Twelve Month Safety and Efficacy Study of CVT-301 In Parkinson's Disease Patients With OFF Episodes

NCT ID: NCT02242487

Last Updated: 2019-08-14

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

325 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-03-31

Study Completion Date

2018-05-31

Brief Summary

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This study is a 12-month, dose-level blinded, multicenter study of 2 inhaled dose levels of CVT-301 for the treatment of up to 5 OFF episodes per day in PD patients experiencing motor fluctuations (OFF episodes). All patients will receive active treatment, but patients will be blinded to dose level. This will serve as an extension to the CVT-301-004 (NCT02240030) study for those patients who participated in that study and remain eligible for this study. In addition, patients who previously completed the CVT-301-003 (NCT01777555), CVT-301-009 (NCT02807675) and CVT-301-005 (NCT02352363) (observational arm completers), as well as CVT-301 naïve patients may be enrolled if they meet the CVT-301-004E eligibility criteria.

Detailed Description

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Conditions

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Idiopathic Parkinson's Disease

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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CVT-301 Low Dose

Capsules of levodopa inhalational powder used up to 5 times/day for OFF episodes for 12 months duration

Group Type EXPERIMENTAL

CVT-301

Intervention Type DRUG

CVT-301 High Dose

Capsules of levodopa inhalational powder used up to 5 times/day for OFF episodes for 12 months duration

Group Type EXPERIMENTAL

CVT-301

Intervention Type DRUG

Interventions

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CVT-301

Intervention Type DRUG

Other Intervention Names

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Inhaled levodopa

Eligibility Criteria

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Inclusion Criteria

* Idiopathic Parkinson's Disease (PD) diagnosed between the ages of 30 and 80 years;
* Hoehn and Yahr Stage 1-3 in an "on" state;
* Require levodopa-containing medication regimen at least 3 times during the waking day;
* Experience motor fluctuations with a minimum of 2 hours of average daily "off" time per waking day (excluding early morning "off" time) and demonstrate levodopa responsiveness;
* Are on stable PD medication regimen;
* Total daily levodopa (LD) dose \<1600 mg/day;
* Able to perform a spirometry maneuver in the ON and OFF states
* Normal cognition confirmed by Mini Mental State Examination (MMSE) score ≥25 ;

Exclusion Criteria

* Pregnant or lactating females;
* Previous surgery for PD or plan to have stereotactic surgery during the study period. Patients who have had deep brain stimulation \[DBS\] will also be excluded unless the procedure was performed more than 6 months prior to study enrollment.
* History of psychotic symptoms requiring treatment, or suicide ideation or attempt within last year;
* Known contraindication to the use of levodopa;
* Any significant condition, severe concurrent disease, abnormality or finding that would make patients unsuitable or may compromise patient safety;
* Any any contraindication to performing routine spirometry.
Minimum Eligible Age

30 Years

Maximum Eligible Age

86 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Acorda Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Charles Oh, MD

