Dapagliflozin Evaluation in Patients With Inadequately Controlled Type 1 Diabetes

NCT ID: NCT02268214

Last Updated: 2018-09-13

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

833 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-11-11

Study Completion Date

2017-08-25

Brief Summary

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The purpose of this study is to determine if adding dapagliflozin to insulin is a safe and effective therapy to improve glycemic control in patients with type 1 diabetes.

Detailed Description

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Study Classification: Safety, Efficacy and Pharmacokinetics/dynamics

Conditions

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Type 1 Diabetes Mellitus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Arm A: Dapagliflozin

Dapagliflozin 5 mg tablet orally, once daily for 52 weeks

Group Type EXPERIMENTAL

Dapagliflozin

Intervention Type DRUG

Tablets

Arm B: Dapagliflozin

Dapagliflozin 10 mg tablet orally, once daily for 52 weeks

Group Type EXPERIMENTAL

Dapagliflozin

Intervention Type DRUG

Tablets

Arm C: Placebo for Dapagliflozin

Placebo tablet orally, once daily for 52 weeks

Group Type PLACEBO_COMPARATOR

Placebo for dapagliflozin

Intervention Type DRUG

Tablets

Interventions

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Dapagliflozin

Tablets

Intervention Type DRUG

Placebo for dapagliflozin

Tablets

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of Type 1 Diabetes mellitus (T1DM)
* Central laboratory C-peptide \< 0.7 ng/ml (0.23 nmol/L)
* Insulin use for at least 12 months per patient reported or medical records
* Method of insulin administration (MDI or CSII) must have been unchanged for at least 3 months prior to screening
* Subjects must be on a total insulin dose of ≥ 0.3 U/kg/day for at least 3 months prior to screening
* If on MDI insulin administration, subject must be on ≥ 3x injections per day
* Screening Visit: Central laboratory HbA1c ≥ 7.7% and ≤ 11.0%
* Body mass index (BMI) ≥ 18.5 kg/m2

Exclusion Criteria

* History of Type 2 Diabetes mellitus (T2DM) or maturity onset diabetes of the young (MODY), pancreatic surgery, or chronic pancreatitis that could result in decreased beta cell capacity
* Taking metformin and/or thiazolidinediones within 2 months prior to screening
* Taking any antidiabetic medication (other than insulin), within 1 month prior to screening

\- Taking GLP-1 receptor agonist within 2 months prior to screening for once weekly administration and within 1 month prior to screening for once or twice daily administration
* History of diabetes ketoacidosis requiring medical intervention within 1 month prior to screening
* History of hospital admission for glycemic control (either hyperglycemia or hypoglycemia) within 1 month prior to screening
* Frequent episodes of severe hypoglycemia (more than one episode requiring medical assistance, emergency care), and/or glucagon therapy administered by a third-party individual within 1 month prior to screening
* History of Addison's disease
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role collaborator

AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Anna Maria Langkilde

Role: STUDY_DIRECTOR

AstraZeneca

Locations

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Little Rock, Arkansas, United States

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Encino, California, United States

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La Mesa, California, United States

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San Diego, California, United States

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Tarzana, California, United States

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Torrance, California, United States

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Aurora, Colorado, United States

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Denver, Colorado, United States

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Cooper City, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Port Orange, Florida, United States

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Idaho Falls, Idaho, United States

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Des Moines, Iowa, United States

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Louisville, Kentucky, United States

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Portland, Maine, United States

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Hyattsville, Maryland, United States

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Rockville, Maryland, United States

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Kalamazoo, Michigan, United States

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Minneapolis, Minnesota, United States

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Chesterfield, Missouri, United States

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Las Vegas, Nevada, United States

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Albany, New York, United States

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Buffalo, New York, United States

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Asheville, North Carolina, United States

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Chapel Hill, North Carolina, United States

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Greenville, North Carolina, United States

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Morehead City, North Carolina, United States

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Langhorne, Pennsylvania, United States

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Kingsport, Tennessee, United States

