Phase I/II Study of Avelumab in Pediatric Cancer Participants

NCT ID: NCT03451825

Last Updated: 2024-06-24

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE1

Total Enrollment

21 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-03-07

Study Completion Date

2021-07-27

Brief Summary

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This is a multi-center, open-label, international study to evaluate the dose, safety and tolerability, antitumor activity, pharmacokinetic and pharmacodynamics of avelumab in pediatric subjects 0 to less than 18 years of age with refractory or relapsed malignant solid tumors (including central nervous system tumors) and lymphoma for which no standard therapy is available or for which the subject is not eligible for the existing therapy.

The study was planned to be conducted in 2 parts: the dose-finding part (Phase I) and the tumor-specified expansion part (Phase II). However, Phase II was cancelled due to limited clinical benefit of PD-L1 monotherapy in pediatric participants.

Detailed Description

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Conditions

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Refractory or Relapsed Solid Tumors Lymphoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Avelumab: 10 miligram per kilogram (mg/kg)

Group Type EXPERIMENTAL

Avelumab

Intervention Type DRUG

Participants received an intravenous infusion of avelumab 10mg/kg intervention (IV) once every 2 weeks until confirmed progression, death, unacceptable toxicity, or any criterion for withdrawal occurred.

Avelumab 20mg/kg

Group Type EXPERIMENTAL

Avelumab

Intervention Type DRUG

Participants received an intravenous infusion of avelumab 20mg/kg intervention (IV) once every 2 weeks until confirmed progression, death, unacceptable toxicity, or any criterion for withdrawal occurred.

Interventions

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Avelumab

Participants received an intravenous infusion of avelumab 10mg/kg intervention (IV) once every 2 weeks until confirmed progression, death, unacceptable toxicity, or any criterion for withdrawal occurred.

Intervention Type DRUG

Avelumab

Participants received an intravenous infusion of avelumab 20mg/kg intervention (IV) once every 2 weeks until confirmed progression, death, unacceptable toxicity, or any criterion for withdrawal occurred.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male or female subjects 0 to less than 18 years of age at the time of first treatment dose with histologically or cytologically confirmed solid malignant tumors (including CNS tumors) or lymphoma for which no standard therapy is available
* Confirmed progression on or refractory to standard therapy or no standard therapy available.
* Availability of archival formalin-fixed, paraffin-embedded block containing tumor tissue, or slides, or a fresh/recent tumor biopsy prior to avelumab treatment for subjects in Phase 2
* Adequate bone marrow, kidney, and liver function

Exclusion Criteria

* Prior therapy with any antibody or drug targeting T-cell coregulatory proteins
* Concurrent anticancer treatment or immunosuppressive agents
* Prior organ transplantation
* Significant acute or chronic infections
* Other significant diseases or conditions that might impair the subject's tolerance of trial treatment
Minimum Eligible Age

0 Years

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck KGaA, Darmstadt, Germany

INDUSTRY

Sponsor Role collaborator

EMD Serono Research & Development Institute, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Responsible

Role: STUDY_DIRECTOR

Merck KGaA, Darmstadt, Germany

Locations

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Children's Hospital Colorado

Aurora, Colorado, United States

Site Status

The Children's Hospital at Montefiore (CHAM)

The Bronx, New York, United States

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

Children's Hospital - London Health Sciences Centre

London, , Canada

Site Status

CHU Sainte-Justine

Montreal, , Canada

Site Status

The Hospital for Sick Children

Toronto, , Canada

Site Status

Rigshospitalet

Copenhagen, , Denmark

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University

Seoul, , South Korea

Site Status

Countries

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United States Belgium Canada Denmark South Korea

References

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Vugmeyster Y, Grisic AM, Brockhaus B, Rueckert P, Ruisi M, Dai H, Khandelwal A. Avelumab Dose Selection for Clinical Studies in Pediatric Patients with Solid Tumors. Clin Pharmacokinet. 2022 Jul;61(7):985-995. doi: 10.1007/s40262-022-01111-8. Epub 2022 Apr 29.

Reference Type RESULT
PMID: 35484319 (View on PubMed)

Loeb DM, Lee JW, Morgenstern DA, Samson Y, Uyttebroeck A, Lyu CJ, Van Damme A, Nysom K, Macy ME, Zorzi AP, Xiong J, Pollert P, Joerg I, Vugmeyster Y, Ruisi M, Kang HJ. Avelumab in paediatric patients with refractory or relapsed solid tumours: dose-escalation results from an open-label, single-arm, phase 1/2 trial. Cancer Immunol Immunother. 2022 Oct;71(10):2485-2495. doi: 10.1007/s00262-022-03159-8. Epub 2022 Mar 9.

Reference Type RESULT
PMID: 35262780 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://medical.emdserono.com/en_US/home.html

US Medical Information website, Medical Resources

Other Identifiers

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2017-002985-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MS100070-0306

Identifier Type: -

Identifier Source: org_study_id

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