Role: STUDY_DIRECTOR

Acorda Therapeutics

Locations

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Acorda Site #5020

Scottsdale, Arizona, United States

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Acorda Site #5042

Fresno, California, United States

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Acorda Site #5064

Fullerton, California, United States

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Acorda Site #5035

Loma Linda, California, United States

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Acorda Site #5027

Long Beach, California, United States

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Acorda Site #5037

Los Angeles, California, United States

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Acorda Site #5070

Pasadena, California, United States

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Acorda Site #5047

Reseda, California, United States

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Acorda Site #5068

Santa Ana, California, United States

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Acorda Site #5069

Torrance, California, United States

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Acorda Site #5052

Washington D.C., District of Columbia, United States

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Acorda Site #5046

Atlantis, Florida, United States

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Acorda Site #5053

Aventura, Florida, United States

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Acorda Site #5013

Boca Raton, Florida, United States

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Acorda Site #5016

Jacksonville, Florida, United States

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Acorda Site #5071

Maitland, Florida, United States

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Acorda Site #5044

Orlando, Florida, United States

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Acorda Site #5060

Palm Beach Gardens, Florida, United States

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Acorda Site #5001

Port Charlotte, Florida, United States

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Acorda Site #5065

St. Petersburg, Florida, United States

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Acorda Site #5012

Tampa, Florida, United States

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Acorda Site #5040

Atlanta, Georgia, United States

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Acorda Site #5025

Chicago, Illinois, United States

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Acorda Site #5030

Chicago, Illinois, United States

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Acorda Site #5011

Elk Grove Village, Illinois, United States

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Acorda Site #5003

Kansas City, Kansas, United States

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Acorda Site #5067

Baton Rouge, Louisiana, United States

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Acorda Site #5057

Baltimore, Maryland, United States

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Acorda Site #5056

Boston, Massachusetts, United States

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Acorda Site #5018

Boston, Massachusetts, United States

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Acorda Site #5002

Bingham Farms, Michigan, United States

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Acorda Site #5014

West Bloomfield, Michigan, United States

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Acorda Site #5041

Golden Valley, Minnesota, United States

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Acorda Site #5006

St Louis, Missouri, United States

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Acorda Site #5023

Las Vegas, Nevada, United States

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Acorda Site #5028

Albany, New York, United States

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Acorda Site #5039

Brooklyn, New York, United States

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Acorda Site #5031

New York, New York, United States

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Acorda Site #5032

New York, New York, United States

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Acorda Site #5004

New York, New York, United States

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Acorda Site #5038

Syracuse, New York, United States

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Acorda Site #5048

Charlotte, North Carolina, United States

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Acorda Site #5005

Cleveland, Ohio, United States

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Acorda Site #5050

Norwood, Ohio, United States

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Acorda Site #5062

Portland, Oregon, United States

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Acorda Site #5036

Allentown, Pennsylvania, United States

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Acorda Site #5010

Philadelphia, Pennsylvania, United States

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Acorda Site #5058

Willow Grove, Pennsylvania, United States

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Acorda Site #5022

Charleston, South Carolina, United States

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Acorda Site #5029

Nashville, Tennessee, United States

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Acorda Site #5019

Houston, Texas, United States

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Acorda Site #5045

Houston, Texas, United States

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Acorda Site #5049

Henrico, Virginia, United States

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Acorda Site #5059

Virginia Beach, Virginia, United States

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Acorda Site #5051

Kirkland, Washington, United States

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Acorda Site #5103

London, Ontario, Canada

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Acorda Site #5104

Ottawa, Ontario, Canada

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Acorda Site #5105

Toronto, Ontario, Canada

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Acorda Site #5201

Prague, , Czechia

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Acorda Site #5203

Prague, , Czechia

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Acorda Site #5305

Gdansk, Zappa, Poland

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Acorda Site #5304

Katowice, , Poland

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Acorda Site #5306

Krakow, , Poland

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Acorda Site #5303

Krakow, , Poland

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Acorda Site #5307

Krakow, , Poland

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Acorda Site #5302

Lodz, , Poland

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Acorda Site #5308

Warsaw, , Poland

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Acorda Site #5301

Warsaw, , Poland

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Acorda Site #5407

Pamplona, Navarre, Spain

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Acorda Site #5404

Barcelona, , Spain

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Acorda Site #5406

Barcelona, , Spain

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Acorda Site #5405

Madrid, , Spain

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Acorda Site #5403

San Sebastián, , Spain

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Acorda Site #5401

Sant Cugat del Vallès, , Spain

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Countries

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United States Canada Czechia Poland Spain

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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http://cvt301.acordatrials.com/en/patient/?src=clinicaltrialsgov004

Click here for more information about this study:CVT-301-004E

Other Identifiers

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CVT-301-004E

Identifier Type: -

Identifier Source: org_study_id

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