Efficacy, Safety, and Tolerability Study of Sotagliflozin as Adjunct Therapy in Adult Patients With Type 1 Diabetes Mellitus Who Have Inadequate Glycemic Control With Insulin Therapy

NCT ID: NCT02384941

Last Updated: 2020-02-12

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

793 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-03-31

Study Completion Date

2017-02-28

Brief Summary

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This Phase 3 study was intended to demonstrate superiority of either sotagliflozin high dose or low dose versus placebo on glycosylated hemoglobin A1C (A1C) reduction at Week 24 when used as an adjunct in adult participants with type 1 diabetes mellitus (T1D) who have inadequate glycemic control with insulin therapy.

Detailed Description

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Conditions

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Type 1 Diabetes Mellitus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Placebo

Two placebo-matching sotagliflozin tables, orally for 24 weeks followed by a 28 week extension period.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo once daily, before first meal of the day.

Sotagliflozin 200 milligrams (mg)

Sotagliflozin 200 mg (one 200 mg tablet and one placebo tablet), orally, for 24 weeks followed by a 28 week extension period.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Placebo once daily, before first meal of the day.

Sotagliflozin

Intervention Type DRUG

Sotagliflozin once daily, before first meal of the day.

Sotagliflozin 400 mg

Sotagliflozin 400 mg (two 200 mg tablets), orally, for 24 weeks followed by a 28 week extension period.

Group Type EXPERIMENTAL

Sotagliflozin

Intervention Type DRUG

Sotagliflozin once daily, before first meal of the day.

Interventions

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Placebo

Placebo once daily, before first meal of the day.

Intervention Type DRUG

Sotagliflozin

Sotagliflozin once daily, before first meal of the day.

Intervention Type DRUG

Other Intervention Names

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LX4211

Eligibility Criteria

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Inclusion Criteria

* Participants had given written informed consent to participate in the study in accordance with local regulations.
* Adult participants 18 years and older with a diagnosis of T1D made at least 1 year prior to informed consent.
* Participants were being treated with insulin or insulin analog delivered. via continuous subcutaneous insulin infusion (CSII) or multiple daily injections (MDI).
* Willing and able to perform self-monitored blood glucose (SMBG) and complete the study diary as required per protocol.
* At the Screening Visit, A1C must be between 7.0% to 11.0%.
* Females of childbearing potential must use an adequate method of contraception and have a negative pregnancy test .

Exclusion Criteria

* Use of antidiabetic agent other than insulin or insulin analog at the time of screening.
* Use of sodium-glucose cotransporter (SGLT) inhibitors within 8 weeks prior to randomization.
* Chronic systemic corticosteroid use.
* Type 2 diabetes mellitus (T2D), or severely uncontrolled T1D as determined by the Investigator.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sanofi

INDUSTRY

Sponsor Role collaborator

Lexicon Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sangeeta Sawhney, M.D.

Role: STUDY_DIRECTOR

Lexicon Pharmaceuticals, Inc.

Locations

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Lexicon Investigational Site

Birmingham, Alabama, United States

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Little Rock, Arkansas, United States

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Escondido, California, United States

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Greenbrae, California, United States

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Huntington Beach, California, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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Orange, California, United States

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Palm Springs, California, United States

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San Mateo, California, United States

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Tarzana, California, United States

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Tustin, California, United States

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Walnut Creek, California, United States

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Aurora, Colorado, United States

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Longmont, Colorado, United States

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Fleming Island, Florida, United States

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Jacksonville, Florida, United States

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Jacksonville, Florida, United States

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New Port Richey, Florida, United States

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Ormond Beach, Florida, United States

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West Palm Beach, Florida, United States

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Atlanta, Georgia, United States

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Lawrenceville, Georgia, United States

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Roswell, Georgia, United States

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Honolulu, Hawaii, United States

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Crystal Lake, Illinois, United States

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Elgin, Illinois, United States

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Springfield, Illinois, United States

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Topeka, Kansas, United States

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Lexington, Kentucky, United States

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Bangor, Maine, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Detroit, Michigan, United States

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Chesterfield, Missouri, United States