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Nashville, Tennessee, United States

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Amarillo, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Salt Lake City, Utah, United States

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Olympia, Washington, United States

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Concord, , Australia

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Daw Park, , Australia

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Fitzroy, , Australia

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Heidelberg West, , Australia

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Newcastle, , Australia

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Southport, , Australia

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Wollongong, , Australia

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Innsbruck, , Austria

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Saint Stefan/Stainz, , Austria

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Vienna, , Austria

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Vienna, , Austria

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Vienna, , Austria

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Bonheiden, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Vancouver, British Columbia, Canada

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Winnipeg, Manitoba, Canada

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London, Ontario, Canada

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Laval, Quebec, Canada

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Arhus C, , Denmark

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Esbjerg, , Denmark

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Odense, , Denmark

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Randers NØ, , Denmark

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Helsinki, , Finland

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Jyväskylä, , Finland

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Kuopio, , Finland

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Oulu, , Finland

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Tampere, , Finland

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Besançon, , France

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Corbeil-Essonnes, , France

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Dijon, , France

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Saint-Herblain, , France

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Vandœuvre-lès-Nancy, , France

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Aschaffenburg, , Germany

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Aßlar, , Germany

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Bad Oeynhausen, , Germany

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Falkensee, , Germany

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Munich, , Germany

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Münster, , Germany

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Neuwied, , Germany

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Oldenburg, , Germany

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Pohlheim, , Germany

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Schweinfurt, , Germany

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Sulzbach, , Germany

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Witten, , Germany

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Baja, , Hungary

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Balatonfüred, , Hungary

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Budapest, , Hungary

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Létavértes, , Hungary

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Szeged, , Hungary

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Zalaegerszeg, , Hungary

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Haifa, , Israel

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Jerusalem, , Israel

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Safed, , Israel

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Tel Aviv, , Israel

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Tikva, , Israel

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Florence, , Italy

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Milan, , Italy

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Padowa, , Italy

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Palermo, , Italy

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Ravenna, , Italy

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Sesto San Giovanni, , Italy

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Siena, , Italy

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Aguascalientes, , Mexico

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Chihuahua City, , Mexico

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Cuernavaca, , Mexico

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Guadalajara, , Mexico

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Mérida, , Mexico

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México, , Mexico

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Monterrey, , Mexico

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Monterrey, , Mexico

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Torreón, , Mexico

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Zapopan, , Mexico

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Zapopan, Jalisco, , Mexico

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Bucharest, , Romania

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Bucharest, , Romania

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Dolj, , Romania

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Galati, , Romania

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Iași, , Romania

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Timișoara, , Romania

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A Coruña, , Spain

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Almería, , Spain

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Barcelona, , Spain

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Seville, , Spain

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Valencia, , Spain

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Gothenburg, , Sweden

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Karlstad, , Sweden

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Lund, , Sweden

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Uppsala, , Sweden

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Belfast, , United Kingdom

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Chesterfield, , United Kingdom

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Dundee, , United Kingdom

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Nottingham, , United Kingdom

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Sheffield, , United Kingdom

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Welwyn Garden City, , United Kingdom

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Countries

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United States Australia Austria Belgium Canada Denmark Finland France Germany Hungary Israel Italy Mexico Romania Spain Sweden United Kingdom

References

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Nardone M, Kugathasan L, Sridhar VS, Dutta P, Campbell DJT, Layton AT, Perkins BA, Barbour S, Lam TKT, Levin A, Lovblom LE, Mucsi I, Rabasa-Lhoret R, Rac VE, Senior P, Sigal RJ, Stanimirovic A, Persson F, Stougaard EB, Doria A, Cherney DZI. Modeling Cardiorenal Protection with Sodium-Glucose Cotransporter 2 Inhibition in Type 1 Diabetes: An Analysis of DEPICT-1 and DEPICT-2. Clin J Am Soc Nephrol. 2025 Apr 1;20(4):529-538. doi: 10.2215/CJN.0000000641. Epub 2025 Feb 7.

