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Dana-Farber Cancer Institute Department of Pediatric Neuro-oncology

Boston, Massachusetts, United States

Site Status

Amplatz Children's Hospital University of Minnesota Medical Center- Pediatric Hematology Oncology

Minneapolis, Minnesota, United States

Site Status

Steven D Hassenfeld Children's Center - New York University

New York, New York, United States

Site Status

Columbia University Children's Hospital of New York Presbyterian Child & Adolescent Oncology Center

New York, New York, United States

Site Status

Oregon Health & Sciences University Doembecher Children's Hospital

Portland, Oregon, United States

Site Status

Penn State Hershey Children's Hospital

Hershey, Pennsylvania, United States

Site Status

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, United States

Site Status

Children's Medical Center, Dallas Center for Cancer and Blood Disorders

Dallas, Texas, United States

Site Status

University of Wisconsin Pediatric Hematology/Oncology Department

Madison, Wisconsin, United States

Site Status

Strollery Children's Hospital Division of Hematology/Oncology

Edmonton, Alberta, Canada

Site Status

Children's and Women's Health Center of BC Division of Hematology/ Oncology/ BMT

Vancouver, British Columbia, Canada

Site Status

Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

Birmingham Children's Hospital

Birmingham, , United Kingdom

Site Status

Royal Hospital for Sick Children

Glasgow, , United Kingdom

Site Status

Paediatric Oncology and Haematology Offices

Leeds, , United Kingdom

Site Status

Alder Hey Children's NHS Foundation Trust Department of Oncology

Liverpool, , United Kingdom

Site Status

Royal Manchester Children's Hospital Ward 84

Manchester, , United Kingdom

Site Status

University of Nottingham Children's Brain Tumour Research Centre

Nottingham, , United Kingdom

Site Status

Royal Marsden Hospital

Sutton, , United Kingdom

Site Status

Countries

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United States Canada United Kingdom

Related Links

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https://astellasclinicalstudyresults.com/study.aspx?ID=328

Link to results on Astellas Clinical Study Results website

Other Identifiers

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2009-016836-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

OSI-774-205

Identifier Type: -

Identifier Source: org_study_id