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St Louis, Missouri, United States

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Omaha, Nebraska, United States

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Henderson, Nevada, United States

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Las Vegas, Nevada, United States

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Albany, New York, United States

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New York, New York, United States

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Asheville, North Carolina, United States

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Chapel Hill, North Carolina, United States

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Morehead City, North Carolina, United States

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Columbus, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Portland, Oregon, United States

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Greer, South Carolina, United States

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Rapid City, South Dakota, United States

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Chattanooga, Tennessee, United States

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Chattanooga, Tennessee, United States

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Memphis, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Schertz, Texas, United States

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Chesapeake, Virginia, United States

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Renton, Washington, United States

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Seattle, Washington, United States

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Calgary, Alberta, Canada

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Vancouver, British Columbia, Canada

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Winnipeg, Manitoba, Canada

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Halifax, Nova Scotia, Canada

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Barrie, Ontario, Canada

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Hamilton, Ontario, Canada

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London, Ontario, Canada

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Ottawa, Ontario, Canada

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Thornhill, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Lexicon Investigational Site

Saint-Laurent, Quebec, Canada

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Countries

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United States Canada

References

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Peters AL, McGuire DK, Danne T, Kushner JA, Rodbard HW, Dhatariya K, Sawhney S, Banks P, Jiang W, Davies MJ, Lapuerta P. Diabetic Ketoacidosis and Related Events With Sotagliflozin Added to Insulin in Adults With Type 1 Diabetes: A Pooled Analysis of the inTandem 1 and 2 Studies. Diabetes Care. 2020 Nov;43(11):2713-2720. doi: 10.2337/dc20-0924. Epub 2020 Sep 14.

Reference Type DERIVED
PMID: 32928957 (View on PubMed)

Danne T, Joish VN, Afonso M, Banks P, Sawhney S, Lapuerta P, Davies MJ, Buse JB, Lin D, Reaney M, Guillonneau S, Snoek FJ, Bailey TS, Polonsky WH. Improvement in Patient-Reported Outcomes in Adults with Type 1 Diabetes Treated with Sotagliflozin plus Insulin Versus Insulin Alone. Diabetes Technol Ther. 2021 Jan;23(1):70-77. doi: 10.1089/dia.2020.0068.

Reference Type DERIVED
PMID: 32721228 (View on PubMed)

Ervin C, Joish VN, Evans E, DiBenedetti D, Reaney M, Preblick R, Castro R, Danne T, Buse JB, Lapuerta P. Insights Into Patients' Experience With Type 1 Diabetes: Exit Interviews From Phase III Studies of Sotagliflozin. Clin Ther. 2019 Nov;41(11):2219-2230.e6. doi: 10.1016/j.clinthera.2019.09.003. Epub 2019 Oct 3.

Reference Type DERIVED
PMID: 31587812 (View on PubMed)

Danne T, Cariou B, Buse JB, Garg SK, Rosenstock J, Banks P, Kushner JA, McGuire DK, Peters AL, Sawhney S, Strumph P. Improved Time in Range and Glycemic Variability With Sotagliflozin in Combination With Insulin in Adults With Type 1 Diabetes: A Pooled Analysis of 24-Week Continuous Glucose Monitoring Data From the inTandem Program. Diabetes Care. 2019 May;42(5):919-930. doi: 10.2337/dc18-2149. Epub 2019 Mar 4.

Reference Type DERIVED
PMID: 30833371 (View on PubMed)

Buse JB, Garg SK, Rosenstock J, Bailey TS, Banks P, Bode BW, Danne T, Kushner JA, Lane WS, Lapuerta P, McGuire DK, Peters AL, Reed J, Sawhney S, Strumph P. Sotagliflozin in Combination With Optimized Insulin Therapy in Adults With Type 1 Diabetes: The North American inTandem1 Study. Diabetes Care. 2018 Sep;41(9):1970-1980. doi: 10.2337/dc18-0343. Epub 2018 Jun 24.

Reference Type DERIVED
PMID: 29937430 (View on PubMed)

Other Identifiers

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LX4211.1-309-T1DM

Identifier Type: -

Identifier Source: org_study_id

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