Reference Type DERIVED
PMID: 39918875 (View on PubMed)

Natale P, Tunnicliffe DJ, Toyama T, Palmer SC, Saglimbene VM, Ruospo M, Gargano L, Stallone G, Gesualdo L, Strippoli GF. Sodium-glucose co-transporter protein 2 (SGLT2) inhibitors for people with chronic kidney disease and diabetes. Cochrane Database Syst Rev. 2024 May 21;5(5):CD015588. doi: 10.1002/14651858.CD015588.pub2.

Reference Type DERIVED
PMID: 38770818 (View on PubMed)

Melin J, Tang W, Rekic D, Hamren B, Penland RC, Boulton DW, Parkinson J. Dapagliflozin Pharmacokinetics Is Similar in Adults With Type 1 and Type 2 Diabetes Mellitus. J Clin Pharmacol. 2022 Oct;62(10):1227-1235. doi: 10.1002/jcph.2062. Epub 2022 May 2.

Reference Type DERIVED
PMID: 35403243 (View on PubMed)

Groop PH, Dandona P, Phillip M, Gillard P, Edelman S, Jendle J, Xu J, Scheerer MF, Thoren F, Iqbal N, Repetto E, Mathieu C. Effect of dapagliflozin as an adjunct to insulin over 52 weeks in individuals with type 1 diabetes: post-hoc renal analysis of the DEPICT randomised controlled trials. Lancet Diabetes Endocrinol. 2020 Oct;8(10):845-854. doi: 10.1016/S2213-8587(20)30280-1.

Reference Type DERIVED
PMID: 32946821 (View on PubMed)

Mathieu C, Dandona P, Birkenfeld AL, Hansen TK, Iqbal N, Xu J, Repetto E, Scheerer MF, Thoren F, Phillip M. Benefit/risk profile of dapagliflozin 5 mg in the DEPICT-1 and -2 trials in individuals with type 1 diabetes and body mass index >/=27 kg/m2. Diabetes Obes Metab. 2020 Nov;22(11):2151-2160. doi: 10.1111/dom.14144. Epub 2020 Aug 20.

Reference Type DERIVED
PMID: 32691513 (View on PubMed)

Parkinson J, Tang W, Astrand M, Melin J, Ekholm E, Hamren B, Boulton DW. Model-based characterization of the relationship between dapagliflozin systemic exposure and HbA1c response in patients with type 1 diabetes mellitus. Diabetes Obes Metab. 2019 Jun;21(6):1381-1387. doi: 10.1111/dom.13664. Epub 2019 Mar 14.

Reference Type DERIVED
PMID: 30756462 (View on PubMed)

Dandona P, Mathieu C, Phillip M, Hansen L, Tschope D, Thoren F, Xu J, Langkilde AM; DEPICT-1 Investigators. Efficacy and Safety of Dapagliflozin in Patients With Inadequately Controlled Type 1 Diabetes: The DEPICT-1 52-Week Study. Diabetes Care. 2018 Dec;41(12):2552-2559. doi: 10.2337/dc18-1087. Epub 2018 Oct 23.

Reference Type DERIVED
PMID: 30352894 (View on PubMed)

Dandona P, Mathieu C, Phillip M, Hansen L, Griffen SC, Tschope D, Thoren F, Xu J, Langkilde AM; DEPICT-1 Investigators. Efficacy and safety of dapagliflozin in patients with inadequately controlled type 1 diabetes (DEPICT-1): 24 week results from a multicentre, double-blind, phase 3, randomised controlled trial. Lancet Diabetes Endocrinol. 2017 Nov;5(11):864-876. doi: 10.1016/S2213-8587(17)30308-X. Epub 2017 Sep 14.

Reference Type DERIVED
PMID: 28919061 (View on PubMed)

Related Links

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Other Identifiers

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2013-004674-97

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D1695C00006

Identifier Type: OTHER

Identifier Source: secondary_id

MB102-229

Identifier Type: -

Identifier Source: org_study_id

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