Open Label Extension Study To Investigate Long Term Safety, Tolerability And Efficacy Of Pf-02545920 In Subjects With Huntington's Disease Who Completed Study A8241021

NCT ID: NCT02342548

Last Updated: 2018-04-23

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

188 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-02-25

Study Completion Date

2017-02-06

Brief Summary

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This study is a 12 month open label extension study of PF-02545920 20 mg dosed BID following study A8241021 in subjects with HD. Primary endpoints will be to assess long-term safety and tolerability of 20 mg BID of PF-02545920. Secondary endpoints will be the change from baseline in the Total Motor Score (TMS)assessment, and/ior the Total maximum Chorea (TMC) assessment of the Unified Huntington Disease Rating Scale (UHDRS) after 6 and 12 months of treatment, and Clinical Global Impression-Improvement score after 6 and 12 months of treatment. Subjects, who were assigned to the 20 mg PF-02545920 dose group in the preceding A8241021 study, will receive 20 mg PF-02545920 without any titration. All other subjects will be titrated to the 20 mg BID dose as follows: 5 mg BID for 7 days, 10 mg BID for 7 days, 15 mg BID for 7 days, then 20 mg BID for the remainder of the treatment phase. Up to 260 subjects may take part in this open label extension

Detailed Description

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Conditions

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Huntington's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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20 mg BID PF-02545920 non-titrated

Subjects who received 20 mg BID in completed study A8241021 will continue to receive 20 mg BID PF-02545920

Group Type EXPERIMENTAL

20 mg BID of PF-02545920

Intervention Type DRUG

All subject who completed A8241021 will receive 20 mg BID (with or without titration)

20mg BID PF-02545920 titrated

Subjects who received either Placebo or 5mg BID of PF-02545920 in completed study A8241021 will be titrated up to 20 mg with 5mg increment per week, over 4 weeks (5mg increment/wk)

Group Type EXPERIMENTAL

20 mg BID of PF-02545920

Intervention Type DRUG

All subject who completed A8241021 will receive 20 mg BID (with or without titration)

Interventions

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20 mg BID of PF-02545920

All subject who completed A8241021 will receive 20 mg BID (with or without titration)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subjects must have completed study A8241021
* Diagnosis of HD, including ≥36 CAG repeats.

Exclusion Criteria

* Significant neurological disorder other than Huntington's disease.
* WBC ≤ 3500/mm3 AND/OR ANC ≤ 2000/mm3 and history of neutropenia or myeolo-proliferative disorders.
* Any drug related SAE experienced during study A8241021 which were not approved as acceptable for enrollment in A8241022.
Minimum Eligible Age

30 Years

Maximum Eligible Age

66 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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The Kirkland Clinic of UAB Hospital

Birmingham, Alabama, United States

Site Status

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Mayo Clinic Arizona

Scottsdale, Arizona, United States

Site Status

University of California, Irvine

Irvine, California, United States

Site Status

Ronald Reagan UCLA Medical Center Drug Information Center

Los Angeles, California, United States

Site Status

UCLA Neurology Clinic

Los Angeles, California, United States

Site Status

UCLA Radiology

Los Angeles, California, United States

Site Status

Rocky Mountain Movement Disorders Center

Englewood, Colorado, United States

Site Status

University of Florida Center for Movement Disorders & Neurorestoration

Gainesville, Florida, United States

Site Status

Indiana University Health Neuroscience Center

Indianapolis, Indiana, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Wake Forest Baptist Medical Center

Winston-Salem, North Carolina, United States

Site Status

The Ohio State University

Columbus, Ohio, United States

Site Status

The Wexner Medical Center at the Ohio State University

Columbus, Ohio, United States

Site Status

The Wright Center of Innovation- The Ohio State University

Columbus, Ohio, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

The Centre For Huntington Disease, The University of British Columbia

Vancouver, British Columbia, Canada

Site Status

Center For Movement Disorders

Toronto, Ontario, Canada

Site Status

CHUM-Notre-Dame Hospital

Montreal, Quebec, Canada

Site Status

CHUM-Notre-Dame, Pharmacie

Montreal, Quebec, Canada

Site Status

Uniklinik RWTH Aachen

Aachen, , Germany

Site Status

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

St. Josef Hospital

Bochum, , Germany

Site Status

Friedrich-Alexander-Universität

Erlangen, , Germany

Site Status

Universität zu Lübeck

Lübeck, , Germany

Site Status

Philipps Universitat Marburg

Marburg, , Germany

Site Status

Technische Universität München

München, , Germany

Site Status

George-Huntington-Institut

Münster, , Germany

Site Status

Kbo-Isar-Amper-Klinikum gGmbH

Taufkirchen, , Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Universitaetsklinikum Wuerzburg

Würzburg, , Germany

Site Status

Copernicus Podmiot Leczniczy sp.zo.o

Gdansk, , Poland

Site Status

Krakowska Akademia Neurologii Sp. zo.o

Krakow, , Poland

Site Status

Solumed Centrum Medyczne

Poznan, , Poland

Site Status

Instytut Psychiatrii i Neurologii, I Klinika Neurologiczna

Warsaw, , Poland

Site Status

Central Manchester University Hospitals NHS Foundation Trust

Oxford Road, Manchester, United Kingdom

Site Status

St Nicholas Hospital

Gosforth, Newcastle UPON TYNE, United Kingdom

Site Status

Bimingham & Solihull Mental Health NHS Foundation Trust Department of Neuropsychiatry

Birmingham, WEST Midlands, United Kingdom

Site Status

NHS Grampian, Aberdeen Royal Infirmary, Clinical Genetics Centre

Aberdeen, , United Kingdom

Site Status

Institute of Psychological Medicine and Clinical Neurosciences

Cardiff, , United Kingdom

Site Status

NHS Greater Glasgow and Clyde

Glasgow, , United Kingdom

Site Status

Guy's and St. Thomas' NHS Foundation Trust

London, , United Kingdom

Site Status

University College London Hospitals Huntington's Diesease

London, , United Kingdom

Site Status

University College London Hospitals NHS Foundation Trust

London, , United Kingdom

Site Status

The National Institute for Health Research / Wellcome Trust Clinical Research Facility

Manchester, , United Kingdom

Site Status

Newcastle Magnetic Resonance Centre

Newcastle upon Tyne, , United Kingdom

Site Status

Oxford University Hospitals NHS Trust

Oxford, , United Kingdom

Site Status

Sheffield Teaching Hospital NHS Foundation Trust

Sheffield, , United Kingdom

Site Status

University Hospital Southampton NHS Foundation Trust, Wessex Neurological Centre

Southampton, , United Kingdom

Site Status

Countries

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United States Canada Germany Poland United Kingdom

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Other Identifiers

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2014-004900-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

OPEN LABEL TO A8241021

Identifier Type: OTHER

Identifier Source: secondary_id

A8241022

Identifier Type: -

Identifier Source: org_study_id

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